NCT01884311

Brief Summary

The main objective of the study is to determine the pharmacokinetics profile of Subgam-VF. The secondary objectives are to assess the safety of Subgam-VF and refine the dose adjustment coefficient for Subgam-VF needed for subjects switching from prior intravenous immunoglobulin (IGIV) therapy.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
38

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Aug 2015

Geographic Reach
1 country

16 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 14, 2013

Completed
10 days until next milestone

First Posted

Study publicly available on registry

June 24, 2013

Completed
2.2 years until next milestone

Study Start

First participant enrolled

August 20, 2015

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 25, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 25, 2017

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

September 12, 2018

Completed
Last Updated

September 12, 2018

Status Verified

August 1, 2018

Enrollment Period

1.8 years

First QC Date

June 14, 2013

Results QC Date

February 28, 2018

Last Update Submit

August 14, 2018

Conditions

Keywords

Primary Immune Deficiency DisordersCommon Variable ImmunodeficiencyX-linked agammaglobulinaemiaHyper-IgM SyndromeSubcutaneousImmunoglobulins

Outcome Measures

Primary Outcomes (1)

  • Data (Derived From Absolute Concentration) Were Pooled With Historical Data and a Treatment Variable Defined (Subgam-VF or Gammaplex 5% IGIV). Outcome Measure Defined as Log Transformed sAUC0-t Standardized to One Week.

    Log transformed sAUC0-t, (AUC0-t standardized to one week) were analysed using a multiple linear regression model fitted including treatment, allowing for variability between treatment groups. The mean difference (Subgam-VF or Gammaplex IGIV 5%) between treatments with 90% Confidence Interval (CI) were back transformed to give an estimate of the ratio (Subgam-VF/ Gammaplex 5% IGIV) of sAUC(0-t). Data was collected at the following timepoints after week 21 of the clinical trial over a period of 1 week: Pre-dose on Day 0 and post-dose at days 1, 2, 3, 5 and 7.

    1 week

Secondary Outcomes (3)

  • Number of Participants Who Experienced AEs Based on Treatment-emergent AEs (TEAEs)

    30 weeks

  • Dose Refinement in Switching From Gammaplex 5% IGIV to Subgam-VF

    Week 26

  • Number of Infusion Site Reactions

    30 weeks

Other Outcomes (1)

  • Population PK Model for IgG in PID Patients for Alternative Dosing Schedules.

    30 months

Study Arms (1)

Subgam-VF

EXPERIMENTAL

Subgam-VF is a 16% IgG and will be administered weekly, by subcutaneous infusion. The total duration of treatment will be for 26 weeks.

Biological: Subgam

Interventions

SubgamBIOLOGICAL

Subgam-VF dose will be given as 1.37 of the established IGIV dose (expressed in mg/kg/week) for 26 weeks (26 infusions) beginning one week after the last IGIV infusion. Dose of Subgam-VF will then be adjusted based on the ratio of the Immunoglobulin G (IgG) average concentration achieved with Subgam-VF compared to IGIV.

Also known as: Subgam-VF
Subgam-VF

Eligibility Criteria

Age2 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Aged between 2 and 75 years (at time of initial consent).
  • Body Mass Index (BMI) \< 46 for adults (aged 16 years \& older), \& BMI \< 28 for children.
  • Diagnosed with primary immunodeficiency disease e.g. common variable immunodeficiency, X-linked \& autosomal forms of agammaglobulinaemia, hyper-IgM syndrome, Wiskott-Aldrich syndrome.
  • Currently receiving a licensed (or investigational stage III, IIIb) IGIV or SCIG and
  • IGIV dose is between 300 and 800 mg/kg/month. SCIG dose is between 110 \& 300 mg/kg/week;
  • Dose is stable for at least the past three months (i.e. consistent mg/kg +/- 5%);
  • The infusion interval is every 21 or 28 days for IGIV \& seven days for SCIG;
  • Has a documented trough level of ≥ 6 g/L (600 mg/dL) on current IgG therapy. If not available can be obtained at the screening visit, Visit 1 (Week 0).
  • Female subjects who are (or become) sexually active must practice contraception by using a method of proven reliability for the duration of the study.
  • Females of child-bearing potential, (defined from the onset of menstruation to one year post menopause), must have a negative result on a urine HCG-based pregnancy test.
  • Willing to comply with all aspects of the protocol, including blood sampling, for the duration of the study.
  • Signed an informed consent form. In the case of subjects under the legal age the parent/guardian will sign an informed consent form \& where appropriate the subject will sign an assent form.

