NCT01273064

Brief Summary

Placebo controlled, double-blind, multicenter study utilizing standard of care (SOC) treatment (ribavirin plus pegylated interferon) in combination with CTS-1027 in genotype 1 chronic Hepatitis C (HCV) patients who were null-responders to previous SOC therapy(ies). Null-responders are defined as patients who failed to achieve a greater than 2 log drop in HCV-RNA (Hepatitis C Ribonucleic acid, also known as "viral load") levels after 12 weeks of treatment (know as an "early virologic response", or EVR) during previous SOC therapy. If, during previous SOC treatment, a patient had a less than 2 log decline in HCV-RNA at Week 12 but greater than 2 log decline in HCV-RNA at any time from Week 12 to Week 24, that patient is not a null-responder, and is excluded from study participation. If, during previous SOC treatment, a Week 12 HCV-RNA was not obtained, the post Week 12 response must have been \< 2 log decline (and still HCV-RNA positive) in order for the patient to be defined as a null-responder. Patients will be screened and have up to 4 weeks to qualify for study entry. During this screening period, clinical and laboratory tests will be performed. At Week 0/Day 1, patients will undergo centralized, stratified (based on ethnicity), randomization to one of four treatment arms: SOC + one of three doses of CTS-1027 or SOC + placebo. Study treatment will last 24, 48, or 60 weeks, based on each patient's response to study treatment. SOC + placebo patients who do not show a virologic response after 12 weeks of therapy will be rolled onto SOC + 15mg CTS-1027, while maintaining the study blind.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
114

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2011

Shorter than P25 for phase_2

Geographic Reach
1 country

45 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 21, 2010

Completed
11 days until next milestone

Study Start

First participant enrolled

January 1, 2011

Completed
9 days until next milestone

First Posted

Study publicly available on registry

January 10, 2011

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2011

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2011

Completed
8 months until next milestone

Results Posted

Study results publicly available

May 30, 2012

Completed
Last Updated

June 11, 2012

Status Verified

June 1, 2012

Enrollment Period

8 months

First QC Date

December 21, 2010

Results QC Date

March 29, 2012

Last Update Submit

June 4, 2012

Conditions

Keywords

HCVNull Responders

Outcome Measures

Primary Outcomes (1)

  • Sustained Virologic Response

    Percent of patients that achieve a sustained virologic response (SVR) at Week 72 defined as HCV-RNA (Hepatitis C virus ribonucleic acid, also known as 'viral load') level below the quantification limit (BQL) at Week 72.

    Baseline and 24 weeks after the end of treatment (Week 72)

Secondary Outcomes (1)

  • Greater Than 2 Log Decline in HCV-RNA at Study Weeks 12, 24 and 48

    Baseline, and Study Weeks 12, 24, and 48

Study Arms (4)

CTS-1027 60 mg + ribavirin + peglyated interferon

EXPERIMENTAL

Standard of Care (ribavirin plus pegylated interferon) plus CTS-1027, 60 mg (supplied in a blinded kit containing two bottles of 30 mg tablets). One tablet from each of the CTS bottles is taken twice daily, for a total daily dose of 120 mg.

Drug: CTS-1027Drug: pegylated interferonDrug: Ribavirin

CTS-1027 30 mg + ribavirin + pegylated interferon

EXPERIMENTAL

Standard of Care (ribavirin plus pegylated interferon) plus CTS-1027 30 mg, supplied in a blinded kit containing one bottle of 30 mg tablets, and one bottle of placebo tablets (in order to maintain blind). One tablet from each of the bottles is taken twice daily, for a total daily dose of 60 mg of CTS-1027.

Drug: CTS-1027Drug: pegylated interferonDrug: RibavirinDrug: Placebo

CTS-1027 15 mg + ribavirin + pegylated interferon

EXPERIMENTAL

Standard of Care (ribavirin plus pegylated interferon) plus CTS-1027 15 mg (supplied in a blinded kit containing one bottle each of of 5 mg and 10 mg tablets). One tablet from each of the CTS bottles is taken twice daily, for a total daily dose of 30 mg.

Drug: CTS-1027Drug: pegylated interferonDrug: Ribavirin

placebo + ribavirin + pegylated interferon

ACTIVE COMPARATOR

Standard of Care (ribavirin plus pegylated interferon) plus placebo (supplied in a blinded kit containing two bottles of placebo tablets). One tablet is taken from each of the placebo bottles twice daily, for a total daily dose of 4 tablets.

