NCT01563029

Brief Summary

This is a Phase IIb, multi-centre, stratified, randomised, double-blind, double-dummy, parallel-group, placebo and active controlled study in children aged 5-11 years with persistent uncontrolled asthma. Subjects meeting all of the inclusion criteria and none of the exclusion criteria at the screening visit (Visit 1) will enter a four week run-in period during which time they will continue their current medications. Visit 2 will occur two weeks into the run-in period to allow a review of compliance with daily diary and run-in medication. At Visit 3 (end of run-in/randomization visit), subjects meeting the eligibility criteria who remain uncontrolled despite baseline therapy will be stratified based on pre screening inhaled corticosteroid (ICS) use. Once stratified, subjects will be randomised to the treatment phase of the study where they will receive one of five treatments for 12 weeks. Approx 1200 subjects ages 5 to 11 will be screened to achieve 575 randomized for a total of 115 randomized/evaluable subjects per treatment arm. Subjects will attend on-treatment visits at 2, 4, 8 and 12 weeks (Visits 4, 5, 6 and 7 respectively). A follow-up contact will be performed one week after completing study medication. All subjects must attempt spirometry measurements at Visits 1 and 3. For all subjects, a timed 24-hour urine collection for urinary cortisol and creatinine excretion will be performed prior to randomization at Visit 2 and within 7 days prior to Visit 7. All subjects must perform PEF daily between visits 1 and 7. The primary endpoint will be change from baseline in pre-dose (i.e. dosing trough) PM PEF from patient hand held electronic daily diary at Endpoint (Endpoint is defined as the mean over the last 7 days of treatment). Safety assessments include adverse events, oropharyngeal examinations, clinical chemistry, urinary cortisol, and vital signs.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
597

participants targeted

Target at P75+ for phase_2 asthma

Timeline
Completed

Started Mar 2012

Typical duration for phase_2 asthma

Geographic Reach
15 countries

139 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 15, 2012

Completed
11 days until next milestone

First Posted

Study publicly available on registry

March 26, 2012

Completed
2 days until next milestone

Study Start

First participant enrolled

March 28, 2012

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 24, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 24, 2014

Completed
7 months until next milestone

Results Posted

Study results publicly available

April 27, 2015

Completed
Last Updated

May 30, 2017

Status Verified

April 1, 2017

Enrollment Period

2.5 years

First QC Date

March 15, 2012

Results QC Date

April 9, 2015

Last Update Submit

April 25, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Daily Pre-dose Morning (AM) Peak Expiratory Flow (PEF) From Participant Electronic Daily Diary Averaged Over the 12-week Treatment Period

    PEF is defined as the maximum airflow during a forced expiration beginning with the lungs fully inflated. PEF was measured by the participants using a hand-held electronic peak flow meter each morning prior to the dose of study medication and any rescue albuterol/salbutamol inhalation aerosol use. The best of three measurements was recorded. Change from Baseline was calculated as the value of the averaged daily AM PEF over the 12-week Treatment Period minus the Baseline value. The Baseline PEF value is defined as the average of the last 7 days of the Run-in Period. Statistical analysis was performed using an analysis of covariance (ANCOVA) model with covariates of Baseline AM PEF, actual pre-screening inhaled corticosteroid (ICS) use, region, sex, age, and treatment. Particpants analyzed included those who have PEF data for at least 2 non-missing days in the Baseline week prior to randomisation and at least 2 non-missing days after randomisation.

    Baseline; Week 1 up to Week 12

Secondary Outcomes (7)

  • Change From Baseline in Evening Clinic Visit Trough (Pre-bronchodilator and Pre-dose) Forced Expiratory Volume in One Second (FEV1) at the End of the 12-week Treatment Period in Children Who Could Perform the Maneuver

    Baseline, Week 12

  • Change From Baseline in the Percentage of Rescue-free 24-hour Periods During the 12-week Treatment Period

    Baseline; Week 1 up to Week 12

  • Change From Baseline in Daily Evening (PM) PEF Averaged Over the 12-week Treatment Period

    Baseline; Week 1 up to Week 12

  • Change From Baseline in PM PEF Over the Last 7 Days of the Treatment Period (Week 12)

    Baseline; Week 12

  • Change From Baseline in AM PEF Over the Last 7 Days of the Treatment Period (Week 12)

    Baseline; Week 12

  • +2 more secondary outcomes

Study Arms (5)

Arm 1

ACTIVE COMPARATOR

Fluticasone Furoate 100mcg inhalation powder once daily in the evening ICS powder

