NCT00829829

Brief Summary

The purpose of this clinical research study was to determine the safety and effectiveness of an experimental drug called rilonacept in subjects with gout who are beginning allopurinol treatment for gout. Subjects will participate in this study for approximately 22 weeks. Rilonacept is being studied for use in preventing allopurinol-induced gout flares.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
241

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Feb 2009

Shorter than P25 for phase_3

Geographic Reach
2 countries

91 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 23, 2009

Completed
4 days until next milestone

First Posted

Study publicly available on registry

January 27, 2009

Completed
5 days until next milestone

Study Start

First participant enrolled

February 1, 2009

Completed
1.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2010

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2010

Completed
6.9 years until next milestone

Results Posted

Study results publicly available

April 28, 2017

Completed
Last Updated

April 28, 2017

Status Verified

March 1, 2017

Enrollment Period

1.2 years

First QC Date

January 23, 2009

Results QC Date

March 20, 2017

Last Update Submit

March 20, 2017

Conditions

Keywords

Metabolism, Inborn ErrorsAllopurinolMetabolic DiseasesGenetic Diseases, InbornMusculoskeletal DiseasesJoint DiseasesArthritisRheumatic DiseasesMetabolic disorderPurine-Pyrimidine Metabolism, Inborn ErrorsGout

Outcome Measures

Primary Outcomes (1)

  • Number of Gout Flares Per Participant Assessed From Day 1 to Day 112 (Week 16)

    A gout flare was defined as participant reported acute articular pain typical of a gout attack that required treatment with an anti-inflammatory therapeutic: had at least 3 of the following 4 signs or symptoms: joint swelling, tenderness, redness, and pain and with at least 1 of the following: rapid onset of pain, decreased range of motion, joint warmth or other symptoms similar to a prior gout flare. Number of gout flares per participant was reported for this outcome measure. For drop-outs, only flares occurred before Day 112 were counted, regardless whether the flares occurred during the treatment period or not.

    Day 1 to Day 112 (Week 16)

Secondary Outcomes (5)

  • Number of Modified Gout Flares Per Participant From Day 1 to Day 112 (Week 16)

    Day 1 to Day 112 (Week 16)

  • Percentage of Participants With at Least One Gout Flare From Day 1 to Day 112 (Week 16)

    Day 1 to Day 112 (Week 16)

  • Percentage of Participants With at Least Two Gout Flares From Day 1 to Day 112 (Week 16)

    Day 1 to Day 112 (Week 16)

  • Number of Gout Flare Days Per Participant From Day 1 to Day 112 (Week 16)

    Day 1 to Day 112 (Week 16)

  • Number of Gout Flare Days With Participant's Pain Score of 5 or More (From Daily Diary) Per Participant From Day 1 to Day 112 (Week 16)

    Day 1 to Day 112 (Week 16)

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Two subcutaneous injections of Placebo (for Rilonacept) as a loading dose on Day 1 followed by a single injection once a week (qw) from Week 1 to Week 15.

Other: Placebo

Rilonacept 80 mg

ACTIVE COMPARATOR

Two subcutaneous injections of Rilonacept 80 mg (for a total of 160 mg) as a loading dose on Day 1, followed by a single 80 mg injection of Rilonacept qw from Week 1 to Week 15.

Drug: Rilonacept 80 mg

Rilonacept 160 mg

ACTIVE COMPARATOR

Two subcutaneous injections of Rilonacept 160 mg (for a total of 320 mg) as a loading dose on Day 1, followed by a single 160 mg injection of Rilonacept qw from Week 1 to Week 15.

Drug: Rilonacept 160 mg

Interventions

PlaceboOTHER

Placebo loading dose followed by placebo injections (2 mL) qw for 16 weeks.

Placebo

Rilonacept 160 mg loading dose followed by Rilonacept 80 mg/2 mL injections qw for 16 weeks.

Rilonacept 80 mg

Rilonacept 320 mg loading dose followed by Rilonacept 160 mg/2 mL injections qw for 16 weeks.

