NCT01528085

Brief Summary

The goal of this trial is to evaluate the efficacy and the tolerance of the combination of nilotinib with chemotherapy in the front-line setting as induction and consolidation therapy in Ph+ ALL patient aged 55 years and over. A European consensus has been reached to adopt a common chemotherapeutic schedule for patients aged 55 years and over. This schedule will be used in this trial with the addition of nilotinib as concomitant therapy during induction, consolidation and maintenance. The patients will be prospectively monitored for minimal residual disease and bcr-abl tyrosine kinase domain mutations.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
79

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2012

Longer than P75 for phase_2

Geographic Reach
3 countries

69 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2012

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

February 3, 2012

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 7, 2012

Completed
8.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 10, 2020

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

March 10, 2020

Completed
Last Updated

July 30, 2020

Status Verified

July 1, 2020

Enrollment Period

8.2 years

First QC Date

February 3, 2012

Last Update Submit

July 29, 2020

Conditions

Keywords

Philadelphia chromsomeBCR-ABLALLacute lymphoblastic leukemiaNilotinibTasigna

Outcome Measures

Primary Outcomes (1)

  • Evaluation of efficacy of a nilotinib-based induction and consolidation therapy

    rate of patients without event

    after 12 months

Secondary Outcomes (13)

  • complete haematological remission

    after induction treatment (week 5)

  • major molecular response in bone marrow

  • complete molecular response

  • undetectable BCR-ABL level

  • Event free survival

  • +8 more secondary outcomes

Interventions

Nilotinib, p.o Chemotherapy (Dexamethasone, Methotroxate, Cyclophosphamide (optional), Vincristine, Vindesine, Cytarabine, 6-Mercapto-Purine)

Also known as: Tasigna

Eligibility Criteria

Age55 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female patients \> 55 years
  • Philadelphia chromosome- or BCR-ABL positive acute lymphoblastic leukemia
  • Not previously treated except with corticosteroids or single dose vincristine (three doses cyclophosphamide accepted)
  • With or without documented CNS involvement
  • WHO performance status \< 2
  • Normal serum levels \> LLN (lower limit of normal) of potassium, magnesium, total calcium corrected for serum albumin; or corrected to within normal limits with supplements, prior to the first dose of study medication
  • Signed written inform consent
  • Molecular evaluation for BCR-ABL performed
  • Willingness of male subjects whose sexual partners are women of child-bearing potential (WOCBP), to use an effective form of contraception (pearl index \< 1%), such as complete sexual abstinence, combined oral contraceptive, hormone IUCD, vaginal hormone ring, transdermal contraceptive patch, contraceptive implant or depot contraceptive injection in combination with a second method of contraception like a condom or a cervical cap / diaphragm with spermicide or surgical sterilisation (vasectomy) in male patients during the study and at least 6 months thereafter. WOCBP are defined as sexually mature women who have not undergone a hysterectomy or surgical sterilization or who have not been naturally postmenopausal for at least 12 consecutive months (i.e., who has had menses any time in the preceding 12 consecutive months).

You may not qualify if:

  • Patient previously treated with tyrosine kinase inhibitors
  • Known impaired cardiac function, including any of the following:
  • LVEF \< 45%
  • Complete left bundle branch block
  • Right bundle branch block plus left anterior hemiblock, bifascicular block
  • Use of a ventricular-paced pacemaker
  • Congenital long QT syndrome
  • History of or presence of clinically significant ventricular or atrial tachyarrhythmias
  • Clinically significant resting bradycardia (\< 50 beats per minute)
  • QTcF\>450 msec on screening ECG. If QTc \> 450 msec and electrolytes are not within normal ranges before nilotinib dosing, electrolytes should be corrected and then the patient rescreened for QTcF criterion.
  • Myocardial infarction with 12 months prior to starting nilotinib
  • Other clinical significant heart disease (e.g. unstable angina, congestive heart failure, uncontrolled hypertension)
  • Patients with a history of another primary malignancy that is currently clinically significant or currently requires active intervention
  • Known diagnosis of human immunodeficiency virus (HIV) infection (HIV testing is not mandatory) or known infection with Hepatitis B or C
  • Treatment with any, other investigational agent or participating in another trial within 30 days prior to entering this study
  • +18 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (69)

Centre Hospitalier du Pays d'Aix

Aix-en-Provence, 13616, France

Location

CHU d'Amiens - Hôpital Sud

Amiens, 80054, France

Location

Chu Angers

Angers, 49933, France

Location

Centre Hospitalier Victor Dupouy

Argenteuil, 95107, France

Location

Centre Hospitalier de la Côte Basque

Bayonne, 64100, France

Location

CHU de Besançon - Hôpital Jean Minjoz

Besançon, 25030, France

Location

CHU de Brest - Hôpital Morvan

Brest, 29609, France

Location

"CHU Cote de nacre "

