NCT01393496

Brief Summary

To compare the effect of restrictive versus liberal red blood cell transfusion thresholds on long-term neurodevelopmental outcome in extremely low birth weight infants.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,013

participants targeted

Target at P75+ for phase_4

Timeline
Completed

Started Jul 2011

Longer than P75 for phase_4

Geographic Reach
2 countries

32 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
11 days until next milestone

First Submitted

Initial submission to the registry

July 12, 2011

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 13, 2011

Completed
5.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2017

Completed
1.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 31, 2018

Completed
Last Updated

September 16, 2021

Status Verified

September 1, 2021

Enrollment Period

5.8 years

First QC Date

July 12, 2011

Last Update Submit

September 9, 2021

Conditions

Keywords

prematurityanemiatransfusion

Outcome Measures

Primary Outcomes (1)

  • Incidence of death or major neurodevelopmental impairment

    The primary outcome measure of this study will be the incidence of death or major neurodevelopmental impairment determined at 24 months of age corrected for prematurity (where major neurodevelopmental impairment is defined as any of the following: cognitive delay defined as mental developmental index (MDI) score of the Bayley Scales of Infant Development (2nd edition) \< 85, cerebral palsy, or severe visual or hearing impairment

    24 months of age corrected for prematurity

Study Arms (2)

"liberal" transfusion triggers

EXPERIMENTAL

"liberal" guidelines for red blood cell transfusions

Other: red blood cell transfusion

"restrictive" transfusion triggers

ACTIVE COMPARATOR

"restrictive" guidelines for red blood cell transfusions

Other: red blood cell transfusion

Interventions

Implementation of "liberal" guidelines for red blood cell transfusions in extremely low birth weight infants

"liberal" transfusion triggers

Eligibility Criteria

Age0 Days - 3 Days
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Infants with a birth weight of 400 - 999g

You may not qualify if:

  • Missing written parental consent.
  • Gestational age \> 29 + 6/7 weeks
  • Major congenital anomalies (including chromosomal aberrations, cyanotic congenital heart defects, syndromes likely affecting long-term outcome, and major congenital malformations requiring surgical correction during newborn period).
  • Infants who died before 48 hours, infants in whom the clinical decision to withhold intensive care was made, infants who were not considered viable
  • Participation in another study with ongoing use of an unlicensed investigational product from 28 days before study enrollment until the end of the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (32)

Neonatalklinikken

Copenhagen, 2100, Denmark

Location

University Hospital of Aachen

Aachen, 52074, Germany

Location

Children's Hospital

Augsburg, 86156, Germany

Location

Vivantes Children's Hospital

Berlin, 12351, Germany

Location

Charité University Children's Hospital

Berlin, 13353, Germany

Location

University Children's Hospital

Bochum, 44791, Germany

Location

Children's Hospital

Cologne, 50375, Germany

Location

University Children's Hospital

Cologne, 50924, Germany

Location

Children's Hospital

Datteln, 45711, Germany

Location

University Children's Hospital

Dresden, 01307, Germany

Location

University of Duesseldorf

Düsseldorf, 40225, Germany

Location

Helios Children's Hospital

Erfurt, 99089, Germany

Location

Children's Hospital

Erlangen, 91054, Germany

Location

University Children's Hospital

Essen, 45122, Germany

Location

University Children's Hospital

Frankfurt, 60590, Germany

Location

University Children's Hospital

Giessen, 35385, Germany

Location

University of Greifswald

Greifswald, 17475, Germany

Location

Children's Hospital Eppendorf

Hamburg, 20246, Germany

Location

Children's Hospital Altona

Hamburg, 22763, Germany

Location

Children's Hospital

Hanover, 30625, Germany

Location

University Hospital of Leipzig

Leipzig, 04103, Germany

Location

University of Luebeck

Lübeck, 23538, Germany

Location

University Children's Hospital

Magdeburg, 39120, Germany

Location

University Hospital of Marburg

Marburg, 35033, Germany

Location

University Children's Hospital

Munich, 80337, Germany

Location

University Children's Hospital

Münster, 48149, Germany

Location

Children's Hospital

Nuremberg, 90471, Germany

Location

Children's Hospital St. Hedwig

Regensburg, 93049, Germany

Location

DRK Kinderklinik

Siegen, 57072, Germany

Location

Children's Hospital

Stuttgart, 70176, Germany

Location

University Hospital of Tuebingen

Tübingen, 72076, Germany

Location

University Children's Hospital

Ulm, 89075, Germany

Location

Related Publications (6)

