NCT01283139

Brief Summary

To evaluate the efficacy and safety of sifalimumab compared to placebo in subjects with moderately to severely active Systemic Lupus Erythematosus (SLE).

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
834

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2011

Typical duration for phase_2

Geographic Reach
22 countries

107 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 20, 2011

Completed
5 days until next milestone

First Posted

Study publicly available on registry

January 25, 2011

Completed
2 months until next milestone

Study Start

First participant enrolled

March 31, 2011

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 14, 2013

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 17, 2014

Completed
2.2 years until next milestone

Results Posted

Study results publicly available

July 11, 2016

Completed
Last Updated

April 19, 2018

Status Verified

March 1, 2018

Enrollment Period

2.6 years

First QC Date

January 20, 2011

Results QC Date

June 1, 2016

Last Update Submit

March 23, 2018

Conditions

Keywords

SLESystemic Lupus ErythematosusSifalimumabMEDI-545

Outcome Measures

Primary Outcomes (2)

  • Percentage of Participants Achieving a Response in Systemic Lupus Erythematosus Responder Index 4 (SRI [4])

    SRI (4) responder is defined as: 1) a reduction in baseline Systemic Lupus Erythematosus Disease Activity Index 2000 (SLEDAI-2K) disease activity score of greater than or equal to (\>=) 4 points (with increased deoxyribonucleic acid \[DNA\] binding item of SLEDAI-2K score based on the ANA Multi-Lyte® ANA-II Plus Test System); 2) no worsening in Physician Global Assessment (MDGA) (worsening is defined as an increase of \>=0.3 from baseline on a 0-3 visual analogue scale) and 3) no worsening in British Isles Lupus Assessment Group (BILAG-2004) (worsening is defined as at least 1 new 'A' score or 2 new 'B' scores on the BILAG-2004 compared with baseline).

    Day 365

  • Percentage of Participants Achieving a Positive Response in SRI (4) in 4-Gene Interferon Test High Participants

    SRI (4) responder is defined as: 1) a reduction in baseline SLEDAI-2K disease activity score of \>=4 points (with increased DNA binding item of SLEDAI-2K score based on the ANA Multi-Lyte® ANA-II Plus Test System); 2) no worsening in Physician Global Assessment (MDGA) (worsening is defined as an increase of \>=0.3 from baseline on a 0-3 visual analogue scale) and 3) no worsening in BILAG-2004 (worsening is defined as at least 1 new 'A' score or 2 new 'B' scores on the BILAG-2004 compared with baseline).

    Day 365

Secondary Outcomes (7)

  • Percentage of Participants on Greater Than or Equal to 10 mg/Day Oral Prednisone (or Equivalent) at Baseline Who Were Able to Reduce to Less Than or Equal to (<=) 7.5 mg/Day

    Day 365

  • Percentage of Participants With a Cutaneous Lupus Erythematosus Disease Activity and Severity Index (CLASI) Activity Score Greater Than or Equal to (>=) 10 at Baseline Who Achieved a >= 4-point Reduction

    Day 365

  • Percentage of Participants Who Achieved a Greater Than 3-Point Improvement in the Functional Assessment of Chronic Illness Therapy (FACIT)-Fatigue Scale

    Day 365

  • Number of Participants With Treatment-Emergent Adverse Events (TEAEs) and Serious Adverse Events (TESAEs)

    Day 1 up to Week 74

  • Number of Participants With Abnormal Clinical Laboratory Parameters Reported as Treatment-Emergent Adverse Events (TEAEs)

    Day 1 up to Week 61

  • +2 more secondary outcomes

Study Arms (4)

Sifalimumab 200 milligram (mg)

EXPERIMENTAL

Sifalimumab 200 milligram (mg) will be administered intravenously every 2 weeks for 4 weeks and then monthly for 44 weeks for a total of 14 doses.

Biological: Sifalimumab 200 mg

Sifalimumab 600 mg

EXPERIMENTAL

Sifalimumab 600 mg will be administered intravenously every 2 weeks for 4 weeks and then monthly for 44 weeks for a total of 14 doses.

Biological: Sifalimumab 600 mg

Sifalimumab 1,200 mg

EXPERIMENTAL

Sifalimumab 1,200 mg will be administered intravenously every 2 weeks for 4 weeks and then monthly for 44 weeks for a total of 14 doses.

Biological: Sifalimumab 1,200 mg

Placebo

PLACEBO COMPARATOR

Placebo matching to sifalimumab will be administered intravenously at a fixed dose every 2 weeks for 4 weeks and then monthly for 44 weeks for a total of 14 doses.

Other: Placebo

Interventions

Sifalimumab 200 mg intravenously every 2 weeks for 4 weeks and then monthly for 44 weeks for a total of 14 doses.

Also known as: MEDI-545
Sifalimumab 200 milligram (mg)

Sifalimumab 600 mg intravenously every 2 weeks for 4 weeks and then monthly for 44 weeks for a total of 14 doses.

Also known as: MEDI-545
Sifalimumab 600 mg

Sifalimumab 1,200 mg intravenously every 2 weeks for 4 weeks and then monthly for 44 weeks for a total of 14 doses.

