NCT01517698

Brief Summary

This multi-center, randomized, double-blind, placebo-controlled, parallel-group study will investigate the efficacy and safety of RO4917523 in adolescent and adult patients with fragile X syndrome. Patients will be randomized to receive oral doses of 0.5 mg or 1.5 mg of RO4917523, or matching placebo once daily. The anticipated time on study treatment is 12 weeks.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
185

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2012

Geographic Reach
10 countries

51 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 20, 2012

Completed
5 days until next milestone

First Posted

Study publicly available on registry

January 25, 2012

Completed
3 months until next milestone

Study Start

First participant enrolled

May 1, 2012

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2014

Completed
Last Updated

July 11, 2016

Status Verified

July 1, 2016

Enrollment Period

1.9 years

First QC Date

January 20, 2012

Last Update Submit

July 6, 2016

Conditions

Outcome Measures

Primary Outcomes (2)

  • Change in Anxiety Depression and Mood Scale (ADAMS) total score

    12 weeks

  • Safety (incidence of adverse events)

    12 weeks

Secondary Outcomes (6)

  • Change in Social Responsiveness Scale (SRS)

    12 weeks

  • Change in Clinical Global Impressions Scale - Improvement (CGI-I)

    12 weeks

  • Change in Clinical Global Impressions Scale - Severity of Illness (CGI-S)

    12 weeks

  • Change in Aberrant Behavior Checklist total score

    12 weeks

  • Change in Aberrant Behavior Checklist factor scores

    12 weeks

  • +1 more secondary outcomes

Study Arms (3)

RO4917523 0.5 mg

EXPERIMENTAL
Drug: RO4917523 0.5 mg

RO4917523 1.5 mg

EXPERIMENTAL
Drug: RO4917523 1.5 mg

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

placebo to RO4917523 orally once a day for 12 weeks

Placebo

0.5 mg orally once a day for 12 weeks

RO4917523 0.5 mg

1.5 mg orally once a day for 12 weeks

RO4917523 1.5 mg

Eligibility Criteria

Age14 Years - 50 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Adult and adolescent patients, 14-50 years of age
  • Diagnosis of fragile X syndrome with a confirmed fragile X mental retardation 1 (FMR1) full mutation and qualifying scores on the Aberrant Behavior Checklist (ABC) and CGI-S
  • Patients must agree to either remain completely abstinent or to use two effective contraceptive methods during and 3 weeks after the study

You may not qualify if:

  • Previous treatment with another metabotropic glutamate (mGLU) receptor antagonist within 18 months or with RO4917523
  • Participation in a clinical trial involving an investigational (unapproved) drug within 3 months or 5 times the half-life (whichever is longer) before start of this study
  • Any uncontrolled, unstable clinically significant psychiatric condition other than fragile X syndrome
  • History of suicidal behavior

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (51)

Unknown Facility

Phoenix, Arizona, 85006, United States

Location

Unknown Facility

Long Beach, California, 90806, United States

Location

Unknown Facility

Sacramento, California, 95817, United States

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Unknown Facility

Aurora, Colorado, 80045, United States

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Unknown Facility

Washington D.C., District of Columbia, 20010, United States

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Unknown Facility

Decatur, Georgia, 30033, United States

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Unknown Facility

Chicago, Illinois, 60612, United States

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Unknown Facility

Iowa City, Iowa, 52242-1083, United States

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Unknown Facility

Louisville, Kentucky, 40202, United States

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Unknown Facility

Baltimore, Maryland, 21205, United States

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Unknown Facility

Worcester, Massachusetts, 01655, United States

Location

Unknown Facility

New York, New York, 10029, United States

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Unknown Facility

Staten Island, New York, 10314, United States

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Unknown Facility

Durham, North Carolina, 27710, United States

Location

Unknown Facility

Cincinnati, Ohio, 45229, United States

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Unknown Facility

Media, Pennsylvania, 19063, United States

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Unknown Facility

Nashville, Tennessee, 37203, United States

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Unknown Facility

Houston, Texas, 77030, United States

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Unknown Facility

San Antonio, Texas, 78258, United States

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Unknown Facility

Seattle, Washington, 98145, United States

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Unknown Facility

Bahía Blanca, 8000, Argentina

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Unknown Facility

Caba, 1425, Argentina

Location

Unknown Facility

Caba, C1126AAB, Argentina

Location

Unknown Facility

Brampton, Ontario, L6Y 1M5, Canada

Location

Unknown Facility

Sherbrooke, Quebec, J1H 5N4, Canada

Location

Unknown Facility

Santiago, Chile

Location

Unknown Facility

Valparaíso, 2340000, Chile

Location

Unknown Facility

Bordeaux, 33076, France

Location

Unknown Facility

Bron, 69003, France

Location

Unknown Facility

Dijon, 21079, France

Location

Unknown Facility

Marseille, 13385, France

Location

Unknown Facility

Montpellier, 34295, France

Location

Unknown Facility

Paris, 75013, France

Location

Unknown Facility

Tours, 37044, France

Location

Unknown Facility

Aguascalientes, 20030, Mexico

Location

Unknown Facility

México, 04530, Mexico

Location

Unknown Facility

Lima, Lima 33, Peru

Location

Unknown Facility

Lima, Peru

Location

Unknown Facility

San Cugat Del Valles, Barcelona, 08195, Spain

Location

Unknown Facility

Donostia / San Sebastian, Guipuzcoa, 20009, Spain

Location

Unknown Facility

Madrid, Madrid, 28040, Spain

Location

Unknown Facility

Madrid, Madrid, 28046, Spain

Location

Unknown Facility

Torremolinos, Malaga, 29620, Spain

Location

Unknown Facility

El Palmar. Murcia, Murcia, 30120, Spain

Location

Unknown Facility

Gothenburg, 411 19, Sweden

Location

Unknown Facility

Belfast, BT12 6AB, United Kingdom

Location

Unknown Facility

Dundee, DD1 9SY, United Kingdom

Location

Unknown Facility

Edinburgh, EH10 5HF, United Kingdom

Location

Unknown Facility

Glasgow, GS 8SJ, United Kingdom

Location

Unknown Facility

London, W1W 7EJ, United Kingdom

Location

Unknown Facility

Manchester, M13 9WL, United Kingdom

Location

MeSH Terms

Conditions

Fragile X Syndrome

Interventions

2-chloro-4-(1-(4-fluorophenyl)-2,5-dimethyl-1H-imidazol-4-ylethynyl)pyridine

Condition Hierarchy (Ancestors)

X-Linked Intellectual DisabilityIntellectual DisabilityNeurobehavioral ManifestationsNeurologic ManifestationsNervous System DiseasesSex Chromosome DisordersChromosome DisordersCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesGenetic Diseases, InbornGenetic Diseases, X-LinkedHeredodegenerative Disorders, Nervous System

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 20, 2012

First Posted

January 25, 2012

Study Start

May 1, 2012

Primary Completion

April 1, 2014

Study Completion

April 1, 2014

Last Updated

July 11, 2016

Record last verified: 2016-07

Locations