NCT01831726

Brief Summary

The purpose of this signal seeking study was to determine whether treatment with dovitinib (TKI258) demonstrated sufficient efficacy in select pathway-activated solid tumors and/or hematologic malignancies to warrant further study.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
80

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Aug 2013

Geographic Reach
1 country

49 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 11, 2013

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 15, 2013

Completed
4 months until next milestone

Study Start

First participant enrolled

August 1, 2013

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2015

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

March 20, 2017

Completed
Last Updated

March 20, 2017

Status Verified

January 1, 2017

Enrollment Period

2.3 years

First QC Date

April 11, 2013

Results QC Date

January 30, 2017

Last Update Submit

January 30, 2017

Conditions

Keywords

Solid tumor malignancyhematologic malignancymutationtranslocationsFGFRPDGFRVEGFcKITFLT3CSR1TrkRETTKI258dovitinibsignatureAMLacute myelogenous leukemiaGISTgastrointestinal stromal tumorHead and Neck cancerMelanomaNSCLCnon-small cell lung carcinomalung cancerovarian cancerthyroid canceramplification

Outcome Measures

Primary Outcomes (1)

  • Clinical Benefit Rate (CBR)

    CBR determined by investigator assessment for each tumor assessment \& defined as responses of Complete Response (CR) or Partial Response (PR) or Stable Disease (SD) ≥ 16 wks. Confirmed CR/PR or SD prior to 16 wks,but discontinued prior to 16 wks for reasons other than progressive disease,will have their clinical benefit defined non-evaluable; confirmed CR/PR or SD prior to 16 wks,but progressed prior to 16 wks,will be considered not achieving clinical benefit;if CR/PR/SD occurred prior to 16 wks,but progressed at or after 16 wks without evidence of CR/PR/SD at or after 16 wks,will also be considered not achieving clinical benefit. CBR will be analyzed by comparing achieved CBR with a historical control rate of each tumor type,\& if there is at least 90% probability that the response rate in a tumor type exceeds the historical rate,then the tumor type will be considered a success. CBR: CR+PR+SD the assessment criteria was RECIST 1.1

    Week 16

Secondary Outcomes (3)

  • Overall Response (OR) of Partial Response (PR) or Greater

    Week 16

  • Progression-Free Survival (PFS)

    36 months

  • Overall Survival (OS)

    36 months

Study Arms (1)

TKI258

EXPERIMENTAL

Dovitinib (TKI) will be dosed on a flat scale of 500 mg on a 5 days on/2 days off dosing schedule.

Drug: Dovitinib (TKI258)

Interventions

Dovitinib (TKI) will be dosed on a flat scale of 500 mg on a 5 days on/2 days off dosing schedule.

TKI258

Eligibility Criteria

Age18 Years - 100 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patient's age was ≥ 18 years of age at the time of signing informed consent.
  • Patient had a confirmed diagnosis of a selected solid tumor (except for primary diagnosis of urothelial tumors, hepatocellular carcinoma (HCC), endometrial carcinoma, metastatic breast cancer (mBC), squamous NSCLC, and renal cell carcinoma (RCC)) or hematologic malignancies (except for primary diagnosis of FLT3 AML and multiple myeloma). Additional tumor types could be excluded during the course of the study in the case of early futility or success based upon an interim analysis or at the discretion of Novartis.
  • Patient was in need of treatment because of progression or relapse defined as:
  • radiological progression for solid tumor and lymphoma
  • for hematologic malignancies, measureable progression or relapse by appropriate criteria
  • Patients had pre-identified tumor with a mutation and/or translocation of one of the known kinase targets of dovitinib. The qualifying alteration were assessed and reported by a CLIA-certified laboratory. The mutations included:
  • FGFR 1-3 (amplifications were also allowed)
  • PDGFRα or PDGFRβ
  • VEGFR1-2 (KDR)
  • FLT3, cKIT (amplifications are also allowed),
  • RET, TrkA (NTRK1), or CSF-1R
  • Patient had archival tissue available for submission to allow for molecular testing related to pathway activation. If the tissue was not available or not of sufficient quantity the patient was willing to undergo a fresh tumor biopsy to allow for this analysis. The sample was submitted prior to first study dose unless agreed upon between Novartis and the investigator.
  • Patient received at least one prior treatment for recurrent, metastatic and /or locally advanced disease and for whom no standard therapy options were anticipated to result in a durable remission.
  • Diffuse large B cell lymphoma only: Patient received or was ineligible for autologous or allogeneic stem cell transplant. This did not apply to patients with Mantle cell lymphoma or follicular lymphoma
  • Patients with measurable disease as per appropriate guidelines:
  • +22 more criteria