Drug: Fluticasone Furoate

Arm 2

ACTIVE COMPARATOR

Fluticasone Furoate 50mcg inhalation powder once daily in the evening ICS powder

Drug: Fluticasone Furoate

Arm 3

ACTIVE COMPARATOR

Fluticasone Furoate 25mcg inhalation powder once daily in the evening ics powder

Drug: Fluticasone Furoate

Arm 4

ACTIVE COMPARATOR

Fluticasone Propionate 100mcg inhalation powder twice daily ICS powder

Drug: Fluticasone Propionate

Arm 5

PLACEBO COMPARATOR

Placebo inhalation powder once daily in the evening Placebo powder

Drug: Placebo

Interventions

current asthma medicine

Arm 1Arm 2Arm 3

Fluticasone propionate

Arm 4

placebo

Arm 5

Eligibility Criteria

Age5 Years - 11 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Written informed consent from at least one parent/ legal guardian to take part in the study.:
  • Diagnosis of asthma
  • pre-bronchodilator PEF between ≥50% to ≤90% of their best post-bronchodilator value

You may not qualify if:

  • history of life-threatening asthma
  • history of asthma exacerbation for asthma within 6 months prior to screening.
  • Culture-documented or suspected bacterial or viral infection
  • significant abnormality or medical condition
  • Present use of any tobacco products

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (139)

