NCT01586533

Brief Summary

This double-blind, randomized, comparator-controlled Phase II study is designed to establish the safety and efficacy of Zoenasa Rectal Gel compared to mesalamine enema in subjects with left-sided ulcerative colitis, as measured by the modified ulcerative colitis disease activity index (UCDAI), over 6 weeks of treatment. In this study, two cohorts of subjects will receive either Zoenasa-1:4 (1.0g NAC; 4.0g 5-ASA) investigational drug enema therapy or comparator mesalamine enema (4.0g 5-ASA). The study will enroll subjects randomized equally into the 2 cohorts. Each cohort will enroll approximately 60 subjects. The two arms of the trial will be enrolled concurrently in a randomized fashion.

Trial Health

55
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
120

participants targeted

Target at P50-P75 for phase_2

Geographic Reach
1 country

45 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 25, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

April 27, 2012

Completed
1 month until next milestone

Study Start

First participant enrolled

June 1, 2012

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2014

Completed
Last Updated

January 8, 2014

Status Verified

January 1, 2014

Enrollment Period

1.8 years

First QC Date

April 25, 2012

Last Update Submit

January 7, 2014

Conditions

Keywords

ulcerative colitisUCleft-sided ulcerative colitisdistal ulcerative colitisZoenasamesalaminemesalazine5-ASA5-aminosalicylic acidN-acetylcysteineacetylcysteineNACenemarectal gel

Outcome Measures

Primary Outcomes (1)

  • Change in modified UCDAI at 6 weeks

    Change from baseline in the modified Ulcerative Colitis Disease Activity Index (modified UCDAI) score at the end of the 6 week treatment period of Zoenasa™ Rectal Gel compared with mesalamine

    6 weeks

Secondary Outcomes (11)

  • Change in modified UCDAI at 3 weeks

    3 weeks

  • Clinical and endoscopic remission rates at 6 weeks

    6 weeks

  • Clinical and endoscopic remission rates at 3 weeks

    3 weeks

  • Clinical improvement rate after 6 weeks

    6 weeks

  • Clinical improvement rate after 3 weeks

    3 weeks

  • +6 more secondary outcomes

Study Arms (2)

Zoenasa-1:4

EXPERIMENTAL
Drug: Zoenasa-1:4

Mesalamine Enema

ACTIVE COMPARATOR
Drug: Mesalamine Enema

Interventions

Zoenasa Rectal Gel (4.0g mesalamine \[5-ASA\], 1.0g N-acetylcysteine \[NAC\]; 60ml)

Zoenasa-1:4

Mesalamine Rectal Suspension Enema (4.0g mesalamine \[5-ASA\], 60ml)

Mesalamine Enema

Eligibility Criteria

Age18 Years - 64 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • Male and female subjects are eligible if they are ≥ 18 years of age and ≤ 64 years.
  • They have a documented history of idiopathic ulcerative colitis based on endoscopic and/or histologic findings involving the left side of the colon, with mild to moderate active disease.
  • Eligible subjects will have a documented history of ulcerative colitis, and a modified UCDAI score of 4-10, inclusive, with a Physician's rating of disease score of 2 points or less (mild or moderate active ulcerative colitis), rectal bleeding score of 1 or more (based on subject diary), and mucosal appearance score (based on endoscopy) of 1 point or more at baseline.
  • Laboratory data:
  • White blood cell count between 4.0 - 12.0 K/mm3
  • Platelet count: 150 - 500 K/mm3
  • Hemoglobin \> 10.0 g/dL
  • Total bilirubin \< 1.5 mg/dL
  • Aspartate aminotransferase \< 100 u/dL
  • Alanine aminotransferase \< 100 u/dL
  • Alkaline phosphatase \< 250 u/dL
  • Blood urine nitrogen \< 40 mg/dL
  • Creatinine \< 1.5 mg/dL
  • Satisfies one of the following:
  • Female subjects of childbearing potential must have a negative urine pregnancy test at screening; surgically sterile, post-menopausal, abstinent, or patient or partner agree to use a medically appropriate form of birth control from screening to until 1 month after the last dose of study medication.
  • +2 more criteria

You may not qualify if:

