NCT01397578

Brief Summary

This is a Phase II, randomized, double-blind, parallel-group, placebo-controlled study to evaluate the effects of MABT5102A on brain amyloid burden (as assessed by amyloid PET imaging) and other biomarkers in patients with mild to moderate Alzheimer's disease.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
91

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Aug 2011

Geographic Reach
3 countries

29 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

July 18, 2011

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 19, 2011

Completed
1 month until next milestone

Study Start

First participant enrolled

August 31, 2011

Completed
2.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2014

Completed
Last Updated

July 12, 2017

Status Verified

July 1, 2017

Enrollment Period

2.7 years

First QC Date

July 18, 2011

Last Update Submit

July 10, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in brain amyloid load as assessed by amyloid PET imaging

    Baseline to Week 69

Secondary Outcomes (3)

  • Changes in cerebrospinal fluid (CSF) biomarkers relevant to Alzheimer's disease

    Baseline to Week 69

  • Change in brain metabolism as assessed by 18F-fluorodeoxyglucose positron emission tomography (FDG PET) imaging

    Baseline to Week 69

  • Change in Alzheimer's Disease Assessment Scale Cognitive Subscale (ADAS Cog) score

    Baseline to Week 73

Study Arms (4)

Part 1: Subcutaneous cohort exp

EXPERIMENTAL
Drug: MABT5102A

Part 2: Intravenous cohort exp

EXPERIMENTAL
Drug: MABT5102A

Part 1: Subcutaneous cohort

PLACEBO COMPARATOR

Repeating subcutaneous injection

Drug: placebo

Part 2: Intravenous cohort

PLACEBO COMPARATOR

Repeating intravenous injection

Drug: placebo

Interventions

Repeating subcutaneous injection

Part 1: Subcutaneous cohort exp

Repeating subcutaneous injection

Part 1: Subcutaneous cohort

Eligibility Criteria

Age50 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of probable AD according to the National Institute of Neurological and Communicative Disorders and Stroke and the Alzheimer's Disease and Related Disorder Association (NINCDS-ADRDA) criteria
  • Mini-Mental State Examination (MMSE) score of 18-26 points at screening
  • Geriatric Depression Scale (GDS-15) score of \< 6
  • For patients currently receiving treatment with approved AD treatments (AChE inhibitors or memantine): Treatment initiated and continued for at least the last 3 months prior to randomization, at a stable dose for at least the last 2 months prior to randomization

You may not qualify if:

  • Severe or unstable medical condition that, in the opinion of the investigator or Sponsor, would interfere with the patient's ability to complete the study assessments or would require the equivalent of institutional or hospital care
  • History or presence of clinically evident vascular disease potentially affecting the brain (e.g., stroke, clinically significant carotid or vertebral stenosis or plaque, aortic aneurysm, intracranial aneurysm, cerebral hemorrhage, arteriovenous malformation)
  • History of severe, clinically significant (persistent neurologic deficit or structural brain damage) central nervous system trauma (e.g., cerebral contusion)
  • Hospitalization within 4 weeks prior to screening
  • Previous treatment with MABT5102A or any other therapeutic that targets Abeta
  • Treatment with any biologic therapy within 5 half-lives or 3 months prior to screening, whichever is longer, with the exception of routinely recommended vaccinations, which are allowed

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (29)

Banner Alzheimer's Institute

Phoenix, Arizona, 85020, United States

Location

Banner Sun Health Research Insitute

Sun City, Arizona, 85351, United States

Location

NNS Clinical Research LLC

Tucson, Arizona, 85704, United States

Location

Margolin Brain Institute

Fresno, California, 93720, United States

Location

University of California Los Angeles (UCLA)