Drug: pegylated interferonDrug: RibavirinDrug: Placebo

Interventions

Supplied in 30mg, 10mg, or 5mg tablets (depending on dose arm) taken twice daily for up to 48 weeks.

CTS-1027 15 mg + ribavirin + pegylated interferonCTS-1027 30 mg + ribavirin + pegylated interferonCTS-1027 60 mg + ribavirin + peglyated interferon

180 micrograms in 0.5 ml of solution subcutaneously (SQ), delivered in single use syringes administered once per week, for up to 48 weeks.

Also known as: Pegasys
CTS-1027 15 mg + ribavirin + pegylated interferonCTS-1027 30 mg + ribavirin + pegylated interferonCTS-1027 60 mg + ribavirin + peglyated interferonplacebo + ribavirin + pegylated interferon

200 mg capsules of ribavirn taken in two divided daily doses totaling 1000 mg (5 capsules) for patients weighing 75 kg or less, or 1200 mg (6 capsules) for patients weighing more than 75 kg

Also known as: Copegus
CTS-1027 15 mg + ribavirin + pegylated interferonCTS-1027 30 mg + ribavirin + pegylated interferonCTS-1027 60 mg + ribavirin + peglyated interferonplacebo + ribavirin + pegylated interferon

Tablets identical in appearance to CTS-1027 containing inactive ingredients. Placebo arm patients: Two tablets taken twice daily, for a total daily dose of four tablets. 30 mg CTS-1027 patients: One tablet taken twice daily, for a total daily dose of two tablets. One bottle of placebo is added to the 30mg kits in order to maintain the study blind (all patients recieve two-bottle kits of CTS-1027 and/or placebo).

CTS-1027 30 mg + ribavirin + pegylated interferonplacebo + ribavirin + pegylated interferon

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female patients of minimum adult legal age (according to local laws for signing the informed consent document), able to provide written informed consent, and understand and comply with the requirements of the study
  • HCV genotype 1 infected null responders to prior therapy comprised of pegylated interferon and ribavirin (standard of care, SOC) defined as:
  • Failure to achieve an early virologic response (\< 2 log decline in HCV-RNA by Week 12), or
  • If Week 12 HCV-RNA was not obtained, post Week 12 HCV-RNA response was \< 2 log decline
  • Screening HCV-RNA viral load of \> 5.0 log (i.e., \>100,000 IU/mL)
  • alpha-fetoprotein (AFP) less than or equal to 100 ng/mL
  • Hemoglobin greater than or equal to 12 g/dL for women and greater than or equal to 13 g/dL for men, hemoglobin A1c less than or equal to 7.5 %, platelet count greater than or equal to 90 x 10\^9/L, and white blood cell count greater than or equal to 1.5 x 10\^9/L
  • Thyroid Stimulating Hormone (TSH) within normal limits
  • In the opinion of the Principal Investigator, the patient met the 80%/80%/80% rule during the previous pegylated interferon and ribavirin therapy (i.e., received at least 80% of the pegylated interferon and ribavirin doses, at least 80% of the dose size, for at least 80% of the treatment duration)
  • Willingness to utilize two reliable forms of contraception (for both males and females of childbearing potential) from screening to at least six months after the completion of the study.

You may not qualify if:

  • \< 2 log decline in HCV-RNA at Week 12 but \> 2 log decline at any time from Week 12 to Week 24 during prior therapy with pegylated interferon and ribavirin (prior standard of care therapy)
  • Decompensated or severe liver disease defined by one or more of the following criteria:
  • Prothrombin time 4 seconds \> control or INR (international normalized ratio) \> 1.2
  • Total bilirubin ≥ 1.5 mg/dL or direct bilirubin ≥ 1 mg/dL
  • Serum albumin below normal limits
  • aspartate aminotransferase (AST) or alanine aminotransferase (ALT)\> 5 x upper limit of normal (ULN) at screening
  • Presence of ascites
  • Hepatic encephalopathy
  • Hepatocellular carcinoma (HCC) or suspicion of HCC clinically or on ultrasound (or other imaging techniques)
  • Clinically significant ocular findings such as retinopathy, cotton wool spots, optic nerve disorder, retinal hemorrhage, or other abnormality
  • Known history or presence of human immunodeficiency virus (HIV) infection
  • Co-infection with hepatitis B virus (HBV)
  • If female: pregnant, lactating, or positive serum or urine pregnancy test
  • Male partners of women who are currently pregnant
  • Renal impairment (creatinine \> 1.2 x ULN), serum creatinine clearance \< 50 mL/min, or hepatorenal syndrome with ascites
  • +15 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (45)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Southern California Liver Centers

