NCT01314365

Brief Summary

The purpose of the protocol is to determine typical patient response to Dysport in the treatment of adult cervical dystonia (CD).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
350

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Apr 2011

Typical duration for all trials

Geographic Reach
1 country

45 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 10, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

March 14, 2011

Completed
18 days until next milestone

Study Start

First participant enrolled

April 1, 2011

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2013

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2014

Completed
Last Updated

November 5, 2020

Status Verified

November 1, 2020

Enrollment Period

2.6 years

First QC Date

March 10, 2011

Last Update Submit

November 4, 2020

Conditions

Outcome Measures

Primary Outcomes (2)

  • Proportion of treatment responders using the Toronto Western Spasmodic Torticollis Rating Scale (TWSTRS) severity scale score

    Cycle 1 - Baseline and week 4

  • Patient Global Impression of Change using the 7-point Likert scale

    Cycle 1 - Baseline and week 4

Secondary Outcomes (6)

  • Clinical Global Impression of Change using the 7-point Likert scale

    Cycle 1 - Week 4 and early termination visit

  • Patient Global Impression of Change using the 7-point Likert scale

    Cycle 1 - Week 4; Cycles 2 to 4 - Baseline, week 4 and termination visits

  • Time to Waning Effect of Dysport treatment/symptom re-emergence

    Cycles 1 to 4 - Week 8 and at study termination visits

  • Patient-self-administered questionnaire (Cervical Dystonia Impact Profile-58)

    Cycles 1 & 3: Baseline

  • Patient-reported assessment of pain using the Pain Numeric Rating Scale (NRS)

    Cycles 1 to 4 - Baseline, week 4 and at study termination visits

  • +1 more secondary outcomes

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Adult patients with Cervical Dystonia treated with Dysport

You may qualify if:

  • A diagnosis of idiopathic CD as determined by the enrolling investigator
  • If previously treated with a neurotoxin for CD, at least a 12-week interval must have elapsed between the last injection of Botulinum toxin A (BoNT-A) or Botulinum toxin B (BoNT-B) and the first dose of Dysport injected in this study
  • Patient is able to comply with the protocol (e.g., can visit the clinic as required and can complete questionnaires/telephone interviews)
  • Provision of written informed consent prior to enrollment

You may not qualify if:

  • Contraindications to treatment with any BoNT-A or BoNT-B preparations
  • Based on Investigator opinion, patients in whom previous BoNT-A or BoNT-B therapy has failed to produce a clinical response or produced an intolerable adverse reaction
  • Anticipated concomitant treatment with BoNT for other than cervical dystonia
  • Secondary cervical dystonia

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (45)

Arizona Dystonia Institute

Scottsdale, Arizona, 85258, United States

Location

East Bay Physicians Medical Group

Berkeley, California, 94705, United States

Location

Headache Center

Encinitas, California, 92024, United States

Location

The Parkinson's & Movement Disorder Institute

Fountain Valley, California, 92708, United States

Location

Neuro-Pain Medical Center

Fresno, California, 93710, United States

Location

Coastal Neurological Medical Group, Inc.