Rilonacept 160 mg

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female 18 to 80 years of age;
  • Previously met the preliminary criteria of the American Rheumatism Association (ARA) for the classification; of the acute arthritis of primary gout;
  • At least 2 gout flares in the year prior to the screening visit;
  • Serum uric acid greater than or equal to 7.5 mg/dL at the screening visit;

You may not qualify if:

  • Acute gout flare within 2 weeks of the screening visit or during screening;
  • Persistent chronic or active infections;
  • History of an allergic reaction to allopurinol;
  • History or presence of cancer within 5 years of the screening visit;
  • Previous exposure to Rilonacept;
  • Use of allopurinol, benzbromarone, febuxostat, probenecid or sulfinpyrazone within 3 months prior to the screening visit.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (91)

Unknown Facility

Birmingham, Alabama, 35294, United States

Location

Unknown Facility

Gilbert, Arizona, 85296, United States

Location

Unknown Facility

Peoria, Arizona, 85381, United States

Location

Unknown Facility

Searcy, Arkansas, 72143, United States

Location

Unknown Facility

Concord, California, 94520, United States

Location

Unknown Facility

San Diego, California, 92103, United States

Location

Unknown Facility

Santa Maria, California, 93454, United States

Location

Unknown Facility

Trumball, Connecticut, 06611, United States

Location

Unknown Facility

Washington D.C., District of Columbia, 20003, United States

Location

Unknown Facility

Daytona Beach, Florida, 32117, United States

Location

Unknown Facility

Delray Beach, Florida, 33446, United States

Location

Unknown Facility

Jacksonville, Florida, 32205, United States

Location

Unknown Facility

Jupiter, Florida, 33458, United States

Location

Unknown Facility

Naples, Florida, 34102, United States

Location

Unknown Facility

St. Petersburg, Florida, 33702, United States

Location

Unknown Facility

Gainsville, Georgia, 30501, United States

Location

Unknown Facility

Rome, Georgia, 30165, United States

Location

Unknown Facility

Tucker, Georgia, 30084, United States

Location

Unknown Facility

Woodstock, Georgia, 30188, United States

Location

Unknown Facility

Boise, Idaho, 83713, United States

Location

Unknown Facility

Avon, Indiana, 46123, United States

Location

Unknown Facility

Evansville, Indiana, 47714, United States

Location

Unknown Facility

South Bend, Indiana, 46601, United States

Location

Unknown Facility

Wichita, Kansas, 67208, United States

Location

Unknown Facility

Bowling Green, Kentucky, 42101, United States

Location

Unknown Facility

Owensboro, Kentucky, 42303, United States

Location

Unknown Facility

Baltimore, Maryland, 21286, United States

Location

Unknown Facility

Ellicott City, Maryland, 21042, United States

Location

Unknown Facility

Resistertown, Maryland, 01136, United States

Location

Unknown Facility

Troy, Michigan, 48098, United States

Location

Unknown Facility

Jackson, Mississippi, 39202, United States

Location

Unknown Facility

Florissant, Missouri, 63031, United States

Location

Unknown Facility

Las Vegas, Nevada, 89123, United States

Location

Unknown Facility

Las Vegas, Nevada, 89146, United States

Location

Unknown Facility

Berkeley Heights, New Jersey, 07922, United States

Location

Unknown Facility

Freehold, New Jersey, 07728, United States

Location

Unknown Facility

Brooklyn, New York, 11201, United States

Location

Unknown Facility

Greensboro, North Carolina, 27408, United States

Location

Unknown Facility

Hickory, North Carolina, 28601, United States

Location

Unknown Facility

Morehead City, North Carolina, 28516, United States

Location

Unknown Facility

Raleigh, North Carolina, 27607, United States

Location

Unknown Facility

Raleigh, North Carolina, 27612, United States

Location

Unknown Facility

Salisbury, North Carolina, 28144, United States

Location

Unknown Facility

Akron, Ohio, 44313, United States

Location

Unknown Facility

Cincinnati, Ohio, 45246, United States

Location

Unknown Facility

Middleburg Heights, Ohio, 44130, United States

Location

Unknown Facility

Perrysburg, Ohio, 43551, United States

Location

Unknown Facility