You may not qualify if:

  • Patients eligible for this study did not meet any of the following criteria:
  • Patients who received prior treatment with dovitinib (TKI258).
  • Patients with a known hypersensitivity to dovitinib (TKI258) or to its excipients.
  • Patients with brain metastasis or history of brain metastasis or leptomeningeal carcinomatosis.
  • Patients with diarrhea ≥ CTCAE grade 2.
  • Patients with neuropathy ≥ CTCAE grade 2.
  • Patients with acute or chronic pancreatitis.
  • Patients with external biliary drains.
  • Patients with a history of pulmonary embolism (PE), or untreated deep venous thrombosis (DVT) ≤ 6 months prior to starting study drug. Note: Patients with recent DVT who were treated with therapeutic anti-coagulant agents for at least 6 weeks are eligible.
  • Patients with impaired cardiac function or clinically significant cardiac diseases, including any of the following:
  • History or presence of serious uncontrolled ventricular arrhythmias.
  • Clinically significant resting bradycardia.
  • LVEF assessed by either 2-D echocardiogram (ECHO) \< 50% or lower limit of normal (whichever was the higher), or 2-D multiple gated acquisition scan (MUGA) \< 45% or lower limit of normal (whichever was the higher).
  • Any of the following within 6 months prior to starting study drug: myocardial infarction (MI), severe/unstable angina, coronary artery bypass graft (CABG), congestive heart failure (CHF), cerebrovascular accident (CVA), transient ischemic Attack (TIA).
  • Uncontrolled hypertension defined by a SBP ≥ 160 mm Hg and/or DBP ≥ 100 mm Hg, with or without anti-hypertensive medication(s). Initiation or adjustment of antihypertensive medication(s) was allowed prior to study entry.
  • +33 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (49)

Alabama Oncology

Birmingham, Alabama, 35211, United States

Location

Highlands Oncology Group SC

Fayetteville, Arkansas, 72703, United States

Location

PCR Oncology

Pismo Beach, California, 93449, United States

Location

Sarcoma Oncology Center

Santa Monica, California, 90403, United States

Location

Rocky Mountain Cancer Centers Rocky Mountain Cancer Centers

Greenwood Village, Colorado, United States

Location

Whittingham Cancer Center Norwalk Hospital

Norwalk, Connecticut, 06856, United States

Location

Memorial Cancer Institute Memorial Healthcare System

Hollywod, Florida, 33021, United States

Location

Cancer Specialists of North Florida Cancer Specialists (2)

Jacksonville, Florida, 32256, United States

Location

Florida Hospital Cancer Institute

Orlando, Florida, 32804, United States

Location

Space Coast Medical Associates Space Coast Cancer Center

Titusville, Florida, 32796, United States

Location

University Cancer & Blood Center, LLC

Athens, Georgia, 30607, United States

Location

NorthWest Georgia Oncology Centers NW Georgia Oncology

Marietta, Georgia, 30060, United States

Location

Lurie Children's Hospital of Chicago Developmental Therapeutics

Chicago, Illinois, 60611, United States

Location

Illinois Cancer Care

Peoria, Illinois, 61615-7828, United States

Location

Indiana University Indiana Univ. - Purdue Univ.

Indianapolis, Indiana, 46202, United States

Location

Horizon Oncology Center Horizon Oncology Ctr.

Lafayette, Indiana, 47905, United States

Location

St. Agnes Hospital St. Agnes Hospital (2)

Baltimore, Maryland, 21229, United States

Location

University of Michigan Int. Medicine Oncology

Ann Arbor, Michigan, 48109, United States

Location

Minnesota Oncology Hematology, P.A. Minnesota Oncology Hematology

Minneapolis, Minnesota, 55404, United States

Location

Billings Clinic Onc Dept

Billings, Montana, 59107, United States

Location

Southeast Nebraska Oncology Cancer Center

Lincoln, Nebraska, 68510, United States

Location

Comprehensive Cancer Centers of Nevada CCC of Nevada- Southwest (2)

