NCT01856478

Brief Summary

This randomized, open-label, phase III study will be performed in patients with recurrent and/or metastatic head and neck cancer which has progressed after platinum-based therapy. The objectives of this trial are to compare the efficacy and safety of afatinib versus methotrexate.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
340

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jun 2013

Longer than P75 for phase_3

Geographic Reach
8 countries

53 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 15, 2013

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 17, 2013

Completed
21 days until next milestone

Study Start

First participant enrolled

June 7, 2013

Completed
5.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 22, 2018

Completed
6.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 2, 2024

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

January 12, 2026

Completed
Last Updated

January 12, 2026

Status Verified

January 1, 2026

Enrollment Period

5.2 years

First QC Date

May 15, 2013

Results QC Date

October 1, 2025

Last Update Submit

January 7, 2026

Conditions

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS)

    Progression-free survival (PFS) was defined as the time from the date of randomization to the date of disease progression (PD) evaluated according to Response Evaluation Criteria In Solid Tumors (RECIST) version 1.1 (v1.1). or to the date of death from any cause, whichever occurs first. PD was defined as at least a 20% increase in the sum of diameters of target lesions, taking as reference the smallest sum on study. PFS parameters were calculated based on Kaplan-Meier curves generated for each group.

    From randomization until disease progression, death, or primary completion date, whichever occurs first. Up to 35 months.

Secondary Outcomes (12)

  • Objective Response (OR)

    From randomization until earliest of disease progression, death, or interim cut-off date (11-Apr-2019). Up to 35 months.

  • Overall Survival (OS)

    From randomization until death. Up to 6 years.

  • Time to Deterioration in Global Health Status

    From randomization until the earliest of deterioration, death, discontinuation with death within 4 weeks, or primary analysis date. Up to 30 months.

  • Time to Deterioration in Pain Symptoms

    From randomization until the earliest of deterioration, death, discontinuation with death within 4 weeks, or primary analysis date. Up to 19 months.

  • Time to Deterioration in Swallowing

    From randomization until the earliest of deterioration, death, discontinuation with death within 4 weeks, or primary analysis date. Up to 19 months.

  • +7 more secondary outcomes

Study Arms (2)

Afatinib 40 mg

EXPERIMENTAL

Patients with recurrent and/or metastatic (R/M) head and neck squamous cell carcinoma (HNSCC) who progressed after being treated with platinum-based therapy took, orally, once daily one film-coated tablet of afatinib. Patients started with a 40 milligrams (mg) dose which could be escalated to 50 mg and/or reduced to 40 mg, 30 mg, or 20 mg, according to the absence of presence of drug-related adverse events (AEs).

Drug: Afatinib

Methotrexate 40 mg

ACTIVE COMPARATOR

Patients with recurrent and/or metastatic (R/M) head and neck squamous cell carcinoma (HNSCC) who progressed after being treated with platinum-based therapy received once weekly an intravenous bolus injection of methotrexate. Patients started with a 40 milligrams (mg) per square meter of body surface area (m\^2) dose which could be escalated to 50 mg/m\^2 and/or reduced to 40 mg/m\^2, 30 mg/m\^2, or 20 mg/m\^2, according to the absence of presence of drug-related adverse events (AEs).

Drug: Methotrexate

Interventions

intravenous bolus injection once weekly

Methotrexate 40 mg

oral intake of one film-coated tablet once daily

Afatinib 40 mg

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed squamous cell carcinoma of the oral cavity, oropharynx, hypopharynx or larynx, which has recurred/metastasised and is not amenable for salvage surgery or radiotherapy.
  • Documented progressive disease based on investigator assessment according to RECIST, following receipt of a cisplatin and/or carboplatin and/or Nedaplatin based regimen administered for recurrent and/or metastatic disease independent of whether patient progressed during or after platinum based therapy.
  • Measurable disease according to RECIST (version 1.1).
  • Eastern Cooperative Oncology Group (ECOG) performance status 0 or 1 at Visit 2.
  • Male and female patients age is 18 years or older
  • Signed and dated written informed consent that is in compliance with ICH-GCP and local law.

