NCT01719380

Brief Summary

This study will assess the safety and efficacy of LGX818 when combined with cetuximab or combined with cetuximab and BYL719 in patients with BRAF mutant metastatic colorectal cancer

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
156

participants targeted

Target at P75+ for phase_2 colorectal-cancer

Timeline
Completed

Started Nov 2012

Longer than P75 for phase_2 colorectal-cancer

Geographic Reach
12 countries

52 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 30, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 1, 2012

Completed
22 days until next milestone

Study Start

First participant enrolled

November 23, 2012

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 31, 2015

Completed
3.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 12, 2019

Completed
2.4 years until next milestone

Results Posted

Study results publicly available

June 23, 2021

Completed
Last Updated

June 23, 2021

Status Verified

May 1, 2021

Enrollment Period

2.9 years

First QC Date

October 30, 2012

Results QC Date

April 12, 2021

Last Update Submit

May 26, 2021

Conditions

Keywords

Open-label dose escalationBRAF inhibitorLGX818PI3K inhibitorBYL719EGFRcetuximabmetastatic colorectal cancerKRASBRAFV600

Outcome Measures

Primary Outcomes (2)

  • Phase 1b: Number of Participants With Incidence of Dose Limiting Toxicities (DLTs): Cycle 1

    DLTs were defined as an adverse event (AE) or abnormal laboratory value assessed as unrelated to disease, disease progression, inter-current illness, or concomitant medications that occurred within the first 28 days of treatment and meets any of the criteria included blood and lymphatic system disorders, investigations (blood, renal, hepatic, metabolic), skin and subcutaneous tissue disorders: rash, HFSR (hand foot skin reaction) and/or photosensitivity, metabolism and nutrition disorders: hyperglycemia, gastrointestinal disorders, cardiac disorders, vascular disorders, general disorders and administration site conditions, tumor lysis syndrome, ophthalmologic and other adverse events: study drug-related fever, alkaline phosphatase elevation.

    Cycle 1: Day 1 to Day 28

  • Phase 2: Progression Free Survival (PFS)

    PFS was defined as the time from the date of randomization to the date of the first documented disease progression or death due to any cause. Participants who did not progress per RECIST (Response Evaluation Criteria in Solid Tumors) version (v) 1.1, were not known to have died prior to the data cut-off, or received any further anticancer therapy were censored at the date of last adequate tumor assessment or the anticancer therapy date, whichever was earlier.

    From the date of randomization until the first documentation of disease progression or death due to any cause, censored date, whichever occurred first (maximum up to 43 months)

Secondary Outcomes (25)

  • Number of Participants With Treatment - Emergent Adverse Events of Grade 3 or 4 Severity Based on National Cancer Institute of Common Terminology Criteria (NCI-CTCAE), Version 4.0

    From screening up to 30 days after the last dose of study treatment (for a maximum duration of 43 months, approximately)

  • Apparent Total Plasma Clearance (CL/F) of LGX818 (Encorafenib)

    Cycle 1 Day 1: Pre-dose, 0.5, 1, 2, 4, 6, 8 and 24 +/- 2 hours post-dose

  • Apparent Total Plasma Clearance at Steady State (CL/F, ss) of LGX818 (Encorafenib)

    Cycle 1 Day 8, Cycle 2 Day 1: Pre-dose, 0.5, 1, 2, 4, 6, 8 and 24 +/- 2 hours post-dose

  • Apparent Total Plasma Clearance (CL/F) of BYL719 (Alpelisib)

    Cycle 1 Day 1: Pre-dose, 0.5, 1, 2, 4, 6, 8 and 24 +/- 2 hours post-dose

  • Apparent Total Plasma Clearance at Steady State (CL/F, ss) of BYL719 (Alpelisib)

    Cycle 1 Day 8, Cycle 2 Day 1: Pre-dose, 0.5, 1, 2, 4, 6, 8 and 24 +/- 2 hours post-dose

  • +20 more secondary outcomes

Study Arms (2)

LGX818 + cetuximab

EXPERIMENTAL
Drug: LGX818Drug: Cetuximab

LGX818 + BYL719 + cetuximab

EXPERIMENTAL
Drug: LGX818Drug: CetuximabDrug: BYL719

Interventions

LGX818DRUG
LGX818 + BYL719 + cetuximabLGX818 + cetuximab
LGX818 + BYL719 + cetuximabLGX818 + cetuximab
BYL719DRUG
LGX818 + BYL719 + cetuximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Metastatic colorectal cancer
  • Progression after at least one prior standard of care regimen or be intolerant to irinotecan-based regimens
  • Life expectancy ≥ 3 months
  • ECOG performance status ≤ 2

You may not qualify if:

  • Symptomatic or untreated leptomeningeal disease
  • Symptomatic brain metastasis
  • Patients with clinically manifested diabetes
  • Acute or chronic pancreatitis
  • Clinically significant cardiac disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (52)