La Jolla, California, 92037, United States

Location

Valley Parkinson Clinic

Los Gatos, California, 95032, United States

Location

Harvinder S. Birk

Redding, California, 96001, United States

Location

Colorado Springs Neurological Associates

Colorado Springs, Colorado, 80907, United States

Location

University of Colorado Denver

Denver, Colorado, 80045, United States

Location

Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

Neurology Offices of South Florida

Boca Raton, Florida, 33428, United States

Location

Parkinson's Disease and Movement Disorders Center of Boca Raton

Boca Raton, Florida, 33486, United States

Location

Infinity Clinical Research, LLC

Hollywood, Florida, 33021, United States

Location

University of Miami, Dept. of Movement Disorders Clinic

Miami, Florida, 33136, United States

Location

Palm Beach Gardens Medical Center

North Palm Beach, Florida, 33408, United States

Location

Emerald Coast Center for Neurological Disorders

Pensacola, Florida, 32514, United States

Location

Parkinson's Treatment Center of SW Florida

Port Charlotte, Florida, 33980, United States

Location

USF HealthParkinson's Disease and Movement Disorders Center

Tampa, Florida, 33613, United States

Location

Cleveland Clinic Florida

Weston, Florida, 33331, United States

Location

Elks Rehab Hospital - Movement Disorders Center

Boise, Idaho, 83702, United States

Location

Rush University Medical Center Department of Neurological Sciences

Chicago, Illinois, 60612, United States

Location

Kansas City Bone & Joint Clinic, PA Overland Park

Overland Park, Kansas, 66211, United States

Location

Baptist Neurology Center - Lexington

Lexington, Kentucky, 40503, United States

Location

The Neuro Medical Center

Baton Rouge, Louisiana, 70810, United States

Location

The Parkinson's and Movement Disorders Center

Southfield, Michigan, 48034, United States

Location

Rehabilitation Consultants, PA

Eagan, Minnesota, 55121, United States

Location

Methodist Rehabilitation Center

Jackson, Mississippi, 39216, United States

Location

University of Nevada School of Medicine

Reno, Nevada, 89502, United States

Location

Empire Neurology PC, the MS Center of Northeastern New York

Latham, New York, 12110, United States

Location

Raleigh Neurology Associates

Raleigh, North Carolina, 27607, United States

Location

Riverhills Neuroscience

Cincinnati, Ohio, 45219, United States

Location

University Neurology, Inc.

Cincinnati, Ohio, 45267, United States

Location

Cleveland Clinic Center for Neurological Restoration

Cleveland, Ohio, 44195, United States

Location

Capital Neurology Services & MS Institute

Gahanna, Ohio, 43230, United States

Location

Neurological Associates of Tulsa

Tulsa, Oklahoma, 74137, United States

Location

Columbia Pain Management, PC

Hood River, Oregon, 97031, United States

Location

Allegheny General Hospital_Department of Neurology

Pittsburgh, Pennsylvania, 15212, United States

Location

Coastal Neurology, PA

Port Royal, South Carolina, 29935, United States

Location

Victorium Clinical Research

San Antonio, Texas, 78229, United States

Location

Neurology Center of San Antonio

San Antonio, Texas, 78258, United States

Location

Gershon Pain Specialists

Virginia Beach, Virginia, 23454, United States

Location

Evergreen Hospital Medical Center/Booth Gardner Parkinson's Care Center

Kirkland, Washington, 98034, United States

Location

South Puget Sound Neurology

Tacoma, Washington, 98405, United States

Location

Gundersen Clinic, Ltd.

La Crosse, Wisconsin, 54601, United States

Location

Related Publications (2)

  • Trosch RM, Misra VP, Maisonobe P, Om S. Impact of abobotulinumtoxinA on the clinical features of cervical dystonia in routine practice. Clin Park Relat Disord. 2020 Jun 15;3:100063. doi: 10.1016/j.prdoa.2020.100063. eCollection 2020.

  • Espay AJ, Trosch R, Suarez G, Johnson J, Marchese D, Comella C. Minimal clinically important change in the Toronto Western Spasmodic Torticollis Rating Scale. Parkinsonism Relat Disord. 2018 Jul;52:94-97. doi: 10.1016/j.parkreldis.2018.03.002. Epub 2018 Mar 7.

MeSH Terms

Conditions

Torticollis

Condition Hierarchy (Ancestors)

DystoniaDyskinesiasNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Study Officials

  • Ipsen Study Director

    Ipsen

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 10, 2011

First Posted

March 14, 2011

Study Start

April 1, 2011

Primary Completion

November 1, 2013

Study Completion

March 1, 2014

Last Updated

November 5, 2020

Record last verified: 2020-11

Locations