NCT01611597

Brief Summary

Validation of a measure specifically suitable to evaluate the residual function of upper limbs of non-ambulant neuromuscular patients, especially with Duchenne muscular dystrophy and spinal muscular atrophy. This approach is of fundamental importance for clinical monitoring and preparing the future therapeutic trials.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
8

participants targeted

Target at below P25 for not_applicable

Timeline
Completed

Started Jan 2012

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2012

Completed
5 months until next milestone

First Submitted

Initial submission to the registry

May 30, 2012

Completed
6 days until next milestone

First Posted

Study publicly available on registry

June 5, 2012

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2013

Completed
Last Updated

April 19, 2013

Status Verified

April 1, 2013

Enrollment Period

1 year

First QC Date

May 30, 2012

Last Update Submit

April 18, 2013

Conditions

Keywords

accelerometryneuromuscular disease

Outcome Measures

Primary Outcomes (1)

  • Physical activity variables of upper limbs movement at home

    A watch containing and inertial system will be worn by non-ambulant patients with neuromuscular diseases at home for 14 days. Physical activity variables will be deduced from these measurements.

    each day for 14 days

Secondary Outcomes (2)

  • Physical activity variables of upper limbs movement in standardized setting

    at baseline

  • Physical activity variables of upper limbs movement in standardized setting

    14 days after baseline

Interventions

Patients will perform tests like hand grip (MyoGrip), pinch (MyoPinch), Moviplate, box and block test of hand function, Minnesota Manual Dexterity Test. The tests will be performed with the accelerometer device worn on the wrist.

Also known as: MyoGrip, MyoPinch, Moviplate

Eligibility Criteria

Age10 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • age over 10 years
  • neuromuscular disease documented by genetic testing or by muscle biopsy
  • not able to walk 10 meters without support
  • capable of sitting upright in a wheelchair for at least 3 hours
  • subject affiliated to a social security system
  • subject who signed an informed consent

You may not qualify if:

  • severe intellectual impairment limiting the comprehension of the demanded tasks
  • surgery scheduled within 3 weeks after enrollment
  • pregnant or nursing women

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Institut de Myologie - GH Pitié Salpétrière

Paris, 75013, France

Location

Related Publications (1)

  • Le Moing AG, Seferian AM, Moraux A, Annoussamy M, Dorveaux E, Gasnier E, Hogrel JY, Voit T, Vissiere D, Servais L. A Movement Monitor Based on Magneto-Inertial Sensors for Non-Ambulant Patients with Duchenne Muscular Dystrophy: A Pilot Study in Controlled Environment. PLoS One. 2016 Jun 7;11(6):e0156696. doi: 10.1371/journal.pone.0156696. eCollection 2016.

MeSH Terms

Conditions

Neuromuscular Diseases

Condition Hierarchy (Ancestors)

Nervous System Diseases

Study Officials

  • Laurent Servais, MD, PhD

    institut de myologie

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NA
Masking
NONE
Purpose
BASIC SCIENCE
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 30, 2012

First Posted

June 5, 2012

Study Start

January 1, 2012

Primary Completion

January 1, 2013

Study Completion

January 1, 2013

Last Updated

April 19, 2013

Record last verified: 2013-04

Locations