NCT01321541

Brief Summary

The purpose of this study is to evaluate the efficacy of Pixantrone + Rituximab compared to Gemcitabine + Rituximab in patients with relapsed or refractory diffuse large B-cell lymphoma (DLBCL), or follicular grade 3 lymphoma.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
312

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Apr 2011

Longer than P75 for phase_3

Geographic Reach
17 countries

131 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 21, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

March 23, 2011

Completed
28 days until next milestone

Study Start

First participant enrolled

April 20, 2011

Completed
7.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 28, 2018

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

September 14, 2018

Completed
3.2 years until next milestone

Results Posted

Study results publicly available

November 19, 2021

Completed
Last Updated

November 19, 2021

Status Verified

September 1, 2021

Enrollment Period

7.2 years

First QC Date

March 21, 2011

Results QC Date

November 23, 2020

Last Update Submit

October 21, 2021

Conditions

Keywords

non-hodgkin lymphomaDLBCLrelapsedaggressive NHLDiffuse large B-cell lymphomaRituximabRituxanPixantroneNHLnon hodgkin's lymphomade novo DLBCLDLBCL transformed from Indolent LymphomaFollicular Grade 3 Lymphoma

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS)

    PFS is defined as the time of randomization to the date of disease progression or death due to any cause (whichever occurs first)

    From the date of randomization to the date of progressive disease or death due to any cause (whichever is first reported) (Up to 100 weeks)

Secondary Outcomes (4)

  • Overall Survival

    From date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

  • Complete Response Rate

    From date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

  • Overall Response Rate

    From date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

  • Number of Treatment Emergent Adverse Events (TEAE) Related to Study Drug

    From date of randomization to the date of the patient's death due to any cause (Up to 100 weeks)

Other Outcomes (2)

  • Individual Concentration-time Profiles of Patients Will be Compared to Existing Data Using Simulations (Visual Predictive Checks)

    within 1 hour of initiation of infusion to 24-48 hours after start of pixantrone infusion

  • To Generate Individual Secondary PK Parameters (eg, Exposure, Half-life Etc.) Using Descriptive Statistics

    within 1 hour of initiation of infusion to 24-48 hours after start of pixantrone infusion

Study Arms (2)

Pixantrone + Rituximab

EXPERIMENTAL

Pixantrone and Rituximab

Drug: Pixantrone + Rituximab

Gemcitabine + Rituximab

ACTIVE COMPARATOR

Gemcitabine and Rituximab

Drug: Gemcitabine + Rituximab

Interventions

Pixantrone + Rituximab: Rituximab 375 mg/m2 IV on day 1 and pixantrone 50 mg/m2 (equivalent to 85mg/m2 pixantrone dimaleate)IV on days 1, 8, and 15. Regimen is given in 28-day cycles. Up to 6 cycles may be administered.

Pixantrone + Rituximab

Gemcitabine + Rituximab: Rituximab 375 mg/m2 IV on day 1 and gemcitabine 1000 mg/m2 IV on days 1, 8, and 15. Regimen is given in 28-day cycles. Up to 6 cycles may be administered.

Gemcitabine + Rituximab

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of DLBCL (de novo DLBCL, or transformed from indolent lymphoma) or follicular grade 3 lymphoma on the basis of tissue biopsy.
  • Patients with de novo DLBCL must have received 1-3 treatment regimens for DLBCL. Patients with follicular grade 3 lymphoma must have received 1-3 treatment regimens for follicular lymphoma (any grade). Patients with DLBCL transformed from indolent lymphoma must have received at least 1-4 treatment regimens for NHL.
  • Received rituximab containing a multi-agent therapy for the treatment of NHL.
  • Not eligible for high-dose chemotherapy and stem cell transplant.
  • Patients with DLBCL transformed from indolent lymphoma must have had a complete or partial response to a therapy for NHL lasting at least 12 weeks.

