NCT01754987

Brief Summary

This protocol is a phase I/II, study of ascorbic acid (AA) infusions combined with treatment with sorafenib versus treatment with sorafenib alone in subjects with metastatic hepatocellular carcinoma. The phase I aspect will assess the safety and efficacy of the concurrent treatments and the phase II aspect will utilize CT (computer-tomography) scans to assess overall tumor response rate and evaluate disease progression

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
5

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Sep 2012

Typical duration for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2012

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

December 18, 2012

Completed
3 days until next milestone

First Posted

Study publicly available on registry

December 21, 2012

Completed
3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2016

Completed
2.6 years until next milestone

Results Posted

Study results publicly available

August 23, 2018

Completed
Last Updated

May 4, 2025

Status Verified

May 1, 2025

Enrollment Period

3.3 years

First QC Date

December 18, 2012

Results QC Date

June 25, 2018

Last Update Submit

May 1, 2025

Conditions

Keywords

VitaminsMalignant Tumor, TumourIntegrative MedicineComplementary MedicineAlternative Medicine AntioxidantsMolecular Mechanisms of Pharmacological ActionPharmacologic ActionsProtective AgentsPhysiological Effects of DrugsMicronutrientsGrowth SubstancesAntineoplastic Agents, PhytogenicAntineoplastic AgentsTherapeutic UsesRadiation-Sensitizing AgentsLiver Cancer

Outcome Measures

Primary Outcomes (1)

  • Number of Participants That Experience Serious Adverse Events.

    The primary aim is to assess whether or not (IV) Ascorbic Acid (AA) with sorafenib therapy is relatively safe and well-tolerated according to Common Terminology Criteria for Adverse Events (CTCAE)v4.0

    16 weeks +/- 2 weeks

Secondary Outcomes (3)

  • Overall Tumor Response Rate

    16 weeks +/- 2 weeks

  • Mean Value Collected Using the Functional Assessment of Cancer Therapy-General (FACT-G) Quality Assessment Instrument

    16 weeks +/- 2 weeks

  • Number of Participants That Are Alive After 15 Weeks of Treatment.

    15 weeks+

Study Arms (2)

Ascorbic Acid + Sorafenib

EXPERIMENTAL

Drug: Vitamin C Other Names: Ascorbic Acid, Ascorbate Dosage: Vitamin C : 100 grams (infusion) Phase I: 3x a week for 8 weeks Phase II: 3x a week for 16 weeks Sorafenib: taken daily (oral)

Drug: Ascorbic Acid + Sorafenib

Sorafenib alone

OTHER

Sorafenib: taken daily (oral)

Drug: Sorafenib

Interventions

Also known as: Vitamin C, Ascorbate
Ascorbic Acid + Sorafenib
Also known as: Nexavar
Sorafenib alone

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age \> 18 years
  • Metastatic hepatocellular carcinoma
  • G6PD (glucose-6-phosphate dehydrogenase) status \> lower limit of normal
  • Eastern Cooperative Oncology Group (ECOG) performance status 0 to 2.
  • Women of childbearing potential will confirm a negative pregnancy test and must practice effective contraception during the study.
  • Willing and able to provide informed consent and participate in the study procedures.

You may not qualify if:

  • Patients with evidence of a significant current psychiatric disorder that would prevent completion of the study as determined by the PI will not be allowed to participate.
  • Co-morbid medical condition that would affect survival or tolerance as determined by the PI. This includes patients who have not fully recovered from toxicities associated with prior therapy. It also includes subjects who, as determined by the PI, are at risk of experiencing fluid overload (i.e., congestive heart failure).
  • Patients who currently abuse alcohol or drugs.
  • Patients with known glomerular filtration rate of \<60ml/min or with nephrotic range proteinuria.
  • Pregnant or lactating women
  • Enrollment in active clinical trial/ experimental therapy or IND study within the prior 30 days.
  • Contraindication for CT or PET/CT as per the PI.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Thomas Jefferson University

Philadelphia, Pennsylvania, 19107, United States

Location

Related Publications (1)

  • Monti DA, Mitchell E, Bazzan AJ, Littman S, Zabrecky G, Yeo CJ, Pillai MV, Newberg AB, Deshmukh S, Levine M. Phase I evaluation of intravenous ascorbic acid in combination with gemcitabine and erlotinib in patients with metastatic pancreatic cancer. PLoS One. 2012;7(1):e29794. doi: 10.1371/journal.pone.0029794. Epub 2012 Jan 17.

    PMID: 22272248BACKGROUND

MeSH Terms

Conditions

Carcinoma, HepatocellularNeoplasmsLiver Neoplasms

Interventions

Ascorbic AcidSorafenib

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Intervention Hierarchy (Ancestors)

Sugar AcidsAcids, AcyclicCarboxylic AcidsOrganic ChemicalsHydroxy AcidsCarbohydratesPhenylurea CompoundsUreaAmidesBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsNiacinamideNicotinic AcidsAcids, HeterocyclicHeterocyclic CompoundsPyridinesHeterocyclic Compounds, 1-Ring

Results Point of Contact

Title
Dr. Daniel Monti
Organization
Sidney Kimmel Cancer Center at Thomas Jefferson University

Study Officials

  • Daniel A Monti, MD, MBA

    Thomas Jefferson University

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 18, 2012

First Posted

December 21, 2012

Study Start

September 1, 2012

Primary Completion

January 1, 2016

Study Completion

January 1, 2016

Last Updated

May 4, 2025

Results First Posted

August 23, 2018

Record last verified: 2025-05

Data Sharing

IPD Sharing
Will not share

Locations