NCT00817063

Brief Summary

The purpose of this study is to investigate the safety and efficacy of alitretinoin in the treatment of severe chronic hand eczema that does not respond to treatment with potent topical steroids.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
599

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jan 2009

Typical duration for phase_3

Geographic Reach
1 country

70 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 5, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

January 6, 2009

Completed
2 days until next milestone

Study Start

First participant enrolled

January 8, 2009

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 26, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 26, 2012

Completed
5.5 years until next milestone

Results Posted

Study results publicly available

November 9, 2017

Completed
Last Updated

April 27, 2020

Status Verified

April 1, 2020

Enrollment Period

3.3 years

First QC Date

January 5, 2009

Results QC Date

July 17, 2017

Last Update Submit

April 10, 2020

Conditions

Keywords

retinoid treatmentfingertip dermatitishyperkeratotic hand eczemavesicular hand eczemapompholyx

Outcome Measures

Primary Outcomes (1)

  • Number of Participants Who Responded as Per Physician's Global Assessment (PGA) at Week 24

    The investigator assigned PGA grades according to a 5-point scale (clear \[not detectable\], almost clear \[less than 10% of affected hand surface\], mild disease \[less than 10% of affected hand surface\], moderate disease \[10% to 30% of affected hand surface\], severe disease \[\>30% of affected hand surface\]). PGA ratings were based on an integrated clinical picture of signs, symptoms, and the extent of disease. Symptoms included erythema, scaling, hyperkeratosis/lichenification, vesiculation, edema, fissures, and pruritus/pain. The PGA scale ranges from 0 (no symptom) to 4 (severe disease). Participants were considered as responders when they had a PGA of clear or almost clear.

    Week 24 (end-of-treatment)

Secondary Outcomes (18)

  • Percentage Change From Baseline in Modified Total Lesion Symptom Score (mTLSS) at the End-of-treatment

    Baseline (Week 0) and Week 24 (end-of-treatment)

  • Number of Participants Who Responded as Per Patient Global Assessment (PaGA) at End-of-treatment

    Week 24 (end-of-treatment)

  • Percentage Change From Baseline in Extent of Disease at End-of-treatment

    Baseline (Week 0) and Week 24 (end-of-treatment)

  • Response Duration for Responding Participants at the End-of-therapy

    Up to 72 Weeks (including 24 weeks of treatment and 48 weeks of follow-up)

  • Time to Relapse for Responding Participants at the End-of-therapy

    Up to 72 Weeks (including 24 weeks of treatment and 48 weeks of follow-up)

  • +13 more secondary outcomes

Study Arms (2)

Alitretinoin

EXPERIMENTAL

Patients will receive alitretinoin 30mg capsule for up to 24 weeks

Drug: alitretinoin

Placebo

EXPERIMENTAL

Patients will receive placebo 30mg capsule for up to 24 weeks

Drug: Placebo

Interventions

Patients receive alitretinoin 30mg one capsule daily for up to 24 weeks

Alitretinoin

Patients receive matching placebo for up to 24 weeks

Placebo

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • all types of chronic hand eczema, lasting for at least 6 months since initial diagnosis
  • rated as severe by the physician
  • unresponsive to highly potent topical corticosteroids, such as clobetasol

You may not qualify if:

  • patients whose disease is adequately controlled by standard non-medicated therapy, including potent topical steroids, skin moisturizers, and avoidance of allergens and irritants
  • patients with known allergens and irritants, who have not made a reasonable effort to avoid the substances
  • patients with psoriasis lesions
  • active fungal, bacterial or viral infections of the hands
  • female patients who are pregnant or breastfeeding
  • female patients of childbearing potential who cannot use or will not commit to use two effective methods of contraception

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (70)

University of Alabama, Birmingham

Birmingham, Alabama, 35233, United States

Location

Radiant Research Inc.

Tucson, Arizona, 85710, United States

Location

Johnson Dermatology

Fort Smith, Arkansas, 72916, United States

Location

Dermatology Research of Arkansas

Little Rock, Arkansas, 72205, United States

Location

Hull Dermatology

Rogers, Arkansas, 72758, United States

Location

Shahram Jacobs, MD, Inc.

