NCT01604850

Brief Summary

This study was to assess the safety and efficacy of sofosbuvir in combination with ribavirin (RBV) administered for 12 or 16 weeks in participants with genotypes 2 or 3 hepatitis C virus (HCV) infection as assessed by the proportion of participants with sustained virologic response (SVR) 12 weeks after discontinuation of therapy (SVR12).

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
202

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jun 2012

Shorter than P25 for phase_3

Geographic Reach
4 countries

67 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 21, 2012

Completed
3 days until next milestone

First Posted

Study publicly available on registry

May 24, 2012

Completed
8 days until next milestone

Study Start

First participant enrolled

June 1, 2012

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2013

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2013

Completed
1 year until next milestone

Results Posted

Study results publicly available

May 1, 2014

Completed
Last Updated

May 28, 2014

Status Verified

May 1, 2014

Enrollment Period

8 months

First QC Date

May 21, 2012

Results QC Date

March 31, 2014

Last Update Submit

May 9, 2014

Conditions

Keywords

HCV genotype 2 (GT-2)HCV genotype 3 (GT-3)HCVSustained Virologic ResponseDirect Acting AntiviralCombination TherapyTreatment ExperiencedGS-7977Ribavirin

Outcome Measures

Primary Outcomes (2)

  • Percentage of Participants Achieving SVR12

    SVR12 was defined as HCV RNA \< the lower limit of quantitation (LLOQ, ie, \< 25 IU/mL) 12 weeks after cessation of therapy. For the purposes of this efficacy analysis, the posttreatment period began after the end of active treatment (following Week 12 for the SOF+RBV+placebo arm, and Week 16 for the SOF+RBV arm).

    Posttreatment Week 12

  • Adverse Events Leading to Permanent Discontinuation of Study Drug

    Adverse events which led to permanent discontinuation of study drug may or may not have been related to study treatment.

    Baseline to Week 16

Secondary Outcomes (4)

  • Percentage of Participants Achieving SVR4

    Posttreatment Week 4

  • Percentage of Participants Achieving SVR24

    Posttreatment Week 24

  • Percentage of Participants With Viral Breakthrough

    Up to 16 weeks

  • Percentage of Participants With Viral Relapse

    End of treatment to posttreatment Week 24

Study Arms (2)

SOF+RBV+placebo

EXPERIMENTAL

Participants were randomized to receive SOF+RBV for 12 weeks followed by placebo to match SOF plus placebo to match RBV for 4 weeks.

Drug: SOFDrug: RBVDrug: Placebo to match SOFDrug: Placebo to match RBV

SOF+RBV

EXPERIMENTAL

Participants were randomized to receive SOF+RBV for 16 weeks.

Drug: SOFDrug: RBV

Interventions

SOFDRUG

Sofosbuvir (SOF) 400 mg tablet was administered orally once daily.

Also known as: Sovaldi®, GS-7977, PSI-7977
SOF+RBVSOF+RBV+placebo
RBVDRUG

Ribavirin (RBV) tablets was administered orally in a divided daily dose according to package insert weight-based dosing recommendations (\< 75kg = 1000 mg and ≥ 75 kg = 1200 mg).

SOF+RBVSOF+RBV+placebo

Placebo to match SOF was administered orally once daily.

SOF+RBV+placebo

Placebo to match RBV was administered orally twice daily.

SOF+RBV+placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Infection with HCV genotype 2 or 3
  • Had cirrhosis determination
  • Prior treatment failure
  • Screening laboratory values within defined thresholds
  • Subject had not been treated with any investigational drug or device within 30 days of the screening visit
  • Use of highly effective contraception methods if female of childbearing potential or sexually active male

You may not qualify if:

  • Prior exposure to an direct-acting antiviral targeting the HCV nonstructural protein (NS)5B polymerase
  • Pregnant or nursing female or male with pregnant female partner
  • Current or prior history of clinical hepatic decompensation
  • History of clinically significant illness or any other major medical disorder that may have interfered with subject treatment, assessment or compliance with the protocol
  • Excessive alcohol ingestion or significant drug abuse

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (67)

SCTI Research Foundation

Coronado, California, 92118, United States

Location

Kaiser Permanente

Los Angeles, California, 90027, United States

Location

Peter J. Ruane, MD, Inc.

