NCT01145859

Brief Summary

The first study with rivaroxaban in pediatric subjects is a Phase I study, where the pharmacokinetic/pharmacodynamic (PK/PD) profile of rivaroxaban will be investigated to confirm that the exposure is comparable to adults. This study is a single dose study with multiple PK/PD measurements in pediatric subjects at the end of their Venous Thromboembolism (VTE) treatment.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
59

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Nov 2010

Longer than P75 for phase_1

Geographic Reach
9 countries

34 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 16, 2010

Completed
1 day until next milestone

First Posted

Study publicly available on registry

June 17, 2010

Completed
5 months until next milestone

Study Start

First participant enrolled

November 1, 2010

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2015

Completed
Last Updated

August 6, 2015

Status Verified

August 1, 2015

Enrollment Period

4.7 years

First QC Date

June 16, 2010

Last Update Submit

August 5, 2015

Conditions

Keywords

Venous ThrombosisPediatrics

Outcome Measures

Primary Outcomes (2)

  • Pharmacokinetics parameters (AUC and Cmax)

    From Day 1 to Day 2

  • Pharmacodynamics parameters (PT, aPTT and anti-factor Xa)

    From Day 1 to Day 2

Secondary Outcomes (1)

  • Safety and tolerability of rivaroxaban in pediatric subjects

    Day 1, day 2 plus 7 days follow up

Study Arms (1)

Arm 1

EXPERIMENTAL
Drug: Rivaroxaban (Xarelto, BAY59-7939)

Interventions

Weight adjusted dose with equivalent exposure compared to 10 mg or 20 mg doses in adults

Arm 1

Eligibility Criteria

Age6 Months - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Pediatric subjects \> 6 months and \< 18 years of age at the time of administration of study drug.
  • Patients who have completed treatment of VTE, but are considered to have risk for recurrence of VTE

You may not qualify if:

  • Any major or clinically relevant bleeding during prior VTE treatment
  • Abnormal coagulation tests within 7 days prior to study drug administration
  • Severe renal impairment
  • Planned invasive procedures prior to or after 24 hours of study drug administration

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

Unknown Facility

Little Rock, Arkansas, 72202-3500, United States

Location

Unknown Facility

Los Angeles, California, 90027-6089, United States

Location

Unknown Facility

Los Angeles, California, 90095, United States

Location

Unknown Facility

Orange, California, 92868, United States

Location

Unknown Facility

Gainesville, Florida, 32610, United States

Location

Unknown Facility

St. Petersburg, Florida, 33701, United States

Location

Unknown Facility

Chicago, Illinois, 60611, United States

Location

Unknown Facility

Indianapolis, Indiana, 46202, United States

Location

Unknown Facility

Indianapolis, Indiana, 46260, United States

Location

Unknown Facility

Detroit, Michigan, 48201-2196, United States

Location

Unknown Facility

New Hyde Park, New York, 11040, United States

Location

Unknown Facility

Chapel Hill, North Carolina, 27514, United States

Location

Unknown Facility

Durham, North Carolina, 27710, United States

Location

Unknown Facility

Cleveland, Ohio, 44106-6007, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19104, United States

Location

Unknown Facility

Pittsburgh, Pennsylvania, 15224, United States

Location

Unknown Facility

Brisbane, Queensland, 4029, Australia

Location

Unknown Facility

Parkville, Victoria, 3052, Australia

Location

Unknown Facility

Vienna, Vienna, 1090, Austria

Location

Unknown Facility

Linz, 4020, Austria

Location

Unknown Facility

Edmonton, Alberta, T6G 1C9, Canada

Location

Unknown Facility

Hamilton, Ontario, L8N 3Z5, Canada

Location

Unknown Facility

Toronto, Ontario, M5G 1X8, Canada

Location

Unknown Facility

Clermont-Ferrand, 63003, France

Location

Unknown Facility

Montpellier, 34059, France

Location

Unknown Facility

Paris, 75015, France

Location

Unknown Facility

Toulouse, 31059, France

Location

Unknown Facility

Lübeck, Schleswig-Holstein, 23538, Germany

Location

Unknown Facility

Crumlin, Dublin, 12, Ireland

Location

Unknown Facility

Jerusalem, 9112001, Israel

Location

Unknown Facility

Tel Litwinsky, 5262000, Israel

Location

Unknown Facility

Genova, 16147, Italy

Location

Unknown Facility

Milan, 20122, Italy

Location

Unknown Facility

Pavia, 27100, Italy

Location

Unknown Facility

Torino, 10126, Italy

Location

Unknown Facility

Basel, Canton of Basel-City, 4056, Switzerland

Location

Related Publications (3)

  • Willmann S, Thelen K, Kubitza D, Lensing AWA, Frede M, Coboeken K, Stampfuss J, Burghaus R, Muck W, Lippert J. Pharmacokinetics of rivaroxaban in children using physiologically based and population pharmacokinetic modelling: an EINSTEIN-Jr phase I study. Thromb J. 2018 Dec 4;16:32. doi: 10.1186/s12959-018-0185-1. eCollection 2018.

  • Kubitza D, Willmann S, Becka M, Thelen K, Young G, Brandao LR, Monagle P, Male C, Chan A, Kennet G, Martinelli I, Saracco P, Lensing AWA. Exploratory evaluation of pharmacodynamics, pharmacokinetics and safety of rivaroxaban in children and adolescents: an EINSTEIN-Jr phase I study. Thromb J. 2018 Dec 4;16:31. doi: 10.1186/s12959-018-0186-0. eCollection 2018.

  • Willmann S, Becker C, Burghaus R, Coboeken K, Edginton A, Lippert J, Siegmund HU, Thelen K, Muck W. Development of a paediatric population-based model of the pharmacokinetics of rivaroxaban. Clin Pharmacokinet. 2014 Jan;53(1):89-102. doi: 10.1007/s40262-013-0090-5.

MeSH Terms

Conditions

Venous Thrombosis

Interventions

Rivaroxaban

Condition Hierarchy (Ancestors)

ThrombosisEmbolism and ThrombosisVascular DiseasesCardiovascular Diseases

Intervention Hierarchy (Ancestors)

ThiophenesSulfur CompoundsOrganic ChemicalsMorpholinesOxazinesHeterocyclic Compounds, 1-RingHeterocyclic Compounds

Study Officials

  • Bayer Study Director

    Bayer

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 16, 2010

First Posted

June 17, 2010

Study Start

November 1, 2010

Primary Completion

July 1, 2015

Study Completion

July 1, 2015

Last Updated

August 6, 2015

Record last verified: 2015-08

Locations