NCT00739648

Brief Summary

Patients with Chronic Obstructive Pulmonary Disease (COPD) suffer from frequent and recurrent acute exacerbations (AECB) which are associated with enormous healthcare expenditures and significant morbidity, specifically an increased risk of death, a decline in pulmonary function and a significant change in quality of life. Bacteria appear to have an important role in acute exacerbations in chronic bronchitis and COPD. Studies of acute exacerbations in COPD have shown a reduction in bacterial load with prolonged exacerbation-free interval. In addition, recent studies indicate that acquisition of a new strain of H. influenzae, M. catarrhalis, S. pneumoniae or P. aeruginosa are responsible for many of these exacerbations. Chronic inflammation and bacterial infection predispose many patients to frequent and recurrent acute exacerbations. Mpex believes that intermittent administration of inhaled MP-376 in high risk patients will decrease the incidence of acute exacerbations by both by lowering the organism burden, and resultant inflammation, as well as pre-emptive eradication of any newly acquired bacterial strains.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
322

participants targeted

Target at P75+ for phase_2 chronic-obstructive-pulmonary-disease

Timeline
Completed

Started Oct 2008

Geographic Reach
1 country

39 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 20, 2008

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 22, 2008

Completed
1 month until next milestone

Study Start

First participant enrolled

October 1, 2008

Completed
1.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2010

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2010

Completed
1.9 years until next milestone

Results Posted

Study results publicly available

March 2, 2012

Completed
Last Updated

December 27, 2024

Status Verified

December 1, 2024

Enrollment Period

1.3 years

First QC Date

August 20, 2008

Results QC Date

September 4, 2011

Last Update Submit

December 2, 2024

Conditions

Keywords

COPDPatients

Outcome Measures

Primary Outcomes (1)

  • Exacerbation Rate

    The number of acute exacerbations per patient-year of study participation, where an acute exacerbation was defined as a deterioration in respiratory symptoms that required treatment with antibiotics, corticosteroids, hospitalization or a combination of those treatments.

    From randomization to the patients final study visit (up to 12 months)

Secondary Outcomes (3)

  • Duration of Acute Exacerbation

    from randomization to the patient's final study visit (up to 12 months)

  • Percent Change in Forced Vital Capacity (FVC)

    from baseline to the conclusion of the fourth 28-day treatment cycle (4 months)

  • Percent Change in Forced Expiratory Volume in 1 Second (FEV1)

    from baseline to the conclusion of the fourth 28-day treatment cycle (4 months)

Study Arms (2)

Placebo

PLACEBO COMPARATOR

Placebo inhaled twice daily via the PARI eFlow nebulizer for 5 consecutive days within a 28-day treatment cycle for up to 12 cycles

Drug: Placebo

MP-376 240 mg Twice Daily (BID)

EXPERIMENTAL

MP-376 240 mg BID inhaled via the PARI eFlow nebulizer for 5 consecutive days within a 28-day treatment cycle for up to 12 cycles

Drug: MP-376

Interventions

MP-376DRUG

MP-376 administered via inhalation for 5 consecutive days within 28-day treatment cycles for up to 12 cycles

Also known as: Levofloxacin inhalation solution, Aeroquin
MP-376 240 mg Twice Daily (BID)

same frequency as study drug using the same method of delivery

Also known as: MP-376 color-matched placebo
Placebo

Eligibility Criteria

Age40 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • \> 40 years of age
  • History of COPD
  • Forced expiratory volume in 1 second (FEV1) \</= 70% of predicted and FEV1/Forced vital capacity (FVC) \</= 0.7 value at screening
  • Have at least two acute exacerbation episodes in the proceeding year
  • Clinically stable with no changes in health status within the last 30 days
  • Lifetime smoking history of at least 10 pack-years
  • Willing and able to use a daily electronic diary

You may not qualify if:

  • Use of any systemic or inhaled antibiotics within 30 days prior to baseline
  • History of hypersensitivity to fluoroquinolones or intolerance with aerosol medication
  • Creatinine clearance \< 40 mg/ml/min, AST, ALT \>/= 5 x upper limit of normal (ULN) or total bilirubin \>/= 3 x ULN at Screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (39)