You may not qualify if:

  • Primary refractory de novo DLBCL or primary refractory follicular grade 3 lymphoma, defined as documented progression within 12 weeks of the last cycle of the first-line multi-agent regimen.
  • Prior treatment with cumulative dose of doxorubicin or equivalent exceeding 450 mg/m2
  • Any experimental therapy ≤ 28 days prior to randomization
  • Other malignancy within last 5 years except for the following: curatively treated basal cell/squamous cell skin cancer, carcinoma in situ of the cervix, superficial transitional cell bladder carcinoma, or in situ ductal carcinoma of the breast after complete resection
  • Any contraindication or known allergy or hypersensitivity to any study drugs
  • Concomitant therapy with any anticancer agents, immunosuppressive agents, other investigational anticancer therapies. Low-dose corticosteroids for the treatment of non cancer-related illnesses are permitted.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (131)

Arizona Clinical Research Center

Tucson, Arizona, 85715, United States

Location

Arizona Oncology Associates

Tucson, Arizona, 85745, United States

Location

Highlands Oncology Group

Bentonville, Arkansas, 72712, United States

Location

Highlands Oncology Group

Fayetteville, Arkansas, 72703, United States

Location

Rocky Mountain Cancer Centers

Aurora, Colorado, 80012, United States

Location

Rocky Mountain Cancer Centers

Boulder, Colorado, 80303, United States

Location

Rocky Mountain Cancer Centers

Denver, Colorado, 80218, United States

Location

George Washington University Department of Medicine

Washington D.C., District of Columbia, 20037, United States

Location

Integrated Community Oncology Network-St. Vincent's

Jacksonville, Florida, 32204, United States

Location

Integrated Community Oncology Network-Southside

Jacksonville, Florida, 32207, United States

Location

Integrated Community Oncology Network

Orange Park, Florida, 32073, United States

Location

Carle Physician Group

Danville, Illinois, 61832, United States

Location

Cancer Care Specialists of Central Illinois

Decatur, Illinois, 62526, United States

Location

Crossroads Cancer Center

Effingham, Illinois, 62401, United States

Location

Carle Foundation Physician Services

Mattoon, Illinois, 61938, United States

Location

Carle Cancer Center

Urbana, Illinois, 61801, United States

Location

Cancer Center of Kansas

Wichita, Kansas, 67208, United States

Location

Cancer Center of Kansas

Wichita, Kansas, 67215, United States

Location

Baptist Hospital East

Louisville, Kentucky, 40207, United States

Location

Harry and Jeanette Weinberg Cancer Institute at Franklin Square

Baltimore, Maryland, 21237, United States

Location

Center for Cancer and Blood Disorders, PC

Bethesda, Maryland, 20817, United States

Location

Cancer & Hematology Center of Western Michigan

Grand Rapids, Michigan, 49450, United States

Location

Metro Minnesota CCOP-Unity Hospital

Fridley, Minnesota, 55432, United States

Location

Metro Minnesota CCOP-St. Johns

Maplewood, Minnesota, 55109, United States

Location

Metro Minnesota Community Clinical Oncology Program

Saint Louis Park, Minnesota, 55416, United States

Location

Metro Minnesota Community Clinical Oncology Program

Saint Louis Park, Minnesota, 55426, United States

Location

Metro Minnesota CCOP-Regions Hospital

Saint Paul, Minnesota, 55101, United States

Location

Missouri Cancer Associates

Columbia, Missouri, 65201, United States

Location

Nebraska Hematology-Oncology, PC

Lincoln, Nebraska, 68506, United States

Location

Hematology-Oncology Associates of Northern New Jersey

