NCT01282268

Brief Summary

To explore the efficacy, safety and tolerability of STX209 (arbaclofen) administered for the treatment of social withdrawal in adolescents and adults with fragile X syndrome (FXS)

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
125

participants targeted

Target at P25-P50 for phase_3

Geographic Reach
1 country

24 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 20, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

January 24, 2011

Completed
3 months until next milestone

Study Start

First participant enrolled

May 1, 2011

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2012

Completed
Last Updated

July 31, 2013

Status Verified

July 1, 2013

Enrollment Period

1.6 years

First QC Date

January 20, 2011

Last Update Submit

July 30, 2013

Conditions

Keywords

fragile X syndromeautism spectrum disorder

Outcome Measures

Primary Outcomes (1)

  • Aberrant Behavior Checklist - FXS Social Avoidance Subscale

    At 8 weeks of treatment

Study Arms (2)

Arbaclofen

ACTIVE COMPARATOR
Drug: arbaclofen

Placebo

PLACEBO COMPARATOR
Drug: placebo

Interventions

orally disintegrating tablet

Also known as: STX209
Arbaclofen

orally disintegrating tablet

Placebo

Eligibility Criteria

Age12 Years - 50 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Molecular documentation of the full FMR1 mutation
  • Current pharmacological treatment regimen has been stable for at least 4 weeks prior to Screening.
  • Subjects with a history of seizure disorder must currently be receiving treatment with antiepileptics and must have been seizure free for 6 months, or must be seizure free for 3 years if not currently receiving antiepileptics.
  • If the subject is already receiving stable non-pharmacologic educational, behavioral, and/or dietary interventions, participation in these programs must have been continuous during the 2 months prior to Screening

You may not qualify if:

  • Subjects with any condition, including alcohol and drug abuse, which might interfere with the conduct of the study, confound interpretation of the study results, or endanger their own well-being.
  • Subjects who plan to initiate or change pharmacologic or non-pharmacologic interventions during the course of the study.
  • Subjects who have taken another investigational drug within the last 30 days.
  • Subjects who are not able to take oral medications.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (24)

Southwest Autism Research & Resource Center

Phoenix, Arizona, 85006, United States

Location

Miller Children's Hospital Research Administration

Long Beach, California, 90806, United States

Location

University of California-Davis, M.I.N.D. Institute

Sacramento, California, 95817, United States

Location

Psychiatric Centers at San Diego

San Diego, California, 92108, United States

Location

University of Colorado Denver, Children's Hospital

Aurora, Colorado, 80045, United States

Location

University of Miami, Mailman Center for Child Development

Miami, Florida, 33136, United States

Location

Lake Mary Pediatrics

Orange City, Florida, 32763, United States

Location

Emory University School of Medicine

Decatur, Georgia, 30033, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Riley Hospital for Children

Indianapolis, Indiana, 46202, United States

Location

Kennedy Krieger Institute

Baltimore, Maryland, 21205, United States

Location

University of Massachusetts

Worcester, Massachusetts, 01605, United States

Location

University of Missouri, Thompson Research Center for Autism & Neurodevelpmental Disorders

Columbia, Missouri, 65211, United States

Location

Seaver Autism Center, Mount Sinai Medical Center

New York, New York, 10029, United States

Location

New York State Institute for Basic Research in Developmental Disabilities

Staten Island, New York, 10314, United States

Location

Duke University Clinical Research Unit

Durham, North Carolina, 27005, United States

Location

Akron Children's Hospital

Akron, Ohio, 44308, United States

Location

University of Oklahoma, Physician's Child Study Center

Oklahoma City, Oklahoma, 73117, United States

Location

Suburban Research Associates/Elwyn Genetics

Media, Pennsylvania, 19063, United States

Location

Vanderbilt Kennedy Center

Nashville, Tennessee, 37203, United States

Location

Texas Children's Hospital

Houston, Texas, 77030, United States

Location

Red Oaks Psychiatry Associates, P.A.

Houston, Texas, 77090, United States

Location

Road Runner Research

San Antonio, Texas, 78258, United States

Location

Seattle Children's Hospital

Seattle, Washington, 98101, United States

Location

MeSH Terms

Conditions

Fragile X SyndromeAutism Spectrum Disorder

Interventions

arbaclofen placarbil

Condition Hierarchy (Ancestors)

X-Linked Intellectual DisabilityIntellectual DisabilityNeurobehavioral ManifestationsNeurologic ManifestationsNervous System DiseasesSex Chromosome DisordersChromosome DisordersCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesGenetic Diseases, InbornGenetic Diseases, X-LinkedHeredodegenerative Disorders, Nervous SystemChild Development Disorders, PervasiveNeurodevelopmental DisordersMental Disorders

Study Officials

  • Paul Wang, M.D.

    Seaside Therapeutics, Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 20, 2011

First Posted

January 24, 2011

Study Start

May 1, 2011

Primary Completion

December 1, 2012

Last Updated

July 31, 2013

Record last verified: 2013-07

Locations