NCT01143246

Brief Summary

This study is designed to evaluate the efficacy and safety of intravenous terlipressin versus placebo for the treatment of type 1 hepatorenal syndrome (HRS) in participants receiving standard of care albumin therapy.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
196

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Oct 2010

Typical duration for phase_3

Geographic Reach
2 countries

73 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 11, 2010

Completed
3 days until next milestone

First Posted

Study publicly available on registry

June 14, 2010

Completed
4 months until next milestone

Study Start

First participant enrolled

October 11, 2010

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2013

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 10, 2013

Completed
9.6 years until next milestone

Results Posted

Study results publicly available

November 29, 2022

Completed
Last Updated

November 29, 2022

Status Verified

November 1, 2022

Enrollment Period

2.3 years

First QC Date

June 11, 2010

Results QC Date

July 22, 2022

Last Update Submit

November 4, 2022

Conditions

Keywords

Hepatorenal syndromeRenal failureCirrhosisAlcoholic hepatitisAscites

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Confirmed Hepatorenal Syndrome (HRS) Reversal

    Confirmed HRS Reversal: The percentage of participants with two serum creatinine (SCr) values of ≤ 1.5 mg/dL at least 48 hours apart, on treatment, and without intervening renal replacement therapy or liver transplant.

    within 14 days

Secondary Outcomes (4)

  • Percentage of Participants With HRS Reversal

    within 14 days

  • Percentage of Participants With Transplant-free Survival

    Up to 90 days

  • Percentage of Participants With Overall Survival

    Up to 90 days

  • Percentage of Participants With Serious Adverse Events

    Up to 30 days post treatment (within 44 days)

Study Arms (2)

Terlipressin

EXPERIMENTAL

Participants receive terlipressin intravenously as a bolus injection, followed by a saline flush. Dose, duration, retreatment and/or discontinuation may be modified by the investigator, per protocol.

Drug: Terlipressin

Placebo

PLACEBO COMPARATOR

Participants receive matching placebo intravenously as a bolus injection, followed by a saline flush. Dose, duration, retreatment and/or discontinuation may be modified by the investigator, per protocol.

Drug: Placebo

Interventions

Each 6 mL vial contains 1 mg lyophilized terlipressin acetate and 10 mg mannitol in sterile 0.9% sodium chloride solution.

Also known as: Lucassin®
Terlipressin

11 mg mannitol reconstituted with 5 ml of sterile 0.9% sodium chloride solution.

Also known as: Saline
Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Written informed consent by subject or legally authorized representative
  • At least 18 years of age
  • Cirrhosis and ascites
  • Rapidly progressive reduction in renal function characterized by:
  • Serum creatinine (SCr) ≥ 2.5 mg/dL
  • Doubling of SCr within 2 weeks (or for observations of shorter duration, SCr values over time meeting slope-based criteria for proportional increases likely to be representative of at least a doubling within 2 weeks
  • No sustained improvement in renal function (\< 20% decrease in SCr and SCr ≥ 2.25 mg/dL) 48 hours after both diuretic withdrawal and the beginning of plasma volume expansion with albumin:
  • Note: Albumin doses recommended by the International Ascites Club (IAC) are 1 g/kg on the first day (Maximum 100 g) and 20 - 40 g/day thereafter as clinically indicated. It is recommended (if clinically appropriate) that the albumin dose is kept constant during the study drug administration period.
  • Note: The qualifying SCr value is the SCr value at least 48 hrs after both diuretic withdrawal (if applicable) and the beginning of albumin fluid challenge. The qualifying SCr value must be ≥ 2.25 mg/dL AND at least 80% of the diagnostic (pre-fluid challenge) SCr value.

