NCT01618695

Brief Summary

The purpose of this study is to confirm the efficacy and safety of perampanel compared to placebo in patients with refractory partial-onset seizures

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
940

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started May 2012

Longer than P75 for phase_3

Geographic Reach
7 countries

117 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 15, 2012

Completed
27 days until next milestone

First Submitted

Initial submission to the registry

June 11, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

June 13, 2012

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 15, 2014

Completed
5.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

May 28, 2020

Completed
8 days until next milestone

Results Posted

Study results publicly available

June 5, 2020

Completed
Last Updated

July 29, 2021

Status Verified

July 1, 2021

Enrollment Period

2.3 years

First QC Date

June 11, 2012

Results QC Date

May 20, 2020

Last Update Submit

July 9, 2021

Conditions

Keywords

Partial-onset Seizurespartial seizuresseizureepilepsy

Outcome Measures

Primary Outcomes (1)

  • Core Phase: Percent Change in Seizure Frequency (For All Partial Seizures) Per 28 Days in the Randomization Phase Relative to Pre-randomization Phase (Baseline)

    Seizure frequency was based on number of seizures per 28 days, calculated as the number of seizures over the entire time interval divided by the number of days in the interval and multiplied by 28. All partial seizure included simple partial seizures without motor signs, simple partial with motor signs, complex partial, and complex partial with secondary generalized seizures. A simple partial seizure takes place on one side of the brain. Usually, people experiencing a simple partial seizure do not lose consciousness or awareness. A complex partial seizure is a type of seizure that arises in one lobe of the brain, rather than the whole brain. The seizure affects people's awareness and may cause them to lose consciousness.

    Baseline, Week 19

Secondary Outcomes (3)

  • Core Phase: Responder Rate During the Maintenance Period of the Randomization Phase Relative to the Prerandomization Phase (Baseline)- Last Observation Carried Forward (LOCF)

    Baseline, Week 19

  • Core Phase: Percent Change in Seizure Frequency Per 28 Days For Complex Partial Seizures Plus Secondary Generalized Seizures in the Randomization Phase Relative to the Prerandomization Phase (Baseline)

    Baseline, Week 19

  • Core Phase: Number of Participants With Clinical Global Impression of Change (CGIC) Scores

    Baseline, Week 19

Study Arms (2)

Perampanel

EXPERIMENTAL
Drug: Perampanel

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Core study: 4 milligram (mg) group- Week 0 Once daily 2 milligram per day (mg/day), Week 1 to Week 18 Once daily 4 mg/day; 8 mg group- Week 0 Once daily 2 mg/day, Week 1 Once daily 4 mg/day, Week 2 Once daily 6 mg/day, Week 3 to Week 18 Once daily 8 mg/day; 12 mg group- Week 0 Once daily 2 mg/day, Week 1 Once daily 4 mg/day, Week 2 Once daily 6 mg/day, Week 3 Once daily 8 mg/day, Week 4 Once daily 10 mg/day, Week 5 to Week 18 Once daily 12 mg/day. Extension study: 4 mg group- Week 19 to Week 22 Once daily 4 mg/day, Week 23 Once daily 6 mg/day, Week 24 Once daily 8 mg/day, Week 25 Once daily 10 mg/day, Week 26 to Week 75 or more Once daily 12 mg/day; 8 mg group- Week 19 to Week 22 Once daily 8 mg/day, Week 23 Once daily 10 mg/day, Week 24 to Week 75 or more Once daily 12 mg/day; 12 mg group- Week 19 to Week 75 or more Once daily 12 mg/day.

Also known as: E2007
Perampanel

Core study: Week 0 to Week 18 Once daily placebo. Extension study: Week 19 to Week 22 Once daily placebo, Week 23 Once daily perampanel 2 mg/day, Week 24 Once daily perampanel 4 mg/day, Week 25 Once daily perampanel 6 mg/day, Week 26 Once daily perampanel 8 mg/day, Week 27 Once daily perampanel 10 mg/day, Week 28 to Week 75 or more Once daily perampanel 12 mg/day.

