NCT01803321

Brief Summary

This study is a pilot, ascending dose, multi-center, randomized, double blind, placebo controlled, pediatric study conducted in three phases.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
24

participants targeted

Target at P25-P50 for phase_1

Timeline
Completed

Started Nov 2005

Typical duration for phase_1

Geographic Reach
1 country

9 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2005

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2008

Completed
4.7 years until next milestone

First Submitted

Initial submission to the registry

February 28, 2013

Completed
4 days until next milestone

First Posted

Study publicly available on registry

March 4, 2013

Completed
Last Updated

March 4, 2013

Status Verified

February 1, 2013

Enrollment Period

2.6 years

First QC Date

February 28, 2013

Last Update Submit

February 28, 2013

Conditions

Keywords

SJIA

Outcome Measures

Primary Outcomes (1)

  • Frequency of treatment emergent adverse events (TEAEs)

    Baseline to Week 123

Study Arms (2)

Cohort 1

EXPERIMENTAL

Dose 1

Drug: rilonacept (IL-1 Trap)Other: Placebo

Cohort 2

EXPERIMENTAL

Dose 2

Drug: rilonacept (IL-1 Trap)Other: Placebo

Interventions

Cohort 1Cohort 2
PlaceboOTHER
Cohort 1Cohort 2

Eligibility Criteria

Age4 Years - 20 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Patients aged 4 to less than 21 years who meet the criteria for active SJIA
  • Must have been on a stable dose of non-steroidal anti-inflammatory drugs (NSAIDs) for at least 4 weeks prior to the screening visit

You may not qualify if:

  • Use of certain medications prior to the baseline visit
  • History of recurrent infections

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (9)

Unknown Facility

Los Angeles, California, United States

Location

Unknown Facility

Wilmington, Delaware, United States

Location

Unknown Facility

Chicago, Illinois, United States

Location

Unknown Facility

Hackensack, New Jersey, United States

Location

Unknown Facility

Long Island City, New York, United States

Location

Unknown Facility

Cincinnati, Ohio, United States

Location

Unknown Facility

Cleveland, Ohio, United States

Location

Unknown Facility

Dallas, Texas, United States

Location

Unknown Facility

Seattle, Washington, United States

Location

Related Publications (1)

  • Lovell DJ, Giannini EH, Reiff AO, Kimura Y, Li S, Hashkes PJ, Wallace CA, Onel KB, Foell D, Wu R, Biedermann S, Hamilton JD, Radin AR. Long-term safety and efficacy of rilonacept in patients with systemic juvenile idiopathic arthritis. Arthritis Rheum. 2013 Sep;65(9):2486-96. doi: 10.1002/art.38042.

MeSH Terms

Conditions

Arthritis, Juvenile

Interventions

rilonacept

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Clinical Trial Management

    Regeneron Pharmaceuticals

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 28, 2013

First Posted

March 4, 2013

Study Start

November 1, 2005

Primary Completion

June 1, 2008

Study Completion

June 1, 2008

Last Updated

March 4, 2013

Record last verified: 2013-02

Locations