NCT00642668

Brief Summary

This single arm study assessed the efficacy and safety of subcutaneous methoxy polyethylene glycol-epoetin beta (Mircera), a continuous erythropoietin receptor activator (C.E.R.A.), for correction and/or maintenance of hemoglobin levels in participants with chronic kidney disease and renal anemia, who were not treated with erythropoiesis-stimulating agents (ESA) or on dialysis. Eligible participants received monthly subcutaneous injections of methoxy polyethylene glycol-epoetin beta at an initial recommended dose of 1.2 micrograms/kilogram (mcg/kg). The anticipated time on study treatment was 3-10 months, and the target sample size was 200 individuals.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
35

participants targeted

Target at below P25 for phase_4

Timeline
Completed

Started Jun 2008

Geographic Reach
1 country

32 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 19, 2008

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 25, 2008

Completed
3 months until next milestone

Study Start

First participant enrolled

June 30, 2008

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 31, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 31, 2009

Completed
6.6 years until next milestone

Results Posted

Study results publicly available

July 22, 2016

Completed
Last Updated

July 5, 2017

Status Verified

May 1, 2017

Enrollment Period

1.5 years

First QC Date

March 19, 2008

Results QC Date

June 9, 2016

Last Update Submit

June 13, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants Maintaining Average Hemoglobin Concentration During Efficacy Evaluation Period (EEP) Within Target Range

    The EEP was week 29 through week 36. The target range for average hemoglobin concentration was 10.0 - 12.0 g/dL.

    Weeks 29-36

Secondary Outcomes (4)

  • Change From Baseline in Hemoglobin Concentration to Efficacy Evaluation Period (EEP)

    Weeks 0-36

  • Percentage of Participants Maintaining Hemoglobin Concentrations Within Range of 10-12 Grams/Deciliter (g/dL) Throughout Efficacy Evaluation Period (EEP)

    Weeks 29-36

  • Mean Time Spent in Hemoglobin Range of 10-12 g/dL During Efficacy Evaluation Period (EEP)

    Weeks 29-36

  • Percentage of Participants With Adverse Events

    Weeks 1-40

Study Arms (1)

Methoxy Polyethylene Glycol-Epoetin Beta

EXPERIMENTAL

Participants received methoxy polyethylene glycol-epoetin beta treatment monthly for 36 weeks with an efficacy evaluation period (EEP) during weeks 29-36 and followed by a 4 week follow-up period.

Drug: methoxy polyethylene glycol-epoetin beta

Interventions

1.2 mcg/kg administered subcutaneously (sc) monthly for 36 weeks (initial recommended dose)

Also known as: Mircera
Methoxy Polyethylene Glycol-Epoetin Beta

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Adult participants, \>=18 years of age;
  • Chronic renal anemia;
  • No ESA therapy during previous 3 months.

You may not qualify if:

  • Transfusion of red blood cells during previous 2 months;
  • Poorly controlled hypertension requiring hospitalization in previous 6 months;
  • Significant acute or chronic bleeding.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (32)

ASZ Aalst

Aalst, 9300, Belgium

Location

ZNA Middelheim

Antwerp, 2020, Belgium

Location

ZNA Stuivenberg

Antwerp, 2060, Belgium

Location

AZ Sint Lucas Brugge

Assebroek, 8310, Belgium

Location

CH EpiCURA Site Ath

Ath, 7800, Belgium

Location

CH EpiCURA Site Louis Caty

Baudour, 7331, Belgium

Location

Imeldaziekenhuis

Bonheiden, 2820, Belgium

Location

Clinique Saint-Jean- Botanique

Brussels, 1000, Belgium

Location

CHU Brugmann (Victor Horta)

Brussels, 1020, Belgium

Location

Clin Univ de Bxl Hôpital Erasme

Brussels, 1070, Belgium

Location

HIS (Joseph Bracops)

Brussels, 1070, Belgium

Location

UZ Brussel

Brussels, 1090, Belgium

Location

CHIREC Edith Cavell

Brussels, 1180, Belgium

Location

Cliniques Universitaires St-Luc

Brussels, 1200, Belgium

Location

CHU de Charleroi

Charleroi, 6000, Belgium

Location

AZ Sint Blasius (Dendermonde)

Dendermonde, 9200, Belgium

Location

UZ Antwerpen

Edegem, 2650, Belgium

Location

ZOL (Sint Jan)

Genk, 3600, Belgium

Location

AZ Sint Lucas (Sint Lucas)

Ghent, 9000, Belgium

Location

UZ Gent

Ghent, 9000, Belgium

Location

CH EpiCURA Site Hornu

Hornu, 7301, Belgium

Location

CHR Hutois

Huy, 4500, Belgium

Location

Jan Yperman Onze Lieve Vrouw

Ieper, 8900, Belgium

Location

UZ Leuven Gasthuisberg

Leuven, 3000, Belgium

Location

Chr de La Citadelle

Liège, 4000, Belgium

Location

CHU Sart-Tilman

Liège, 4000, Belgium

Location

Clinique Saint-Joseph

Liège, 4000, Belgium

Location

AZ Delta (Campus Wilgenstraat)

Roeselare, 8800, Belgium

Location

AZ Nikolaas (Sint Niklaas)

Sint-Niklaas, 9100, Belgium

Location

CHWapi site IMC

Tournai, 7500, Belgium

Location

AZ Turnhout Sint Jozef

Turnhout, 2300, Belgium

Location

CHR de Verviers - East Belgium

Verviers, 4800, Belgium

Location

MeSH Terms

Conditions

Anemia

Interventions

continuous erythropoietin receptor activator

Condition Hierarchy (Ancestors)

Hematologic DiseasesHemic and Lymphatic Diseases

Results Point of Contact

Title
Medical Communications
Organization
Hoffmann-La Roche

Study Officials

  • Clinical Trials

    Hoffmann-La Roche

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 19, 2008

First Posted

March 25, 2008

Study Start

June 30, 2008

Primary Completion

December 31, 2009

Study Completion

December 31, 2009

Last Updated

July 5, 2017

Results First Posted

July 22, 2016

Record last verified: 2017-05

Locations