NCT01882062

Brief Summary

The purpose of this project is to study the efficacy of an anaplerotic treatment on brain energy profile evolution at an early stage of the Huntington disease.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
10

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started May 2013

Shorter than P25 for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2013

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

June 18, 2013

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 20, 2013

Completed
11 days until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2013

Completed
2.7 years until next milestone

Results Posted

Study results publicly available

March 24, 2016

Completed
Last Updated

March 25, 2026

Status Verified

December 1, 2013

Enrollment Period

2 months

First QC Date

June 18, 2013

Results QC Date

April 30, 2015

Last Update Submit

March 6, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Ratio of Inorganic Phosphate (Pi) Over Phosphocreatine (PCr): Pi/PCr

    The Pi/PCr Ratio is a measure of brain metabolism and it is an index of mitochondrial oxidative regulation. A 6-cm 31P transmit/receive surface coil (RAPID Biomedical GmbH, Rimpar, Germany) was used to collect free induction decays for 4 minutes at rest, 8 minutes during visual activation with 6-Hz red/black checkerboard flashes, and 8 minutes after stimulation. Subjects were able to focus on the flashes with a nonmagnetic mirror mounted above their eyes while all lights in the room were turned off. The Pi/PCr ratio was then calculated to determine brain response to cortical activation.

    visit 1 (baseline), visit 2 (after 1 month of treatment)

Secondary Outcomes (1)

  • Correlation Between Primary Outcome Measure and Clinical Parameters

    1 month

Study Arms (1)

Triheptanoin 1g/kg/day

EXPERIMENTAL

All patients received Triheptanoin oil at 1g/kg/day during 1 month

Drug: Triheptanoin 1g/kg/day

Interventions

Triheptanoin 1g/kg/day

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • \< UHDRS \< 50
  • Age \> 18 years
  • Ability to undergo MR scanning
  • Covered by french social security

You may not qualify if:

  • Evidence of psychiatric disorder
  • Attendant neurological disorder
  • Contraindications to MRI (claustrophobia, metallic or material implants)
  • Severe head injury
  • Unable to understand the protocol
  • Pregnancy
  • Failure to give informed consent
  • Unwillingness to be informed in case of abnormal MRI

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Brain and Spine Institute

Paris, 75013, France

Location

Related Publications (1)

  • Adanyeguh IM, Rinaldi D, Henry PG, Caillet S, Valabregue R, Durr A, Mochel F. Triheptanoin improves brain energy metabolism in patients with Huntington disease. Neurology. 2015 Feb 3;84(5):490-5. doi: 10.1212/WNL.0000000000001214. Epub 2015 Jan 7.

Related Links

MeSH Terms

Conditions

Huntington Disease

Interventions

triheptanoin

Condition Hierarchy (Ancestors)

Basal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesDementiaChoreaDyskinesiasMovement DisordersHeredodegenerative Disorders, Nervous SystemNeurodegenerative DiseasesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCognition DisordersNeurocognitive DisordersMental Disorders

Results Point of Contact

Title
Dr Fanny MOCHEL
Organization
Inserm U1127

Publication Agreements

PI is Sponsor Employee
Yes
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER GOV
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 18, 2013

First Posted

June 20, 2013

Study Start

May 1, 2013

Primary Completion

July 1, 2013

Study Completion

July 1, 2013

Last Updated

March 25, 2026

Results First Posted

March 24, 2016

Record last verified: 2013-12

Locations