Los Angeles, California, 90095, United States

Location

Pacific Neuroscience Med Grp

Oxnard, California, 93030, United States

Location

Stanford Univ Medical Center

Palo Alto, California, 94304, United States

Location

Redwood Regional Medical Group

Santa Rosa, California, 95403, United States

Location

Internal Med Assoc of Lee Cty

Fort Myers, Florida, 33912, United States

Location

Neuropsychiatric Research; Center of Southwest Florida

Fort Myers, Florida, 33912, United States

Location

MD Clinical

Hallandale, Florida, 33009, United States

Location

Compass Research

Orlando, Florida, 32806, United States

Location

Dekalb Neurology Associates

Decatur, Georgia, 30033, United States

Location

Alexian Brothers Neurosci Inst

Elk Grove Village, Illinois, 60007, United States

Location

Hattiesburg Clinic

Hattiesburg, Mississippi, 39401, United States

Location

Cleveland Clinic Lou Ruvo; Center for Brain Research

Las Vegas, Nevada, 89106, United States

Location

Memory Enhancement Center of America, Inc.

Eatontown, New Jersey, 07724, United States

Location

Litwin Zucker Research Ctr.; Feinstein Inst. Med. Rsch.

Manhasset, New York, 11030, United States

Location

Neurology & Neuroscience Ctr of Ohio

Toledo, Ohio, 43623, United States

Location

The Clinical Trial Center, LLC

Jenkintown, Pennsylvania, 19046, United States

Location

Rhode Island Mood & Memory Research Institute

East Providence, Rhode Island, 02914, United States

Location

Butler Hospital

Providence, Rhode Island, 02906, United States

Location

Hopital Central-CHU de Nancy; Pharmacie

Nancy, 54035, France

Location

Hôpital Casselardit; Cons memoire

Toulouse, 31059, France

Location

Clinique Psychiatrique Univ

Tours, 37044, France

Location

Fundació ACE

BArcelon, Barcelona, 08034, Spain

Location

Hospital Universitario de Bellvitge

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

Location

Hospital del Mar

Barcelona, 08003, Spain

Location

Hospital Mutua De Terrasa

Barcelona, 08221, Spain

Location

Related Publications (3)

  • Polhamus DG, Dolton MJ, Rogers JA, Honigberg L, Jin JY, Quartino A. Longitudinal Exposure-Response Modeling of Multiple Indicators of Alzheimer's Disease Progression. J Prev Alzheimers Dis. 2023;10(2):212-222. doi: 10.14283/jpad.2023.13.

  • Yoshida K, Moein A, Bittner T, Ostrowitzki S, Lin H, Honigberg L, Jin JY, Quartino A. Pharmacokinetics and pharmacodynamic effect of crenezumab on plasma and cerebrospinal fluid beta-amyloid in patients with mild-to-moderate Alzheimer's disease. Alzheimers Res Ther. 2020 Jan 22;12(1):16. doi: 10.1186/s13195-020-0580-2.

  • Salloway S, Honigberg LA, Cho W, Ward M, Friesenhahn M, Brunstein F, Quartino A, Clayton D, Mortensen D, Bittner T, Ho C, Rabe C, Schauer SP, Wildsmith KR, Fuji RN, Suliman S, Reiman EM, Chen K, Paul R. Amyloid positron emission tomography and cerebrospinal fluid results from a crenezumab anti-amyloid-beta antibody double-blind, placebo-controlled, randomized phase II study in mild-to-moderate Alzheimer's disease (BLAZE). Alzheimers Res Ther. 2018 Sep 19;10(1):96. doi: 10.1186/s13195-018-0424-5.

MeSH Terms

Conditions

Alzheimer Disease

Interventions

crenezumab

Condition Hierarchy (Ancestors)

DementiaBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Study Officials

  • Robert Paul, M.D., Ph.D.

    Genentech, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 18, 2011

First Posted

July 19, 2011

Study Start

August 31, 2011

Primary Completion

April 30, 2014

Study Completion

April 30, 2014

Last Updated

July 12, 2017

Record last verified: 2017-07

Locations