NCT01396421

Brief Summary

The purpose of this study is to compare the effectiveness, safety and tolerability of three different doses of OPC-34712 with placebo in the treatment of acute schizophrenia in adults.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
636

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jul 2011

Typical duration for phase_3

Geographic Reach
9 countries

60 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
10 days until next milestone

First Submitted

Initial submission to the registry

July 11, 2011

Completed
7 days until next milestone

First Posted

Study publicly available on registry

July 18, 2011

Completed
2.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2014

Completed
1.8 years until next milestone

Results Posted

Study results publicly available

October 29, 2015

Completed
Last Updated

October 29, 2015

Status Verified

September 1, 2015

Enrollment Period

2.5 years

First QC Date

July 11, 2011

Results QC Date

August 4, 2015

Last Update Submit

September 29, 2015

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline to Week 6 Positive and Negative Syndrome Scale (PANSS) Total Score.

    The PANSS consists of 3 subscales (positive subscale, negative subscale and general psychology subscale) containing a total of 30 symptom constructs and was administered using the Structured Clinical Interview (SCI)-PANSS. For each symptom construct, severity was rated on a 7-point scale, with a score of 1 indicating the absence of symptoms and a score of 7 indicating extremely severe symptoms. The PANSS total score ranged from 30 (best possible outcome) to 210 (worst possible outcome).

    Baseline to Week 6

Secondary Outcomes (15)

  • Mean Change From Baseline to Week 6 in Clinical Global Impression - Severity of Illness Scale (CGI-S) Score.

    Baseline to Week 6

  • Mean Change From Baseline to Week 1, 2, 3, 4 and 5 Positive and Negative Syndrome Scale (PANSS) Total Score.

    Baseline to Week 1, 2, 3, 4, 5

  • Mean Change From Baseline to Week 1, 2, 3, 4 and 5 in Clinical Global Impression - Severity of Illness Scale (CGI-S) Score.

    Baseline to Week 1, 2, 3, 4 and 5

  • Mean Change From Baseline to Week 6 in Personal and Social Performance Scale (PSP)

    Baseline to Week 6

  • Mean Change From Baseline to Week 6 in PANSS Positive Subscale Score

    Baseline to Week 6

  • +10 more secondary outcomes

Study Arms (4)

OPC-34712 [Brexpiprazole] High Dose

EXPERIMENTAL

Higher Dose, tablet, once daily, for six weeks

Drug: OPC-34712 [Brexpiprazole] High Dose

OPC-34712 [Brexpiprazole] Middle Dose

EXPERIMENTAL

Middle Dose, tablet, once daily, for six weeks

Drug: Experimental: OPC-34712 [Brexpiprazole] Middle Dose

OPC-34712 [Brexpiprazole] Low Dose

EXPERIMENTAL

Lower Dose, tablet, once daily, for six weeks

Drug: Experimental: OPC-34712 [Brexpiprazole] Low Dose

Placebo

PLACEBO COMPARATOR

Placebo, once daily, for six weeks

Drug: Placebo

Interventions

Higher dose, tablet, once daily, for six weeks

OPC-34712 [Brexpiprazole] High Dose

Middle dose, tablet, once daily, for six weeks

OPC-34712 [Brexpiprazole] Middle Dose

Lower dose, tablet, once daily, for six weeks

OPC-34712 [Brexpiprazole] Low Dose

Placebo, once daily, for six weeks

Placebo

Eligibility Criteria

Age18 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female subjects between 18 and 65 years of age, with a diagnosis of schizophrenia, as defined by the Diagnostic and Statistical Manual of Mental Disorders (DSM-IV-TR) criteria
  • Subjects who have been recently hospitalized or who would benefit from hospitalization for an acute relapse of schizophrenia
  • Subjects experiencing an acute exacerbation of psychotic symptoms

You may not qualify if:

  • Females who are breast-feeding and/or who have a positive pregnancy test result prior to receiving study drug
  • Subjects with a current DSM-IV-TR Axis I diagnosis of:
  • Schizoaffective disorder
  • Major depressive disorder (MDD)
  • Bipolar disorder
  • Delirium, dementia, amnestic or other cognitive disorder
  • Borderline, paranoid, histrionic, schizotypal, schizoid or antisocial personality disorder
  • Subjects presenting with a first episode of schizophrenia

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (60)

Unknown Facility

Little Rock, Arkansas, 72205, United States

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Unknown Facility

Garden Grove, California, 92845, United States

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Unknown Facility

Glendale, California, 91206, United States

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Oakland, California, 94612, United States

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Unknown Facility

Oceanside, California, 92056, United States

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Unknown Facility

San Diego, California, 92102, United States

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Unknown Facility

San Diego, California, 92123, United States

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Unknown Facility

Bradenton, Florida, 34208, United States

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Unknown Facility

Miami Springs, Florida, 33166, United States

Location

Unknown Facility

Orlando, Florida, 32806, United States

Location

Unknown Facility

Fresh Meadows, New York, 11423, United States

Location

Unknown Facility

Jamaica, New York, 11432, United States

Location

Unknown Facility

Dayton, Ohio, 45417, United States

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Unknown Facility

Charleston, South Carolina, 29405, United States

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Charleston, South Carolina, 29407, United States

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Austin, Texas, 78754, United States

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Unknown Facility

Kirkland, Washington, 98033, United States

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Burlington, Ontario, L7R 4E2, Canada

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Chatham, Ontario, N7L 1B7, Canada

Location

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Chatham, Ontario, N7M 5L9, Canada

Location

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Fujisawa-shi, Kanagawa, 251-8530, Japan

Location

Unknown Facility

Kunigami-gun, Okinawa, 904-1201, Japan

Location

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Sakai-shi, Osaka, 590-0018, Japan