Caen, 14000, France

Location

CHU Estaing

Clermont-Ferrand, 63003, France

Location

AP-HP - Hôpital Henri Mondor

Créteil, 94010, France

Location

CHRU de Dijon

Dijon, 21079, France

Location

CHU de Grenoble

Grenoble, 38043, France

Location

CH de Versailles - Hôpital André Mignot

Le Chesnay, 78157, France

Location

Groupe Hospitalier de l'Institut Catholique de Lille, hôpital Saint-Vincent

Lille, 59020, France

Location

CHRU de Lille

Lille, 59037, France

Location

C H U de Limoges - Hôpital Dupuytren

Limoges, 87042, France

Location

Institut Paoli-Calmettes

Marseille, 13273, France

Location

CH de Meaux

Meaux, 77104, France

Location

Hôpital Saint-Eloi

Montpellier, 34295, France

Location

CH de Mulhouse - Hôpital Emile Muller

Mulhouse, 68070, France

Location

CHU Hôtel Dieu, Nantes

Nantes, 44000, France

Location

CHU de Nice - Hôpital l'Archet 1

Nice, 06200, France

Location

CHR d'Orléans - Hôpital La Source

Orléans, 45032, France

Location

AP-HP - Hôpital Saint Louis

Paris, 75010, France

Location

AP-HP - Hôpital SAINT-ANTOINE

Paris, 75571, France

Location

AP-HP - Hôpital Necker

Paris, 75743, France

Location

CH de Perpignan - Hôpital Saint-Jean

Perpignan, 66046, France

Location

CHU de Bordeaux - Hôpital Haut-Lévêque

Pessac, 33604, France

Location

Centre Hospitalier Lyon Sud

Pierre-Bénite, 69495, France

Location

CHU de Poitiers - Hôpital La Milétrie

Poitiers, 86021, France

Location

CH de la Région d'Annecy

Pringy, 74374, France

Location

CHU de Reims - Hôpital Robert Debré

Reims, 51092, France

Location

CHU de Rennes, Hôpital Pontchaillou

Rennes, 35033, France

Location

Centre Henri Becquerel, Rouen

Rouen, 76038, France

Location

CHU de La Réunion - Hôpital Félix Guyon

Saint-Denis, 97405, France

Location

CHRU de Strasbourg - Hôpital Hautepierre

Strasbourg, 67098, France

Location

HIA Sainte Anne

Toulon, 83041, France

Location

"Institut Universitaire du Cancer (CHU de Toulouse - Hôpital Purpan)"

Toulouse, 31100, France

Location

CHRU de Tours - Hôpital Bretonneau

Tours, 37044, France

Location

Centre Hospitalier de Valenciennes

Valenciennes, 59322, France

Location

CHU de Nancy - Hôpital Brabois

Vandœuvre-lès-Nancy, 54511, France

Location

Robert Bosch Krankenhaus

Stuttgart, Baden-Wurttemberg, 70376, Germany

Location

Klinikum der Universität Regensburg

Regensburg, Bavaria, 93042, Germany

Location

University Hospital of Frankfurt, Medical Dept. II

Frankfurt am Main, Hesse, 60590, Germany

Location

Medizinische Hochschule Hannover

Hanover, Lower Saxony, 30625, Germany

Location

Universitätsklinikum Essen

Essen, North Rhine-Westphalia, 45147, Germany

Location

Universitätsklinik Münster

Münster, North Rhine-Westphalia, 48149, Germany

Location

Universitätsklinik Dresden

Dresden, Saxony, 01307, Germany

Location

Uniklinik Aachen

Aachen, 52074, Germany

Location

Charité Universitätsmedizin Berlin

Berlin, 13353, Germany

Location

University Hospital Düsseldorf

Düsseldorf, 40225, Germany

Location

Universitätsklinikum Göttingen

Göttingen, 37075, Germany

Location

Asklepios Klinik St. Georg

Hamburg, 20099, Germany

Location

Universitätsklinikum Schleswig-Holstein Campus Kiel

Kiel, 24116, Germany

Location

Universität Leipzig, José-Carreras-Haus

Leipzig, 04103, Germany

Location

Universitätskliniken Mainz

Mainz, 55101, Germany

Location

Klinikum Mannheim

Mannheim, 68167, Germany

Location

Universitätsklinikum Großhadern

München, 81377, Germany

Location

Klinikum Nürnberg Nord

Nuremberg, 90419, Germany

Location

Klinikum Oldenburg

Oldenburg, 26133, Germany

Location

Universität Rostock

Rostock, 18055, Germany

Location

Medizinische Universitätsklinik Ulm

Ulm, 89070, Germany

Location

Universität Würzburg

Würzburg, 97080, Germany

Location

Hospital Clínic de Barcelona

Barcelona, 08036, Spain

Location

Hospital Universitario Germans Trias i Pujol (ICO - Badalona)

Barcelona, 08916, Spain

Location

Hospital Universitario 12 de Octubre (Madrid)

Madrid, 28041, Spain

Location

Hospital Clínico Universitario de Salamanca

Salamanca, 37007, Spain

Location

Hospital Universitario Virgen del Rocío (Sevilla)

Seville, 41013, Spain

Location

Hospital Universitario y Politécnico La Fe (Valencia)

Valencia, 46026, Spain

Location

Related Links

MeSH Terms

Conditions

Precursor Cell Lymphoblastic Leukemia-Lymphoma

Interventions

nilotinib

Condition Hierarchy (Ancestors)

Leukemia, LymphoidLeukemiaNeoplasms by Histologic TypeNeoplasmsHematologic DiseasesHemic and Lymphatic DiseasesLymphoproliferative DisordersLymphatic DiseasesImmunoproliferative DisordersImmune System Diseases

Study Officials

  • Heike Pfeifer, Dr.med.

    Johann Wolfgang Goethe University Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Dr.med.

Study Record Dates

First Submitted

February 3, 2012

First Posted

February 7, 2012

Study Start

January 1, 2012

Primary Completion

March 10, 2020

Study Completion

March 10, 2020

Last Updated

July 30, 2020

Record last verified: 2020-07

Locations