Los Angeles, California, 90036, United States

Location

Anthony Mills MD, Inc.

Los Angeles, California, 90069, United States

Location

UCSD Antiviral Research Center

San Diego, California, 92103, United States

Location

Medical Associates Research Group, Inc.

San Diego, California, 92123, United States

Location

Kaiser Permanente

San Diego, California, 92154, United States

Location

Quest Clinical Research

San Francisco, California, 94115, United States

Location

University of Colorado

Aurora, Colorado, 80045, United States

Location

South Denver Gastroenterology, PC

Englewood, Colorado, 80113, United States

Location

Whitman Walker Clinic

Washington D.C., District of Columbia, 20009, United States

Location

University of Florida

Gainesville, Florida, 32610-0277, United States

Location

Borland-Groover Clinic Baptist

Jacksonville, Florida, 32256, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Advanced Research Institute

New Port Richey, Florida, 34653, United States

Location

Orlando Immunology Center (ACH)

Orlando, Florida, 32803-1851, United States

Location

Internal Medicine Specialists

Orlando, Florida, 32806, United States

Location

South Florida Center of Gastroenterology, P.A.

Wellington, Florida, 33414, United States

Location

Digestive Healthcare of Georgia

Atlanta, Georgia, 30309, United States

Location

Gastrointestinal Specialists of Georgia, PC

Marietta, Georgia, 30060, United States

Location

Indianapolis Gastroenterology Research Foundation

Indianapolis, Indiana, 46237, United States

Location

Graves-Gilbert Clinic

Bowling Green, Kentucky, 42101, United States

Location

Gastroenterology Associates, LLC

Baton Rouge, Louisiana, 70809, United States

Location

Johns Hopkins University

Lutherville, Maryland, 21093, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114-2696, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02115, United States

Location

The Research Institute

Springfield, Massachusetts, 01105, United States

Location

Henry Ford Health System

Novi, Michigan, 48377, United States

Location

Minnesota Gastroenterology, P.A.

Minneapolis, Minnesota, 55414, United States

Location

Kansas City Gastroenterology and Hepatology

Kansas City, Missouri, 64131, United States

Location

Comprehensive Clinical Research

Berlin, New Jersey, 08009, United States

Location

ID Care

Hillsborough, New Jersey, 08844, United States

Location

Southwest C.A.R.E. Center

Santa Fe, New Mexico, 87505, United States

Location

Binghamton Gastroenterology Associates

Binghamton, New York, 13903, United States

Location

Mount Sinai School of Medicine

New York, New York, 10029, United States

Location

Asheville Gastroenterology Associates, P.A.

Asheville, North Carolina, 28801, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Digestive Health Specialists, PA

Winston-Salem, North Carolina, 27103, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

University Gastroenterology

Providence, Rhode Island, 02905, United States

Location

The Miriam Hospital

Providence, Rhode Island, 02906, United States

Location

Gastro One

Germantown, Tennessee, 38138, United States

Location

Nashville Gastrointestinal Specialists, Inc

Nashville, Tennessee, 37211, United States

Location

Texas Clinical Research Institute, LLC

Arlington, Texas, 76012, United States

Location

Southwest Infectious Disease Clinical Research, Inc.

Dallas, Texas, 75219, United States

Location

Alamo Medical Research

San Antonio, Texas, 78215, United States

Location

Metropolitan Research

Fairfax, Virginia, 22031, United States

Location

Inova Fairfax Hospital Center for Liver Diseases

Falls Church, Virginia, 22042, United States

Location

Digestive and Liver Disease Specialists

Norfolk, Virginia, 23502, United States

Location

Bon Secours St. Mary's Hospital of Richmond, Inc.

