NCT01287585

Brief Summary

This is a study of ADI-PEG 20 (pegylated arginine deiminase), an arginine degrading enzyme versus placebo in patients with hepatocellular carcinoma who have failed prior systemic treatment (chemotherapy). Hepatocellular carcinomas have been found to require arginine, an amino acid. Thus the hypothesis is that by restricting arginine with ADI-PEG 20, the hepatocellular carcinoma cells will starve and die.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
636

participants targeted

Target at P75+ for phase_3 hepatocellular-carcinoma

Timeline
Completed

Started Jul 2011

Geographic Reach
6 countries

73 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 25, 2011

Completed
7 days until next milestone

First Posted

Study publicly available on registry

February 1, 2011

Completed
5 months until next milestone

Study Start

First participant enrolled

July 1, 2011

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2015

Completed
Last Updated

September 6, 2019

Status Verified

August 1, 2016

Enrollment Period

4 years

First QC Date

January 25, 2011

Last Update Submit

August 27, 2019

Conditions

Keywords

Hepatocellular carcinomaArginineArginine deiminaseADI-PEG 20

Outcome Measures

Primary Outcomes (1)

  • Overall survival

    Overall survival - until death or study closure.

    18 months

Secondary Outcomes (1)

  • Safety and tolerability - number of participants with adverse events.

    18 months - at anticipated end of study.

Study Arms (2)

ADI-PEG 20

EXPERIMENTAL

Arginine deiminase formulated with polyethylene glycol.

Drug: ADI-PEG 20 (arginine deiminase formulated with polyethylene glycol)Other: Best Supportive Care

Placebo

PLACEBO COMPARATOR

an inert treatment with no therapeutic value.

Drug: PlaceboOther: Best Supportive Care

Interventions

18 mg/m2, weekly, intramuscular, until disease progression or toxicity.

ADI-PEG 20

weekly, intramuscular, until disease progression or toxicity.

Placebo

treatment of disease-related symptoms throughout the study.

ADI-PEG 20Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Prior diagnosis of HCC confirmed histologically.
  • Prior treatment with at least 1 systemic agent, with documented progressive disease after systemic agent(s), or adverse event(s)associated with prior systemic agent(s) that resulted in discontinuance of that agent(s).
  • Cirrhotic status of Child-Pugh grade B7.
  • Expected survival of at least 3 months.
  • Adequate hematologic, hepatic, and renal function.

You may not qualify if:

  • Candidate for potential curative therapies (i.e., resection or transplantation) or loco-regional approaches (i.e., ablation, embolization).
  • Significant cardiac disease.
  • Serious infection requiring treatment with systemically administered antibiotics.
  • Pregnancy or lactation.
  • Expected non-compliance.
  • Uncontrolled intercurrent illness, or psychiatric illness or social situations that would limit compliance with study requirements.
  • Subjects who have had any anticancer treatment within 2 weeks prior to entering the study.
  • Subjects who have not fully recovered from toxicities associated with previous HCC loco-regional or systemic therapies.
  • Subjects with history of another primary cancer, with the exception of: a) curatively resected non-melanoma skin cancer; b) curatively treated cervical carcinoma in situ; or c) other primary solid tumor with no known active disease present in the opinion of the investigator will not affect patient outcome in the setting of current HCC diagnosis.
  • Allergy to pegylated products.
  • Bleeding esophageal or gastric varices within the prior three months, except if banded or treated.
  • Subjects known to be HIV positive.
  • Uncontrolled ascites (defined as not easily controlled with diuretic treatment).
  • Having received any blood transfusion, blood component preparation, erythropoietin, albumin preparation, or granulocyte colony stimulating factors (G-CSF) within 7 days prior to screening laboratories or after screening laboratories have been obtained until first dose of study drug or placebo.
  • Use of traditional medicines approved by local authorities, including but not limited to Chinese herbs within 14 days of first dose of study drug or placebo.
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (73)