Placebo

Eligibility Criteria

Age12 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female and greater than or equal to 12 years of age;
  • Have a diagnosis of epilepsy with partial seizures with or without secondarily generalized seizures
  • Participants with computed tomography (CT) or magnetic resonance imaging (MRI) diagnosis within the last 10 years (for adults) and 5 years (for adolescents) prior to visit 1 that ruled out progressive central nervous system (CNS) disorders, example, neurodegenerative disorders, brain tumors. For participants without existing CT or MRI results, CT or MRI was performed at or after Visit 1 but results evaluation was performed by Visit 2
  • Participants who had been treated for at least 12 weeks but confirmed to be uncontrolled with more than one standard antiepileptic drug (AED) for 2 years before enrollment
  • During the 6-week Prerandomization Phase participants must have had greater than or equal to 5 partial seizures per 6-week
  • Are currently being treated with stable doses and administrations of 1, 2, or a maximum of 3 approved AEDs. Only 1 inducer AED (defined as carbamazepine, phenytoin or oxcarbazepine only) out of the maximum of 3 AEDs is allowed

You may not qualify if:

  • Presence of nonmotor simple partial seizures only;
  • Presence of primary generalized epilepsies or seizures, such as absences and/or myoclonic epilepsies;
  • Presence or previous history of Lennox-Gastaut syndrome;
  • A history of status epilepticus within 1 year prior to screening
  • Seizure clusters where individual seizures cannot be counted
  • A history of psychogenic seizures within 5 years prior to screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (117)