Encino, California, 91436, United States

Location

University of California, San Diego Dermatology Clinical Trials Unit

La Jolla, California, 92037, United States

Location

Dermatology Research Associates

Los Angeles, California, 90045, United States

Location

Laser and Dermatology Center

Marina del Rey, California, 90292, United States

Location

Integrated Research Group

Riverside, California, 92506, United States

Location

University of California, Davis

Sacramento, California, 95816, United States

Location

Therapeutics Clinical Research

San Diego, California, 92123, United States

Location

East Bay Psoriasis Treatment Center

San Ramon, California, 94583, United States

Location

Stanford University Dept of Dermatology

Stanford, California, 94305, United States

Location

Solano Clinical Research, Dow Pharmaceutical Sciences

Vallejo, California, 94589, United States

Location

Longmont Clinic, P.C.

Longmont, Colorado, 80501, United States

Location

Western State Clinical Research Inc.

Wheat Ridge, Colorado, 80033, United States

Location

George Washington University - Medical Faculty Associates

Washington D.C., District of Columbia, 20037, United States

Location

Park Avenue Dermatology, PA

Orange Park, Florida, 32073, United States

Location

Palm Beach Research Center

West Palm Beach, Florida, 33409, United States

Location

Toccoa Clinic Medical Associates

Toccoa, Georgia, 30577, United States

Location

Saltzer Medical Group

Nampa, Idaho, 83687, United States

Location

Michael Bukhalo MD

Arlington Heights, Illinois, 60005, United States

Location

Dermassociates, Ltd

Belleville, Illinois, 62226, United States

Location

Schaumburg Dermatology

Schaumburg, Illinois, 60194, United States

Location

Dundee Dermatology

West Dundee, Illinois, 60118, United States

Location

Deaconess Clinic, Inc.

Evansville, Indiana, 47713, United States

Location

Indiana University Dermatology

Indianapolis, Indiana, 37660, United States

Location

The Dermatology Center

New Albany, Indiana, 47150, United States

Location

Dermatology Center of Indiana/Indiana Clinical Trials Center

Plainfield, Indiana, 46168, United States

Location

Kansas City Dermatology, PA

Overland Park, Kansas, 66215, United States

Location

American Dermatology Association

Shawnee Mission, Kansas, 66216, United States

Location

Kansas Medical Clinic

Topeka, Kansas, 66614, United States

Location

Dermatology Specialists

Louisville, Kentucky, 40202, United States

Location

Derm Research, PLLC

Louisville, Kentucky, 40217, United States

Location

Tulane University Health Sciences, Dermatology Dept

New Orleans, Louisiana, 70112, United States

Location

Hamzavi Dermatology Clinic

Fort Gratiot, Michigan, 48059, United States

Location

Silverton Skin Institute

Grand Blanc, Michigan, 48439, United States

Location

Grekin Skin Institute

Warren, Michigan, 48088, United States

Location

MAPS Applied Research Center

Edina, Minnesota, 55435, United States

Location

Minnesota Clinical Studies Research Center

Fridley, Minnesota, 55432, United States

Location

Washington University Dermatology Research

St Louis, Missouri, 63110, United States

Location

South Lincoln Dermatology

Lincoln, Nebraska, 68502, United States

Location

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

UMDNJ - Robert Wood Johnson School of Medicine, Dermatology

Somerset, New Jersey, 08873, United States

Location

St.Luke's/Roosevelt Hospital Center

New York, New York, 10025, United States

Location

Mount Sinai School of Medicine Clinical Dermatology

New York, New York, 10029, United States

Location

Helendale Dermatology and Medical Spa

Rochester, New York, 14609, United States

Location

Derm Research Center of New York Inc.

Stony Brook, New York, 11790, United States

Location

University of North Carolina, Dermatology Department

Chapel Hill, North Carolina, 918-843-9447, United States

Location

Azalea Research Center

Wilmington, North Carolina, 28403, United States

Location

Wake Forrest University School of Medicine

Winston-Salem, North Carolina, 27157, United States

Location

Bernstein Clinical Research Center

Cincinnati, Ohio, 45242, United States

Location

Oregon Dermatology and Research Center

Portland, Oregon, 97210, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Paddington Testing Co.Inc

Philadelphia, Pennsylvania, 19103, United States

Location

University of Pittsburgh Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Rhode Island Hospital

Providence, Rhode Island, 02903, United States

Location

Dermatology Associates of Kingsport

Kingsport, Tennessee, 37660, United States

Location

Tennessee Clinical Research Center

Nashville, Tennessee, 37215, United States

Location

Academy of Clinical Research

Arlington, Texas, 76011, United States

Location

Modern Research Associates

Dallas, Texas, 75231, United States

Location

Center for Clinical Studies

Houston, Texas, 77030, United States

Location

Dermatology Clinical Research Center of San Antonio

San Antonio, Texas, 77056, United States

Location

Center for Clinical Studies

Webster, Texas, 77598, United States

Location

Fletcher Allen Health Care

Burlington, Vermont, 05401, United States

Location

Virginia Clinical Research Inc.

