NCT00812240

Brief Summary

Masitinib in First Line Treatment of Gastro-Intestinal Stromal Tumor (GIST)

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
335

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jan 2009

Longer than P75 for phase_3

Geographic Reach
3 countries

41 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 19, 2008

Completed
3 days until next milestone

First Posted

Study publicly available on registry

December 22, 2008

Completed
10 days until next milestone

Study Start

First participant enrolled

January 1, 2009

Completed
9.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2018

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2018

Completed
Last Updated

February 1, 2023

Status Verified

December 1, 2019

Enrollment Period

9.5 years

First QC Date

December 19, 2008

Last Update Submit

January 31, 2023

Conditions

Keywords

Gastro-Intestinal Stromal TumorGISTmetastaticnon resectable locally advanced

Outcome Measures

Primary Outcomes (1)

  • Progression Free Survival (PFS)

    Progression Free Survival is defined as the time from randomization to first documentation of objective tumor progression (date of tumor assessment documenting progressive disease assessed by CT Scan according to RECIST 1.1 and based on central review) or to death due to any cause (whichever comes first).

    From day of randomization to disease progression or death, assessed for a maximum of 96 months]

Secondary Outcomes (1)

  • Overall Survival (OS)

    From day of randomization to death, assessed for a maximum of 96 months

Study Arms (4)

Masitinib (7.5)

EXPERIMENTAL

Participants receive masitinib (7.5 mg/kg/day), given orally twice daily.

Drug: Masitinib

Masitinib (6.0)

EXPERIMENTAL

Participants receive masitinib (6.0 mg/kg/day), given orally twice daily

Drug: Masitinib

Active Comparator (7.5)

ACTIVE COMPARATOR

Participants receive imatinib at 400 or 600 mg per day

Drug: Imatinib

Active Comparator (6.0)

ACTIVE COMPARATOR

Participants receive imatinib at 400 or 600 mg per day

Drug: Imatinib

Interventions

Also known as: AB1010
Masitinib (6.0)Masitinib (7.5)

imatinib 400 mg or 600 mg per day, per os

Also known as: Gleevec
Active Comparator (6.0)Active Comparator (7.5)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically proven, metastatic or locally advanced non resectable, or recurrent post-surgery GIST
  • Naïve patient or patient previously treated with imatinib as neoadjuvant/adjuvant who relapsed after imatinib discontinuation
  • c-Kit (CD117) positive tumours detected by immuno-histochemically or PDGFR positive if c-Kit negative

You may not qualify if:

  • Patient treated for a cancer other than GIST within 5 years before enrolment, with the exception of basal cell carcinoma or cervical cancer in situ
  • Patient with active central nervous system (CNS) metastasis or with history of CNS metastasis

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (41)

MD Anderson Cancer Center

Orlando, Florida, 32806, United States

Location

The Emory Clinic

Atlanta, Georgia, 30322, United States

Location

Henry Ford Health System

Detroit, Michigan, 48202, United States

Location

Beth Israel Medical Center

New York, New York, 10003, United States

Location

Ohio State University

Columbus, Ohio, 43210, United States

Location

Cancer Centers of the Carolinas

Greenville, South Carolina, 290605, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Centre Hospitalier d'Abbeville

Abbeville, 80142, France

Location

Institut Sainte Catherine

Avignon, 84000, France

Location

Hôpital Jean Minjoz

Besançon, 25000, France

Location

Institut Bergonié

Bordeaux, 33000, France

Location

Hôpital Morvan

Brest, 29200, France

Location

Hôpitalo Henri Mondor

Créteil, 94000, France

Location

Centre Georges François Leclerc

Dijon, 21000, France

Location

Hopital Bocage

Dijon, 21079, France

Location

Centre Hospitalier Victor Jousselin

Dreux, 28100, France

Location

Clinique Pasteur

Évreux, 27000, France

Location

Centre Hospitalier de Gap

Gap, 05000, France

Location

CHD de Vendée

La Roche-sur-Yon, 85925, France

Location

Centre Hsopitalier de La Rochelle

La Rochelle, 17000, France

Location

Centre Hospitalier Robert Boulin

Libourne, 33500, France

Location

Centre Oscar Lambret

Lille, 59000, France

Location

Centre Léon Bérard

Lyon, 69000, France

Location

Institut Paoli Calmette

Marseille, 13200, France

Location

Centre Val d'Aurèle

Montpellier, 34000, France

Location

Centre René Gauducheau

Nantes, 44800, France

Location

Hôpital de la Source

Orléans, 45000, France

Location

Groupe Hospitalier Diaconesse Croix Saint Simon

Paris, 75012, France

Location

Hôpital Européen Georges Pompidou

Paris, 75015, France

Location

Hôpital Bichat Claude Bernard

Paris, 75018, France

Location

Hôpital Tenon

Paris, 75020, France

Location

Hôpital Robert Debré

Reims, 51000, France

Location

Hôpital Charles Nicolle

Rouen, 76000, France

Location

Clinique Armoricaine de Radiologie

Saint-Brieuc, 22000, France

Location

Centre René Huguenin

Saint-Cloud, 92210, France

Location

Institut de Cancérologie de la Loire

Saint-Priest-en-Jarez, 42270, France

Location

Hotel Dieu de France

Beirut, Lebanon

Location

Hôpital Saint-Georges

Beirut, Lebanon

Location

Makassed General Hospital Tarik Jadide

Beirut, Lebanon

Location

Rafik Hariri University Hospital

Beirut, Lebanon

Location

Hôpital Saint-Joseph

Jdeïdé, Lebanon

Location

MeSH Terms

Conditions

Gastrointestinal Stromal TumorsNeoplasm Metastasis

Interventions

masitinibImatinib Mesylate

Condition Hierarchy (Ancestors)

Neoplasms, Connective TissueNeoplasms, Connective and Soft TissueNeoplasms by Histologic TypeNeoplasmsGastrointestinal NeoplasmsDigestive System NeoplasmsDigestive System DiseasesGastrointestinal DiseasesNeoplastic ProcessesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

BenzamidesAmidesOrganic ChemicalsBenzoatesAcids, CarbocyclicCarboxylic AcidsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPiperazinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPyrimidines

Study Officials

  • Antoine Adenis, MD

    Centre Oscar Lambret, Lille, France

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 19, 2008

First Posted

December 22, 2008

Study Start

January 1, 2009

Primary Completion

July 1, 2018

Study Completion

July 1, 2018

Last Updated

February 1, 2023

Record last verified: 2019-12

Locations