GSK Investigational Site

Little Rock, Arkansas, 72205, United States

Location

GSK Investigational Site

Costa Mesa, California, 92626, United States

Location

GSK Investigational Site

Huntington Beach, California, 92647, United States

Location

GSK Investigational Site

Long Beach, California, 90808, United States

Location

GSK Investigational Site

Newport Beach, California, 92663, United States

Location

GSK Investigational Site

Orange, California, 92868, United States

Location

GSK Investigational Site

Rolling Hills Estates, California, 90274, United States

Location

GSK Investigational Site

Aventura, Florida, 33180, United States

Location

GSK Investigational Site

Cocoa, Florida, 32927, United States

Location

GSK Investigational Site

Miami, Florida, 33173, United States

Location

GSK Investigational Site

Columbus, Georgia, 31904, United States

Location

GSK Investigational Site

Eagle, Idaho, 83616, United States

Location

GSK Investigational Site

Normal, Illinois, 61761, United States

Location

GSK Investigational Site

Shiloh, Illinois, 62269, United States

Location

GSK Investigational Site

Lenexa, Kansas, 66215, United States

Location

GSK Investigational Site

Owensboro, Kentucky, 42301, United States

Location

GSK Investigational Site

Stevensville, Michigan, 49127, United States

Location

GSK Investigational Site

Plymouth, Minnesota, 55441, United States

Location

GSK Investigational Site

Columbia, Missouri, 65203, United States

Location

GSK Investigational Site

Rolla, Missouri, 65401, United States

Location

GSK Investigational Site

Corning, New York, 14830, United States

Location

GSK Investigational Site

Raleigh, North Carolina, 27607, United States

Location

GSK Investigational Site

Canton, Ohio, 44718, United States

Location

GSK Investigational Site

Cincinnati, Ohio, 45231, United States

Location

GSK Investigational Site

Oklahoma City, Oklahoma, 73112, United States

Location

GSK Investigational Site

Medford, Oregon, 97504, United States

Location

GSK Investigational Site

Portland, Oregon, 97202, United States

Location

GSK Investigational Site

Pittsburgh, Pennsylvania, 15241, United States

Location

GSK Investigational Site

Charleston, South Carolina, 29407, United States

Location

GSK Investigational Site

Orangeburg, South Carolina, 29118, United States

Location

GSK Investigational Site

Austin, Texas, 78750, United States

Location

GSK Investigational Site

Dallas, Texas, 75230, United States

Location

GSK Investigational Site

El Paso, Texas, 79925, United States

Location

GSK Investigational Site

San Antonio, Texas, 78229, United States

Location

GSK Investigational Site

San Antonio, Texas, 78258, United States

Location

GSK Investigational Site

Waco, Texas, 76712, United States

Location

GSK Investigational Site

South Burlington, Vermont, 05403, United States

Location

GSK Investigational Site

Plovdiv, 4002, Bulgaria

Location

GSK Investigational Site

Plovdiv, 4003, Bulgaria

Location

GSK Investigational Site

Rousse, 7000, Bulgaria

Location

GSK Investigational Site

Sofia, Bulgaria

Location

GSK Investigational Site

Tbilisi, 0119, Georgia

Location

GSK Investigational Site

Tbilisi, 0159, Georgia

Location

GSK Investigational Site

Tbilisi, 0160, Georgia

Location

GSK Investigational Site

Tbilisi, 0186, Georgia

Location

GSK Investigational Site

Mannheim, Baden-Wurttemberg, 68163, Germany

Location

GSK Investigational Site

Berchtesgaden, Bavaria, 83471, Germany

Location

GSK Investigational Site

Rosenheim, Bavaria, 83026, Germany

Location

GSK Investigational Site

Frankfurt am Main, Hesse, 60596, Germany

Location

GSK Investigational Site

Neu-Isenburg, Hesse, 63263, Germany

Location

GSK Investigational Site

Niedernhausen, Hesse, 65527, Germany

Location

GSK Investigational Site

Göttingen, Lower Saxony, 37073, Germany

Location

GSK Investigational Site

Wolfenbüttel, Lower Saxony, 38302, Germany

Location

GSK Investigational Site

Bochum, North Rhine-Westphalia, 44791, Germany

Location

GSK Investigational Site

Hamm, North Rhine-Westphalia, 59063, Germany

Location

GSK Investigational Site

Kleve-Materborn, North Rhine-Westphalia, 47533, Germany

Location

GSK Investigational Site

Telgte, North Rhine-Westphalia, 48291, Germany

Location

GSK Investigational Site

Dresden, Saxony, 01307, Germany

Location

GSK Investigational Site

Geesthacht, Schleswig-Holstein, 21502, Germany

Location

GSK Investigational Site

Neuhaus am Rennweg, Thuringia, 98724, Germany

Location

GSK Investigational Site

Berlin, 10785, Germany

Location

GSK Investigational Site

Hamburg, 22415, Germany

Location

GSK Investigational Site

Chiba, 260-0001, Japan

Location

GSK Investigational Site

Fukuoka, 811-1394, Japan

Location

GSK Investigational Site

Hiroshima, 720-8520, Japan

Location

GSK Investigational Site

Hokkaido, 006-0831, Japan

Location

GSK Investigational Site

Hokkaido, 064-0821, Japan

Location

GSK Investigational Site

Hyōgo, 653-0021, Japan

Location

GSK Investigational Site

Kagawa, 762-0031, Japan

Location

GSK Investigational Site

Mie, 514-0125, Japan

Location

GSK Investigational Site

Osaka, 583-8588, Japan

Location

GSK Investigational Site

Tokyo, 154-0017, Japan

Location

GSK Investigational Site

Tokyo, 157-0066, Japan

Location

GSK Investigational Site

Tokyo, 158-0097, Japan

Location

GSK Investigational Site

Wakayama, 646-8558, Japan

Location

GSK Investigational Site

Daugavpils, LV5403, Latvia

Location

GSK Investigational Site

Rēzekne, LV-4601, Latvia

Location

GSK Investigational Site

