NCT01600716

Brief Summary

This study will evaluate the safety and efficacy of OnabotulinumtoxinA (BOTOX®) for the treatment of urinary incontinence due to NDO in non-catheterizing patients with MS.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
144

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Jun 2012

Typical duration for phase_3

Geographic Reach
8 countries

10 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 15, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

May 17, 2012

Completed
27 days until next milestone

Study Start

First participant enrolled

June 13, 2012

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 4, 2014

Completed
12 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 27, 2015

Completed
12 months until next milestone

Results Posted

Study results publicly available

March 22, 2016

Completed
Last Updated

April 30, 2019

Status Verified

April 1, 2019

Enrollment Period

1.8 years

First QC Date

May 15, 2012

Results QC Date

February 17, 2016

Last Update Submit

April 17, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Daily Average Frequency of Urinary Incontinence Episodes

    Incontinence is defined as involuntary loss of urine as recorded in a patient bladder diary. The number of episodes of urinary incontinence is recorded over a 3-day period the week of the study visit. A negative number change from baseline indicates a reduction in incontinence episodes (improvement) and a positive number change indicates an increase in incontinence episodes (worsening).

    Baseline, Week 6

Secondary Outcomes (3)

  • Change From Baseline in Maximum Cystometric Capacity (MCC)

    Baseline, Week 6

  • Change From Baseline in Maximum Detrusor Pressure During the First Involuntary Detrusor Contraction (IDC)

    Baseline, Week 6

  • Change From Baseline in Incontinence Quality of Life Instrument (I-QOL) Total Summary Score

    Baseline, Week 6

Other Outcomes (1)

  • Duration of Treatment Effect Through Week 52

    Up to 52 Weeks

Study Arms (2)

OnabotulinumtoxinA

EXPERIMENTAL

OnabotulinumtoxinA 100 U is administered into the detrusor at Day 1. After a minimum of 12 weeks, patients could request/qualify for a second onabotulinumtoxinA 100 U injection.

Biological: OnabotulinumtoxinA

Placebo (Normal Saline)

OTHER

Placebo (normal saline) is administered into the detrusor at Day 1. After a minimum of 12 weeks, patients could request/qualify for an onabotulinumtoxinA injection.

Biological: OnabotulinumtoxinADrug: Placebo (Normal Saline)

Interventions

OnabotulinumtoxinA 100 U is administered into the detrusor at Day 1 in the onabotulinumtoxinA 100 U arm. After a minimum of 12 weeks, patients in both the onabotulinumtoxinA 100 U arm and the placebo arm could request/qualify for an onabotulinumtoxinA injection.

Also known as: BOTOX®, botulinum toxin Type A
OnabotulinumtoxinAPlacebo (Normal Saline)

Placebo (normal saline) is administered into the detrusor at Day 1.

Placebo (Normal Saline)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • At least 3 episodes of urinary incontinence over a 3-day period
  • History of Multiple Sclerosis (MS)
  • Urinary incontinence not adequately controlled by anticholinergic medication

You may not qualify if:

  • Current use of intermittent catheter or indwelling catheter to manage urinary incontinence
  • Previous or current botulinum toxin therapy of any serotype for any urological condition
  • Previous or current botulinum toxin therapy of any serotype for any non-urological condition within the last 12 weeks
  • Diagnosis of myasthenia gravis, Eaton-Lambert Syndrome, or Amyotrophic Lateral Sclerosis

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (10)

Unknown Facility

Mountlake Terrace, Washington, United States

Location

Unknown Facility

Liège, Belgium

Location

Unknown Facility

Victoria, British Columbia, Canada

Location

Unknown Facility

Kitchener, Ontario, Canada

Location

Unknown Facility

Olomouc, Czechia

Location

Unknown Facility

Garches, France

Location

Unknown Facility

Marseille, France

Location

Unknown Facility

Warsaw, Poland

Location

Unknown Facility

Porto, Portugal

Location

Unknown Facility

Saint Petersburg, Russia

Location

Related Publications (1)

  • Tullman M, Chartier-Kastler E, Kohan A, Keppenne V, Brucker BM, Egerdie B, Mandle M, Nicandro JP, Jenkins B, Denys P. Low-dose onabotulinumtoxinA improves urinary symptoms in noncatheterizing patients with MS. Neurology. 2018 Aug 14;91(7):e657-e665. doi: 10.1212/WNL.0000000000005991. Epub 2018 Jul 20.

    PMID: 30030330BACKGROUND

MeSH Terms

Conditions

Urinary IncontinenceMultiple SclerosisUrinary Bladder, Neurogenic

Interventions

Botulinum Toxins, Type ASaline Solution

Condition Hierarchy (Ancestors)

Urination DisordersUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesLower Urinary Tract SymptomsUrological ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesAutoimmune DiseasesImmune System DiseasesNeurologic ManifestationsUrinary Bladder Diseases

Intervention Hierarchy (Ancestors)

Botulinum ToxinsMetalloendopeptidasesEndopeptidasesPeptide HydrolasesHydrolasesEnzymesEnzymes and CoenzymesMetalloproteasesBacterial ProteinsProteinsAmino Acids, Peptides, and ProteinsBacterial ToxinsToxins, BiologicalBiological FactorsCrystalloid SolutionsIsotonic SolutionsSolutionsPharmaceutical Preparations

Results Point of Contact

Title
Therapeutic Area Head,
Organization
Allergan, Inc

Study Officials

  • Medical Director

    Allergan

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 15, 2012

First Posted

May 17, 2012

Study Start

June 13, 2012

Primary Completion

April 4, 2014

Study Completion

March 27, 2015

Last Updated

April 30, 2019

Results First Posted

March 22, 2016

Record last verified: 2019-04

Locations