Duncansville, Pennsylvania, 16635, United States

Location

Unknown Facility

Fountain Hill, Pennsylvania, 18105, United States

Location

Unknown Facility

Huntingdon Valley, Pennsylvania, 19006, United States

Location

Unknown Facility

Lancaster, Pennsylvania, 17601, United States

Location

Unknown Facility

Charleston, South Carolina, 29406, United States

Location

Unknown Facility

Columbia, South Carolina, 29204, United States

Location

Unknown Facility

Greer, South Carolina, 29651, United States

Location

Unknown Facility

North Charleston, South Carolina, 29406, United States

Location

Unknown Facility

Rock Hill, South Carolina, 29732, United States

Location

Unknown Facility

Memphis, Tennessee, 38120, United States

Location

Unknown Facility

Dallas, Texas, 75224, United States

Location

Unknown Facility

Dallas, Texas, 75231, United States

Location

Unknown Facility

Houston, Texas, 77074, United States

Location

Unknown Facility

Longview, Texas, 75605, United States

Location

Unknown Facility

Richardson, Texas, 75080, United States

Location

Unknown Facility

San Antonio, Texas, 78229, United States

Location

Unknown Facility

Burke, Virginia, 22015, United States

Location

Unknown Facility

Richmond, Virginia, 23219, United States

Location

Unknown Facility

Spokane, Washington, 99204, United States

Location

Unknown Facility

Tacoma, Washington, 98405, United States

Location

Unknown Facility

Calgary, Alberta, T2X3X7, Canada

Location

Unknown Facility

Burnaby, British Columbia, V5G1T4, Canada

Location

Unknown Facility

Kamloops, British Columbia, V2C1K7, Canada

Location

Unknown Facility

Kelowna, British Columbia, V1Y3G8, Canada

Location

Unknown Facility

Quesnel, British Columbia, V2J2K3, Canada

Location

Unknown Facility

Victoria, British Columbia, V8R 6V4, Canada

Location

Unknown Facility

Mount Pearl, Newfoundland and Labrador, A1N1W7, Canada

Location

Unknown Facility

St. John's, Newfoundland and Labrador, A1E2E2, Canada

Location

Unknown Facility

Brampton, Ontario, L6W3E1, Canada

Location

Unknown Facility

Corunna, Ontario, N0N1G0, Canada

Location

Unknown Facility

Fort Erie, Ontario, L2A1Z3, Canada

Location

Unknown Facility

Greater Sudbury, Ontario, P3E1H5, Canada

Location

Unknown Facility

Kitchener, Ontario, N2M5N6, Canada

Location

Unknown Facility

Listowel, Ontario, N4W2P4, Canada

Location

Unknown Facility

London, Ontario, N5Z3L2, Canada

Location

Unknown Facility

London, Ontario, N6B2E5, Canada

Location

Unknown Facility

Mississauga, Ontario, L5M2V8, Canada

Location

Unknown Facility

Newmarket, Ontario, L3Y5G8, Canada

Location

Unknown Facility

Toronto, Ontario, M9W4L6, Canada

Location

Unknown Facility

Windsor, Ontario, N8X5A6, Canada

Location

Unknown Facility

Montreal, Quebec, H1T2M4, Canada

Location

Unknown Facility

Québec, Quebec, G1V3M7, Canada

Location

Unknown Facility

Trois-Rivières, Quebec, G8Z1YZ, Canada

Location

Unknown Facility

Saskatoon, Saskatchewan, S7K0H6, Canada

Location

Related Publications (1)

  • Schumacher HR Jr, Evans RR, Saag KG, Clower J, Jennings W, Weinstein SP, Yancopoulos GD, Wang J, Terkeltaub R. Rilonacept (interleukin-1 trap) for prevention of gout flares during initiation of uric acid-lowering therapy: results from a phase III randomized, double-blind, placebo-controlled, confirmatory efficacy study. Arthritis Care Res (Hoboken). 2012 Oct;64(10):1462-70. doi: 10.1002/acr.21690.

Related Links

MeSH Terms

Conditions

Metabolism, Inborn ErrorsMetabolic DiseasesGenetic Diseases, InbornMusculoskeletal DiseasesJoint DiseasesArthritisRheumatic DiseasesPurine-Pyrimidine Metabolism, Inborn ErrorsGout

Interventions

rilonacept

Condition Hierarchy (Ancestors)

Congenital, Hereditary, and Neonatal Diseases and AbnormalitiesNutritional and Metabolic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesCrystal Arthropathies

Results Point of Contact

Title
Clinical Trial Management
Organization
Regeneron Pharmaceuticals, Inc. Phone:

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 23, 2009

First Posted

January 27, 2009

Study Start

February 1, 2009

Primary Completion

May 1, 2010

Study Completion

June 1, 2010

Last Updated

April 28, 2017

Results First Posted

April 28, 2017

Record last verified: 2017-03

Locations