NCT01381094

Brief Summary

The purpose of this study is to evaluate the dose response (efficacy), pharmacodynamic response, pharmacokinetics, safety, and tolerability of orally administered AKB-6548 in pre-dialysis participants with anemia with repeat dosing for 42 days.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
93

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jun 2011

Shorter than P25 for phase_2

Geographic Reach
1 country

28 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 15, 2011

Completed
8 days until next milestone

First Submitted

Initial submission to the registry

June 23, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

June 27, 2011

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 16, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 16, 2012

Completed
10.4 years until next milestone

Results Posted

Study results publicly available

July 1, 2022

Completed
Last Updated

July 1, 2022

Status Verified

June 1, 2022

Enrollment Period

8 months

First QC Date

June 23, 2011

Results QC Date

April 22, 2022

Last Update Submit

June 7, 2022

Conditions

Keywords

anemiachronic kidney diseaseCKDchronic renal insufficiencyrenal impairmenterythropoietinsafetyefficacytolerabilitypharmacokinetics

Outcome Measures

Primary Outcomes (1)

  • Absolute Change From Baseline in Hemoglobin (Hgb) to End of Treatment (Week 6)

    Absolute change from Baseline was calculated as the Week 6 (end of treatment) value minus the Baseline value. Baseline Hgb was defined as the average of the last two measurements obtained prior to dosing. If there was only one measurement prior to dosing, this measurement served as Baseline. A positive change from Baseline indicated that hemoglobin concentration increased.

    Baseline, Week 6

Secondary Outcomes (28)

  • Change From Baseline in Hgb at Week 1, Week 2, Week 4, Week 6, and Follow-up Visit (up to Week 8)

    Baseline, Week 1, Week 2, Week 4, Week 6, Follow-up Visit (up to Week 8)

  • Change From Baseline in Hematocrit (HCT) at Week 1, Week 2, Week 4, Week 6, and Follow-up Visit (up to Week 8)

    Baseline, Week 1, Week 2, Week 4, Week 6, Follow-up Visit (up to Week 8)

  • Change From Baseline in Red Blood Cell (RBC) Count at Week 1, Week 2, Week 4, Week 6, and Follow-up Visit (up to Week 8)

    Baseline, Week 1, Week 2, Week 4, Week 6, Follow-up Visit (up to Week 8)

  • Change From Baseline in Absolute Reticulocyte Count at Week 1, Week 2, Week 4, Week 6, and Follow-up Visit (up to Week 8)

    Baseline, Week 1, Week 2, Week 4, Week 6, Follow-up Visit (up to Week 8)

  • Change From Baseline in Reticulocyte Hgb Content at Week 6

    Baseline, Week 6

  • +23 more secondary outcomes

Study Arms (5)

AKB-6548 240 mg

EXPERIMENTAL
Drug: AKB-6548

AKB-6548 370 mg

EXPERIMENTAL
Drug: AKB-6548

AKB-6548 500 mg

EXPERIMENTAL
Drug: AKB-6548

AKB-6548 630 mg

EXPERIMENTAL
Drug: AKB-6548

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

oral dose administered once daily for 42 days

AKB-6548 240 mgAKB-6548 370 mgAKB-6548 500 mgAKB-6548 630 mg

oral Placebo administered once daily for 42 days

Placebo

Eligibility Criteria

Age18 Years - 79 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • to 79 years of age, inclusive
  • Chronic Kidney Disease (eGFR \<60 mL/min), not yet on dialysis
  • Hemoglobin (Hgb) ≤ 10.5 g/dL
  • Transferring saturation ≥ 20%
  • Ferritin ≥ 50 ng/mL

You may not qualify if:

  • Body mass index \>42
  • Red blood cell transfusion within 12 weeks
  • Androgen therapy within the previous 21 days prior to study dosing
  • Therapy with any approved or experimental erythropoiesis stimulating agent (ESA) within the 11 weeks prior to the Screening visit
  • Participants meeting the criteria of ESA resistance within the previous 4 months
  • Individual doses of intravenous iron of greater than 250 mg within the past 21 days
  • Aspartate aminotransferase or alanine aminotransferase \>1.8x upper limit of normal (ULN)
  • Alkaline phosphatase \>2x ULN
  • Total bilirubin \>1.5x ULN
  • Uncontrolled hypertension
  • New York Heart Association Class III or IV congestive heart failure
  • Myocardial infarction, acute coronary syndrome, or stroke within 6 months prior to dosing

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (28)

Unknown Facility

Pine Bluff, Arkansas, United States

Location

Unknown Facility

Covina, California, United States

Location

Unknown Facility

Los Angeles, California, United States

Location

Unknown Facility

Lynwood, California, United States

Location

Unknown Facility

Riverside, California, United States

Location

Unknown Facility

San Dimas, California, United States

Location

Unknown Facility

Whittier, California, United States

Location

Unknown Facility

Coral Springs, Florida, United States

Location

Unknown Facility

Lauderdale Lakes, Florida, United States

Location

Unknown Facility

Miami, Florida, United States

Location

Unknown Facility

Ocala, Florida, United States

Location

Unknown Facility

Augusta, Georgia, United States

Location

Unknown Facility

Macon, Georgia, United States

Location

Unknown Facility

Wichita, Kansas, United States

Location

Unknown Facility

Shreveport, Louisiana, United States

Location

Unknown Facility

Springfield, Massachusetts, United States

Location

Unknown Facility

Detroit, Michigan, United States

Location

Unknown Facility

Pontiac, Michigan, United States

Location

Unknown Facility

Warren, Michigan, United States

Location

Unknown Facility

Bethpage, New York, United States

Location

Unknown Facility

Mineola, New York, United States

Location

Unknown Facility

Wilmington, North Carolina, United States

Location

Unknown Facility

Oklahoma City, Oklahoma, United States

Location

Unknown Facility

Knoxville, Tennessee, United States

Location

Unknown Facility

Austin, Texas, United States

Location

Unknown Facility

Fort Worth, Texas, United States

Location

Unknown Facility

Houston, Texas, United States

Location

Unknown Facility

San Antonio, Texas, United States

Location

Related Publications (2)

  • Natale P, Palmer SC, Jaure A, Hodson EM, Ruospo M, Cooper TE, Hahn D, Saglimbene VM, Craig JC, Strippoli GF. Hypoxia-inducible factor stabilisers for the anaemia of chronic kidney disease. Cochrane Database Syst Rev. 2022 Aug 25;8(8):CD013751. doi: 10.1002/14651858.CD013751.pub2.

  • Martin ER, Smith MT, Maroni BJ, Zuraw QC, deGoma EM. Clinical Trial of Vadadustat in Patients with Anemia Secondary to Stage 3 or 4 Chronic Kidney Disease. Am J Nephrol. 2017;45(5):380-388. doi: 10.1159/000464476. Epub 2017 Mar 25.

MeSH Terms

Conditions

AnemiaKidney DiseasesRenal Insufficiency, ChronicRenal Insufficiency

Interventions

vadadustat

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Akebia Therapeutics, Inc.
Organization
Akebia Therapeutics, Inc.

Study Officials

  • Chief Medical Officer

    Akebia Therapeutics Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 23, 2011

First Posted

June 27, 2011

Study Start

June 15, 2011

Primary Completion

February 16, 2012

Study Completion

February 16, 2012

Last Updated

July 1, 2022

Results First Posted

July 1, 2022

Record last verified: 2022-06

Data Sharing

IPD Sharing
Will not share

Locations