Morristown, New Jersey, 07962, United States

Location

North Shore Hematology/Oncology Associates

East Setauket, New York, 11733, United States

Location

Gabrail Cancer Center

Canton, Ohio, 44718, United States

Location

Gabrail Cancer Center

Dover, Ohio, 44622, United States

Location

Toledo Clinical Cancer Center

Toledo, Ohio, 43617, United States

Location

Mercy Cancer Center at St. Anne's

Toledo, Ohio, 43623, United States

Location

Toledo Clinic Cancer Center-Toledo

Toledo, Ohio, 43623, United States

Location

Northwest Cancer Specialists, PC

Portland, Oregon, 97213, United States

Location

Northwest Cancer Specialists, PC

Portland, Oregon, 97225, United States

Location

Northwest Cancer Specialists, PC

Tualatin, Oregon, 97062, United States

Location

Fox Chase Cancer Center

Philadelphia, Pennsylvania, 19111, United States

Location

Upstate Oncology Associates

Greenville, South Carolina, 29615, United States

Location

South Carolina Cancer Specialists

Hardeeville, South Carolina, 29927, United States

Location

South Carolina Cancer Specialists

Hilton Head Island, South Carolina, 29926, United States

Location

Joe Arrington Cancer Research and Treatment Center

Lubbock, Texas, 79410, United States

Location

Cancer Care Centers of South Texas-HOAST

New Braunfels, Texas, 78130, United States

Location

Cancer Care Centers of South Texas-HOAST

San Antonio, Texas, 78229, United States

Location

Blue Ridge Cancer Care

Roanoke, Virginia, 24014, United States

Location

Northwest Cancer Specialists, PC

Vancouver, Washington, 98684, United States

Location

Northwest Cancer Specialists, PC

Vancouver, Washington, 98686, United States

Location

Saint Vincent Hospital Green Bay Oncology

Green Bay, Wisconsin, 54301, United States

Location

Green Bay Oncology-St. Mary's Hospital MC

Green Bay, Wisconsin, 54303, United States

Location

Medical University Innsbruck, Department of Internal Medicine V (Hematology and Oncology)

Innsbruck, 6020, Austria

Location

Hospital Elisabethinen Linz, Internal Department 1 - Hemato-Oncology

Linz, 4020, Austria

Location

Hanusch Hospital, Department of Internal Medicine III

Vienna, 1140, Austria

Location

Saint Luc University Hospital, Department of Hematology

Brussels, 1200, Belgium

Location

General Hospital Delta, Hematology Department

Roeselare, 8800, Belgium

Location

General Hospital Turnhout, Hematology Department

Turnhout, 2300, Belgium

Location

UMHAT "Sveti Georgi", Plovdiv, Clinical Hematology Clinic

Plovdiv, 4002, Bulgaria

Location

UMHAT "Sveti Georgi", Plovdiv, Department of Medical Oncology

Plovdiv, 4002, Bulgaria

Location

MHAT "Tokuda Hospital Sofia", Hematology Clinic

Sofia, 1407, Bulgaria

Location

University Multiprofile Hospital for Active Treatment "Sveti Ivan Rilski", Department of Clinical Hematology

Sofia, 1431, Bulgaria

Location

Specialized Hospital For Active Treatment Of Hematological Diseases, Sofia, Clinical Hematology Clinic

Sofia, 1756, Bulgaria

Location

MHAT Hristo Botev, Vratsa, First Department of Internal Medicine

Vratsa, 3000, Bulgaria

Location

University Hospital Brno, Clinic of Internal Medicine - Hematology and Oncology

Brno, 62500, Czechia

Location

University Hospital Hradec Kralove, 4th Department of Internal Medicne, Clinical Hematology

Hradec Králové, 500 05, Czechia

Location

University Hospital Ostrava, Institute of Clinical Hematology

Ostrava, 70852, Czechia

Location

University Hospital Kralovske Vinohrady, Department of Clinical Hematology

Prague, 10034, Czechia

Location

General University Hospital in Prague, 1st Department of Internal Medicine - Department of Hematology