Richmond, Virginia, 23226, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

University of Calgary

Calgary, Alberta, T2N 4Z6, Canada

Location

University of Alberta Hospital

Edmonton, Alberta, T6G 2B7, Canada

Location

University of Alberta Hospital

Edmonton, Alberta, T6G 2X8, Canada

Location

Gordon & Leslie Diamond Health Care Centre

Vancouver, British Columbia, V5Z 1M9, Canada

Location

University of British Columbia

Vancouver, British Columbia, V6Z 2C9, Canada

Location

(G.I.R.I.) Gastrointestinal Research Institute

Vancouver, British Columbia, V6Z 2K5, Canada

Location

University of Manitoba Health Sciences Center

Winnipeg, Manitoba, R3E 3P4, Canada

Location

The Ottawa Hospital

Ottawa, Ontario, K1H 8L6, Canada

Location

Mount Sinai Hospital

Toronto, Ontario, M5G 1X5, Canada

Location

Toronto Western Hospital

Toronto, Ontario, M5T 2S8, Canada

Location

Toronto Liver Centre

Toronto, Ontario, M6H 3M1, Canada

Location

Hopital St. Luc

Montreal, Quebec, H2X 3J4, Canada

Location

Auckland Clinical Studies Limited

Auckland, 1640, New Zealand

Location

Christchurch Hospital

Christchurch, 8011, New Zealand

Location

Clinical Research Puerto Rico Inc

San Juan, PR, 00909-1711, Puerto Rico

Location

Fundacion De Investigacion De Diego

San Juan, PR, 00927, Puerto Rico

Location

Related Publications (3)

  • Younossi ZM, Stepanova M, Sulkowski M, Naggie S, Puoti M, Orkin C, Hunt SL. Sofosbuvir and Ribavirin for Treatment of Chronic Hepatitis C in Patients Coinfected With Hepatitis C Virus and HIV: The Impact on Patient-Reported Outcomes. J Infect Dis. 2015 Aug 1;212(3):367-77. doi: 10.1093/infdis/jiv005. Epub 2015 Jan 12.

  • Stepanova M, Nader F, Cure S, Bourhis F, Hunt S, Younossi ZM. Patients' preferences and health utility assessment with SF-6D and EQ-5D in patients with chronic hepatitis C treated with sofosbuvir regimens. Aliment Pharmacol Ther. 2014 Sep;40(6):676-85. doi: 10.1111/apt.12880. Epub 2014 Jul 15.

  • Jacobson IM, Gordon SC, Kowdley KV, Yoshida EM, Rodriguez-Torres M, Sulkowski MS, Shiffman ML, Lawitz E, Everson G, Bennett M, Schiff E, Al-Assi MT, Subramanian GM, An D, Lin M, McNally J, Brainard D, Symonds WT, McHutchison JG, Patel K, Feld J, Pianko S, Nelson DR; POSITRON Study; FUSION Study. Sofosbuvir for hepatitis C genotype 2 or 3 in patients without treatment options. N Engl J Med. 2013 May 16;368(20):1867-77. doi: 10.1056/NEJMoa1214854. Epub 2013 Apr 23.

MeSH Terms

Conditions

Hepatitis C, Chronic

Interventions

Sofosbuvir

Condition Hierarchy (Ancestors)

Hepatitis CBlood-Borne InfectionsCommunicable DiseasesInfectionsHepatitis, Viral, HumanVirus DiseasesFlaviviridae InfectionsRNA Virus InfectionsHepatitis, ChronicHepatitisLiver DiseasesDigestive System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Uridine MonophosphateUracil NucleotidesPyrimidine NucleotidesPyrimidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsNucleotidesNucleic Acids, Nucleotides, and NucleosidesRibonucleotides

Results Point of Contact

Title
Clinical Trial Disclosures
Organization
Gilead Sciences, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 21, 2012

First Posted

May 24, 2012

Study Start

June 1, 2012

Primary Completion

February 1, 2013

Study Completion

May 1, 2013

Last Updated

May 28, 2014

Results First Posted

May 1, 2014

Record last verified: 2014-05

Locations