  • They have documented history of proximal or universal ulcerative colitis, proctitis or active proctitis confined to 15cm or less from the anal verge.
  • They demonstrate signs and symptoms of fulminant colitis, bowel stricture, toxic megacolon, an anticipated need for blood transfusion for gastrointestinal bleeding, or demonstrate evidence of peritonitis.
  • They receive a Physician's rating of disease severity as part of the modified UCDAI of 3 (severe disease) or an aggregate score of 11 or greater.
  • They have shown prior documented history of evidence of high grade dysplasia on biopsy from endoscopic examinations.
  • Their stool contains enteric pathogens or Clostridium difficile toxins.
  • They have a history of recurrent Clostridium difficile infection.
  • They have prior history of biologic therapy within the previous 4 years.
  • They have received systemic steroids or immunosuppressants within the previous 4 weeks.
  • Treatment in the last 14 days that included antibiotic, antifungal, antiparasitic medications, or rectally administered steroids (e.g. Cortenema®) or mesalamine enema (Rowasa®).
  • Treatment in the last 7 days that included mesalamine (5-ASA) via oral administration (e.g. Asacol®, Lialda®, balsalazide, etc).
  • They have a history of cancer (defined as malignancy within 5 years except for squamous cell or basal cell cancers of the skin), asthma, or bronchospasm.
  • Positive pregnancy test or lactating subjects.
  • There is evidence of chemical substance abuse.
  • They have had repeated anti-inflammatory drug treatment (longer than 3 days at doses that exceed those available without a prescription) within the previous 7 days (with exception of aspirin at doses of 325mg/day or less for prophylaxis of cardiac disease), or initiated new non-steroidal anti-inflammatory (NSAID) treatment within the last 30 days.
  • They have a known allergy to N-acetylcysteine or mesalamine, or have a history of serious AEs related to their use (including, but not limited to pancreatitis or hepatitis).
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (45)

Birmingham Gastroenterology Associates

Birmingham, Alabama, 35209, United States

Location

Digestive Health Specialists of the Southeast

Dothan, Alabama, 36305, United States

Location

Rocky Mountain Gastroenterology

Lakewood, Colorado, 80214, United States

Location

Digestive Disease Associates

Gainesville, Florida, 32605, United States

Location

Digestive Medical Associates

Hialeah, Florida, 33016, United States

Location

The Center for Gastrointestinal Disorders

Hollywood, Florida, 33021, United States

Location

Miami Gastroenterology Consultants P.A.

Miami, Florida, 33156, United States

Location

South Medical Research Group

Miami, Florida, 33186, United States

Location

Gastroenterology of Naples

Naples, Florida, 34102, United States

Location

Advanced Gastroenterology Associates

Palm Harbor, Florida, 34684, United States

Location

Shafran Gastroenterology

Winter Park, Florida, 32789, United States

Location

Tri-County Research

Athens, Georgia, 30606, United States

Location

Digestive Healthcare of Georgia

Atlanta, Georgia, 30309, United States

Location

The Atlanta Center for Gastroenterology

Decatur, Georgia, 30033, United States

Location

St. Josephs Candler Health System

Savannah, Georgia, 31405, United States

Location

NCH Medical Group

Arlington Heights, Illinois, 60004, United States

Location

Gastrointestinal Clinic of Quad Cities

Davenport, Iowa, 52807, United States

Location

Professional Research Network of Kansas

Wichita, Kansas, 67203, United States

Location

Clinical Trials Management of Louisiana

Metairie, Louisiana, 70006, United States

Location

Dr. Jason Bozdin, M.D.

Berkley, Michigan, 48072, United States

Location

Clinical Research Institute of Michigan, LLC

Chesterfield, Michigan, 48047, United States

Location

Gregory Cammel, MD PLC

Wyoming, Michigan, 48418, United States

Location

GI Associates and Endoscopy Center

Jackson, Mississippi, 39202, United States

Location

Long Island Clinical Research Associates

Great Neck, New York, 11021, United States

Location

Research Associates of New York

New York, New York, 10028, United States

Location

Asheville Gastroenterology Associates, P.A.

Asheville, North Carolina, 28801, United States

Location

Carolina Digestive Health Associates

Davidson, North Carolina, 28036, United States

Location

LeBauer Research Associates, P.A.

Greensboro, North Carolina, 27403, United States

Location

Greater Cincinnati Gastroenterology

Cincinnati, Ohio, 45219, United States

Location

Central Sooner Research

Norman, Oklahoma, 73071, United States

Location

Oklahoma Foundation for Digestive Research

Oklahoma City, Oklahoma, 73104, United States

Location

Options Health Research

Tulsa, Oklahoma, 74104, United States

Location

Gastroenterology United Tulsa

Tulsa, Oklahoma, 74135, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15213, United States

Location

Gastro One

Germantown, Tennessee, 38138, United States

Location

Memphis Gastroenterology Group

Germantown, Tennessee, 38138, United States

Location

Dallas VA Medical Center

Dallas, Texas, 75216, United States

Location

Houston Digestive Disease Clinic

Houston, Texas, 77090, United States

Location

Digestive Health Associates of Texas

Plano, Texas, 75075, United States

Location

Advanced Research Institute

South Ogden, Utah, 84405, United States

Location

New River Valley Research Institute

Christiansburg, Virginia, 24073, United States

Location

Digestive & Liver Disease Specialists

Norfolk, Virginia, 23502, United States

Location

Digestive Disease Institute

Seattle, Washington, 98101, United States

Location

Franciscan Research Center

Tacoma, Washington, 98405, United States

Location

Wisconsin Center for Advanced Research

Milwaukee, Wisconsin, 53215, United States

Location

MeSH Terms

Conditions

Colitis, Ulcerative

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 25, 2012

First Posted

April 27, 2012

Study Start

June 1, 2012

Primary Completion

April 1, 2014

Last Updated

January 8, 2014

Record last verified: 2014-01

Locations