You may not qualify if:

  • SCr \> 7 mg/dL
  • Shock Note: Hypotension (Mean Arterial Pressure \< 70 mm Hg or a decrease \> 40 mm Hg in systolic blood pressure from baseline) with evidence of hypoperfusion abnormalities despite adequate fluid resuscitation.
  • Sepsis or systemic inflammatory response syndrome (SIRS)
  • Note: SIRS: Presence of 2 or more of the following findings:
  • Temperature \> 38°C or \< 36°C; heart rate \> 90/min; respiratory rate of \> 20/min or a PaCO2 of \< 32 mm Hg; white blood cell count of \> 12,000 cells/µL or \< 4,000/ µL.
  • Note: Sepsis: Documented infection and systemic inflammatory response syndrome.
  • \< 2 days anti-infective therapy for documented or suspected infection
  • Proteinuria \> 500 mg/day
  • Hematuria or microhematuria (\> 50 red blood cells per high power field)
  • Clinically significant casts on urinalysis, including granular casts Note: Urine sediment examination is required to exclude presence of granular casts and other clinically significant casts \[e.g., red blood cell (RBC) casts\].
  • Evidence of intrinsic or parenchymal renal disease (including acute tubular necrosis)
  • Obstructive uropathy or other renal pathology on ultrasound or other medical imaging
  • Current or recent treatment (within 4 weeks) with nephrotoxic drugs, e.g., aminoglycosides, nonsteroidal anti-inflammatory drugs (NSAID) Note: Up to 3 doses of an NSAID within the prior month (prescription or over the counter) is acceptable Note: Use of short-term (\< 2 weeks) oral neomycin for acute encephalopathy is acceptable.
  • Current or recent (within 4 weeks) renal replacement therapy
  • Superimposed acute liver failure/injury due to factors other than alcoholic hepatitis, including acute viral hepatitis, drugs, medications (e.g., acetaminophen), or other toxins (e.g., mushroom \[Amanita\] poisoning)
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (73)

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Banner Good Samaritan Medical Center/Liver Disease Center

Phoenix, Arizona, 85006, United States

Location

Mayo Clinic Arizona

Phoenix, Arizona, 85054, United States

Location

University of Arizona Medical Center South Campus

Tucson, Arizona, 85713, United States

Location

University of Arizona Liver Research Institute

Tucson, Arizona, 85724, United States

Location

Arrowhead Regional Medical Center

Colton, California, 92324, United States

Location

SCTI Research Foundation

Coronado, California, 92118, United States

Location

Scripps Clinic

La Jolla, California, 92037, United States

Location

USC University Hospital

Los Angeles, California, 90033, United States

Location

UC Davis Medical Center

Sacramento, California, 95817, United States

Location

Veteran's Administration Medical Center

San Diego, California, 92161, United States

Location

California Pacific Medical Center

San Francisco, California, 94115, United States

Location

University of Colorado Denver

Aurora, Colorado, 80045, United States

Location

Hartford Hospital

Hartford, Connecticut, 06102, United States

Location

Yale University School of Medicine

New Haven, Connecticut, 06520, United States

Location

Georgetown University Hospital

Washington D.C., District of Columbia, 20007, United States

Location

Mayo Clinic

Jacksonville, Florida, 32224, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Emory University Hospital

Atlanta, Georgia, 30322, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

University of Chicago

Chicago, Illinois, 60637, United States

Location

Loyola University Medical Center

Maywood, Illinois, 60153, United States

Location

Indiana University Health - University Hospital

Indianapolis, Indiana, 46202, United States

Location

Iowa City VA Health Care System

Iowa City, Iowa, 52246, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

University of Kentucky Chandler Medical Center

Lexington, Kentucky, 40536, United States

Location

University of Louisville

Louisville, Kentucky, 40202, United States

Location

Tulane Medical Center

New Orleans, Louisiana, 70112, United States

Location

University of Maryland

Baltimore, Maryland, 21201, United States

Location

Beth Lsrael Deaconess Medical Center

Boston, Massachusetts, 02215, United States

Location

Lahey Clinic Medical Center

Burlington, Massachusetts, 01805, United States

Location

University of Massachusetts Medical Center

Worcester, Massachusetts, 01655, United States

Location

Henry Ford Hospital

Detroit, Michigan, 48202, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55414, United States