Prague, 128 20, Czechia

Location

Aalborg University Hospital, Department of Hematology

Aalborg, 9100, Denmark

Location

Service d'hématologie clinique, Avenue Laennec Salouel

Amiens, 80054, France

Location

Centre hopitalier de la cote basque

Bayonne, 64190, France

Location

Centre hospitalier de Beziers

Béziers, 34500, France

Location

Polyclinique de Bordeaux nord Acquitaine

Bordeaux, 33077, France

Location

Centre hospitalier du Mans

Le Mans, 72037, France

Location

Centre hospitalier Lyon Sud

Pierre-Bénite, 69495, France

Location

Saint Quentin Hospital Center, Department of Oncology-Hematology

Saint-Quentin, France

Location

Hautepierre Hospital, Department of Hematology and Oncology

Strasbourg, 97098, France

Location

Gemeinschaftspraxis Drs. Klausmann

Aschaffenburg, 63739, Germany

Location

Klinikum Chemnitz gGmbH

Chemnitz, 09113, Germany

Location

Universitätsklinik Köln

Cologne, 50924, Germany

Location

Klinik für Innere Medizin III

Frankfurt (a.M.), 65929, Germany

Location

Universitaetsklinikum Halle

Halle, 06120, Germany

Location

St. Marien Hospital Hamm

Hamm, 59071, Germany

Location

Klinikum Nürnberg Nord

Nuremberg, 90419, Germany

Location

Klinikum Mutterhaus der Borromäerinnen

Trier, 54290, Germany

Location

St. Istvan and St. Laszlo Hospital of Budapest

Budapest, H-1097, Hungary

Location

University of Debrecen

Debrecen, H-4032, Hungary

Location

Moritz Kaposi General Hospital

Kaposvár, 7400, Hungary

Location

University Hospital "Ospedali Riuniti Umberto I - G.M. Lancisi - G. Salesi"

Ancona, 70126, Italy

Location

Bologna University Hospital Authority St. Orsola-Malpighi Polyclinic

Bologna, 40138, Italy

Location

Scientific Institute of Romagna for the Study and Treatment of Cancer (I.R.S.T.) S.R.L.

Meldola, 47014, Italy

Location

"Ospedali Riuniti Villa Sofia-Cervello" Hospital

Palermo, 90146, Italy

Location

Romagna Local Health Authority (AUSL Romagna) - "Santa Maria delle Croci"

Ravenna, 48121, Italy

Location

Romagna Local Health Authority (AUSL Romagna) - "Infermi" Hospital

Rimini, 47900, Italy

Location

Siena University Hospital Authority Santa Maria alle Scotte Polyclinic

Siena, 53100, Italy

Location

Santa Maria Hospital

Terni, 5100, Italy

Location

A.O.U. Città della Salute e della Scienza di Torino

Torino, 10126, Italy

Location

Independent Public Healthcare Facility Municipal Hospital Group

Chorzów, 41-500, Poland

Location

Marine Hospital of Polish Red Cross, Department of Chemotheraphy

Gdynia, 81-519, Poland

Location

Silesia Medical University, Department of Hematology and Bone Marrow Transplantation

Katowice, 40-032, Poland

Location

Malopolskie Medical Center S.C. , Department of Hematology

Krakow, 30-510, Poland

Location

Nicolaus Copernicus Memorial Provincial Specialist Hospital in Lodz

Lodz, 93-513, Poland

Location

Oncology Center of Lublin Land, Department of Clinical Oncology

Lublin, 20-090, Poland

Location

Institute of Hematology and Transfusion Medicine, Clinic of Hematology

Warsaw, 02-776, Poland

Location

Wroclaw Medical University, Department and Clinic of Hematology, Blood Neoplasms and Bone Marrow Transplantation

Wroclaw, 50-367, Poland

Location

Rapid Diagnosis Polyclinic SA

Brasov, Romania

Location

Fundeni Clinical Institute Center for Hematology and Bone Marrow Transplantation

Bucharest, 022328, Romania

Location

Bucharest University Emergency Hospital, Hematology Clinic

Bucharest, 050098, Romania

Location

Federal State Public Institution: Main Military Clinical Hospital n.a. N.N. Burdenko of the Russian Ministry of Defense

Moscow, 105229, Russia

Location

Moscow State Budget Medical Institution: City Clinical Hospital n.a. S.P.Botkin

Moscow, Russia

Location

State Medical Institution: Republican Hospital named after V.A. Baranov

Petrozavodsk, 18500, Russia

Location

St. Petersburg Clinical Research and Practical Center for Specialized Types of Medical Care

Saint Petersburg, 197758, Russia

Location

State Healthcare Institution: Republican Clinical Oncology Center

Ufa, 450054, Russia

Location

State Budget Healthcare Institution of Sverdlovsk region: Sverdlovsk Regional Clinical Hospital #1

