NCT01639300

Brief Summary

The purpose of this study is to assess the safety and tolerability of single ascending doses, as well as of repeated administrations of GNbAC1 in MS patients. Scientific research has shown that the expression of genes of a virus which is integrated in the Human genetic material, the Multiple Sclerosis associated RetroVirus (MSRV) could play a critical role in the causation of multiple sclerosis. GNbAC1 is an experimental medication, which neutralizes (i.e. inactivates) a protein of MSRV that might contribute to the development or deterioration of multiple sclerosis.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
10

participants targeted

Target at below P25 for phase_2 multiple-sclerosis

Timeline
Completed

Started Jul 2012

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2012

Completed
9 days until next milestone

First Submitted

Initial submission to the registry

July 10, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 12, 2012

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2014

Completed
Last Updated

February 8, 2021

Status Verified

February 1, 2021

Enrollment Period

1.8 years

First QC Date

July 10, 2012

Last Update Submit

February 5, 2021

Conditions

Keywords

Relapsing Forms of Multiple SclerosisProgressive Forms of Multiple SclerosisGNbAC1Monoclonal antibodyMultiple Sclerosis Associated Retrovirus (MSRV)Temelimab

Outcome Measures

Primary Outcomes (1)

  • To assess the safety and tolerability of single ascending doses, as well as of repeated administrations of GNbAC1 in MS patients.

    177 days

Secondary Outcomes (3)

  • To determine the pharmacokinetics (PK) characteristics following administration of single ascending doses, as well as of repeated administrations, of GNbAC1 in MS patients

    177 days

  • To determine pharmacodynamic markers of MS disease activity in patients including measurement of MSRV-Env markers and magnetic resonance imaging (MRI)

    177 days

  • To assess the immunogenicity of GNbAC1.

    177 days

Study Arms (2)

GNbAC1

EXPERIMENTAL
Biological: GNbAC1

GNbAC1 placebo

PLACEBO COMPARATOR
Biological: GNbAC1 placebo

Interventions

GNbAC1BIOLOGICAL

Single dose intravenous (IV) GNbAC1 2mg/kg or 6mg/kg

GNbAC1
GNbAC1 placeboBIOLOGICAL

Single dose intravenous (IV) GNbAC1 placebo

GNbAC1 placebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female patients (if female, neither pregnant nor breast-feeding, should be post-menopausal or surgically sterile, or should use two highly effective method of contraception such as oral contraception plus mechanical barrier); Male subjects with partners of childbearing potential have to use adequate contraception during the study. Contraception methods should be followed during the study and up to 3 months after the last study drug administration. Female subjects who are women of childbearing potential (WOCBP) will have to be tested negative with a pregnancy test (serum or urine) at screening and Day 1 and before each repeated administrations of GNbAC1.
  • Between 18 and 65 years of age;
  • Patients with Primary Progressive MS (PPMS) according to the Revised McDonald criteria 2010 or patients with Secondary Progressive MS (SPMS) or patients with Relapsing-Remitting MS(RRMS)according to the Revised McDonald criteria 2010 who cannot be treated with available treatments for MS due to intolerance, non response or refusal of treatment;
  • Score ≤ 6.5 on the Expanded Disability Status Scale (EDSS);
  • Body weight between 40 and 100kg.

You may not qualify if:

  • Positive serology for viral hepatitis and HIV;
  • Disease other than MS that could better explain his/her signs and symptoms;
  • Previously treated with cladribine, lymphoid irradiation or depleting antibodies;
  • Usage in the last 3 months of interferon beta or glatiramer acetate;
  • Any usage in the last 6 months of mitoxantrone, cytotoxic immunosuppressive therapy, natalizumab, fingolimod or immunoglobulin;
  • Usage within 30 days prior to baseline of oral or systemic corticosteroids or ACTH;
  • Inadequate liver function;
  • Severe renal impairment;
  • Severe psychiatric disorder;
  • Known inability to undergo an MRI scan;
  • Having participated in another clinical study within 6 months prior to study baseline except for patients who have participated or who are currently participating in an interventional study without any study drug intake.
  • Pregnancy or breastfeeding
  • Female subjects considering becoming pregnant during the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

University Hospital Basel

Basel, 4031, Switzerland

Location

Hopitaux Universitaires de Genève - HUG

Geneva, 1211, Switzerland

Location

Related Publications (1)

  • Derfuss T, Curtin F, Guebelin C, Bridel C, Rasenack M, Matthey A, Du Pasquier R, Schluep M, Desmeules J, Lang AB, Perron H, Faucard R, Porchet H, Hartung HP, Kappos L, Lalive PH. A phase IIa randomised clinical study of GNbAC1, a humanised monoclonal antibody against the envelope protein of multiple sclerosis-associated endogenous retrovirus in multiple sclerosis patients. Mult Scler. 2015 Jun;21(7):885-93. doi: 10.1177/1352458514554052. Epub 2014 Nov 12.

Related Links

MeSH Terms

Conditions

Multiple Sclerosis

Interventions

temelimab

Condition Hierarchy (Ancestors)

Demyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Tobias Derfuss, MD

    University Hospital, Basel, Switzerland

    PRINCIPAL INVESTIGATOR
  • Patrice Lalive, MD

    HUG

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
PARTICIPANT
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 10, 2012

First Posted

July 12, 2012

Study Start

July 1, 2012

Primary Completion

April 1, 2014

Study Completion

April 1, 2014

Last Updated

February 8, 2021

Record last verified: 2021-02

Locations