You may not qualify if:

  • Progressive disease within three months after completion of curatively intended treatment for locoregionally advanced or for metastatic head and neck squamous cell cancer (HNSCC).
  • Primary tumour site nasopharynx (of any histology), sinuses, and/or salivary glands.
  • Any other than one previous platinum based systemic regimen given for recurrent and/or metastatic disease, with the exception of immunotherapy used either before or after platinum based treatment. Re-challenge with the platinum based regimen after a temporary break is considered an additional line regimen only in case of progression within the break.
  • Prior treatment with EGFR-targeted small molecules.
  • Treatment with any investigational drug less than four weeks or anti-cancer therapy less than three weeks prior to randomization (except palliative radiotherapy to bones to alleviate pain).
  • Unresolved chronic toxicity, other than hearing loss, tinnitus or dry mouth, CTCAE grade \>2 from previous anti-cancer therapy or unresolved skin toxicities CTCAE grade \>1 and/or diarrhoea CTCAE grade \>1 caused by prior treatment with EGFR targeted antibodies.
  • Previous tumour bleeding CTCAE grade =3.
  • Requirement for treatment with any of the prohibited concomitant medications.
  • Major surgical or planned procedure less than four weeks prior to randomization (isolated biopsies are not considered as major surgical procedures).
  • Any other malignancy unless free of disease for at least five years except for:
  • Appropriately treated superficial basal cell skin cancer
  • Surgically cured cervical cancer in situ
  • For Korea: endoscopically cured superficial esophageal and/or gastric cancer is allowed
  • Known lesion or signs of brain metastasis.
  • Known pre-existing interstitial lung disease (ILD).
  • +14 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (53)

