NCT01342211

Brief Summary

This study will investigate the effect of PF-04950615, a new investigational lipid lowering agent, on LDL-C and other lipids.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
93

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jul 2011

Shorter than P25 for phase_2

Geographic Reach
2 countries

44 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 25, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

April 27, 2011

Completed
2 months until next milestone

Study Start

First participant enrolled

July 1, 2011

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2012

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2012

Completed
5.4 years until next milestone

Results Posted

Study results publicly available

October 11, 2017

Completed
Last Updated

October 11, 2017

Status Verified

September 1, 2017

Enrollment Period

7 months

First QC Date

April 25, 2011

Results QC Date

September 8, 2017

Last Update Submit

September 11, 2017

Conditions

Keywords

PF-04950615RN316

Outcome Measures

Primary Outcomes (1)

  • Percent Change From Baseline in Low-density Lipoprotein Cholesterol (LDL-C) at Day 85

    Baseline value was calculated as the average of Day 7 and Day 1 measurements collected prior to study drug administration.

    Baseline, Day 85

Secondary Outcomes (9)

  • Percentage of Participants Achieving Low-density Lipoprotein Cholesterol (LDL-C) Less Than (<) 70 and <100 Milligram Per Deciliter (mg/dL)

    Day 29, 57, 85

  • Percentage of Participants Achieving at Least 30 Percent Decrease in Low-density Lipoprotein Cholesterol (LDL-C)

    Day 29, 57, 85

  • Change From Baseline in Lipid Parameters at Day 29, 57 and 85

    Baseline, Day 29, 57, 85

  • Percent Change From Baseline in Lipid Parameters at Day 29, 57 and 85

    Baseline, Day 29, 57, 85

  • Number of Participants With Treatment-Emergent Adverse Events (TEAEs)

    Day 1 up to Day 141

  • +4 more secondary outcomes

Other Outcomes (2)

  • Change From Baseline in Lipoprotein (a) (Lp[a]) at Day 29, 57, 71, 85, 99, 127 and 141

    Baseline, Day 29, 57, 71, 85, 99, 127, 141

  • Percent Change From Baseline in Lipoprotein (a) (Lp[a]) at Day 29, 57, 71, 85, 99, 127 and 141

    Baseline, Day 29, 57, 71, 85, 99, 127, 141

Study Arms (5)

Treatment A

PLACEBO COMPARATOR
Biological: PlaceboDrug: Statin

Treatment B

EXPERIMENTAL
Biological: PF-04950615 (RN316)Drug: Statin

Treatment C

EXPERIMENTAL
Biological: PF-04950615 (RN316)Drug: Statin

Treatment D

EXPERIMENTAL
Biological: PF-04950615 (RN316)Drug: Satin

Treatment E

EXPERIMENTAL
Biological: PF-04950615 (RN316)Drug: Statin

Interventions

PlaceboBIOLOGICAL

Intravenous placebo monthly during treatment phase.

Treatment A
StatinDRUG

Single daily dose of atorvastatin (40 or 80 mg), rosuvastatin (20 or 40 mg) or simvastatin (40 or 80 mg) from Day 1 to Day 141/ET.

Treatment A

Intravenous 10mg/mL based on weight monthly during treatment phase.

Treatment B
SatinDRUG

Single daily dose of atorvastatin (40 or 80 mg), rosuvastatin (20 or 40 mg) or simvastatin (40 or 80 mg) from Day 1 to Day 141/ET.

Treatment D

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • On a stable daily dose of atorvastatin, rosuvastatin or simvastatin.
  • Lipids meet the following criteria at screening and prior to dosing: Fasting LDL-C greater than 100 mg/dL and fasting TG less than 400 mg/dL

You may not qualify if:

  • History of a cardiovascular or cerebrovascular event or procedure during the past year.
  • Poorly controlled type 1 or type 2 diabetes mellitus.
  • Poorly controlled hypertension.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (44)

Orange County Research Center

Tustin, California, 92780, United States

Location

Diablo Clinical Research, Inc.

Walnut Creek, California, 94598, United States

Location

Innovative Research of West Florida, Inc.

Clearwater, Florida, 33756, United States

Location

Avail Clinical Research, LLC

DeLand, Florida, 32720, United States

Location

In Vivo Clinical Research, Inc.

Doral, Florida, 33166, United States

Location

Jacksonville Center for Clinical Research

Jacksonville, Florida, 32216, United States

Location

Kendall South Medical Center

Miami, Florida, 33185, United States

Location

North Georgia Clinical Research

Woodstock, Georgia, 30189, United States

Location

North Georgia Internal Medicine

Woodstock, Georgia, 30189, United States

Location

Vince and Associates Clinical Research

Overland Park, Kansas, 66212, United States

Location

Heartland Research Associates, LLC

Wichita, Kansas, 67207, United States

Location

L-MARC Research Center

Louisville, Kentucky, 40213, United States

Location

Commonwealth Biomedical Research, LLC

Madisonville, Kentucky, 42431, United States

Location

Maine Research Associates

Auburn, Maine, 04210, United States

Location

Infinity Medical Research

North Dartmouth, Massachusetts, 02747, United States

Location

Saint Luke's Hospital

Kansas City, Missouri, 64111, United States

Location

Saint Luke's Lipid and Diabetes Research Center

Kansas City, Missouri, 64111, United States

Location

The Center for Pharmaceutical Research, P.C.