Yekaterinburg, 620102, Russia

Location

University Hospital with Outpatient Clinic F.D. Roosevelt Banska Bystrica, Department of Hematology

Banská Bystrica, 975 17, Slovakia

Location

National Cancer Institute, Department of Hematology and Transfusiology

Bratislava, 83310, Slovakia

Location

University Hospital Martin, Department of Hematology and Transfusiology

Martin, 3659, Slovakia

Location

J. A. Reiman University Hospital with Polyclinic in Presov

Prešov, 08181, Slovakia

Location

A Coruña University Hospital

A Coruña, 15006, Spain

Location

Hospital Universitario Vall Hebrón

Barcelona, 08035, Spain

Location

Hospital Iniversitario Puerta del Mar

Cadiz, 11009, Spain

Location

Institut Català de Oncologia (ICO), Hospital Dr Trueta

Girona, 17007, Spain

Location

Hospital Iniversitario La Paz

Madrid, 28046, Spain

Location

Hospital Universitario Araba

Vitoria-Gasteiz, 01009, Spain

Location

Cherkasy Regional Oncology Center, Regional Treatment and Diagnostic Hematology Center

Cherkasy, 18009, Ukraine

Location

Kharkiv Regional Clinical Oncology Center

Kharkiv, 61070, Ukraine

Location

National Institute of Cancer

Kyiv, 03022, Ukraine

Location

State Institution: Institute of Blood Pathology and Transfusion Medicine

Lviv, 79044, Ukraine

Location

Beatson West of Scotland Cancer Center

Glasgow, G12 0YN, United Kingdom

Location

St. George's Healthcare NHS Trust

London, SW17 0QT, United Kingdom

Location

Christie Hospital, Department of Medical Oncology

Manchester, M20 4BX, United Kingdom

Location

Related Publications (2)

  • Pettengell R, Dlugosz-Danecka M, Andorsky D, Belada D, Georgiev P, Quick D, Singer JW, Singh SB, Pallis A, Egorov A, Salles G. Pixantrone plus rituximab versus gemcitabine plus rituximab in patients with relapsed aggressive B-cell non-Hodgkin lymphoma not eligible for stem cell transplantation: a phase 3, randomized, multicentre trial (PIX306). Br J Haematol. 2020 Jan;188(2):240-248. doi: 10.1111/bjh.16255. Epub 2019 Dec 27.

  • Belada D, Georgiev P, Dakhil S, Inhorn LF, Andorsky D, Beck JT, Quick D, Pettengell R, Daly R, Dean JP, Pavlyuk M, Failloux N, Hubel K. Pixantrone-rituximab versus gemcitabine-rituximab in relapsed/refractory aggressive non-Hodgkin lymphoma. Future Oncol. 2016 Aug;12(15):1759-68. doi: 10.2217/fon-2016-0137. Epub 2016 Apr 20.

MeSH Terms

Conditions

Lymphoma, Large B-Cell, DiffuseLymphoma, FollicularLymphoma, Non-HodgkinRecurrence

Interventions

pixantroneRituximabGemcitabine

Condition Hierarchy (Ancestors)

Lymphoma, B-CellLymphomaNeoplasms by Histologic TypeNeoplasmsLymphoproliferative DisordersLymphatic DiseasesHemic and Lymphatic DiseasesImmunoproliferative DisordersImmune System DiseasesDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Antibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulinsHeterocyclic CompoundsDeoxycytidineCytidinePyrimidine NucleosidesPyrimidinesHeterocyclic Compounds, 1-Ring

Results Point of Contact

Title
Anton Egorov, Associate Project Director Clinical Development
Organization
Institut de Recherches Internationales Servier

Study Officials

  • Simran B Singh, MS, GWCP

    Sr. Director, Clinical Operations

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 21, 2011

First Posted

March 23, 2011

Study Start

April 20, 2011

Primary Completion

June 28, 2018

Study Completion

September 14, 2018

Last Updated

November 19, 2021

Results First Posted

November 19, 2021

Record last verified: 2021-09

Locations