Riga, LV 1003, Latvia

Location

GSK Investigational Site

Riga, LV 1004, Latvia

Location

GSK Investigational Site

Riga, LV1011, Latvia

Location

GSK Investigational Site

Guadalajara, Jalisco, 44100, Mexico

Location

GSK Investigational Site

Zapopan, Jalisco, 45040, Mexico

Location

GSK Investigational Site

Morelia, Michoacán, 58070, Mexico

Location

GSK Investigational Site

Villahermosa, Tabasco, 86100, Mexico

Location

GSK Investigational Site

Mexico City, 06720, Mexico

Location

GSK Investigational Site

Mexico City, 07760, Mexico

Location

GSK Investigational Site

México, 04530, Mexico

Location

GSK Investigational Site

Lima, Lima Province, Lima 27, Peru

Location

GSK Investigational Site

Lima, Lima Province, Peru

Location

GSK Investigational Site

San Borja, Lima region, Lima 41, Peru

Location

GSK Investigational Site

San Miguel, Lima region, Lima 32, Peru

Location

GSK Investigational Site

Lima, Lima 11, Peru

Location

GSK Investigational Site

Lima, Lima 27, Peru

Location

GSK Investigational Site

Lima, Lima 29, Peru

Location

GSK Investigational Site

Manila, 1000, Philippines

Location

GSK Investigational Site

Manila, 1003, Philippines

Location

GSK Investigational Site

Quezon City, 1113, Philippines

Location

GSK Investigational Site

Bialystok, 15-183, Poland

Location

GSK Investigational Site

Bialystok, 15-430, Poland

Location

GSK Investigational Site

Bydgoszcz, 85-046, Poland

Location

GSK Investigational Site

Dębica, 39-200, Poland

Location

GSK Investigational Site

Kielce, 25-017, Poland

Location

GSK Investigational Site

Lodz, 93-513, Poland

Location

GSK Investigational Site

Lublin, 20-089, Poland

Location

GSK Investigational Site

Lublin, 20-093, Poland

Location

GSK Investigational Site

Lublin, 20-552, Poland

Location

GSK Investigational Site

Poznan, 60-693, Poland

Location

GSK Investigational Site

Tarnów, 33-100, Poland

Location

GSK Investigational Site

Hato Rey, Puerto Rico, 00917, Puerto Rico

Location

GSK Investigational Site

Blagoveshchensk, 675000, Russia

Location

GSK Investigational Site

Moscow, 119991, Russia

Location

GSK Investigational Site

Murmansk, 183031, Russia

Location

GSK Investigational Site

Novokuznetsk, 654063, Russia

Location

GSK Investigational Site

Novosibirsk, 630091, Russia

Location

GSK Investigational Site

Saint Petersburg, 194356, Russia

Location

GSK Investigational Site

Voronezh, 394036, Russia

Location

GSK Investigational Site

Yaroslavl, 150003, Russia

Location

GSK Investigational Site

Panorama, Western Province, 7500, South Africa

Location

GSK Investigational Site

CapeTown, 7764, South Africa

Location

GSK Investigational Site

Middelburg, 1501, South Africa

Location

GSK Investigational Site

Gothenburg, SE-416 85, Sweden

Location

GSK Investigational Site

Kungsbacka, SE-434 30, Sweden

Location

GSK Investigational Site

Örebro, SE-701 85, Sweden

Location

GSK Investigational Site

Stockholm, SE-118 83, Sweden

Location

GSK Investigational Site

Stockholm, SE171 76, Sweden

Location

GSK Investigational Site

Uppsala, SE-752 26, Sweden

Location

GSK Investigational Site

Visby, SE-621 84, Sweden

Location

GSK Investigational Site

Chernivtsi, 58001, Ukraine

Location

GSK Investigational Site

Ivano-Frankivsk, 76018, Ukraine

Location

GSK Investigational Site

Kharkiv, 61093, Ukraine

Location

GSK Investigational Site

Kherson, 73000, Ukraine

Location

GSK Investigational Site

Kyiv, 03680, Ukraine

Location

GSK Investigational Site

Kyiv, 04050, Ukraine

Location

GSK Investigational Site

Luhansk, 91000, Ukraine

Location

GSK Investigational Site

Simferopol, 95034, Ukraine

Location

GSK Investigational Site

Vinnytsia, 21021, Ukraine

Location

GSK Investigational Site

Yevpatoriia, 97408, Ukraine

Location

GSK Investigational Site

Zaporizhia, 69063, Ukraine

Location

GSK Investigational Site

Zaporizhia, 69076, Ukraine

Location

Related Publications (1)

  • Oliver AJ, Covar RA, Goldfrad CH, Klein RM, Pedersen SE, Sorkness CA, Tomkins SA, Villaran C, Grigg J. Randomized Trial of Once-Daily Fluticasone Furoate in Children with Inadequately Controlled Asthma. J Pediatr. 2016 Nov;178:246-253.e2. doi: 10.1016/j.jpeds.2016.08.010. Epub 2016 Sep 9.

Related Links

MeSH Terms

Conditions

Asthma

Interventions

fluticasone furoateFluticasone

Condition Hierarchy (Ancestors)

Bronchial DiseasesRespiratory Tract DiseasesLung Diseases, ObstructiveLung DiseasesRespiratory HypersensitivityHypersensitivity, ImmediateHypersensitivityImmune System Diseases

Intervention Hierarchy (Ancestors)

AndrostadienesAndrostenesAndrostanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Results Point of Contact

Title
GSK Response Center
Organization
GlaxoSmithKline

Study Officials

  • GSK Clinical Trials

    GlaxoSmithKline

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 15, 2012

First Posted

March 26, 2012

Study Start

March 28, 2012

Primary Completion

September 24, 2014

Study Completion

September 24, 2014

Last Updated

May 30, 2017

Results First Posted

April 27, 2015

Record last verified: 2017-04

Data Sharing

IPD Sharing
Will share

Patient-level data for this study will be made available through www.clinicalstudydatarequest.com following the timelines and process described on this site.

Available IPD Datasets

Individual Participant Data Set (106855)Access
Statistical Analysis Plan (106855)Access
Study Protocol (106855)Access
Annotated Case Report Form (106855)Access
Clinical Study Report (106855)Access
Dataset Specification (106855)Access
Informed Consent Form (106855)Access

Locations