NCT01791842

Brief Summary

Bone pain due to fibrous dysplasia of bone is usually treated with bisphosphonates. A small proportion of patients fail to respond adequately. Mutated bone cells produce large amounts of Interleukin-6 (IL-6), with increased bone resorption as a result. Inhibition of IL-6 may be of interest to reduce bone resorption and therefore bone pain. TOCIDYS is a placebo-controlled randomized cross-over trial to test the hypothesis that tocilizumab can reduce bone resorption in those patients with fibrous dysplasia who have already received bisphosphonates.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
19

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started May 2013

Longer than P75 for phase_2

Geographic Reach
1 country

3 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 13, 2013

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 15, 2013

Completed
3 months until next milestone

Study Start

First participant enrolled

May 5, 2013

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2015

Completed
3.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

June 19, 2018

Completed
Last Updated

October 2, 2025

Status Verified

September 1, 2025

Enrollment Period

2 years

First QC Date

February 13, 2013

Last Update Submit

September 27, 2025

Conditions

Keywords

fibrous dysplasia of bonetocilizumabMcCune-Albright syndrome

Outcome Measures

Primary Outcomes (1)

  • serum CTX (type 1 collagen C-terminal breakdown product)

    6 months

Secondary Outcomes (4)

  • Bone pain

    6 months

  • serum ICTP (Carboxyterminal Telopeptide of Type I Collagen)

    6 months

  • bone alkaline phosphatase

    6 months

  • radiographs of mostly affected area

    12 months

Other Outcomes (1)

  • Biological safety

    12 months

Study Arms (2)

Tocilizumab first, then placebo

EXPERIMENTAL

one IV infusion per month of Tocilizumab for 6 months followed by 1 infusion per month of placebo, for 6 months.

Drug: TocilizumabDrug: Placebo

Placebo first, then Tocilizumab

EXPERIMENTAL

one IV infusion per month of Placebo for 6 months followed by 1 infusion per month of Tocilizumab, for 6 months.

Drug: TocilizumabDrug: Placebo

Interventions

8 mg/kg/month

Placebo first, then TocilizumabTocilizumab first, then placebo
Placebo first, then TocilizumabTocilizumab first, then placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • fibrous dysplasia of bone
  • previously treated with IV bisphosphonates
  • persistent bone pain and increased bone remodeling

You may not qualify if:

  • Chronic renal failure
  • serious infectious diseases
  • liver enzymes abnormality
  • pregnancy
  • dyslipidemia

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (3)

Service de Rhumatologie, Groupe Hospitalier Pellegrin

Bordeaux, France

Location

Service de rhumatologie, Hopital Edouard Herriot, HCL

Lyon, 69003, France

Location

Service de rhumatologie, Hôpital Lariboisière

Paris, 75010, France

Location

Related Publications (1)

  • Chapurlat R, Gensburger D, Trolliet C, Rouanet S, Mehsen-Cetre N, Orcel P. Inhibition of IL-6 in the treatment of fibrous dysplasia of bone: The randomized double-blind placebo-controlled TOCIDYS trial. Bone. 2022 Apr;157:116343. doi: 10.1016/j.bone.2022.116343. Epub 2022 Jan 29.

    PMID: 35104665BACKGROUND

Related Links

MeSH Terms

Conditions

Fibrous Dysplasia of BoneFibrous Dysplasia, Polyostotic

Interventions

tocilizumab

Condition Hierarchy (Ancestors)

OsteochondrodysplasiasBone Diseases, DevelopmentalBone DiseasesMusculoskeletal Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
CROSSOVER
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 13, 2013

First Posted

February 15, 2013

Study Start

May 5, 2013

Primary Completion

May 1, 2015

Study Completion

June 19, 2018

Last Updated

October 2, 2025

Record last verified: 2025-09

Locations