Kansas City, Missouri, 64114, United States

Location

Medex Healthcare Research, Inc.

St Louis, Missouri, 63117, United States

Location

New Mexico Clinical Research & Osteoporosis Center, Incorporated

Albuquerque, New Mexico, 87106, United States

Location

North Carolina Clinical Research

Raleigh, North Carolina, 27607, United States

Location

PMG Research of Salisbury

Salisbury, North Carolina, 28144, United States

Location

Lynn Health Science Institute

Oklahoma City, Oklahoma, 73112, United States

Location

Oklahoma Cardiovascular Research Group (OCRG)

Oklahoma City, Oklahoma, 73120, United States

Location

Oklahoma Heart Hospital Physicians

Oklahoma City, Oklahoma, 73120, United States

Location

Oklahoma Heart Hospital

Oklahoma City, Oklahoma, 73120, United States

Location

Altoona Center for Clinical Research

Duncansville, Pennsylvania, 16635, United States

Location

Perelman Center for Advanced Medicine

Philadelphia, Pennsylvania, 19104, United States

Location

Translational Research Center

Philadelphia, Pennsylvania, 19104, United States

Location

Spartanburg Medical Research

Spartanburg, South Carolina, 29303, United States

Location

New Orleans Center for Clinical Research

Knoxville, Tennessee, 37920, United States

Location

Volunteer Research Group

Knoxville, Tennessee, 37920, United States

Location

Texas Center for Drug Development, Inc.

Houston, Texas, 77081, United States

Location

Paragon Research Center, LLC

San Antonio, Texas, 78205, United States

Location

Clinical Trials of Texas, Inc.

San Antonio, Texas, 78229, United States

Location

San Antonio Preventive & Diagnostic Medicine, PA

San Antonio, Texas, 78229, United States

Location

National Clinical Research - Norfolk, Inc.

Norfolk, Virginia, 23502, United States

Location

National Clinical Research - Richmond, Inc.

Richmond, Virginia, 23294, United States

Location

The Medical Arts Health Research Group

Kelowna, British Columbia, V1Y 3G8, Canada

Location

Q & T Research Chicoutimi

Chicoutimi, Quebec, G7H 7Y8, Canada

Location

Centre de Recherche Clinique de Laval

Laval, Quebec, H7T 2P5, Canada

Location

Diex Research Montreal Inc.

Montreal, Quebec, H4N 3C5, Canada

Location

Clinique des Maladies Lipidiques de Quebec Inc.

Québec, Quebec, G1V 4M6, Canada

Location

Diex Research Sherbrooke Inc.

Sherbrooke, Quebec, J1H 1Z1, Canada

Location

Related Publications (3)

  • Wang EQ, Kaila N, Plowchalk D, Gibiansky L, Yunis C, Sweeney K. Population PK/PD modeling of low-density lipoprotein cholesterol response in hypercholesterolemic participants following administration of bococizumab, a potent anti-PCSK9 monoclonal antibody. CPT Pharmacometrics Syst Pharmacol. 2023 Dec;12(12):2013-2026. doi: 10.1002/psp4.13050. Epub 2023 Nov 22.

  • Wan H, Gumbiner B, Joh T, Riel T, Udata C, Forgues P, Garzone PD. Effects of Proprotein Convertase Subtilisin/Kexin Type 9 (PCSK9) Inhibition with Bococizumab on Lipoprotein Particles in Hypercholesterolemic Subjects. Clin Ther. 2017 Nov;39(11):2243-2259.e5. doi: 10.1016/j.clinthera.2017.09.009. Epub 2017 Oct 14.

  • Udata C, Garzone PD, Gumbiner B, Joh T, Liang H, Liao KH, Williams JH, Meng X. A Mechanism-Based Pharmacokinetic/Pharmacodynamic Model for Bococizumab, a Humanized Monoclonal Antibody Against Proprotein Convertase Subtilisin/Kexin Type 9, and Its Application in Early Clinical Development. J Clin Pharmacol. 2017 Jul;57(7):855-864. doi: 10.1002/jcph.867. Epub 2017 Feb 9.

Related Links

MeSH Terms

Conditions

HypercholesterolemiaDyslipidemias

Interventions

Hydroxymethylglutaryl-CoA Reductase Inhibitorsbococizumab

Condition Hierarchy (Ancestors)

HyperlipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

Anticholesteremic AgentsHypolipidemic AgentsAntimetabolitesMolecular Mechanisms of Pharmacological ActionPharmacologic ActionsChemical Actions and UsesEnzyme InhibitorsLipid Regulating AgentsTherapeutic Uses

Limitations and Caveats

Due to an inadvertent omission in the protocol at Day 85, presented limitations in the assessment of treatment effect on ApoA1, ApoB and Lp(a) for Day 85.

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 25, 2011

First Posted

April 27, 2011

Study Start

July 1, 2011

Primary Completion

February 1, 2012

Study Completion

June 1, 2012

Last Updated

October 11, 2017

Results First Posted

October 11, 2017

Record last verified: 2017-09

Locations