You may not qualify if:

  • Has a history of any severe anaphylactic reaction to blood or any blood-derived product.
  • Has selective IgA deficiency or has a history of antibodies to IgA.
  • Has clinically significant impairment of cellular or innate immunity at the discretion of the Investigator
  • Has evidence of an active infection at the time of enrolment (i.e. on day of first infusion). Subjects who are asymptomatic but have not completed their course of antibiotics are eligible.
  • Has previously completed or withdrawn from this study.
  • Is currently receiving, or has received, any investigational agent within the prior three months, unless it is an investigational stage III, IIIb IGIV or SCIG.
  • Is pregnant (confirmed by a positive result on an HCG-based pregnancy test) or is nursing.
  • Is positive for any of the following at screening:
  • Serological test for HIV 1\&2, HCV, or HBsAg
  • Has levels at screening greater than 2.5 times the upper limit of normal as defined at the central laboratory of any of the following:
  • Alanine transaminase (ALT)
  • Aspartate transaminase (AST)
  • Has severe renal impairment (defined as serum creatinine greater than two times the upper limit of normal or BUN greater than two times the upper limit of normal for the range of the laboratory doing the analysis); the subject is on dialysis; or has a history of acute renal failure.
  • Is known to abuse alcohol, opiates, psychotropic agents, or other chemicals or drugs, or has done so within the past 12 months.
  • Has a history of DVT, or thrombotic complications of IgG therapy, or a prior diagnosis of thrombophilia.
  • +9 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (16)

Arizona Allergy Associates

Chandler, Arizona, 85224, United States

Location

University of California, Irvine

Irvine, California, 92697, United States

Location

University of California San Diego-- Rady's Children's Hospital

San Diego, California, 92123, United States

Location

Immunoe International Research

Centennial, Colorado, 80112, United States

Location

Allergy Associate of the Palm Beaches

North Palm Beach, Florida, 33408, United States

Location

Ann and Robert H Lurie Children's Hospital

Chicago, Illinois, 60611, United States

Location

Cardinal Glennon Children's Medical Center

Minneapolis, Minnesota, 63104, United States

Location

Optimed Research

Columbus, Ohio, 43235, United States

Location

Oklahoma Institute of Allergy & Asthma Clinical Research, LLC

Oklahoma City, Oklahoma, 73131, United States

Location

Pennsylvania State University

Hershey, Pennsylvania, 174033, United States

Location

Dallas Allergy Immunology

Dallas, Texas, 75230, United States

Location

AARA Research Center

Dallas, Texas, 75231, United States

Location

University of Utah

Salt Lake City, Utah, 84112, United States

Location

O&O Alpan, LLC

Fairfax, Virginia, 22030, United States

Location

Bellingham Asthma Allergy Clinic

Bellingham, Washington, 98225, United States

Location

The Medical College of Wisconsin/Children's Hospital of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

Primary Immunodeficiency DiseasesCommon Variable ImmunodeficiencyBruton type agammaglobulinemiaHyper-IgM Immunodeficiency Syndrome

Condition Hierarchy (Ancestors)

Genetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesImmunologic Deficiency SyndromesImmune System DiseasesDysgammaglobulinemiaBlood Protein DisordersHematologic DiseasesHemic and Lymphatic Diseases

Results Point of Contact

Title
European Medical Affairs Lead
Organization
Bio Products Laboratory Ltd

Study Officials

  • Eric Wolford

    Bio Products Laboratory Limited

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
OTHER
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 14, 2013

First Posted

June 24, 2013

Study Start

August 20, 2015

Primary Completion

May 25, 2017

Study Completion

May 25, 2017

Last Updated

September 12, 2018

Results First Posted

September 12, 2018

Record last verified: 2018-08

Locations