NCT00632814

Brief Summary

A prospective study to evaluate the effect of rFVIII-FS in different prophylactic regimens on bleeding events frequency and development of arthropathy in Previously Treated and Minimally treated Hemophilia A pediatric population.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
32

participants targeted

Target at below P25 for phase_4

Timeline
Completed

Started Jun 2007

Typical duration for phase_4

Geographic Reach
1 country

4 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2007

Completed
9 months until next milestone

First Submitted

Initial submission to the registry

March 4, 2008

Completed
7 days until next milestone

First Posted

Study publicly available on registry

March 11, 2008

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2009

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

February 8, 2011

Completed
Last Updated

July 1, 2015

Status Verified

June 1, 2015

Enrollment Period

2.3 years

First QC Date

March 4, 2008

Results QC Date

January 14, 2011

Last Update Submit

June 4, 2015

Conditions

Keywords

Kogenate,Children,Factor VIII,Hemophilia A,Prophylactic

Outcome Measures

Primary Outcomes (1)

  • Percentage of Participants With Less Than 2 Joint Bleeds During the 9-month Treatment Period

    Up to 9 months

Secondary Outcomes (8)

  • Number of Bleeds Per Participant During the 9-month Treatment Period

    Up to 9 months

  • Number of Participants With Bleeding Events During the 9-month Treatment Period

    Up to 9 months

  • Number of Participants With Joint Bleeds During the 9-month Treatment Period

    Up to 9 months

  • Number of Participants in Each Group at the End of the Study

    Up to 9 months

  • Actual Monthly rFVIII-FS Consumption

    Up to 9 months

  • +3 more secondary outcomes

Study Arms (3)

rFVIII-FS (Kogenate FS, BAY14-2222), 70 IU/kg qw

EXPERIMENTAL

rFVIII-FS (Octocog-alfa, antihemophilic factor \[recombinant\]) 70 IU/kg, dosing by injection once per week \[qw\] (weekly on Day 7 + 1 after previous injection) for 9 months. Dose escalation was permitted due to joint bleeding (escalation to 35 IU/kg twice a week or further escalation to 25 IU/kg three times a week)

Drug: rFVIII-FS (Kogenate FS, BAY14-2222) 70 IU/kg, dosing once per week

rFVIII-FS (Kogenate FS, BAY14-2222), biw (30 IU/kg + 40 IU/kg)

EXPERIMENTAL

rFVIII-FS (Octocog-alfa, antihemophilic factor \[recombinant\]) 70 IU/kg, dosing by injection twice per week \[biw\] (30 IU/kg \[day 1\] + 40 IU/kg \[day 4\]) for 9 months. Dose escalation was permitted due to joint bleeding (escalation to 25 IU/kg three times a week)

Drug: rFVIII-FS (Kogenate FS, BAY14-2222), 70 IU/kg twice per week (30 IU/kg + 40 IU/kg)

rFVIII-FS (Kogenate FS, BAY14-2222), tiw (3 x 25 IU/kg)

EXPERIMENTAL

rFVIII-FS (Octocog-alfa, antihemophilic factor \[recombinant\]) 75 IU/kg, dosing by injection three times per week \[tiw\] (3 x 25 IU/kg \[day 1, 3, 5\]) for 9 months. No escalation opportunity for participants in this group

Drug: rFVIII-FS (Kogenate FS, BAY14-2222) 75 IU/kg, dosing three times per week (3 x 25 IU/kg)

Interventions

rFVIII-FS (Octocog-alfa, antihemophilic factor \[recombinant\]) 70 IU/kg, dosing by injection once per week (weekly on Day 7 + 1 after previous injection) for 9 months. Dose escalation was permitted due to joint bleeding (escalation to 35 IU/kg twice a week or further escalation to 25 IU/kg three times a week)

rFVIII-FS (Kogenate FS, BAY14-2222), 70 IU/kg qw

rFVIII-FS (Octocog-alfa, antihemophilic factor \[recombinant\]) 70 IU/kg, dosing by injection twice per week (30 IU/kg \[day 1\] + 40 IU/kg \[day 4\]) for 9 months. Dose escalation was permitted due to joint bleeding (escalation to 25 IU/kg three times a week)

rFVIII-FS (Kogenate FS, BAY14-2222), biw (30 IU/kg + 40 IU/kg)

rFVIII-FS (Octocog-alfa, antihemophilic factor \[recombinant\]) 75 IU/kg, dosing by injection three times per week (3 x 25 IU/kg \[day 1, 3, 5\]) for 9 months. No escalation opportunity for patients in this group

rFVIII-FS (Kogenate FS, BAY14-2222), tiw (3 x 25 IU/kg)

Eligibility Criteria

Age1 Year - 12 Years
Sexmale
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Male
  • Severe hemophilia A or moderate hemophilia A
  • years of age
  • Requiring treatment with FVIII

You may not qualify if:

  • Current or prior inhibitor or familial antecedents of inhibitor
  • Surgery required during the study (9 months)
  • Positive for HIV

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

Unknown Facility

Kirov, 610 027, Russia

Location

Unknown Facility

Moscow, 105077, Russia

Location

Unknown Facility

Saint Petersburg, 191186, Russia

Location

Unknown Facility

Yekaterinburg, 620149, Russia

Location

Related Publications (1)

  • V.V. Vdovin, T.A. Andreeva, T.A. Chernova, F.G. Perina, E.E.M. Shiller, P.V. Svirin, M. Maas Enriquez, and S. Rauchensteiner. Prophylaxis with Once, Twice or Three-Times Weekly Dosing of rFVIII-FS Prevents Joint Bleeds in a Previously Treated Pediatric Population with Moderate/Severe Hemophilia A. Journal of Coagulation Disorders 2011; 3:(1). October 2011

    RESULT

Related Links

MeSH Terms

Conditions

Hemophilia A

Interventions

recombinant FVIII, sugar formulatedF8 protein, humanBAY 14-2222

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesCoagulation Protein DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Limitations and Caveats

Protocol deviations were not excluded: e.g. a previously untreated patient developed the transitory inhibitor; change to a higher group did not always occur according protocol; there was temporary lack of smaller vial sizes at the centers.

Results Point of Contact

Title
Therapeutic Area Head
Organization
BAYER

Study Officials

  • Bayer Study Director

    Bayer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 4, 2008

First Posted

March 11, 2008

Study Start

June 1, 2007

Primary Completion

September 1, 2009

Study Completion

September 1, 2009

Last Updated

July 1, 2015

Results First Posted

February 8, 2011

Record last verified: 2015-06

Locations