  • ETTNO Investigators. The 'Effects of Transfusion Thresholds on Neurocognitive Outcome of Extremely Low Birth-Weight Infants (ETTNO)' Study: Background, Aims, and Study Protocol. Neonatology. 2012 Jun;101(4):301-305. doi: 10.1159/000335030. Epub 2012 Jan 27.

    PMID: 22298226BACKGROUND
  • Franz AR, Engel C, Bassler D, Rudiger M, Thome UH, Maier RF, Krageloh-Mann I, Kron M, Essers J, Buhrer C, Rellensmann G, Rossi R, Bittrich HJ, Roll C, Hohn T, Ehrhardt H, Avenarius S, Korner HT, Stein A, Buxmann H, Vochem M, Poets CF; ETTNO Investigators. Effects of Liberal vs Restrictive Transfusion Thresholds on Survival and Neurocognitive Outcomes in Extremely Low-Birth-Weight Infants: The ETTNO Randomized Clinical Trial. JAMA. 2020 Aug 11;324(6):560-570. doi: 10.1001/jama.2020.10690.

  • Carson JL, Stanworth SJ, Dennis JA, Fergusson DA, Pagano MB, Roubinian NH, Turgeon AF, Valentine S, Trivella M, Doree C, Hebert PC. Transfusion thresholds and other strategies for guiding red blood cell transfusion. Cochrane Database Syst Rev. 2025 Oct 20;10(10):CD002042. doi: 10.1002/14651858.CD002042.pub6.

  • Franz AR, Engel C, Bassler D, Rudiger M, Thome UH, Maier RF, Krageloh-Mann I, Essers J, Buhrer C, Bittrich HJ, Roll C, Hohn T, Ehrhardt H, Boettger R, Korner HT, Stein A, Neuberger P, Henriksen TB, Greisen G, Poets CF; ETTNO Investigators. Effects of liberal versus restrictive transfusion strategies on intermittent hypoxaemia in extremely low birthweight infants: secondary analyses of the ETTNO randomised controlled trial. Arch Dis Child Fetal Neonatal Ed. 2025 Oct 17;110(6):564-570. doi: 10.1136/archdischild-2024-327643.

  • Radford M, Estcourt LJ, Sirotich E, Pitre T, Britto J, Watson M, Brunskill SJ, Fergusson DA, Doree C, Arnold DM. Restrictive versus liberal red blood cell transfusion strategies for people with haematological malignancies treated with intensive chemotherapy or radiotherapy, or both, with or without haematopoietic stem cell support. Cochrane Database Syst Rev. 2024 May 23;5(5):CD011305. doi: 10.1002/14651858.CD011305.pub3.

  • Carson JL, Stanworth SJ, Dennis JA, Trivella M, Roubinian N, Fergusson DA, Triulzi D, Doree C, Hebert PC. Transfusion thresholds for guiding red blood cell transfusion. Cochrane Database Syst Rev. 2021 Dec 21;12(12):CD002042. doi: 10.1002/14651858.CD002042.pub5.

MeSH Terms

Conditions

AnemiaPremature Birth

Interventions

Erythrocyte Transfusion

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic DiseasesObstetric Labor, PrematureObstetric Labor ComplicationsPregnancy ComplicationsFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital Diseases

Intervention Hierarchy (Ancestors)

Blood Component TransfusionBlood TransfusionBiological TherapyTherapeutics

Study Officials

  • Axel R Franz, MD

    University Hospital of Tuebingen

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Coordinating Investigator

Study Record Dates

First Submitted

July 12, 2011

First Posted

July 13, 2011

Study Start

July 1, 2011

Primary Completion

April 30, 2017

Study Completion

October 31, 2018

Last Updated

September 16, 2021

Record last verified: 2021-09

Locations