NCT01243892

Brief Summary

This is a Phase IV, open label, case-controlled, observational study to evaluate the age-adjusted cumulative height velocity in pre-pubertal isolated growth hormone deficient (IGHD) and idiopathic short stature (ISS) participants receiving daily doses of somatropin (recombinant human growth hormone \[rhGH\]; Nutropin) using NuSpin device compared to historical controls from the national cooperative growth study (NCGS).

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
18

participants targeted

Target at below P25 for all trials

Timeline
Completed

Started Nov 2010

Shorter than P25 for all trials

Geographic Reach
1 country

14 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2010

Completed
16 days until next milestone

First Submitted

Initial submission to the registry

November 17, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

November 19, 2010

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2011

Completed
5.3 years until next milestone

Results Posted

Study results publicly available

December 1, 2016

Completed
Last Updated

December 1, 2016

Status Verified

October 1, 2016

Enrollment Period

9 months

First QC Date

November 17, 2010

Results QC Date

October 7, 2016

Last Update Submit

October 7, 2016

Conditions

Outcome Measures

Primary Outcomes (1)

  • Annualized Height Velocity in Response to rhGH Treatment Using the NuSpin Device After Two Years of Treatment

    The annualized height velocity (cm per year \[cm/yr\]) over 2 years was calculated as: \[(height in cm at t24 minus (-) height in cm at t0) divided by (date at t24 - date at t0)\] multiplied by 365.25, where, t0 is the baseline measurement visit and t24 is the 2-year measurement visit.

    Baseline up to Month 24 (Year 2)

Secondary Outcomes (2)

  • Annualized Height Velocity in Response to rhGH Treatment Using the NuSpin Device for First Year of Treatment

    Baseline up to Month 12 (Year 1)

  • Annualized Height Velocity in Response to rhGH Treatment Using the NuSpin Device During the Second Year of Therapy

    Month 12 to Month 24 (Year 1 to Year 2)

Study Arms (2)

Cohort 1: IGHD participants

Isolated growth hormone deficient (IGHD) participants who initiated somatropin (Deoxyribonucleic acid \[DNA\] origin) (recombinant human growth hormone \[rhGH\]) using the NuSpin device, will be observed for at least 2 years. The choice of initiation of NuSpin treatment and the treatment regimen will be as per treating physician's discretion, the study protocol does not enforce or specify any treatment regimen.

Device: NuSpinDrug: Somatropin

Cohort 2: ISS participants

Idiopathic short stature (ISS) participants who initiated somatropin (DNA origin) (rhGH) using the NuSpin device, will be observed for at least 2 years. The choice of initiation of NuSpin treatment and the treatment regimen will be as per treating physician's discretion, the study protocol does not enforce or specify any treatment regimen.

Device: NuSpinDrug: Somatropin

Interventions

NuSpinDEVICE

Device for administration of doses of somatropin.

Cohort 1: IGHD participantsCohort 2: ISS participants

Somatropin using either NuSpin or Nutropin AQ Pen, as per standard dosing.

Also known as: Nutropin AQ (Somatropin [DNA Origin] injection)
Cohort 1: IGHD participantsCohort 2: ISS participants

Eligibility Criteria

Age2 Years - 14 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)
Sampling MethodNon-Probability Sample
Study Population

Somatropin-naive pre-pubertal participants with growth hormone deficiency or ISS

You may qualify if:

  • Bone age less than or equal to (\</=) 8 years (females) or \</= 10 years (males) as determined by x-ray of the left hand and wrist obtained within six months before enrollment
  • Prepubertal males and females by physical exam
  • Naive to rhGH therapy
  • Diagnosis of IGHD or ISS by standard pharmacologic testing and no other discernable etiology for short stature
  • Height standard deviation score (Ht SDS) \</= -1.5 (\</= 5th percentile) for IGHD participants; Ht SDS \</= -2.25 (\</= 1.2 percentile) for ISS participants

You may not qualify if:

  • Short stature etiologies other than IGHD or ISS
  • Participants receiving chronic corticosteroid therapy (greater than \[\>\] 3 months) for other medical conditions
  • Participants with active malignancy or any other condition that the investigator believes would pose a significant hazard to the participant if rhGH were initiated
  • Females with turner syndrome
  • Any previous rhGH treatment
  • Participation in another simultaneous medical investigation or trial
  • Pediatric participants with closed epiphyses
  • Participants prescribed rhGH doses outside the variance of NCGS control participant dosing

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (14)

Unknown Facility

Birmingham, Alabama, 35233, United States

Location

Unknown Facility

Scottsdale, Arizona, 85258, United States

Location

Unknown Facility

Sacramento, California, 95819, United States

Location

Unknown Facility

San Diego, California, 92123, United States

Location

Unknown Facility

Greenwood Village, Colorado, 80111, United States

Location

Unknown Facility

Palm Bay, Florida, 32905, United States

Location

Unknown Facility

Pembrook Pines, Florida, 33028, United States

Location

Unknown Facility

Atlanta, Georgia, 30342, United States

Location

Unknown Facility

Wheaton, Illinois, 60187, United States

Location

Unknown Facility

Minneapolis, Minnesota, 55455, United States

Location

Unknown Facility

Mount Kisco, New York, 10549, United States

Location

Unknown Facility

New Rochelle, New York, 10801, United States

Location

Unknown Facility

Columbus, Ohio, 43235, United States

Location

Unknown Facility

Knoxville, Tennessee, 37916, United States

Location

MeSH Terms

Conditions

Dwarfism, Pituitary

Interventions

Human Growth HormoneGrowth HormoneInjections

Condition Hierarchy (Ancestors)

DwarfismBone Diseases, DevelopmentalBone DiseasesMusculoskeletal DiseasesBone Diseases, EndocrineHypopituitarismPituitary DiseasesHypothalamic DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesEndocrine System Diseases

Intervention Hierarchy (Ancestors)

Pituitary Hormones, AnteriorPituitary HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsPeptidesAmino Acids, Peptides, and ProteinsDrug Administration RoutesDrug TherapyTherapeutics

Limitations and Caveats

The study was terminated prematurely due to slow enrollment.

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • D. Aaron Davis, M.D.

    Genentech, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 17, 2010

First Posted

November 19, 2010

Study Start

November 1, 2010

Primary Completion

August 1, 2011

Study Completion

August 1, 2011

Last Updated

December 1, 2016

Results First Posted

December 1, 2016

Record last verified: 2016-10

Locations