Location

Saint Luke's Hospital

Kansas City, Missouri, 64111, United States

Location

Saint Louis University

St Louis, Missouri, 63110, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

University of Nebraska Medical Center

Omaha, Nebraska, 68198, United States

Location

Bellevue Hospital

New York, New York, 10016, United States

Location

NYU Langhorn Medical Center

New York, New York, 10016, United States

Location

Mount Sinai Medical Center

New York, New York, 10029, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

New York Medical College/Westchester Medical Center

Valhalla, New York, 10595, United States

Location

Carolinas Medical Center

Charlotte, North Carolina, 28203, United States

Location

University of Cincinnati, Internal Medicine-Digestive Diseases

Cincinnati, Ohio, 45267, United States

Location

Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

INTEGRIS Baptist Medical Center

Oklahoma City, Oklahoma, 73112, United States

Location

Orgeon Health & Science University

Portland, Oregon, 97239, United States

Location

Drexel University College of Medicine

Philadelphia, Pennsylvania, 19102, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Temple University Hospital

Philadelphia, Pennsylvania, 19140, United States

Location

Albert Einstein Medical Center

Philadelphia, Pennsylvania, 19141, United States

Location

VA Pittsburgh Healthcare System

Pittsburgh, Pennsylvania, 15240, United States

Location

WJB Dorn VA Medical Center

Columbia, South Carolina, 29209, United States

Location

Vanderbilt Medical Center

Nashville, Tennessee, 37212, United States

Location

Dallas VA Medical Center

Dallas, Texas, 75216, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

UT Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Baylor All Saints Medical Center

Fort Worth, Texas, 76104, United States

Location

The University of Texas Medical Branch at Galveston

Galveston, Texas, 77555, United States

Location

St. Luke's Advanced Liver Therapies

Houston, Texas, 77030, United States

Location

The Methodist Hospital

Houston, Texas, 77030, United States

Location

University of Texas Health Science Center at Houston - Memorial Hermann Hospital

Houston, Texas, 77030, United States

Location

Methodist Specialty Transplant Hospital Lab

San Antonio, Texas, 78229, United States

Location

The University of Texas Health Science Center at San Antonio

San Antonio, Texas, 78229, United States

Location

University of Texas Health Science Center

San Antonio, Texas, 78229, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

McGuire DVAMC

Richmond, Virginia, 23249, United States

Location

Virginia Commonwealth University Health System

Richmond, Virginia, 23298, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

University of Wisconsin

Madison, Wisconsin, 53792, United States

Location

Toronto General Hospital

Toronto, Ontario, M5G 2C4, Canada

Location

CHUM, Hopital St-Luc

Montreal, Quebec, H2X 3J4, Canada

Location

Related Publications (7)

  • Bajaj JS, Kwo P, Pappas SC, O'Leary JG, Jamil K, Cardoza S, Wong F. Bradycardia and Other Arrhythmias in Patients With Hepatorenal Syndrome-Acute Kidney Injury Following Terlipressin Treatment: A Pooled Analysis of Three North American Phase III Clinical Studies. Aliment Pharmacol Ther. 2025 Dec;62(11-12):1192-1201. doi: 10.1111/apt.70297. Epub 2025 Jul 24.

  • Mujtaba MA, Gamilla-Crudo AK, Merwat SN, Hussain SA, Kueht M, Karim A, Khattak MW, Rooney PJ, Jamil K. Terlipressin in combination with albumin as a therapy for hepatorenal syndrome in patients aged 65 years or older. Ann Hepatol. 2023 Sep-Oct;28(5):101126. doi: 10.1016/j.aohep.2023.101126. Epub 2023 Jun 10.