Also known as: MEDI-545
Sifalimumab 1,200 mg
PlaceboOTHER

IV Placebo every 2 weeks for 4 weeks and then monthly for 44 weeks

Placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (107)

Research Site

La Jolla, California, United States

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Palm Desert, California, United States

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San Leandro, California, United States

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Fort Lauderdale, Florida, United States

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Orlando, Florida, United States

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Stockbridge, Georgia, United States

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Idaho Falls, Idaho, United States

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Shreveport, Louisiana, United States

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Baltimore, Maryland, United States

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Lansing, Michigan, United States

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Brooklyn, New York, United States

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Manhasset, New York, United States

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New York, New York, United States

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Charlotte, North Carolina, United States

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Raleigh, North Carolina, United States

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Dallas, Texas, United States

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Seattle, Washington, United States

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Buenos Aires, Argentina

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Ciudad Autonoma de Buenos Aire, Argentina

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Ciudad de Buenos Aires, Argentina

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La Plata, Argentina

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Quilmes, Argentina

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San Miguel de Tucumán, Argentina

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Curitiba, Brazil

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Goiânia, Brazil

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Juiz de Fora, Brazil

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Porto Alegre, Brazil

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Salvador, Brazil

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São Paulo, Brazil

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Plovdiv, Bulgaria

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Sofia, Bulgaria

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Québec, Quebec, Canada

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Sherbrooke, Quebec, Canada

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Osorno, Chile

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Santiago, Chile

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Viña del Mar, Chile

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Bordeaux, France

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Le Kremlin-Bicêtre, France

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Paris, France

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Strasbourg, France

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Berlin, Germany

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Cologne, Germany

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Dresden, Germany

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Frankfurt, Germany

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Kiel, Germany

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Leipzig, Germany

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Mainz, Germany

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Münster, Germany

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Regensburg, Germany

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Würzburg, Germany

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Budapest, Hungary

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Debrecen, Hungary

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Miskolc, Hungary

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Zalaegerszeg, Hungary

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Bangalore, India

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Secunderabad, India

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Brescia, Italy

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Florence, Italy

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Milan, Italy

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Padua, Italy

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Pisa, Italy

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Roma, Italy

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Kingston, Jamaica

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Chihuahua City, Mexico

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Guadalajara, Mexico

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México, Mexico

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San Luis Potosí City, Mexico

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Amsterdam, Netherlands

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Lima, Peru

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San Borja, Peru

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Cebu City, Philippines

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Iloilo City, Philippines

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Manila, Philippines

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Bialystok, Poland

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Bydgoszcz, Poland

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Katowice, Poland

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Krakow, Poland

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Lublin, Poland

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Olsztyn, Poland

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Poznan, Poland

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Warsaw, Poland

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Brasov, Romania

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Bucharest, Romania

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Cluj-Napoca, Romania

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Tg Mures, Romania

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Cape Town, South Africa

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Durban, South Africa

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Johannesburg, South Africa

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Pinelands, South Africa

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Soweto, South Africa

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Barcelona, Spain

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Guadalajara, Spain

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La Laguna (Tenerife), Spain

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Madrid, Spain

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Majadahonda, Spain

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Málaga, Spain

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Mérida, Spain

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Santiago de Compostela, Spain

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Seville, Spain

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Bangkok, Thailand

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Brighton, United Kingdom

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Cambridge, United Kingdom

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Cannock, United Kingdom

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Guildford, United Kingdom

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Leeds, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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Related Publications (3)

  • Khamashta M, Merrill JT, Werth VP, Furie R, Kalunian K, Illei GG, Drappa J, Wang L, Greth W; CD1067 study investigators. Sifalimumab, an anti-interferon-alpha monoclonal antibody, in moderate to severe systemic lupus erythematosus: a randomised, double-blind, placebo-controlled study. Ann Rheum Dis. 2016 Nov;75(11):1909-1916. doi: 10.1136/annrheumdis-2015-208562. Epub 2016 Mar 23.

    PMID: 27009916BACKGROUND
  • Hannon CW, McCourt C, Lima HC, Chen S, Bennett C. Interventions for cutaneous disease in systemic lupus erythematosus. Cochrane Database Syst Rev. 2021 Mar 9;3(3):CD007478. doi: 10.1002/14651858.CD007478.pub2.

  • Brohawn PZ, Streicher K, Higgs BW, Morehouse C, Liu H, Illei G, Ranade K. Type I interferon gene signature test-low and -high patients with systemic lupus erythematosus have distinct gene expression signatures. Lupus. 2019 Nov;28(13):1524-1533. doi: 10.1177/0961203319885447. Epub 2019 Oct 29.

MeSH Terms

Conditions

Lupus Erythematosus, Systemic

Interventions

sifalimumab

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Gabor Illei, MD, Senior Director, Clinical Development
Organization
MedImmune, LLC

Study Officials

  • Gabor Illei, MD

    MedImmune LLC

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 20, 2011

First Posted

January 25, 2011

Study Start

March 31, 2011

Primary Completion

November 14, 2013

Study Completion

April 17, 2014

Last Updated

April 19, 2018

Results First Posted

July 11, 2016

Record last verified: 2018-03

Locations