Coronado, California, 92118, United States

Location

Scripps Clinic

La Jolla, California, 92037, United States

Location

Loma Linda University MC

Loma Linda, California, 92354, United States

Location

Huntington Medical Research Institute

Pasadena, California, 91105, United States

Location

Medical Associates Research Group

San Diego, California, 92123, United States

Location

UCSD

San Diego, California, 92161, United States

Location

University of Colorado Denver

Aurora, Colorado, 80045, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06520, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Atlanta Medical Center, Inc.

Atlanta, Georgia, 30309, United States

Location

Liver Center of Atlanta

Atlanta, Georgia, 30309, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Loyola University

Maywood, Illinois, 60153, United States

Location

Indiana University School of Medicine

Indianapolis, Indiana, 46201, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Louisville

Louisville, Kentucky, 40202, United States

Location

Tulane University Health Sciences Center

New Orleans, Louisiana, 70112, United States

Location

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

Location

Beth Israel Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

University of Massachusetts Memorial Medical Center

Worcester, Massachusetts, 01655, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202-2689, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

St. Louis University

St Louis, Missouri, 63104, United States

Location

Concorde Medical Group

New York, New York, 10016, United States

Location

New York University

New York, New York, 10016, United States

Location

Weill Medical College of Cornell

New York, New York, 10021, United States

Location

Columbia Presbyterian Medical Center

New York, New York, 10032, United States

Location

Einstein College of Medicine (Jacobi Medical Center)

The Bronx, New York, 10461, United States

Location

New York Medical College

Valhalla, New York, 10595, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Consultants for Clinical Research

Cincinnati, Ohio, 45219, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Albert Einstein Medical Center

Philadelphia, Pennsylvania, 19141, United States

Location

Baylor All Saints Medical Center

Fort Worth, Texas, 76104, United States

Location

University of Texas Medical Branch at Galveston

Galveston, Texas, 77555, United States

Location

Research Specialists of Texas

Houston, Texas, 77030, United States

Location

St. Luke's Episcopal Hospital

Houston, Texas, 77030, United States

Location

University of Texas HSC at Houston

Houston, Texas, 77030, United States

Location

VAMC Houston

Houston, Texas, 77030, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

Metropolitan Research Group Washington DC

Fairfax, Virginia, 22031, United States

Location

Liver Institute of Virginia

Newport News, Virginia, 23602, United States

Location

Virginia Commonwealth University (VCU)

Richmond, Virginia, 23298, United States

Location

Benaroya Research Institute at Virginia Mason

Seattle, Washington, 98101, United States

Location

MeSH Terms

Conditions

Hepatitis C

Interventions

peginterferon alfa-2aRibavirin

Condition Hierarchy (Ancestors)

Blood-Borne InfectionsCommunicable DiseasesInfectionsHepatitis, Viral, HumanVirus DiseasesFlaviviridae InfectionsRNA Virus InfectionsHepatitisLiver DiseasesDigestive System Diseases

Intervention Hierarchy (Ancestors)

RibonucleosidesNucleosidesNucleic Acids, Nucleotides, and Nucleosides

Limitations and Caveats

This study was terminated early after 3 reports of hyperbilirubinemia occurred(2 on 60mg bid and 1 on 30mg bid of CTS 1027). Two incidents were reported as part of an SAE. The risk/benefit ratio did not warrant further continuation of the study.

Results Point of Contact

Title
MiRa Huyghe, Vice President, Clinical Development
Organization
Conatus Pharmaceuticals Inc.

Study Officials

  • Erin Castelloe, MD

    Conatus Pharmaceuticals Inc.

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 21, 2010

First Posted

January 10, 2011

Study Start

January 1, 2011

Primary Completion

September 1, 2011

Study Completion

October 1, 2011

Last Updated

June 11, 2012

Results First Posted

May 30, 2012

Record last verified: 2012-06

Locations