Norfolk, Virginia, 23507, United States

Location

Dermatology and Laser Center NW

Bellingham, Washington, 98281, United States

Location

Premier Clinical Research

Seattle, Washington, 99204, United States

Location

Madison Skin & Research Inc.

Madison, Wisconsin, 53719, United States

Location

Related Publications (4)

  • Diepgen TL, Agner T, Aberer W, Berth-Jones J, Cambazard F, Elsner P, McFadden J, Coenraads PJ. Management of chronic hand eczema. Contact Dermatitis. 2007 Oct;57(4):203-10. doi: 10.1111/j.1600-0536.2007.01179.x.

    PMID: 17868211BACKGROUND
  • Ruzicka T, Larsen FG, Galewicz D, Horvath A, Coenraads PJ, Thestrup-Pedersen K, Ortonne JP, Zouboulis CC, Harsch M, Brown TC, Zultak M. Oral alitretinoin (9-cis-retinoic acid) therapy for chronic hand dermatitis in patients refractory to standard therapy: results of a randomized, double-blind, placebo-controlled, multicenter trial. Arch Dermatol. 2004 Dec;140(12):1453-9. doi: 10.1001/archderm.140.12.1453.

    PMID: 15611422BACKGROUND
  • Ruzicka T, Lynde CW, Jemec GB, Diepgen T, Berth-Jones J, Coenraads PJ, Kaszuba A, Bissonnette R, Varjonen E, Hollo P, Cambazard F, Lahfa M, Elsner P, Nyberg F, Svensson A, Brown TC, Harsch M, Maares J. Efficacy and safety of oral alitretinoin (9-cis retinoic acid) in patients with severe chronic hand eczema refractory to topical corticosteroids: results of a randomized, double-blind, placebo-controlled, multicentre trial. Br J Dermatol. 2008 Apr;158(4):808-17. doi: 10.1111/j.1365-2133.2008.08487.x. Epub 2008 Feb 21.

    PMID: 18294310BACKGROUND
  • Fowler JF, Graff O, Hamedani AG. A phase 3, randomized, double-blind, placebo-controlled study evaluating the efficacy and safety of alitretinoin (BAL4079) in the treatment of severe chronic hand eczema refractory to potent topical corticosteroid therapy. J Drugs Dermatol. 2014 Oct;13(10):1198-204.

MeSH Terms

Conditions

EczemaEczema, Dyshidrotic

Interventions

Alitretinoin

Condition Hierarchy (Ancestors)

DermatitisSkin DiseasesSkin and Connective Tissue DiseasesSkin Diseases, EczematousSkin Diseases, Vesiculobullous

Intervention Hierarchy (Ancestors)

TretinoinVitamin ARetinoidsCarotenoidsPolyenesAlkenesHydrocarbons, AcyclicHydrocarbonsOrganic ChemicalsCyclohexenesCyclohexanesCycloparaffinsHydrocarbons, AlicyclicHydrocarbons, CyclicTerpenesDiterpenesPigments, BiologicalBiological Factors

Results Point of Contact

Title
GSK Response Center
Organization
GlaxoSmithKline

Study Officials

  • GSK Clinical Trials

    GlaxoSmithKline

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 5, 2009

First Posted

January 6, 2009

Study Start

January 8, 2009

Primary Completion

April 26, 2012

Study Completion

April 26, 2012

Last Updated

April 27, 2020

Results First Posted

November 9, 2017

Record last verified: 2020-04

Data Sharing

IPD Sharing
Will share

IPD for this study will be made available via the Clinical Study Data Request site.

Shared Documents
STUDY PROTOCOL, SAP, ICF, CSR
Time Frame
IPD for this study will be made available via the Clinical Study Data Request site.
Access Criteria
IPD for this study will be made available via the Clinical Study Data Request site.
More information

Locations