  • Velez JCQ, Wong F, Reddy KR, Sanyal AJ, Vargas HE, Curry MP, Gonzalez SA, Pappas SC, Jamil K. The Effect of Terlipressin on Renal Replacement Therapy in Patients with Hepatorenal Syndrome. Kidney360. 2023 Aug 1;4(8):1030-1038. doi: 10.34067/KID.0000000000000132. Epub 2023 May 5.

  • Curry MP, Vargas HE, Befeler AS, Pyrsopoulos NT, Patwardhan VR, Jamil K. Early treatment with terlipressin in patients with hepatorenal syndrome yields improved clinical outcomes in North American studies. Hepatol Commun. 2023 Jan 3;7(1):e1307. doi: 10.1097/01.HC9.0000897228.91307.0c. eCollection 2023 Jan 1.

  • Sanyal AJ, Boyer TD, Frederick RT, Wong F, Rossaro L, Araya V, Vargas HE, Reddy KR, Pappas SC, Teuber P, Escalante S, Jamil K. Reversal of hepatorenal syndrome type 1 with terlipressin plus albumin vs. placebo plus albumin in a pooled analysis of the OT-0401 and REVERSE randomised clinical studies. Aliment Pharmacol Ther. 2017 Jun;45(11):1390-1402. doi: 10.1111/apt.14052. Epub 2017 Mar 29.

  • Wong F, Pappas SC, Boyer TD, Sanyal AJ, Bajaj JS, Escalante S, Jamil K; REVERSE Investigators. Terlipressin Improves Renal Function and Reverses Hepatorenal Syndrome in Patients With Systemic Inflammatory Response Syndrome. Clin Gastroenterol Hepatol. 2017 Feb;15(2):266-272.e1. doi: 10.1016/j.cgh.2016.07.016. Epub 2016 Jul 25.

  • Boyer TD, Sanyal AJ, Wong F, Frederick RT, Lake JR, O'Leary JG, Ganger D, Jamil K, Pappas SC; REVERSE Study Investigators. Terlipressin Plus Albumin Is More Effective Than Albumin Alone in Improving Renal Function in Patients With Cirrhosis and Hepatorenal Syndrome Type 1. Gastroenterology. 2016 Jun;150(7):1579-1589.e2. doi: 10.1053/j.gastro.2016.02.026. Epub 2016 Feb 16.

MeSH Terms

Conditions

Hepatorenal SyndromeRenal InsufficiencyFibrosisHepatitis, AlcoholicAscites

Interventions

TerlipressinSodium Chloride

Condition Hierarchy (Ancestors)

Liver DiseasesDigestive System DiseasesKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesPathologic ProcessesPathological Conditions, Signs and SymptomsHepatitisLiver Diseases, AlcoholicAlcohol-Induced DisordersAlcohol-Related DisordersSubstance-Related DisordersChemically-Induced Disorders

Intervention Hierarchy (Ancestors)

LypressinVasopressinsPituitary Hormones, PosteriorPituitary HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsNeuropeptidesPeptidesAmino Acids, Peptides, and ProteinsOligopeptidesNerve Tissue ProteinsProteinsChloridesHydrochloric AcidChlorine CompoundsInorganic ChemicalsSodium Compounds

Results Point of Contact

Title
Medical Information Call Center
Organization
Mallinckrodt

Study Officials

  • Clinical Team Leader

    Mallinckrodt

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 11, 2010

First Posted

June 14, 2010

Study Start

October 11, 2010

Primary Completion

February 1, 2013

Study Completion

May 10, 2013

Last Updated

November 29, 2022

Results First Posted

November 29, 2022

Record last verified: 2022-11

Data Sharing

IPD Sharing
Will not share

Discussion of statistical endpoints and analysis are included in manuscripts. Summary aggregate (basic) results (including adverse events information) and the study protocol are made available on clinicaltrials.gov (NCT02770716) when required by regulation. Individual de-identified patient data will not be disclosed. Requests for additional information should be directed to the company at medinfo@mnk.com.

Locations