Keck Hospital of USC

Los Angeles, California, 90033, United States

Location

LAC&USC Medical Center

Los Angeles, California, 90033, United States

Location

USC/Norris Comprehensive Cancer Center

Los Angeles, California, 90033, United States

Location

Ronald Reagan UCLA Medical Center

Los Angeles, California, 90095, United States

Location

UCLA University of California Los Angeles

Los Angeles, California, 90095, United States

Location

Westwood Bowyer Clinic, Peter Morton Medical Building

Los Angeles, California, 90095, United States

Location

UCLA Hematology Oncology

Santa Monica, California, 90404, United States

Location

UCLA Santa Monica Medical Center & Orthopaedic Hospital

Santa Monica, California, 90404, United States

Location

Smilow Cancer Hospital at Yale-New Haven

New Haven, Connecticut, 06510, United States

Location

Yale University

New Haven, Connecticut, 06520, United States

Location

Smilow Cancer Hospital Care Center at North Haven

North Haven, Connecticut, 06473, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114-2620, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

John Theurer Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Memorial Sloan-Kettering Cancer Center

New York, New York, 10017-6706, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10022, United States

Location

Tennessee Oncology, PLLC

Dickson, Tennessee, 37055, United States

Location

Tennessee Oncology, PLLC

Franklin, Tennessee, 37067, United States

Location

Tennessee Oncology, PLLC

Gallatin, Tennessee, 37066, United States

Location

Tennessee Oncology, PLLC

Hermitage, Tennessee, 37076, United States

Location

Tennessee Oncology, PLLC

Lebanon, Tennessee, 37909, United States

Location

Tennessee Oncology, PLLC

Murfreesboro, Tennessee, 37129, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37203, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37205, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37207, United States

Location

Tennessee Oncology, PLLC

Nashville, Tennessee, 37211, United States

Location

Tennessee Oncology, PLLC

Shelbyville, Tennessee, 37160, United States

Location

Tennessee Oncology, PLLC

Smyrna, Tennessee, 37167, United States

Location

University of Utah - Huntsman Cancer Institute - PPDS

Salt Lake City, Utah, 84112-5550, United States

Location

Huntsman Cancer Hospital

Salt Lake City, Utah, 84112, United States

Location

Redwood Health Center - ARUP Lab Draw Location

Salt Lake City, Utah, 84119, United States

Location

John A Moran Eye Center

Salt Lake City, Utah, 84132, United States

Location

Royal Melbourne Hospital

Parkville, Victoria, 3050, Australia

Location

UZ Gasthuisberg

Leuven, Vlaams Brabant, 3000, Belgium

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

Sir Mortimer B. Davis Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

Centre Régional de Lutte Contre Le Cancer Val D'aurelle Paul Lamarque

Montpellier, 34298, France

Location

EDOG - Institut Claudius Regaud - PPDS

Toulouse, 31052, France

Location

University Hospital of Koln

Cologne, North Rhine-Westphalia, 50937, Germany

Location

Universitätsklinikum Essen

Essen, 45147, Germany

Location

Ospedaliero Universitaria di Modena Policlinico

Modena, 41100, Italy

Location

Pharmacy of National Cancer Center Hospital East

Kashiwa, Chiba, 277-8577, Japan

Location

National Cancer Center Hospital

Chuo-ku, Tokyo, 104-0045, Japan

Location

Het Nederlands Kanker Instituut Antoni Van Leeuwenhoek Ziekenhuis

Amsterdam, North Holland, 1066 CX, Netherlands

Location

Erasmus MC

Rotterdam, South Holland, 3015 CE, Netherlands

Location

Universitair Medisch Centrum Utrecht

Utrecht, 3584 CX, Netherlands

Location

Oslo Myeloma Center - PPDS

Oslo, 0379, Norway

Location

Samsung Medical Center - PPDS

Gangnam-Gu, Seoul Teugbyeolsi, 06351, South Korea

Location

Asan Medical Center - PPDS

Songpa-Gu, Seoul Teugbyeolsi, 05505, South Korea

Location

Instituto de Investigacion Oncologica Vall d'Hebron (VHIO) - EPON

Barcelona, 08035, Spain

Location

Hospital Universitario 12 de Octubre

Madrid, 28026, Spain

Location

Hospital Universitario Virgen del Rocio - PPDS

Seville, 41013, Spain

Location

MeSH Terms

Conditions

Colorectal Neoplasms

Interventions

encorafenibCetuximabAlpelisib

Condition Hierarchy (Ancestors)

Intestinal NeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesGastrointestinal DiseasesColonic DiseasesIntestinal DiseasesRectal Diseases

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, HumanizedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 30, 2012

First Posted

November 1, 2012

Study Start

November 23, 2012

Primary Completion

October 31, 2015

Study Completion

February 12, 2019

Last Updated

June 23, 2021

Results First Posted

June 23, 2021

Record last verified: 2021-05

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations