NCT01835782

Brief Summary

The purpose of this study is to determine the safety of L-Serine in subjects with Amyotrophic Lateral Sclerosis (ALS) at varied doses.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at P25-P50 for phase_1

Geographic Reach
1 country

2 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2013

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

March 27, 2013

Completed
23 days until next milestone

First Posted

Study publicly available on registry

April 19, 2013

Completed
3.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2016

Completed
Last Updated

July 30, 2015

Status Verified

July 1, 2015

Enrollment Period

3.9 years

First QC Date

March 27, 2013

Last Update Submit

July 28, 2015

Conditions

Keywords

ALSL-SerineBMAA

Outcome Measures

Primary Outcomes (1)

  • Safety of L-Serine

    Determining the safety of L-Serine given at 0.5 gm twice daily (BID), 2.5gm BID, 7.5g BID or 15 grams BID for six months by assessing the total number of adverse events (AE)during treatment

    1-6 months

Secondary Outcomes (1)

  • Measure levels of β-Methylamino-L-alanine (BMAA) in blood, urine and Cerebrospinal fluid (CSF) to determine if there is a decline in levels over the course of treatment

    1-6 months

Study Arms (4)

2.5 grams BID

ACTIVE COMPARATOR

5 Patients will be evenly randomized into this group

Drug: L-Serine

.5 grams BID

ACTIVE COMPARATOR

5 Patients will be evenly randomized into this group

Drug: L-Serine

7.5 grams BID

ACTIVE COMPARATOR

5 Patients will be evenly randomized into this group

Drug: L-Serine

15 grams BID

ACTIVE COMPARATOR

5 Patients will be evenly randomized into this group

Drug: L-Serine

Interventions

.5 grams BID15 grams BID2.5 grams BID7.5 grams BID

Eligibility Criteria

Age18 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18-85
  • Male or Female
  • Clinically diagnosed with probable or definite ALS based on El Escorial criteria
  • ALSFRS-R \> 25
  • Able to provide informed consent to and comply with all medical procedures

You may not qualify if:

  • Outside age range of 18-85
  • Subjects with forced vital capacity (FVC) below 60%
  • Evidence of any motor neuron disease for over 3 years

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Phoenix Neurological Associates

Phoenix, Arizona, 85018, United States

Location

Forbes Norris MDA/ALS Research Center

San Francisco, California, 94115, United States

Location

MeSH Terms

Conditions

Amyotrophic Lateral Sclerosis

Interventions

Serine

Condition Hierarchy (Ancestors)

Spinal Cord DiseasesCentral Nervous System DiseasesNervous System DiseasesMotor Neuron DiseaseNeurodegenerative DiseasesTDP-43 ProteinopathiesNeuromuscular DiseasesProteostasis DeficienciesMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

Amino Acids, NeutralAmino AcidsAmino Acids, Peptides, and Proteins

Study Officials

  • Todd D Levine, MD

    Phoenix Neurological Associates, LTD

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
FACTORIAL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 27, 2013

First Posted

April 19, 2013

Study Start

January 1, 2013

Primary Completion

December 1, 2016

Last Updated

July 30, 2015

Record last verified: 2015-07

Locations