NCT01454297

Brief Summary

The primary objective of this observational study is to identify the molecular profiles and clinical characteristics that define subsets of myeloma patients during the course of the disease.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,154

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Jul 2011

Longer than P75 for all trials

Geographic Reach
3 countries

73 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

October 7, 2011

Completed
12 days until next milestone

First Posted

Study publicly available on registry

October 19, 2011

Completed
12.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 30, 2023

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2023

Completed
Last Updated

January 3, 2024

Status Verified

January 1, 2024

Enrollment Period

12.4 years

First QC Date

October 7, 2011

Last Update Submit

January 2, 2024

Conditions

Keywords

MyelomaMultiple MyelomaObservationalLongitudinal

Outcome Measures

Primary Outcomes (1)

  • Molecular profiles and clinical characteristics that define subsets of myeloma patients at initial diagnosis and at relapse of disease.

    Standard clinical and laboratory assessments. Genomic tests (DNA and RNA sequencing, etc.) on bone marrow aspirates obtained at baseline, suspected complete response, and relapse/progression.

    Baseline to 8 years.

Secondary Outcomes (6)

  • Response rates

    Up to one year after baseline.

  • Survival rates

    Five to eight years after baseline

  • Bone disease assessed radiographically

    Baseline and during five to eight years of follow-up

  • Health-related quality of life

    Baseline and during five to eight years of follow-up

  • Resource utilization

    Baseline and during five to eight years of follow-up

  • +1 more secondary outcomes

Study Arms (1)

Newly diagnosed Multiple Myeloma

This is a prospective observational study in patients with symptomatic multiple myeloma who have not yet initiated therapy for their disease.

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Newly diagnosed, symptomatic, multiple myeloma, candidates for systemic treatment

You may qualify if:

  • Patient is at least 18 years old.
  • Patient has been diagnosed with symptomatic MM with measurable disease that includes at least one of the following:
  • Serum M protein ≥ 1g/dl Urine M protein ≥ 200 mg/24 hrs Involved free light chain level ≥ 10 mg/dl and an abnormal serum free light chain ratio (\<0.26 or \>1.65).
  • The patient is a candidate for systemic therapy that includes an IMiD® (e.g., lenalidomide, pomalidomide, thalidomide) and/or proteasome inhibitor (e.g., bortezomib, carfilzomib) as part of the initial regimen.
  • No more than 30 days from baseline bone marrow evaluation as per this protocol to initiation of first-line therapy.
  • Patient has read, understood and signed informed consent.

You may not qualify if:

  • Patient is already receiving systemic therapy for MM (a single dose of bisphosphonates and up to 100 mg total dose of dexamethasone or equivalent corticosteroids are permitted prior to registration on study).
  • Patient had another malignancy within the last 5 years (except for basal or squamous cell carcinoma, or in situ cancer of the cervix).
  • Patient is enrolled in a blinded clinical trial for the first-line treatment of multiple myeloma. Patients may be enrolled in subsequent clinical trials as long as continued access to data and tissue, as per this protocol, is not prohibited.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (73)

Mayo Clinic Campus in Scottsdale, AZ

Scottsdale, Arizona, 85259, United States

Location

UC San Diego Moores Cancer Center

San Diego, California, 92093, United States

Location

Sharp Health Care

San Diego, California, 92123, United States

Location

VA San Diego Healthcare System

San Diego, California, 92161, United States

Location

San Francisco VA Medical Center

San Francisco, California, 94121, United States

Location

UCSF Medical Center

San Francisco, California, 94143, United States

Location

Kaiser Permanente of Colorado

Denver, Colorado, 80205, United States

Location

Rocky Mountain Cancer Centers

Denver, Colorado, 80218, United States

Location

Carl and Dorothy Bennett Cancer Center

Stamford, Connecticut, 06907, United States

Location

VA Medical Center, Washington DC,

Washington D.C., District of Columbia, 20422, United States

Location

Ocala Oncology Center

Ocala, Florida, 34471, United States

Location

Winship Cancer Institute - Emory University

Atlanta, Georgia, 30322, United States

Location

Atlanta VA Medical Center

Decatur, Georgia, 30033, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Illinois Cancer Specialists

Niles, Illinois, 60714, United States

Location

Cancer Center of Kansas

Wichita, Kansas, 67214, United States

Location

Peninsula Regional Cancer Center

Salisbury, Maryland, 21801, United States

Location

Holy Cross Hospital

Silver Spring, Maryland, 20902, United States

Location

Barbara Ann Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Grand Rapids Clinical Oncology Program

Grand Rapids, Michigan, 49503, United States

Location

Mayo Clinic-Rochester

Rochester, Minnesota, 55905, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

Kansas City VA Medical Center

Kansas City, Missouri, 64128, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

Billings Clinic

Billings, Montana, 59101, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198, United States

Location

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03784, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Saint Barnabas Medical Center

Livingston, New Jersey, 07039, United States

Location

Broome Oncology

Johnson City, New York, 13790, United States

Location

New York University Medical Center

New York, New York, 10016, United States

Location

Mt Sinai Medical Center

New York, New York, 10029, United States

Location

Memorial Sloan Kettering Cancer Center

New York, New York, 10065, United States

Location

Weill Cornell Medical College-NY Presbyterian Hospital

New York, New York, 10065, United States

Location

St Francis Hospital

Roslyn, New York, 11576, United States

Location

Eastchester Center for Cancer Care

The Bronx, New York, 10469, United States

Location

Waverly Hematology Oncology

Cary, North Carolina, 27518, United States

Location

Levine Cancer Institute

Charlotte, North Carolina, 28204, United States

Location

Duke University Hospital

Durham, North Carolina, 27710, United States

Location

East Carolina University

Greenville, North Carolina, 27834, United States

Location

First Health Outpatient Cancer Center

Pinehurst, North Carolina, 28374, United States

Location

Ohio State University Wexner Medical Center

Columbus, Ohio, 43210, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Northwest Cancer Specialists, PC

