NCT01624285

Brief Summary

The purpose of this study is to determine if sorafenib (sorafenib tosylate) is a safe and effective treatment option for preventing liver cancer in high risk patients following liver transplantation. Liver transplantation is a treatment option for liver cancer patients, but despite transplantation, the liver cancer can recur in the new, transplanted liver. It is not known whether sorafenib is effective in preventing cancer recurrence in high risk patients following liver transplantation

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Jul 2012

Longer than P75 for phase_2

Geographic Reach
1 country

21 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 18, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 20, 2012

Completed
26 days until next milestone

Study Start

First participant enrolled

July 16, 2012

Completed
10.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2023

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2023

Completed
Last Updated

December 14, 2023

Status Verified

February 1, 2023

Enrollment Period

10.6 years

First QC Date

June 18, 2012

Last Update Submit

December 8, 2023

Conditions

Outcome Measures

Primary Outcomes (1)

  • Recurrence-free survival, evaluated using the new international criteria proposed by the Modified Response Evaluation Criteria in Solid Tumors (mRECIST) Committee

    Estimated using the Kaplan-Meier method. Compared between the drug verses placebo groups using the unstratified log rank test. Hazard rates, hazard rate ratios and median times to recurrence (or 25 percentiles if median time is not reached) and their corresponding 95% confidence bounds will be reported. A secondary analysis will also be presented stratified by macro versus non-macro status, the most important potential covariate.

    Defined as the time from randomization to the first documented disease recurrence by radiological assessment or death due to any cause whichever occurs first, assessed at 2 years

Secondary Outcomes (7)

  • Overall survival

    From randomization to the date of death or the last date the subject was known to be alive, assessed up to 2 years after completion of study treatment

  • Recurrence-free survival, evaluated using the new international criteria proposed by the mRECIST Committee

    Defined as the time from randomization to the first documented disease recurrence by radiological assessment or death due to any cause whichever occurs first, assessed at 1 year

  • Adverse events assessed in terms of seriousness, severity, and relationship to the study material according to the National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) version 4.0

    Assessed up to 2 years

  • Impact of drug-drug interactions

    Assessed up to 2 years after completion of study treatment

  • Impact of biomarkers (AFP and PIVKA II)

    Assessed up to 2 years after completion of study treatment

  • +2 more secondary outcomes

Study Arms (2)

Arm I (sorafenib tosylate)

EXPERIMENTAL

Patients receive sorafenib tosylate PO BID.

Drug: sorafenib tosylateOther: laboratory biomarker analysis

Arm II (placebo)

PLACEBO COMPARATOR

Patients receive placebo PO BID.

Other: placeboOther: laboratory biomarker analysis

Interventions

Given PO

Also known as: BAY 43-9006, BAY 43-9006 Tosylate Salt, BAY 54-9085, Nexavar, SFN
Arm I (sorafenib tosylate)
placeboOTHER

Given PO

Also known as: PLCB
Arm II (placebo)

Correlative studies

Arm I (sorafenib tosylate)Arm II (placebo)

Eligibility Criteria

Age19 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients must have hepatocellular carcinoma (HCC) with one of the following on explant: microvascular/macrovascular invasion, tumor outside of Milan criteria, poor tumor differentiation; patients with macrovascular invasion on explant pathology will be stratified
  • \* Additionally, the following will be included
  • \*\* Patients with elevated surrogate markers (AFP \> 500 or PIVKA \> 400) pre transplant and with biopsy proven HCC prior to orthotopic liver transplantation (OLT) or on explant
  • Eastern Cooperative Oncology Group (ECOG) performance status (PS) 0-2
  • Patients with a life expectancy \> 12 weeks
  • Patients must have completed prednisone taper within 6 weeks post OLT
  • Patients must be enrolled between 6 to 12 weeks post OLT
  • Cadaveric donors only (no living donor liver transplantation \[LDLT\] or donor after cardiac death transplantation \[DCDT\])
  • Platelet count \> 50 x 10\^9/L
  • Hemoglobin \>= 8.5 g/dL
  • Total bilirubin =\< 5 mg/dL
  • Alanine transaminase (ALT) and aspartate aminotransferase (AST) =\< 5 x upper limit of normal
  • Amylase and lipase =\< 1.5 x the upper limit of normal
  • Serum creatinine \< 2 x the upper limit of normal
  • Prothrombin time (PT) =\< 6 seconds or international normalized ratio (INR) =\< 2.3
  • +8 more criteria

You may not qualify if:

  • Significant ongoing immunologic rejection based on pathology and clinical diagnosis (from time of transplant until randomization)
  • Use of T cell depleting agents for prevention or treatment of rejection at any point prior to or after enrollment in the study
  • Patient with documented evidence of metastatic disease
  • % tumor necrosis on explant pathology
  • Use of mammalian target of rapamycin (mTOR) inhibitors prior to transplant and as post-transplant immunosuppression
  • Use of alemtuzumab
  • Living donor liver transplant (LDLT) or donation after cardiac death transplant (DCDT)
  • Human immunodeficiency virus (HIV) positive patients
  • Hepatitis C virus (HCV) recurrence at the time of randomization
  • Use of direct acting antivirals for HCV recurrence
  • Requirement of re-transplantation for primary non function
  • Uncontrolled hypertension, defined as systolic blood pressure \> 140 mmHg or diastolic pressure \> 90 mmHg, despite optimal medical management
  • Active or clinically significant cardiac disease including:
  • Congestive heart failure - New York Heart Association (NYHA) \> class II
  • Coronary artery disease
  • +31 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (21)

University of Alabama

Birmingham, Alabama, 35294-0007, United States

Location

Jonsson Comprehensive Cancer Center

Los Angeles, California, 90095, United States

Location

University of Colorado

Denver, Colorado, 80217-3364, United States

Location

Mount Sinai Hospital

Hartford, Connecticut, 06112, United States

Location

Lombardi Comprehensive Cancer Center at Georgetown University

Washington D.C., District of Columbia, 20057, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

Location

Johns Hopkins University

Baltimore, Maryland, 21287-8936, United States

Location

Lahey Clinic Medical Center

Burlington, Massachusetts, 01805, United States

Location

University of Michigan University Hospital

Ann Arbor, Michigan, 48109, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198-7830, United States

Location

University of Pennsylvania Health System

Cherry Hill, New Jersey, 08034, United States

Location

New York University Langone Medical Center

New York, New York, 10016, United States

Location

New York Presbyterian-The University Hospital of Columbia and Cornell

New York, New York, 10065, United States

Location

Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

Integris-Baptist Medical

Oklahoma City, Oklahoma, 73112, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15213, United States

Location

Vanderbilt University

Nashville, Tennessee, 37232, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

The Methodist Hospital Research Institute

Houston, Texas, 77030, United States

Location

MeSH Terms

Conditions

Carcinoma, Hepatocellular

Interventions

Sorafenib

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Intervention Hierarchy (Ancestors)

Phenylurea CompoundsUreaAmidesOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsNiacinamideNicotinic AcidsAcids, HeterocyclicHeterocyclic CompoundsPyridinesHeterocyclic Compounds, 1-Ring

Study Officials

  • Ronald Busuttil

    Jonsson Comprehensive Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
PARTICIPANT
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 18, 2012

First Posted

June 20, 2012

Study Start

July 16, 2012

Primary Completion

February 1, 2023

Study Completion

February 1, 2023

Last Updated

December 14, 2023

Record last verified: 2023-02

Locations