NCT01917630

Brief Summary

To determine the effects of 12 weeks administration of different dose levels of ALV003 on the mucosal lining of the small intestine and symptoms in celiac disease patients.

Trial Health

50
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
500

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Aug 2013

Geographic Reach
6 countries

88 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2013

Completed
1 day until next milestone

First Submitted

Initial submission to the registry

August 2, 2013

Completed
5 days until next milestone

First Posted

Study publicly available on registry

August 7, 2013

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2015

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2015

Completed
Last Updated

December 17, 2014

Status Verified

December 1, 2014

Enrollment Period

1.7 years

First QC Date

August 2, 2013

Last Update Submit

December 16, 2014

Conditions

Keywords

Celiac diseaseGluten-free dietCoeliac diseaseCeliac sprue

Outcome Measures

Primary Outcomes (1)

  • Efficacy: Intestinal mucosal morphometry

    Change in villus height to crypt depth (Vh:Cd) ratio between baseline and week 12

    12 weeks

Secondary Outcomes (2)

  • Efficacy: Intestinal intraepithelial lymphocyte density

    12 weeks

  • Safety: safety and tolerability of ALV003

    12 weeks

Other Outcomes (2)

  • Celiac disease-specific serology

    12 weeks

  • Quality of life

    12 weeks

Study Arms (2)

ALV003

EXPERIMENTAL
Drug: ALV003

Placebo

PLACEBO COMPARATOR
Drug: placebo

Interventions

ALV003DRUG

ALV003 is an orally administered mixture of two enzymes (cysteine endoprotease B-isoform 2 and prolyl endopeptidase)

ALV003
Placebo

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ages 18 to 80 years
  • Physician diagnosed celiac disease
  • Adherence to a gluten-free diet
  • Experiencing symptoms of celiac disease over a 1-month period
  • Willing to take study medication for 12 weeks
  • Willing to comply with all study procedures
  • Sign informed consent

You may not qualify if:

  • Active inflammatory bowel disease
  • Active dermatitis herpetiformis
  • Use of certain specific medications prior to entry
  • History of alcohol or illicit drug abuse in previous 6 months
  • Pregnant or lactating
  • Received any experimental drug within 30 days of enrollment
  • Uncontrolled chronic disease or condition

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (88)

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Decatur, Alabama, 35601, United States

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Huntsville, Alabama, 35801, United States

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Huntsville, Alabama, 35802, United States

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Scottsdale, Arizona, 85259, United States

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Scottsdale, Arizona, 85260, United States

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Tucson, Arizona, 85712, United States

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Los Angeles, California, 90025, United States

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Los Angeles, California, 90027, United States

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Modesto, California, 95355, United States

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Newport Beach, California, 92660, United States

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Oceanside, California, 92056, United States

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Orange, California, 92868, United States

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Palo Alto, California, 94301, United States

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Poway, California, 92064, United States

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Roseville, California, 95661, United States

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San Diego, California, 92114, United States

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San Jose, California, 95117, United States

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San Marcos, California, 92069, United States

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Aurora, Colorado, 80045, United States

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Bridgeport, Connecticut, 06606, United States

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Boynton Beach, Florida, 33426, United States

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Hollywood, Florida, 33021, United States

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Jacksonville, Florida, 32224, United States

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Jacksonville, Florida, 32256, United States

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Largo, Florida, 33777, United States

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Miami, Florida, 33137, United States

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Miami, Florida, 33165, United States

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Naples, Florida, 34102, United States

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Orlando, Florida, 32806, United States

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Atlanta, Georgia, 30328, United States

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Idaho Falls, Idaho, 83404, United States

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Meridian, Idaho, 83642, United States

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Chicago, Illinois, 60612, United States

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Chicago, Illinois, 60637, United States

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Evanston, Illinois, 60201, United States

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Oak Lawn, Illinois, 60453, United States

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Des Moines, Iowa, 50266, United States