Location

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Setagaya-ku, Tokyo-To, 156-0057, Japan

Location

Unknown Facility

Kumamoto, 861-8002, Japan

Location

Unknown Facility

Daugavpils, LV-5417, Latvia

Location

Unknown Facility

Jelgava, LV-3008, Latvia

Location

Unknown Facility

Liepāja, LV-3401, Latvia

Location

Unknown Facility

Riga, LV-1005, Latvia

Location

Unknown Facility

Strenči, LV-4730, Latvia

Location

Unknown Facility

Choroszcz, 16-070, Poland

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Gdansk, 80-282, Poland

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Gdansk, 80-952, Poland

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Lodz, 91-229, Poland

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Arad, 310022, Romania

Location

Unknown Facility

Bucharest, 010825, Romania

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Unknown Facility

Bucharest, 030442, Romania

Location

Unknown Facility

Bucharest, 041914, Romania

Location

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Cluj-Napoca, 400012, Romania

Location

Unknown Facility

Focşani, 620165, Romania

Location

Unknown Facility

Piteşti, 110069, Romania

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Unknown Facility

Târgovişte, 130086, Romania

Location

Unknown Facility

Belgrade, 11000, Serbia

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Unknown Facility

Kragujevac, 34000, Serbia

Location

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Novi Sad, 21000, Serbia

Location

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Incheon, 400-711, South Korea

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Unknown Facility

Incheon, 405-760, South Korea

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Seoul, 136-705, South Korea

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Unknown Facility

Seoul, 137-710, South Korea

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Unknown Facility

Seoul, 143-711, South Korea

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Unknown Facility

Chernihiv, 14000, Ukraine

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Unknown Facility

Dnipropetrovsk, 49005, Ukraine

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Unknown Facility

Dnipropetrovsk, 49115, Ukraine

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Unknown Facility

Hlevakha, 08631, Ukraine

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Unknown Facility

Kherson, Vil. Stepanivka, 73488, Ukraine

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Unknown Facility

Kyiv, 02660, Ukraine

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Unknown Facility

Kyiv, 04080, Ukraine

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Unknown Facility

Lviv, 79021, Ukraine

Location

Unknown Facility

Simferopol, 95006, Ukraine

Location

Unknown Facility

Vinnytsia, 21005, Ukraine

Location

Related Publications (7)

  • Ismail Z, Kapadia S, Palma AM, Yildirim M, Farovik A. Brexpiprazole for anxiety symptoms in schizophrenia: a pooled analysis of short- and long-term trials. Curr Med Res Opin. 2025 Aug;41(8):1535-1548. doi: 10.1080/03007995.2025.2552286. Epub 2025 Sep 11.

  • Ismail Z, Meehan SR, Farovik A, Kapadia S, Palma AM, Zhang Z, McIntyre RS. Effects of brexpiprazole on patient life engagement in schizophrenia: post hoc analysis of Positive and Negative Syndrome Scale data. Curr Med Res Opin. 2025 Jan;41(1):145-153. doi: 10.1080/03007995.2024.2440059. Epub 2025 Jan 3.

  • Correll CU, He Y, Therrien F, MacKenzie E, Meehan SR, Weiss C, Hefting N, Hobart M. Effects of Brexpiprazole on Functioning in Patients With Schizophrenia: Post Hoc Analysis of Short- and Long-Term Studies. J Clin Psychiatry. 2022 Mar 1;83(2):20m13793. doi: 10.4088/JCP.20m13793.

  • Marder SR, Meehan SR, Weiss C, Chen D, Hobart M, Hefting N. Effects of Brexpiprazole Across Symptom Domains in Patients With Schizophrenia: Post Hoc Analysis of Short- and Long-Term Studies. Schizophr Bull Open. 2021 May 1;2(1):sgab014. doi: 10.1093/schizbullopen/sgab014. eCollection 2021 Jan.

  • Newcomer JW, Eriksson H, Zhang P, Weiller E, Weiss C. Changes in metabolic parameters and body weight in brexpiprazole-treated patients with acute schizophrenia: pooled analyses of phase 3 clinical studies. Curr Med Res Opin. 2018 Dec;34(12):2197-2205. doi: 10.1080/03007995.2018.1498779. Epub 2018 Jul 27.

  • Kane JM, Skuban A, Hobart M, Ouyang J, Weiller E, Weiss C, Correll CU. Overview of short- and long-term tolerability and safety of brexpiprazole in patients with schizophrenia. Schizophr Res. 2016 Jul;174(1-3):93-98. doi: 10.1016/j.schres.2016.04.013. Epub 2016 May 14.

  • Correll CU, Skuban A, Ouyang J, Hobart M, Pfister S, McQuade RD, Nyilas M, Carson WH, Sanchez R, Eriksson H. Efficacy and Safety of Brexpiprazole for the Treatment of Acute Schizophrenia: A 6-Week Randomized, Double-Blind, Placebo-Controlled Trial. Am J Psychiatry. 2015 Sep 1;172(9):870-80. doi: 10.1176/appi.ajp.2015.14101275. Epub 2015 Apr 16.

MeSH Terms

Interventions

brexpiprazole

Results Point of Contact

Title
Global Medical Affairs
Organization
Otsuka Pharmaceutical Development & Commercialization, Inc

Study Officials

  • Aleksandar Skuban, M.D.

    Otsuka Pharmaceutical Development & Commercialization, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 11, 2011

First Posted

July 18, 2011

Study Start

July 1, 2011

Primary Completion

January 1, 2014

Study Completion

January 1, 2014

Last Updated

October 29, 2015

Results First Posted

October 29, 2015

Record last verified: 2015-09

Locations