NCT01193660

Brief Summary

This randomized control study is aimed to determine efficacy of umbilical cord blood and erythropoietin combination therapy for children with cerebral palsy.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
105

participants targeted

Target at P50-P75 for not_applicable

Timeline
Completed

Started May 2010

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2010

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

August 29, 2010

Completed
4 days until next milestone

First Posted

Study publicly available on registry

September 2, 2010

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2011

Completed
11 months until next milestone

Results Posted

Study results publicly available

March 1, 2012

Completed
Last Updated

November 24, 2020

Status Verified

November 1, 2020

Enrollment Period

11 months

First QC Date

August 29, 2010

Results QC Date

October 11, 2011

Last Update Submit

November 6, 2020

Conditions

Keywords

umbilical cord bloodstem cellcerebral palsy

Outcome Measures

Primary Outcomes (2)

  • Changes in Motor Performance

    GMPM (Gross Motor Performance Measure) as a standardized measurement tool for assessing quality of movement regarding 3 properties of 5 ones; alignment, coordination, dissociated movement, stability, and weight shift (range: 0\~100, Higher value means better motor quality). We reported changes of GMPM score between each assessment time points. Categories of outcome table are baseline and values of just subtracting the latter raw scores from the former ones.

    Baseline -1 month - 3 months - 6 months

  • Changes in Standardized Gross Motor Function

    GMFM (Gross Motor Function Measure) as a standardized measurement tool for assessing Gross Motor Function consisting of sub-scales; lying \& rolling, sitting, crawling \& kneeling, standing, walking, running \& jumping (range: 0\~100 , Higher value means better gross motor function). We reported changes of GMFM between each assessment time points. Categories of outcome table are baseline and values of just subtracting the latter raw scores from the former ones.

    Baseline - 1 month - 3 months - 6 months

Secondary Outcomes (9)

  • Changes in Cognitive Neurodevelopmental Outcome

    Baseline -1 month - 3 months - 6 months

  • Changes in Motor Neurodevelopmental Outcome

    Baseline - 1 month - 3 months - 6 months

  • Changes in Brain MRI

    Baseline - 6 months

  • Comparison of Changes in Brain Glucose Metabolism Using by Brain 18F-FDG PET: Increased and Decreased Areas of Brain Glucose Metabolism

    Baseline - 2 weeks

  • Changes in Functional Performance in Daily Activities

    Baseline -1 month - 3 months - 6 months

  • +4 more secondary outcomes

Study Arms (3)

Umbilical Cord Blood & Erythropoietin & Rehabilitation

EXPERIMENTAL

Allogenic umbilical cord blood infusion, erythropoietin injection \& active rehabilitation

Biological: Umbilical Cord Blood InfusionDrug: Erythropoietin InjectionOther: Active Rehabilitation

Erythropoietin & Rehabilitation

ACTIVE COMPARATOR

Erythropoietin injection, active rehabilitation

Drug: Erythropoietin InjectionOther: Active RehabilitationOther: Placebo Umbilical Cord Blood

Only Rehabilitation

PLACEBO COMPARATOR

Active rehabilitation

Other: Active RehabilitationOther: Placebo Umbilical Cord BloodOther: Placebo Erythropoietin

Interventions

The subjects will be undertaken allogeneic umbilical cord blood infusion (total nucleated cells \> 3x10\^7/kg) intravenously under non-myeloablative immunosuppression (maintaining blood level of cyclosporine as 100-200ng/mL for 1 month).

Also known as: Donated Umbilical Cord Blood Units from Affiliated Cord Blood Bank
Umbilical Cord Blood & Erythropoietin & Rehabilitation

Erythropoietin will be given as the schedule of twice a week for 4 weeks with the dosage of 500 IU/kg for 2 times intravenously and 250 IU/kg subcutaneously for 6 times.

Also known as: Brand name of Erythropoietin: Espogen (made by LG Life Science)
Erythropoietin & RehabilitationUmbilical Cord Blood & Erythropoietin & Rehabilitation

All subjects should participate in active rehabilitation. They received two physical and occupational therapy sessions per day. Post discharge, each participant continued to receive rehabilitation therapy at least 3 days per week for additional 5 months.

Erythropoietin & RehabilitationOnly RehabilitationUmbilical Cord Blood & Erythropoietin & Rehabilitation

Placebo Umbilical Cord Blood will be given except the Experimental arm. Placebo Umbilical Cord Blood was made using peripheral blood. Participants and Investigators maintained as blind.

Also known as: Placebo Umbilical Cord Blood that resembles cord blood in appearance was designed, : 1.5 to 3 ml of the subject's own blood was collected and mixed with 15 to 20 ml of albumin.
Erythropoietin & RehabilitationOnly Rehabilitation

Placebo Erythropoietin containing Normal Saline

Only Rehabilitation

Eligibility Criteria

Age10 Months - 10 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Known cerebral palsy
  • Willing to comply with all study procedure

You may not qualify if:

  • High risk of pneumonia or renal function deterioration after using of immunosuppressant
  • Presence of known genetic disease
  • Possibility of drug hypersensitivity which is related to this study remedy
  • History of previous cell therapy
  • Poor cooperation of guardian,including inactive attitude for rehabilitation
  • Intractable seizure disorder
  • Autism

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

CHA Bundang Medical Center

Seongnam-si, Gyeonggi-do, South Korea

Location

MeSH Terms

Conditions

Cerebral Palsy

Interventions

ErythropoietinAlbumins

Condition Hierarchy (Ancestors)

Brain Damage, ChronicBrain DiseasesCentral Nervous System DiseasesNervous System Diseases

Intervention Hierarchy (Ancestors)

Colony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Minyoung Kim, MD, PhD
Organization
CHA Bundang Medical Center, CHA University

Study Officials

  • Minyoung Kim, MD, PhD

    CHA University

    STUDY CHAIR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
not applicable
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 29, 2010

First Posted

September 2, 2010

Study Start

May 1, 2010

Primary Completion

April 1, 2011

Study Completion

April 1, 2011

Last Updated

November 24, 2020

Results First Posted

March 1, 2012

Record last verified: 2020-11

Locations