NCT01650038

Brief Summary

Ulcerative colitis (UC) is a chronic inflammatory bowel disease (IBD) of the colon. Complaints such as abdominal pain, cramps and bloody diarrhoea usually start in early adulthood and lead to life-long substantial morbidity. There is no medical treatment available that meets the desired criteria of high efficacy versus low adverse effects. The current prevailing hypothesis regarding the cause of UC states that the pathogenesis involves an inappropriate and ongoing activation of the mucosal immune system driven by the intestinal microbiota in a genetically predisposed individual. Systematic investigation into the effect of correcting the dysbiosis in ulcerative colitis patients has never been performed. The most radical way to restore the presumably disturbed natural homeostasis in UC is to perform faecal transplantation from a healthy donor. In this trial the potential beneficial effects of restoring microbial homeostasis by faecal transplantation through a duodenal tube will be studied in a phase II randomised placebo controlled design. Endpoints are clinical remission and reduction of endoscopic inflammation after 12 weeks (primary), as well as time to recurrence, intra individual changes in faecal samples and mucosal biopsies. Follow up is 12 months.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started May 2011

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2011

Completed
1.2 years until next milestone

First Submitted

Initial submission to the registry

July 18, 2012

Completed
8 days until next milestone

First Posted

Study publicly available on registry

July 26, 2012

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2014

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2014

Completed
Last Updated

December 30, 2014

Status Verified

December 1, 2014

Enrollment Period

3.3 years

First QC Date

July 18, 2012

Last Update Submit

December 28, 2014

Conditions

Keywords

faecal transplantationulcerative colitisinflammatory bowel disease

Outcome Measures

Primary Outcomes (1)

  • co-primary endpoint of clinical remission, as well as reduction of Mayo endoscopic inflammation score

    * clinical remission = questionnaire: SCCAI 2 or lower * reduction of Mayo endoscopic inflammation score= decrement of 1 or more as assessed by sigmoidoscopy

    at 12 weeks after treatment.

Secondary Outcomes (3)

  • Simple clinical colitis activity index (SCCAI) score reduction

    time: 6 weeks after treatment

  • Frequency of bowel movements

    start at baseline up to 6 weeks after treatment

  • Time to recurrence

    from timepoint 12 weeks after treatment up to 12 months

Study Arms (2)

faecal transplantation; donor faeces

ACTIVE COMPARATOR

2 times treatment with faecal transplantation: faeces from a healthy donor processed for duodenal tube infusion. after bowel lavage with macrogol.

Other: treatment with faecal transplantation (donor faeces)

faecal transplantation; placebo

PLACEBO COMPARATOR

2 times treatment with (own) faecal transplantation: faeces from the patient processed for duodenal tube infusion. after bowel lavage with macrogol.

Other: treatment with faecal transplantation (own faeces)

Interventions

faecal transplantation

faecal transplantation; donor faeces

faecal transplantation

faecal transplantation; placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age ≥ 18
  • Ability to give informed consent
  • Established ulcerative colitis with known involvement of the left colon according to the Lennard-Jones criteria
  • SCCAI of 4 \> \< 11
  • Endoscopic Mayo score of \> 1
  • Stable dose of thiopurines in preceding 8 weeks
  • Stable dose of corticosteroids and 5-ASA in preceding 2 weeks

You may not qualify if:

  • Condition leading to profound immunosuppression
  • Anti-TNF treatment in preceding 2 months
  • Cyclosporine treatment in preceding 4 weeks
  • Use of Methotrexate in preceding 2 months
  • Prednisolone dose \> 10 mg
  • Life expectancy \< 12 months
  • Use of systemic antibiotics in preceding 6 weeks
  • Use of probiotic treatment in preceding 6 weeks
  • Positive stool cultures for common enteric pathogens (Salmonella, Shigella, Yersinia, Campylobacter, enteropathogenic e coli)
  • Positive faecal PCR-test (positive PCR means: \> 1 of the following viruses is present) for: Rotavirus, Norovirus, Enterovirus, Parechovirus Sapovirus, Adenovirus 40/41/52. Astrovirus.
  • Pregnancy or women who give breastfeeding
  • Vasopressive medication, icu stay

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Academic_Medical_Center

Amsterdam, 1100DD, Netherlands

Location

Related Publications (1)

  • Rossen NG, Fuentes S, van der Spek MJ, Tijssen JG, Hartman JH, Duflou A, Lowenberg M, van den Brink GR, Mathus-Vliegen EM, de Vos WM, Zoetendal EG, D'Haens GR, Ponsioen CY. Findings From a Randomized Controlled Trial of Fecal Transplantation for Patients With Ulcerative Colitis. Gastroenterology. 2015 Jul;149(1):110-118.e4. doi: 10.1053/j.gastro.2015.03.045. Epub 2015 Mar 30.

MeSH Terms

Conditions

Colitis, UlcerativeInflammatory Bowel Diseases

Interventions

TherapeuticsFecal Microbiota Transplantation

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesColonic DiseasesIntestinal Diseases

Intervention Hierarchy (Ancestors)

Biological Therapy

Study Officials

  • C Ponsioen, MD PhD

    Academisch Medisch Centrum - Universiteit van Amsterdam (AMC-UvA)

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
MD PhD

Study Record Dates

First Submitted

July 18, 2012

First Posted

July 26, 2012

Study Start

May 1, 2011

Primary Completion

August 1, 2014

Study Completion

December 1, 2014

Last Updated

December 30, 2014

Record last verified: 2014-12

Locations