Key Highlights

Risk & Performance

Pipeline Risk Assessment

Pipeline Risk Assessment

Based on historical performance

Moderate Risk

Score: 45/100

Failure Rate

0.0%

0 terminated/withdrawn out of 33 trials

Success Rate

100.0%

+13.5% vs industry average

Late-Stage Pipeline

0%

0 trials in Phase 3/4

Results Transparency

5%

1 of 21 completed trials have results

Key Signals

5 recruiting1 with results

Enrollment Performance

Analytics

N/A
19(95.0%)
Phase 1
1(5.0%)
20Total
N/A(19)
Phase 1(1)

Activity Timeline

Global Presence

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Clinical Trials (33)

Showing 20 of 33 trials
NCT06866652Recruiting

Evaluating Dyspnea in Autoimmune Myasthenia Gravis "Why am I Short of Breath?"

Role: lead

NCT05199246Not ApplicableCompleted

Assessment of Safety and Acute Effects of a Lower-limb Powered Dermoskeleton in Patients With Neuromuscular Disorders

Role: lead

NCT05200702Not ApplicableCompleted

Assessment of Safety and Acute Effects of a Knee-hip Powered Soft Exoskeleton in Patients With Neuromuscular Disorders

Role: lead

NCT07362316Completed

Longitudinal Evaluation of Neuromuscular Involvement in Type 1 Myotonic Dystrophy

Role: lead

NCT06199284Not ApplicableSuspended

Atalante Exoskeleton in the Rehabilitation of Patients With Amyotrophic Lateral Sclerosis

Role: collaborator

NCT07321977Not ApplicableRecruiting

Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuromuscular Diseases or Asymptomatic Volunteers

Role: lead

NCT07321990Recruiting

Study of the Reproducibility of the French Version of the Modified SMAFRS Scale

Role: lead

NCT06354790Recruiting

Natural History Study of Children With LAMA2-related Dystrophies

Role: lead

NCT06616545Recruiting

French Observatory for Patients with Type 3 Glycogenosis

Role: lead

NCT05234099Not ApplicableCompleted

Sensitivity and Reproducibility of 18F-fluorodeoxyglucose Positron Emission Tomography for Assessment of Respiratory Muscle Activity

Role: lead

NCT05839145Not ApplicableUnknown

Home Monitoring of Adult Patients With SMA: a Pilot Multicenter Validation Study

Role: lead

NCT05916677Not ApplicableUnknown

Virtual Reality-training in Theory of Mind in the Childhood Form of Myotonic Dystrophy Type 1

Role: lead

NCT05798325Not ApplicableUnknown

Feasibility, Validation and Application of Digital Tools for the Follow-up of Neuromuscular Patient Mobility in Daily Living

Role: lead

NCT05265351Not ApplicableUnknown

Ultrafast Ultrasound for the Functional Assessment of the Diaphragm

Role: lead

NCT03351270Not ApplicableCompleted

Prospective Natural History Study of Patients With Myotubular Myopathy and Other CentroNuclear Myopathies

Role: lead

NCT05408702Completed

Exercise in Autoimmune Myasthenia Gravis and Myasthenic Syndromes

Role: lead

NCT03339830Completed

European Registry of Patients With Infantile-onset Spinal Muscular Atrophy

Role: lead

NCT02310906Phase 1Completed

Phase I/II Study of SRP-4053 in DMD Patients

Role: collaborator

NCT02196909Not ApplicableCompleted

Clinical, Biological and NMR Outcome Measures Study for Hereditary Inclusion Body Myopathy Due to Mutation of UDP-N-acetylglucosamine 2-epimerase/N-acetylmannosamine Kinase Gene (GNE)

Role: lead

NCT02391831Not ApplicableCompleted

Prospective Study of the Natural History of Patients With Type 2 and 3 Spinal Muscular Atrophy

Role: lead