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Topeka, Kansas, 66606, United States

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Baltimore, Maryland, 21229, United States

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Chevy Chase, Maryland, 20815, United States

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Boston, Massachusetts, 02215, United States

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Chesterfield, Michigan, 48047, United States

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Wyoming, Michigan, 49519, United States

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Rochester, Minnesota, 55905, United States

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Jackson, Mississippi, 39202, United States

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Kansas City, Missouri, 64131, United States

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Mexico, Missouri, 65265, United States

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Marlton, New Jersey, 08053, United States

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Great Neck, New York, 11023, United States

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New York, New York, 10032, United States

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Poughkeepsie, New York, 12601, United States

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Rochester, New York, 14618, United States

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Asheville, North Carolina, 28801, United States

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Salisbury, North Carolina, 28144, United States

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Winston-Salem, North Carolina, 27103, United States

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Cincinnati, Ohio, 45219, United States

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Cleveland, Ohio, 44122, United States

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Dayton, Ohio, 45415, United States

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Mentor, Ohio, 44060, United States

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Oklahoma City, Oklahoma, 73103, United States

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Tulsa, Oklahoma, 74104, United States

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Portland, Oregon, 97225, United States

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Malvern, Pennsylvania, 19355, United States

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Philadelphia, Pennsylvania, 19107, United States

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Pittsburgh, Pennsylvania, 15243, United States

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Warwick, Rhode Island, 02886, United States

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Mt. Pleasant, South Carolina, 29464, United States

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Chattanooga, Tennessee, 37421, United States

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Hermitage, Tennessee, 37076, United States

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Houston, Texas, 77094, United States

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Irving, Texas, 75063, United States

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Southlake, Texas, 76092, United States

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West Jordan, Utah, 84088, United States

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Alexandria, Virginia, 22304, United States

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Virginia Beach, Virginia, 23454, United States

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Bellevue, Washington, 98004, United States

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Seattle, Washington, 98104, United States

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Madison, Wisconsin, 53705, United States

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Milwaukee, Wisconsin, 53215, United States

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Edmonton, Alberta, T6G 2X8, Canada

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Vancouver, British Columbia, V6Z 2K5, Canada

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Hamilton, Ontario, L8S 4K1, Canada

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Ottawa, Ontario, K2H 7B3, Canada

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Toronto, Ontario, M9C 4Z5, Canada

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Tampere, Finland

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Galway, Ireland

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Oslo, Norway

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Sheffield, S11 7FF, United Kingdom

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Related Publications (2)

  • Syage JA, Murray JA, Green PHR, Khosla C. Latiglutenase Improves Symptoms in Seropositive Celiac Disease Patients While on a Gluten-Free Diet. Dig Dis Sci. 2017 Sep;62(9):2428-2432. doi: 10.1007/s10620-017-4687-7. Epub 2017 Jul 28.

  • Murray JA, Kelly CP, Green PHR, Marcantonio A, Wu TT, Maki M, Adelman DC; CeliAction Study Group of Investigators. No Difference Between Latiglutenase and Placebo in Reducing Villous Atrophy or Improving Symptoms in Patients With Symptomatic Celiac Disease. Gastroenterology. 2017 Mar;152(4):787-798.e2. doi: 10.1053/j.gastro.2016.11.004. Epub 2016 Nov 15.

MeSH Terms

Conditions

Celiac Disease

Interventions

ALV003

Condition Hierarchy (Ancestors)

Malabsorption SyndromesIntestinal DiseasesGastrointestinal DiseasesDigestive System DiseasesMetabolic DiseasesNutritional and Metabolic Diseases

Study Officials

  • Daniel Adelman, MD

    Alvine Pharmaceuticals Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 2, 2013

First Posted

August 7, 2013

Study Start

August 1, 2013

Primary Completion

April 1, 2015

Study Completion

June 1, 2015

Last Updated

December 17, 2014

Record last verified: 2014-12

Locations