NCT00865228

Brief Summary

The purpose of this study is to determine the role of time of dosing on the lipid-lowering effects of lapaquistat acetate, once daily (QD) or twice daily (BID), in subjects with hypercholesterolemia.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
224

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Jul 2007

Shorter than P25 for phase_2

Geographic Reach
1 country

22 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2007

Completed
4 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 1, 2007

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2007

Completed
1.4 years until next milestone

First Submitted

Initial submission to the registry

March 18, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 19, 2009

Completed
Last Updated

May 24, 2012

Status Verified

May 1, 2012

Enrollment Period

4 months

First QC Date

March 18, 2009

Last Update Submit

May 23, 2012

Conditions

Keywords

HyperlipidemiaDyslipidemiaHigh CholesterolDrug Therapy

Outcome Measures

Primary Outcomes (1)

  • Percent change from Baseline in the Fasting Plasma Low-Density Lipoprotein Cholesterol concentration

    Week 6

Secondary Outcomes (11)

  • Change from Baseline in Total Cholesterol

    Week 6

  • Percent change from Baseline in apolipoprotein B

    Week 6

  • Percent change from Baseline in apolipoprotein A1

    Week 6

  • Change from Baseline in Triglycerides

    Week 6

  • Percent change from Baseline in High-Density Lipoprotein Cholesterol

    Week 6

  • +6 more secondary outcomes

Study Arms (4)

Lapaquistat Acetate 100 mg QD (morning)

EXPERIMENTAL
Drug: Lapaquistat acetate

Lapaquistat Acetate 100 mg QD (evening)

EXPERIMENTAL
Drug: Lapaquistat acetate

Lapaquistat Acetate 50 mg BID

EXPERIMENTAL
Drug: Lapaquistat acetate

Placebo BID

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Lapaquistat acetate 100 mg, tablets, orally, once daily in the morning and Lapaquistat acetate placebo-matching tablets, orally, once daily in the evening for up to six weeks.

Also known as: TAK-475
Lapaquistat Acetate 100 mg QD (morning)

Lapaquistat acetate placebo-matching tablets, orally, once daily in the morning and Lapaquistat acetate placebo-matching tablets, orally, once daily in the evening for up to six weeks.

Placebo BID

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Females of childbearing potential who are sexually active must agree to use a medically accepted means of contraception, and can neither be pregnant nor lactating from Screening throughout the duration of the study.
  • Has prior to Randomization a mean low-density lipoprotein cholesterol greater than or equal to 130 mg/dL and less than or equal to 220 mg/dL for 2 consecutive samples.
  • Has prior to Randomization mean triglycerides less than 400 mg/dL for 2 consecutive samples.
  • Is willing and able to comply with a standardized, therapeutic lifestyle change diet or equivalent.

You may not qualify if:

  • Has an alanine aminotransferase or aspartate aminotransferase level greater than 2 times the upper limit of normal during the screening period.
  • Has a serum creatinine greater than133 mmol/L during the screening period.
  • Has a creatine phosphokinase greater than 3 times the upper limit of normal, identified during the screening period.
  • Has active liver disease or jaundice.
  • Has a history of cancer that has been in remission for less than 5 years prior to the first dose of study medication.
  • Has an endocrine disorder, such as Cushing syndrome, hyperthyroidism, or inappropriately treated hypothyroidism, affecting lipid metabolism.
  • Has a history of myocardial infarction, angina pectoris, unstable angina, transient ischemic attacks, cerebrovascular accident, peripheral vascular disease, abdomin al aorticaneurysm, coronary angioplasty, coronary or peripheral arterial surgery or multiple risk factors that confer a 10-year risk for cardiovascular disease greater than 20% based on Framingham risk scoring.
  • Has a positive hepatitis B surface antigen, or antibody to hepatitis C virus, as determined by medical history and/or subject's verbal report.
  • Has a positive human immunodeficiency virus status or is taking antiretroviral medications, as determined by medical history and/or subject's verbal report.
  • Has received any investigational compound within 30 days prior to screening Visit 1, or is currently participating in another investigational study.
  • Has received lapaquistat acetate in a previous clinical study or as a therapeutic agent.
  • Has a history or presence of clinically significant food allergy that would prevent adherence to the specialized diet.
  • Has a known heterozygous or homozygous familial hypercholesterolemia or known type III hyperlipoproteinemia.
  • Has fibromyalgia, myopathy, rhabdomyolysis, or unexplained muscle pain.
  • Has uncontrolled hypertension despite treatment at Screening Visit 1.
  • +32 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Unknown Facility

Long Beach, California, United States

Location

Unknown Facility

Sacramento, California, United States

Location

Unknown Facility

San Diego, California, United States

Location

Unknown Facility

Hollywood, Florida, United States

Location

Unknown Facility

Jacksonville, Florida, United States

Location

Unknown Facility

New Port Richey, Florida, United States

Location

Unknown Facility

Chicago, Illinois, United States

Location

Unknown Facility

Wichita, Kansas, United States

Location

Unknown Facility

Louisville, Kentucky, United States

Location

Unknown Facility

Margate City, New Jersey, United States

Location

Unknown Facility

Charlotte, North Carolina, United States

Location

Unknown Facility

Raleigh, North Carolina, United States

Location

Unknown Facility

Statesville, North Carolina, United States

Location

Unknown Facility

Wilmington, North Carolina, United States

Location

Unknown Facility

Winston-Salem, North Carolina, United States

Location

Unknown Facility

Medford, Oregon, United States

Location

Unknown Facility

Perkasie, Pennsylvania, United States

Location

Unknown Facility

Sellerville, Pennsylvania, United States

Location

Unknown Facility

Bristol, Tennessee, United States

Location

Unknown Facility

Norfolk, Virginia, United States

Location

Unknown Facility

Richmond, Virginia, United States

Location

Unknown Facility

Madison, Wisconsin, United States

Location

MeSH Terms

Conditions

HypercholesterolemiaHyperlipidemiasDyslipidemias

Interventions

1-((1-(3-acetoxy-2,2-dimethylpropyl)-7-chloro-5-(2,3-dimethoxyphenyl)-2-oxo-1,2,3,5-tetrahydro-4,1-benzoxazepin-3-yl)acetyl)piperidine-4-acetic acid

Condition Hierarchy (Ancestors)

Lipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Study Officials

  • VP, Clinical Science

    Takeda

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 18, 2009

First Posted

March 19, 2009

Study Start

July 1, 2007

Primary Completion

November 1, 2007

Study Completion

November 1, 2007

Last Updated

May 24, 2012

Record last verified: 2012-05

Locations