NCT01362179

Brief Summary

This is an observational study of unstimulated bone marrow (BM) and filgrastim-mobilized peripheral blood stem cell (PBSC) donors. The primary goal is to evaluate the hypothesis that the incidence of targeted malignant, thrombotic and autoimmune disorders after unrelated hematopoietic stem cell donation are similar between unstimulated BM and filgrastim-mobilized PBSC donors.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
21,974

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Oct 2010

Longer than P75 for all trials

Geographic Reach
2 countries

29 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2010

Completed
8 months until next milestone

First Submitted

Initial submission to the registry

May 26, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

May 30, 2011

Completed
9.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 30, 2020

Completed
15 days until next milestone

Study Completion

Last participant's last visit for all outcomes

October 15, 2020

Completed
Last Updated

October 20, 2020

Status Verified

March 1, 2020

Enrollment Period

10 years

First QC Date

May 26, 2011

Last Update Submit

October 19, 2020

Conditions

Keywords

malignant myeloid hematologic disordersfilgrastimlong term incidencedonors who received and in those who did not receive filgrastim.

Outcome Measures

Primary Outcomes (1)

  • Incidence of malignant myeloid hematologic disorders

    To describe the long-term incidence of malignant myeloid hematologic disorders in donors who received and in those who did not receive filgrastim.

    Post HSCT donation

Study Arms (2)

unstimulated BM donors

Observational (non-interventional) study.

filgrastim-mobilized PBSC donors

Observational (non-interventional) study.

Eligibility Criteria

Age18 Years - 60 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64)
Sampling MethodNon-Probability Sample
Study Population

10,000 unstimulated BM donors and 20,000 filgrastim-mobilized PBSC donors

You may qualify if:

  • Unrelated donor who donated either unstimulated BM or filgrastim-mobilized PBSC between July 1, 1999 and approximately five years post study activation.
  • Unrelated donor who received at least one injection of filgrastim or more, but did not donate filgrastim-mobilized PBSC between July 1, 1999 and approximately five years post study activation.
  • Donation was managed by a U.S. NMDP donor center.
  • Signed informed consent for participation in this long-term donor follow-up study. Concurrent enrollment on other studies is permitted.

You may not qualify if:

  • Unrelated donor who donated filgrastim-mobilized bone marrow.
  • Donation was managed by a non-U.S. donor center.
  • Donor is unable to verbally communicate in any of the following languages: English, Spanish, Mandarin Chinese, Cantonese Chinese, Vietnamese, Korean, or Portuguese.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (29)

City of Hope

Duarte, California, 91010-3012, United States

Location

National Marrow Donor Program Northern California & Northwest District

Oakland, California, 94612, United States

Location

National Marrow Donor Program Southern California & Southwest District

Santa Ana, California, 92705, United States

Location

Colorado Marrow Donor Program

Denver, Colorado, 80230-6918, United States

Location

OneBlood

Fort Lauderdale, Florida, 33309, United States

Location

Hawaii Bone Marrow Donor Registry

Honolulu, Hawaii, 96817-1651, United States

Location

LifeSource

Glenview, Illinois, 60025-2498, United States

Location

Rock River Valley Blood Center

Rockford, Illinois, 61107, United States

Location

Indiana Blood Center

Indianapolis, Indiana, 46208-4437, United States

Location

National Marrow Donor Program Southcentral District, Heart of America

Leawood, Kansas, 66206, United States

Location

Dana-Farber Cancer Institute

Boston, Massachusetts, 02115-6013, United States

Location

Michigan Blood

Grand Rapids, Michigan, 49503, United States

Location

The HLA Registry

Oradell, New Jersey, 07649, United States

Location

New York Blood Center

Brooklyn, New York, 11201, United States

Location

DKMS Americas

New York, New York, 10016, United States

Location

National Marrow Donor Program Southeast District

Charlotte, North Carolina, 28269, United States

Location

National Marrow Donor Program Northcentral District

Cleveland, Ohio, 44131, United States

Location

Oklahoma Blood Institute

Oklahoma City, Oklahoma, 73104-3251, United States

Location

National Marrow Donor Program Northeast District

Philadelphia, Pennsylvania, 19123-3594, United States

Location

Rhode Island Blood Center

Providence, Rhode Island, 02908-4811, United States

Location

Blood Assurance, Inc.

Chattanooga, Tennessee, 37403-1207, United States

Location

Cooperative Appalachian Marrow Program Medic Regional Blood Center

Knoxville, Tennessee, 37601, United States

Location

Baylor Research Institute

Dallas, Texas, 75246-2029, United States

Location

Cook Children's

El Paso, Texas, 79913, United States

Location

Gulf Coast Regional Blood Center

Houston, Texas, 77054-1802, United States

Location

South Texas Blood and Tissue Center

San Antonio, Texas, 78201-2023, United States

Location

Scott & White Clinic

Temple, Texas, 76508-0001, United States

Location

Community Blood Center, Inc.

Appleton, Wisconsin, 54914-9106, United States

Location

National Marrow Donor Program at Puerto Rico

Guaynabo, PR, 00968-2710, Puerto Rico

Location

MeSH Terms

Conditions

Hematologic Neoplasms

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Study Officials

  • John P Miller, MD, PhD

    National Marrow Donor Program

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
OTHER
Sponsor Type
NETWORK
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 26, 2011

First Posted

May 30, 2011

Study Start

October 1, 2010

Primary Completion

September 30, 2020

Study Completion

October 15, 2020

Last Updated

October 20, 2020

Record last verified: 2020-03

Locations