Facility #1

Bedford Park, Australia

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Facility #1

Camperdown, Australia

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Clayton, Australia

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Fitzroy, Australia

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Heidelberg, Australia

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Melbourne, Australia

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Randwick, Australia

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Facility #1

Beijing, Beijing Municipality, China

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Facility #1

Chongqing, Chongqing Municipality, China

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Facility #1

Xiamen, Fujian, China

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Facility #1

Guangzhou, Guangdong, China

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Facility #2

Guangzhou, Guangdong, China

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Facility #1

Harbin, Heilongjiang, China

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Facility #1

Changchun, Jilin, China

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Facility #1

Xi'an, Shaanxi, China

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Facility #2

Xi'an, Shaanxi, China

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Facility #3

Xi'an, Shaanxi, China

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Facility #1

Taiyuan, Shan'xi, China

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Facility #1

Jinan, Shandong, China

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Facility #2

Jinan, Shandong, China

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Facility #1

Qingdao, Shandong, China

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Facility #1

Shanghai, Shanghai Municipality, China

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Facility #2

Shanghai, Shanghai Municipality, China

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Facility #3

Shanghai, Shanghai Municipality, China

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Facility #1

Chengdu, Sichuan, China

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Facility #2

Chengdu, Sichuan, China

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Facility #1

Tianjin, Tianjin Municipality, China

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Facility #1

Kunming, Yunnan, China

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Facility #1

Wenzhou, Zhejiang, China

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Eisai Trial Site #1

Nagoya, Aichi-ken, Japan

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Eisai Trial Site #2

Nagoya, Aichi-ken, Japan

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Eisai Trial Site #3

Nagoya, Aichi-ken, Japan

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Eisai Trial Site #1

Tōon, Ehime, Japan

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Eisai Trial Site #1

Yoshida-gun, Fukui, Japan

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Eisai Trial Site #1

Kitakyushu, Fukuoka, Japan

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Eisai Trial Site #1

Koga, Fukuoka, Japan

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Eisai Trial Site #1

Kurume, Fukuoka, Japan

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Eisai Trial Site #1

Sapporo, Hokkaido, Japan

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Eisai Trial Site #2

Sapporo, Hokkaido, Japan

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Eisai Trial Site #1

Itami, Hyōgo, Japan

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Eisai Trial Site #1

Tsuchiura, Ibaraki, Japan

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Eisai Trial Site #1

Kanazawa, Ishikawa-ken, Japan

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Eisai Trial Site #1

Zentsujichó, Kagawa-ken, Japan

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Eisai Trial Site #1

Fujisawa, Kanagawa, Japan

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Eisai Trial Site #1

Kawasaki, Kanagawa, Japan

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Eisai Trial Site #1

Gōshi, Kumamoto, Japan

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Eisai Trial Site #1

Tamana, Kumamoto, Japan

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Eisai Trial Site #1

Iwanuma, Miyagi, Japan

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Eisai Trial Site #1

Sendai, Miyagi, Japan

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Eisai Trial Site #1

Miyakonojō, Miyazaki, Japan

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Eisai Trial Site #1

Ōmura, Nagasaki, Japan

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Eisai Trial Site #1

Beppu, Oita Prefecture, Japan

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Eisai Trial Site #1

Kurashiki, Okayama-ken, Japan

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Eisai Trial Site #1

Izumi, Osaka, Japan

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Eisai Trial Site #1

Sakai, Osaka, Japan

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Eisai Trial Site #2

Sakai, Osaka, Japan

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Eisai Trial Site #1

Sayama, Osaka, Japan

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Eisai Trial Site #1

Takatsuki, Osaka, Japan

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Eisai Trial Site #1

Asaka, Saitama, Japan

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Eisai Trial Site #1

Higashimurayama, Saitama, Japan

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Eisai Trial Site #1

Moriyama, Shiga, Japan

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Eisai Trial Site #1

Matsue, Shimane, Japan

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Eisai Trial Site #1

Hamamatsu, Shizuoka, Japan

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Eisai Trial Site #1

Komatsushimachō, Tokushima, Japan

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Eisai Trial Site #1

Kodaira, Tokyo, Japan

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Eisai Trial Site #1

Kokubunji, Tokyo, Japan

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Eisai Trial Site #1

Ube, Yamaguchi, Japan

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Eisai Trial Site #1

Akita, Japan

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Eisai Trial Site #1

Aomori, Japan

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Eisai Trial Site #1

Fukui, Japan

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Eisai Trial Site #1

Fukuoka, Japan

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Eisai Trial Site #2

Fukuoka, Japan

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Eisai Trial Site #1

Gifu, Japan

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Eisai Trial Site #1

Hiroshima, Japan

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Eisai Trial Site #2

Hiroshima, Japan

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Eisai Trial Site #1

Kagoshima, Japan

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Eisai Trial Site #2

Kagoshima, Japan

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Eisai Trial Site #1

Kumamoto, Japan

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Eisai Trial Site #1

Kyoto, Japan

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Eisai Trial Site #1

Miyazaki, Japan

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Eisai Trial Site #1

Nara, Japan

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Eisai Trial Site #1

Niigata, Japan

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Eisai Trial Site #1

Okayama, Japan

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Eisai Trial Site #1

Saitama, Japan

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Eisai Trial Site #2

Saitama, Japan

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Eisai Trial Site #1

Shizuoka, Japan

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Eisai Trial Site #2

Shizuoka, Japan

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Eisai Trial Site #1

Toyama, Japan

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Eisai Trial Site #1

Yamagata, Japan

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Facility #1

Kuala Lumpur, Malaysia

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Facility #1

Perak, Malaysia

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Facility #1

Pulau Pinang, Malaysia

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Facility #1

Terengganu, Malaysia

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Facility #1

Busan, South Korea

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Facility #2

Busan, South Korea

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Facility #1

Daegu, South Korea

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Facility #1

Daejeon, South Korea

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Facility #1

Gwangju, South Korea

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Facility #1

Incheon, South Korea

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Facility #1

Seoul, South Korea

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Facility #2

Seoul, South Korea

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Facility #3

Seoul, South Korea

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Facility #4

Seoul, South Korea

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Facility #5

Seoul, South Korea

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Facility #6

Seoul, South Korea

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Facility #7

Seoul, South Korea

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Facility #8

Seoul, South Korea

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Facility #1

Taichung, Taiwan

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Facility #1

Tainan, Taiwan

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Facility #1

Taipei, Taiwan

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Facility #2

Taipei, Taiwan

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Facility #1

Taoyuan District, Taiwan

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Facility #1

Rajathevee, Thailand

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Facility #1

Tha Muang, Thailand

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Facility #2

Tha Muang, Thailand

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Facility #3

Tha Muang, Thailand

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Facility #4

Tha Muang, Thailand

Location

Related Publications (2)

  • Bresnahan R, Hill RA, Wang J. Perampanel add-on for drug-resistant focal epilepsy. Cochrane Database Syst Rev. 2023 Apr 14;4(4):CD010961. doi: 10.1002/14651858.CD010961.pub2.

  • Nishida T, Lee SK, Inoue Y, Saeki K, Ishikawa K, Kaneko S. Adjunctive perampanel in partial-onset seizures: Asia-Pacific, randomized phase III study. Acta Neurol Scand. 2018 Apr;137(4):392-399. doi: 10.1111/ane.12883. Epub 2017 Dec 17.

MeSH Terms

Conditions

SeizuresEpilepsy

Interventions

perampanel

Condition Hierarchy (Ancestors)

Neurologic ManifestationsNervous System DiseasesSigns and SymptomsPathological Conditions, Signs and SymptomsBrain DiseasesCentral Nervous System Diseases

Results Point of Contact

Title
Inquiry Service.
Organization
Eisai Co., Ltd.

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 11, 2012

First Posted

June 13, 2012

Study Start

May 15, 2012

Primary Completion

September 15, 2014

Study Completion

May 28, 2020

Last Updated

July 29, 2021

Results First Posted

June 5, 2020

Record last verified: 2021-07

Locations