University of Alabama

Birmingham, Alabama, United States

Location

Southern California Research Center

Coronado, California, 92118, United States

Location

Catherine Frenette

La Jolla, California, 92037, United States

Location

Stanford University

Palo Alto, California, United States

Location

University of California at San Diego Moores Cancer Center

San Diego, California, United States

Location

Pacific Medical Center

San Francisco, California, United States

Location

Piedmont Research Institute

Atlanta, Georgia, United States

Location

University of Hawaii

Honolulu, Hawaii, United States

Location

University of Maryland Greenbaum Cancer Center

Baltimore, Maryland, 21201, United States

Location

Johns Hopkins University Hospital

Baltimore, Maryland, United States

Location

Wayne State University School of Medicine, Dept Oncology

Detroit, Michigan, 48201, United States

Location

University of Minnesota Cancer Center

Minneapolis, Minnesota, United States

Location

Nebraska Hem-Onc

Lincoln, Nebraska, United States

Location

Memorial Sloan-Kettering Cancer Center

New York, New York, 10065, United States

Location

University of Oregon

Portland, Oregon, United States

Location

Drexel University

Philadelphia, Pennsylvania, United States

Location

University of Pennsylvania Abramson Cancer Center

Philadelphia, Pennsylvania, United States

Location

UPMC Cancer Centers

Pittsburgh, Pennsylvania, United States

Location

UT Southwestern

Dallas, Texas, United States

Location

Michael E. DeBakey VA Medical Center

Houston, Texas, United States

Location

University of Washington

Seattle, Washington, United States

Location

A ward of Oncology-287 Changhuai Rd

Bengbu, Anhui, 233000, China

Location

Oncology, No. 678, Furong Rd

Hefei, Anhui, 230601, China

Location

The First Hospital of Medical University Of Anhui

Hefei, Anhui, China

Location

5th Fl, Inpatient Bldg, No. 8,

Fengtai Distrcit, Beijing Municipality, 100071, China

Location

No. 156 North Road of West Second Ring

Gulou District, Fujian, 350025, China

Location

15th Floor, In-patient Building (East), No. 651 Dongfeng East Road

Guangzhou, Guangdong, 510060, China

Location

5th Fl, Inpatient Bldg, No. 71, Heti Rd

Qingxiu Disttrict, Guangxi, 530021, China

Location

3rd Floor, Medicine Building, No. 150 Haping Rd

Harbin, Heilongjiang, 150040, China

Location

Oncology, 185 Road Juqian Street

Changzhou, Jiangsu, 213003, China

Location

The Chinese people's liberation army 81 hospital

Nanjing, Jiangsu, China

Location

5th Floor, Medical Building, No. 1018 Huguang Rd

Changchun, Jilin, 116011, China

Location

No. 193, Lianhe Rd, Shahekou Dist.

Dalian, Liaoning, 116011, China

Location

No. 596, Xinsi Rd., Baqiao Dist.

Xi'an, Shaanxi, 710038, China

Location

Floor 7, 3rd Inpatient Building No. 37, Guoxue Xiang

Chengdu, Sichuan, 610041, China

Location

13th Floor, Internal Medicine Building, No. 29 Gaotanyan Main St.

Chongqing, 400038, China

Location

Bldg No. 5, 3rd Floor, Dongan Rd

Shanghai, China

Location

Istituto Tumori "Giovanni Paolo II"

Bari, Italy

Location

Policlinico S. Orsola-Malpighi

Bologna, Italy

Location

Azienda Ospedaliera Niguarda CĂ  Granda

Milan, Italy

Location

Fondazione Centro San Raffaele del Monte Tabor

Milan, Italy

Location

Fondazione IRCCs "Ca Granda" Ospedale Maggiore Policlinico

Milan, Italy

Location

Policlinico di Monza

Monza, Italy

Location

Istituto Nazionale per lo Studio e la Cura dei Tumori

Naples, Italy

Location

Azienda Ospedaliera di Padova

Padua, Italy

Location

Azienda Ospedaliera San Camillo Forlanini

Roma, Italy

Location

Instituto Nazionale pler le Malattie Infettive

Rome, Italy

Location

Asan Medical Center

Seoul, South Korea

Location

Korea University Anam Hospital

Seoul, South Korea

Location

Samsung Medical Center

Seoul, South Korea

Location

Seoul St. Mary's Hospital

Seoul, South Korea

Location

Severance Hospital

Seoul, South Korea

Location

CGMHCY

Chiayi City, Taiwan

Location

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, Taiwan

Location

Chang Gung Medical Foundation-Kaohsiung

Kaohsiung County, Taiwan

Location

China Medicine University Hospital

Taichung, 40447, Taiwan

Location

CMMC-LY

Tainan, Taiwan

Location

CMMC-YK

Tainan, Taiwan

Location

National Cheng Kung University Hospital

Tainan, Taiwan

Location

Mackay Memorial Hospital-Taipei Branch

Taipei, Taiwan

Location

Northern Taiwan University Hospital

Taipei, Taiwan

Location

Taipei Veterans General Hospital

Taipei, Taiwan

Location

Chang Gung Medical Foundation-Linkou

Taoyuan, Taiwan

Location

Clatterbridge Cancer Center

Bebington, United Kingdom

Location

University Hospitals Birmingham NHS Foundation Trust

Birmingham, United Kingdom

Location

Hammersmith Hospital

London, United Kingdom

Location

King's College Hospital

London, United Kingdom

Location

Royal Free Hospital

London, United Kingdom

Location

St. Bartholomew's Hospital

London, United Kingdom

Location

The Royal Marsden Hospital

London, United Kingdom

Location

Christie NHS Trust

Manchester, United Kingdom

Location

Nottingham University Hospital

Nottingham, United Kingdom

Location

Royal Marsden

Sutton, United Kingdom

Location

Related Publications (1)

  • Abou-Alfa GK, Qin S, Ryoo BY, Lu SN, Yen CJ, Feng YH, Lim HY, Izzo F, Colombo M, Sarker D, Bolondi L, Vaccaro G, Harris WP, Chen Z, Hubner RA, Meyer T, Sun W, Harding JJ, Hollywood EM, Ma J, Wan PJ, Ly M, Bomalaski J, Johnston A, Lin CC, Chao Y, Chen LT. Phase III randomized study of second line ADI-PEG 20 plus best supportive care versus placebo plus best supportive care in patients with advanced hepatocellular carcinoma. Ann Oncol. 2018 Jun 1;29(6):1402-1408. doi: 10.1093/annonc/mdy101.

    PMID: 29659672BACKGROUND

MeSH Terms

Conditions

Carcinoma, Hepatocellular

Interventions

ADI PEG20Polyethylene Glycols

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Intervention Hierarchy (Ancestors)

Ethylene GlycolsGlycolsAlcoholsOrganic ChemicalsPolymersMacromolecular SubstancesBiomedical and Dental MaterialsManufactured MaterialsTechnology, Industry, and Agriculture

Study Officials

  • John S Bomalaski, M.D.

    Polaris Group

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 25, 2011

First Posted

February 1, 2011

Study Start

July 1, 2011

Primary Completion

July 1, 2015

Study Completion

July 1, 2015

Last Updated

September 6, 2019

Record last verified: 2016-08

Locations