Beijing Chao-Yang Hospital

Beijing, 100020, China

Location

Cancer Hospital of Chinese Academy of Medical Science

Beijing, 100021, China

Location

Navy General Hospital

Beijing, 100037, China

Location

Peking Union Medical College Hospital

Beijing, 100730, China

Location

The First Affiliated Hospital Of Bengbu Medical College

Bengbu, 233004, China

Location

The First Hospital of Jilin University

Changchun, 130021, China

Location

Sichuan Cancer Hospital

Chengdu, 610041, China

Location

West China Hospital

Chengdu, 610042, China

Location

Sun Yat-Sen University Cancer Center

Guangzhou, 510060, China

Location

Zhejiang Cancer Hospital

Hangzhou, 310022, China

Location

Harbin Medical University Cancer Hospital

Harbin, 150081, China

Location

the 81th Hospital of PLA

Nanjing, 210002, China

Location

Renji Hospital Shanghai Jiaotong Univesrity School of Medicine

Shanghai, 200001, China

Location

Shanghai Changzheng Hospital

Shanghai, 200003, China

Location

Shanghai Ninth People's Hospital

Shanghai, 200011, China

Location

Fudan University Shanghai Cancer Center

Shanghai, 200032, China

Location

Shanghai Ninth People's Hospital

Shanghai, 200125, China

Location

Wuhan Union Hospital

Wuhan, 430022, China

Location

Tongji Hospital, Tongji University

Wuhan, 430030, China

Location

Alexandria Clinical Research Center

Alexandria, 21131, Egypt

Location

National Cancer Institute, Cairo University

Cairo, 11796, Egypt

Location

Mansoura University Faculty of Medicine

Dakahlia, 35516, Egypt

Location

Pamela Youde Nethersole Eastern Hospital

Hong Kong, 999077, Hong Kong

Location

Queen Mary Hospital

Hong Kong, 999077, Hong Kong

Location

Prince of Wales Hospital

Shatin, 999077, Hong Kong

Location

Sujan Surgical Cancer Hospital

Amravati, 444606, India

Location

Pristine Hospital

Bengaluru, 560086, India

Location

Acharya Tulsi Regional Cancer Treatment & Research Institute

Bikaner, 334001, India

Location

Rajiv Gandhi Government General Hospital

Chennai, 600003, India

Location

M N J Institute of Oncology and Regional Cancer Centre

Hyderabad, 500004, India

Location

Geetanjali Medical College and Hospital

Jaipur, 313002, India

Location

J K Cancer Institute

Kanpur, 208005, India

Location

B. P .Poddar Hospital & Medical Research Ltd.

Kolkata, West Bengal, 700053, India

Location

King George Medical University

Lucknow, 226003, India

Location

Government Medical College & Hospital

Nagpur, 440009, India

Location

Shatabdi Hospital, Nashik

Nashik, 422002, India

Location

Ruby Hall Clinic

Pune, 411001, India

Location

Noble Hospital Pvt Ltd

Pune, 411013, India

Location

Perpetual Succour Hospital (Cebu)

Cebu City, 6000, Philippines

Location

St. Luke's Medical Center

Quezon City, 1102, Philippines

Location

National Cancer Center

Goyang, 10408, South Korea

Location

Severance Hospital

Seoul, 120-752, South Korea

Location

Samsung Medical Center

Seoul, 135-710, South Korea

Location

The Catholic University of Korea, Seoul St.Mary's Hospital

Seoul, 137-701, South Korea

Location

Asan Medical Center

Seoul, 138-736, South Korea

Location

Keelung Chang Gung Memorial Lover's Lake Branch

Keelung, 204, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 407, Taiwan

Location

National Taiwan University Hospital

Taipei, 100, Taiwan

Location

Tri-Service General Hospital

Taipei, 11490, Taiwan

Location

Maharaj Nakom Chiangmai Hospital

Chiang Mai, 50200, Thailand

Location

Srinagarind Hospital

Muang, 40002, Thailand

Location

Naresuan University Hospital

Phitsanulok, 65000, Thailand

Location

Songklanagarind Hospital

Songkhla, 90110, Thailand

Location

Related Publications (1)

  • Guo Y, Ahn MJ, Chan A, Wang CH, Kang JH, Kim SB, Bello M, Arora RS, Zhang Q, He X, Li P, Dechaphunkul A, Kumar V, Kamble K, Li W, Kandil A, Cohen EEW, Geng Y, Zografos E, Tang PZ. Afatinib versus methotrexate as second-line treatment in Asian patients with recurrent or metastatic squamous cell carcinoma of the head and neck progressing on or after platinum-based therapy (LUX-Head & Neck 3): an open-label, randomised phase III trial. Ann Oncol. 2019 Nov 1;30(11):1831-1839. doi: 10.1093/annonc/mdz388.

Related Links

MeSH Terms

Conditions

Head and Neck Neoplasms

Interventions

MethotrexateAfatinib

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasms

Intervention Hierarchy (Ancestors)

AminopterinPterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic CompoundsAmidesOrganic ChemicalsQuinazolines

Results Point of Contact

Title
Boehringer Ingelheim, Call Center
Organization
Boehringer Ingelheim

Study Officials

  • Boehringer Ingelheim

    Boehringer Ingelheim

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 15, 2013

First Posted

May 17, 2013

Study Start

June 7, 2013

Primary Completion

August 22, 2018

Study Completion

October 2, 2024

Last Updated

January 12, 2026

Results First Posted

January 12, 2026

Record last verified: 2026-01

Data Sharing

IPD Sharing
Will share

Once the criteria in section "Time Frame" are fulfilled, researchers can use the following link https://www.mystudywindow.com/msw/datasharing to request access to the clinical study documents regarding this study, and upon a signed "Document Sharing Agreement". Furthermore, researchers can request access to the clinical study data, for this and other listed studies, after the submission of a research proposal and according to the terms outlined in the website.

Shared Documents
STUDY PROTOCOL, SAP, CSR
Time Frame
One year after the approval has been granted by major Regulatory Authorities and after the primary manuscript has been accepted for publication, or after termination of the development program.
Access Criteria
For study documents - upon signing of a 'Document Sharing Agreement'. For study data - 1. after the submission and approval of the research proposal (checks will be performed by the sponsor and/or the independent review panel, including checking that the planned analysis does not compete with sponsor's publication plan); 2. and upon signing of a legal agreement.
More information

Locations