NCT00848107

Brief Summary

This open label extension trial will allow ongoing treatment of subjects who participated in the randomized controlled trials, and will provide long term information about the safety of treprostinil diethanolamine SR in subjects with SSc and digital ulcers.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
115

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Sep 2009

Geographic Reach
3 countries

26 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 16, 2009

Completed
4 days until next milestone

First Posted

Study publicly available on registry

February 20, 2009

Completed
6 months until next milestone

Study Start

First participant enrolled

September 1, 2009

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2011

Completed
2.4 years until next milestone

Results Posted

Study results publicly available

February 7, 2014

Completed
Last Updated

June 18, 2024

Status Verified

January 1, 2014

Enrollment Period

2 years

First QC Date

February 16, 2009

Results QC Date

July 12, 2013

Last Update Submit

May 24, 2024

Conditions

Keywords

systemic sclerosissclerodermadigital ulcersvasculopathy

Outcome Measures

Primary Outcomes (3)

  • Net Ulcer Burden- Mean Change From Time of Study Entry for Each Scheduled Visit Assessment

    Net ulcer burden at any given assessment was defined as the number of "new" or "active" ulcers at that assessment, plus the number of "indeterminate" ulcers at that assessment that had previously been classified as either "active" or "new" at any earlier assessment during the study. The mean change in net ulcer burden from time of study entry was summarized for each scheduled visit assessment.

    Baseline and Months 1, 3, 6, 9, 12, and 18

  • Total Ulcer Number- Mean Change From Time of Study Entry for Each Scheduled Visit Assessment

    The total ulcer number includes all ulcers designated as "active", "indeterminate", or "new" for a given visit. The mean change in the total number of ulcers present from time of study entry was summarized for each scheduled visit assessment.

    Baseline and Months 1, 3, 6, 9, 12, and 18

  • Formation of New Ulcers

    The number and percentage of subjects who developed new ulcers during the study were summarized.

    18 months (or last study visit)

Secondary Outcomes (2)

  • Patient Function and QOL Measure: Scleroderma Health Assessments Questionnaire (SHAQ)- Mean Change From Study Entry in SHAQ Component Scores at Each Scheduled Assessment

    Baseline and Months 1, 3, 6, and 12

  • Patient Function and Quality of Life Measure: Cochin Hand Function Scale (CHFS)-Mean Change From Study Entry in CHFS Score at Each Scheduled Assessment

    Baseline and Months 1, 3, 6, and 12

Study Arms (1)

Treprostinil

EXPERIMENTAL

Treprostinil diethanolamine sustained release tablet initiated at 0.25 mg and titrated up to a maximum dose of 16 mg BID or the individual's maximum tolerated dose (MTD).

Drug: treprostinil diethanolamine

Interventions

sustained release tablet; BID dosing; up to 16 mg BID

Treprostinil

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Eligible subjects who completed assessments for the final visit of the previous TDE-DU-201 controlled trial and who signed appropriate informed consent were eligible to enroll in this extension study.
  • If a female of childbearing potential, the subject must have agreed to continue practicing an acceptable method of birth control (i.e., surgical sterilization, approved hormonal contraceptives, barrier methods \[such as a condom or diaphragm\] used with a spermicide, or an intrauterine device).

You may not qualify if:

  • Have had any change in clinical status that, in the opinion of the Investigator, would pose a safety risk for participation in this extension study;
  • Have been found to be unable to complete study assessments in the previous controlled trial;
  • Have prematurely discontinued study drug during the previous study due to clinical worsening or treatment related adverse events.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (26)

University of Alabama - Birmingham - Arthritis Clinical Intervention Program

Birmingham, Alabama, 35294-7201, United States

Location

Mayo Clinic Scottsdale

Scottsdale, Arizona, 85259, United States

Location

UCLA

Los Angeles, California, 90095-1670, United States

Location

Barbara Davis Centre

Aurora, Colorado, 80045, United States

Location

University of Connecticut Health Center

Farmington, Connecticut, 06030-1310, United States

Location

Georgetown University - Dept. of Medicine/Rheumatology

Washington D.C., District of Columbia, 20007, United States

Location

Northwestern University - Feinberg School of Medicine

Chicago, Illinois, 60611, United States

Location

Johns Hopkins University - Division of Rheumatology

Baltimore, Maryland, 21224, United States

Location

Boston University School of Medicine

Boston, Massachusetts, 02118-2526, United States

Location

University of Michigan - Scleroderma Program

Ann Arbor, Michigan, 48106, United States

Location

University of Minnesota

Minneapolis, Minnesota, 55455, United States

Location

UMDNJ Clinical Research Center

New Brunswick, New Jersey, 08903, United States

Location

North Shore - LIJ Health System

Lake Success, New York, 11042, United States

Location

The Hospital for Special Surgery

New York, New York, 10021, United States

Location

The Cleveland Clinic Foundation

Cleveland, Ohio, 44195, United States

Location

University of Toledo

Toledo, Ohio, 43614, United States

Location

University of Pittsburgh

Pittsburgh, Pennsylvania, 15261, United States

Location

Medical University of South Carolina

Charleston, South Carolina, 29425-8900, United States

Location

University of Texas - Houston

Houston, Texas, 77030, United States

Location

University of Utah

Salt Lake City, Utah, 84132, United States

Location

Virginia Mason Medical

Seattle, Washington, 98101, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

St Joseph's Health Care

London, Ontario, N6A 4V2, Canada

Location

Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

Royal Free Hospital - Center for Rheumatology

London, NW3 2QG, United Kingdom

Location

Salford Royal Hospital

Manchester, M13 9PT, United Kingdom

Location

MeSH Terms

Conditions

Scleroderma, SystemicScleroderma, Diffusedigital ulcersVascular Diseases

Interventions

treprostinil

Condition Hierarchy (Ancestors)

Connective Tissue DiseasesSkin and Connective Tissue DiseasesSkin DiseasesCardiovascular Diseases

Limitations and Caveats

Interpretation of the change in digital ulcer status was limited by the lack of a control group and the discontinuation of the study prior to subjects completing all scheduled visits.

Results Point of Contact

Title
Rex Mauthe, Assoc VP, Regulatory Affairs
Organization
United Therapeutics Corporation

Study Officials

  • James Seibold, MD

    Scleroderma Research Consultants LLC

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 16, 2009

First Posted

February 20, 2009

Study Start

September 1, 2009

Primary Completion

September 1, 2011

Study Completion

September 1, 2011

Last Updated

June 18, 2024

Results First Posted

February 7, 2014

Record last verified: 2014-01

Locations