Unknown Facility

Haleyville, Alabama, 35565, United States

Location

Unknown Facility

Hueytown, Alabama, 35023, United States

Location

Unknown Facility

Mobile, Alabama, 36608, United States

Location

Unknown Facility

Montgomery, Alabama, 36117, United States

Location

Unknown Facility

Glendale, Arizona, 85306, United States

Location

Unknown Facility

Phoenix, Arizona, 85006, United States

Location

Unknown Facility

Chula Vista, California, 91911, United States

Location

Unknown Facility

Lomita, California, 90717, United States

Location

Unknown Facility

Long Beach, California, 90822, United States

Location

Unknown Facility

Mission Viejo, California, 92691, United States

Location

Unknown Facility

Oceanside, California, 92056, United States

Location

Unknown Facility

Palo Alto, California, 94304, United States

Location

Unknown Facility

Riverside, California, 92506, United States

Location

Unknown Facility

San Diego, California, 92117, United States

Location

Unknown Facility

San Jose, California, 95124, United States

Location

Unknown Facility

Wheat Ridge, Colorado, 80033, United States

Location

Unknown Facility

Clearwater, Florida, 33765, United States

Location

Unknown Facility

DeBary, Florida, 32713, United States

Location

Unknown Facility

DeLand, Florida, 32720, United States

Location

Unknown Facility

Orlando, Florida, 32806, United States

Location

Unknown Facility

Savannah, Georgia, 31406, United States

Location

Unknown Facility

New Orleans, Louisiana, 70115, United States

Location

Unknown Facility

Taylor, Michigan, 48180, United States

Location

Unknown Facility

Omaha, Nebraska, 68198, United States

Location

Unknown Facility

Buffalo, New York, 14215, United States

Location

Unknown Facility

Ithaca, New York, 14850, United States

Location

Unknown Facility

Greenville, North Carolina, 27834, United States

Location

Unknown Facility

Columbus, Ohio, 43210, United States

Location

Unknown Facility

Maumee, Ohio, 43537, United States

Location

Unknown Facility

Toledo, Ohio, 43614, United States

Location

Unknown Facility

Medford, Oregon, 97504, United States

Location

Unknown Facility

Johnston, Rhode Island, 02919, United States

Location

Unknown Facility

Easley, South Carolina, 29640, United States

Location

Unknown Facility

Gaffney, South Carolina, 29340, United States

Location

Unknown Facility

Spartanburg, South Carolina, 29303, United States

Location

Unknown Facility

Union, South Carolina, 29379, United States

Location

Unknown Facility

San Antonio, Texas, 78212, United States

Location

Unknown Facility

Richmond, Virginia, 23225, United States

Location

Unknown Facility

Salem, Virginia, 24153, United States

Location

Related Publications (2)

  • Leidy NK, Murray LT, Monz BU, Nelsen L, Goldman M, Jones PW, Dansie EJ, Sethi S. Measuring respiratory symptoms of COPD: performance of the EXACT- Respiratory Symptoms Tool (E-RS) in three clinical trials. Respir Res. 2014 Oct 7;15(1):124. doi: 10.1186/s12931-014-0124-z.

  • Leidy NK, Murray LT, Jones P, Sethi S. Performance of the EXAcerbations of chronic pulmonary disease tool patient-reported outcome measure in three clinical trials of chronic obstructive pulmonary disease. Ann Am Thorac Soc. 2014 Mar;11(3):316-25. doi: 10.1513/AnnalsATS.201309-305OC.

MeSH Terms

Conditions

Pulmonary Disease, Chronic Obstructive

Condition Hierarchy (Ancestors)

Lung Diseases, ObstructiveLung DiseasesRespiratory Tract DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Jeffery Nieves, PharmD, Senior Director
Organization
Horizon Pharma USA, Inc.

Study Officials

  • MD

    Amgen

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 20, 2008

First Posted

August 22, 2008

Study Start

October 1, 2008

Primary Completion

January 1, 2010

Study Completion

April 1, 2010

Last Updated

December 27, 2024

Results First Posted

March 2, 2012

Record last verified: 2024-12

Locations