Tualatin, Oregon, 97062, United States

Location

Sarah Cannon Research Institute

Nashville, Tennessee, 37203, United States

Location

Baylor Research Institute

Dallas, Texas, 75246, United States

Location

University of Texas Southwest Medical Center

Dallas, Texas, 75390, United States

Location

Cancer Care Centers of South Texas

San Antonio, Texas, 78217, United States

Location

Central Texas VA Healthcare Center

Temple, Texas, 76504, United States

Location

Texas Oncology - Tyler

Tyler, Texas, 75702, United States

Location

Texas Oncology- Waco

Waco, Texas, 76712, United States

Location

Virginia Cancer Specialists PV

Fairfax, Virginia, 22013, United States

Location

Cancer Care Northwest

Spokane, Washington, 99202, United States

Location

Yakima Valley Memorial Hospital/North Star Lodge

Yakima, Washington, 98902, United States

Location

Marshfield Clinic

Marshfield, Wisconsin, 54449, United States

Location

Tom Baker Cancer Centre, Alberta Health Services

Calgary, Alberta, T2N 2T9, Canada

Location

Cross Cancer Institute, Alberta Health Services

Edmonton, Alberta, T6G 1Z2, Canada

Location

Princess Margaret Cancer Centre

Toronto, Ontario, M5G 2M9, Canada

Location

McGill University Health Center, Royal Victoria Hospital

Montreal, Quebec, H3A1A1, Canada

Location

Hospital Clinica Universitari Lozano Blesa

Zaragoza, Aragon, 50012, Spain

Location

Hospital Univ Son Espases

Palma de Mallorca, Balearic Islands, 07120, Spain

Location

Hospital Son Llàtze

Palma de Mallorca, Balearic Islands, 07198, Spain

Location

Hospital University de Salamanca

Salamanca, Castille and León, 37007, Spain

Location

H. U. Germans Trias i Pujol

Badalona, Catalonia, 08916, Spain

Location

Hospital Quirón de Madrid

Pozuelo de Alarcón, Madrid, 28223, Spain

Location

University Hospital Infanta Sofia

San Sebastián de los Reyes, Madrid, 28702, Spain

Location

Clínica Universitaria de Navarra

Pamplona, Navarre, 31008, Spain

Location

Hospital Universitari de Canarias

Santa Cruz de Tenerife, Santa Cruz, 38320, Spain

Location

Hospital del Mar

Barcelona, 08003, Spain

Location

Hospital Santa Creu I Sant Pau

Barcelona, 08026, Spain

Location

Hospital Clinic i Provincial

Barcelona, 08036, Spain

Location

Hospital Ramón y Cajal

Madrid, 28034, Spain

Location

Hospital Puerta de Hierro

Madrid, 28222, Spain

Location

Related Publications (4)

  • Auclair D, Mansfield C, Fiala MA, Chari A, Cole CE, Kaufman JL, Orloff GJ, Siegel DS, Zonder JA, Mange B, Yesil J, Dalal M, Mikhael JR. Preferences and Priorities for Relapsed Multiple Myeloma Treatments Among Patients and Caregivers in the United States. Patient Prefer Adherence. 2022 Mar 1;16:573-585. doi: 10.2147/PPA.S345906. eCollection 2022.

  • Barwick BG, Gupta VA, Matulis SM, Patton JC, Powell DR, Gu Y, Jaye DL, Conneely KN, Lin YC, Hofmeister CC, Nooka AK, Keats JJ, Lonial S, Vertino PM, Boise LH. Chromatin Accessibility Identifies Regulatory Elements Predictive of Gene Expression and Disease Outcome in Multiple Myeloma. Clin Cancer Res. 2021 Jun 1;27(11):3178-3189. doi: 10.1158/1078-0432.CCR-20-2931. Epub 2021 Mar 17.

  • Foltz SM, Gao Q, Yoon CJ, Sun H, Yao L, Li Y, Jayasinghe RG, Cao S, King J, Kohnen DR, Fiala MA, Ding L, Vij R. Evolution and structure of clinically relevant gene fusions in multiple myeloma. Nat Commun. 2020 May 29;11(1):2666. doi: 10.1038/s41467-020-16434-y.

  • Miller A, Asmann Y, Cattaneo L, Braggio E, Keats J, Auclair D, Lonial S; MMRF CoMMpass Network; Russell SJ, Stewart AK. High somatic mutation and neoantigen burden are correlated with decreased progression-free survival in multiple myeloma. Blood Cancer J. 2017 Sep 22;7(9):e612. doi: 10.1038/bcj.2017.94.

Related Links

Biospecimen

Retention: SAMPLES WITH DNA

Bone marrow, Peripheral Blood

MeSH Terms

Conditions

Multiple MyelomaNeoplasms, Plasma Cell

Condition Hierarchy (Ancestors)

Neoplasms by Histologic TypeNeoplasmsHemostatic DisordersVascular DiseasesCardiovascular DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesHemorrhagic DisordersLymphoproliferative DisordersImmunoproliferative DisordersImmune System Diseases

Study Officials

  • Daniel Auclair

    Multiple Myeloma Research Foundation

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 7, 2011

First Posted

October 19, 2011

Study Start

July 1, 2011

Primary Completion

November 30, 2023

Study Completion

December 31, 2023

Last Updated

January 3, 2024

Record last verified: 2024-01

Data Sharing

IPD Sharing
Will share

Interim Analysis data will be released every 6 months

Locations