Las Vegas, Nevada, 89109, United States

Location

Waverly Hematology Oncology

Cary, North Carolina, 27518, United States

Location

Oncology Hematology Care, Inc. Oncology Hematology Care (2)

Cincinnati, Ohio, 45242, United States

Location

Cleveland Clinic Foundation Cleveland Clinic (19)

Cleveland, Ohio, 44195, United States

Location

St. Charles Cancer Center

Bend, Oregon, 97701, United States

Location

Oregon Health & Science University OHSU Knight Cancer Institute

Portland, Oregon, 97239, United States

Location

University of Pittsburgh Cancer Institute

Pittsburgh, Pennsylvania, 15232-1305, United States

Location

Rhode Island Hospital Rhode Island Hosp. (2)

Providence, Rhode Island, 02903, United States

Location

Gibbs Cancer Center & Research Institute Spartanburg Reg. Healthcare

Spartanburg, South Carolina, 29303, United States

Location

Chattanooga Oncology and Hematology Assoicates, PC Chattanooga Oncology

Chattanooga, Tennessee, 37404, United States

Location

The West Clinic

Memphis, Tennessee, 38120, United States

Location

Sarah Cannon Research Institute Tennessee Oncology

Nashville, Tennessee, 37203, United States

Location

Austin Cancer Centers Austin Cancer Center (2)

Austin, Texas, 78759, United States

Location

Texas Oncology Texas Oncology - Sammons

Dallas, Texas, 75246, United States

Location

Texas Oncology Midtown Texas Oncology

Dallas, Texas, 75251, United States

Location

The Center for Cancer and Blood Disorders

Fort Worth, Texas, 76104, United States

Location

Oncology Consultants Oncology Group

Houston, Texas, 77024, United States

Location

MD Anderson Cancer Center/University of Texas MD Anderson Cancer Center (3)

Houston, Texas, 77030, United States

Location

Tyler Cancer Center

Tyler, Texas, 75702, United States

Location

Intermountain Medical Center Intermountain Healthcare

Murray, Utah, 84157, United States

Location

Virginia Cancer Specialists Virginia Cancer Specialists

Fairfax, Virginia, 22031, United States

Location

Providence Regional Cancer Partnership Providence Reg. Cancer (2)

Everett, Washington, 98201, United States

Location

Evergreen Hematology & Oncology

Spokane, Washington, 99218, United States

Location

Northwest Medical Specialties Hematology/Oncology

Tacoma, Washington, 98405, United States

Location

Wenatchee Valley Medical Center Wenatchee Valley

Wenatchee, Washington, 98801, United States

Location

Yakima Valley Memorial Hospital North Star Lodge Cancer Center

Yakima, Washington, 98902, United States

Location

Aurora Research Institute

Milwaukee, Wisconsin, 53226, United States

Location

Medical College of Wisconsin Cancer Ctr.-Froedtert Hospital

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

Hematologic NeoplasmsLeukemia, Myeloid, AcuteGastrointestinal Stromal TumorsHead and Neck NeoplasmsMelanomaCarcinoma, Non-Small-Cell LungLung NeoplasmsOvarian NeoplasmsThyroid Neoplasms

Interventions

4-amino-5-fluoro-3-(5-(4-methylpiperazin-1-yl)-1H-benzimidazol-2-yl)quinolin-2(1H)-one

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLeukemia, MyeloidLeukemiaNeoplasms by Histologic TypeNeoplasms, Connective TissueNeoplasms, Connective and Soft TissueGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms, Nerve TissueNevi and MelanomasSkin NeoplasmsSkin DiseasesSkin and Connective Tissue DiseasesCarcinoma, BronchogenicBronchial NeoplasmsRespiratory Tract NeoplasmsThoracic NeoplasmsLung DiseasesRespiratory Tract DiseasesEndocrine Gland NeoplasmsOvarian DiseasesAdnexal DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital Neoplasms, FemaleUrogenital NeoplasmsGenital DiseasesEndocrine System DiseasesGonadal DisordersThyroid Diseases

Results Point of Contact

Title
Study Director
Organization
Novartis Pharmaceuticals

Study Officials

  • Novartis Pharmaceuticals

    Novartis Pharmaceuticals

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 11, 2013

First Posted

April 15, 2013

Study Start

August 1, 2013

Primary Completion

December 1, 2015

Study Completion

December 1, 2015

Last Updated

March 20, 2017

Results First Posted

March 20, 2017

Record last verified: 2017-01

Locations