NCT00625846

Brief Summary

This phase II trial studies the side effects and how well pazopanib hydrochloride works in treating patients with advanced thyroid cancer. Pazopanib hydrochloride may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth and by stopping blood flow to the tumor.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
152

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Feb 2008

Longer than P75 for phase_2

Geographic Reach
5 countries

22 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 22, 2008

Completed
5 days until next milestone

First Submitted

Initial submission to the registry

February 27, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

February 28, 2008

Completed
10.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 21, 2018

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

August 13, 2019

Completed
7 months until next milestone

Results Posted

Study results publicly available

February 26, 2020

Completed
Last Updated

February 26, 2020

Status Verified

February 1, 2020

Enrollment Period

10.8 years

First QC Date

February 27, 2008

Results QC Date

February 4, 2020

Last Update Submit

February 4, 2020

Conditions

Outcome Measures

Primary Outcomes (2)

  • Overall Response Rate (in Cohorts 1-3)

    The tumor response rate is defined as the percentage of eligible patients who fulfill RECIST 1.0 for a complete or partial response at two consecutive assessments at least 8 weeks apart for patients in Cohorts 1-3. Per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions and assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>= 30% decrease in the sum of the longest diameter of target lesions; Overall Response (OR) = CR + PR.

    Up to 3 years

  • Confirmed Tumor Response (in the Differentiated Thyroid Cancer Expansion Cohort)

    The confirmed tumor response rate is defined as the percentage of eligible patients who fulfill RECIST 1.0 for a complete or partial response at two consecutive assessments at least 8 weeks apart for patients with differentiated thyroid cancer who are thyroglobulin antibody negative. Per Response Evaluation Criteria In Solid Tumors Criteria (RECIST v1.0) for target lesions and assessed by MRI: Complete Response (CR), Disappearance of all target lesions; Partial Response (PR), \>= 30% decrease in the sum of the longest diameter of target lesions; Overall Response (OR) = CR + PR.

    Up to 3 years

Secondary Outcomes (3)

  • Toxicity as Measured by the Percentage of Patients Reporting a Grade 3+ Adverse Event Deemed Possibly, Probably, or Definitely Related to Treatment

    Up to 3 years

  • Progression-Free Survival at 6 Months (Cohorts 1 and 2 Only)

    Time from registration to the date of progression or last follow-up, whichever comes first, assessed up to 6 months

  • Progression-Free Survival at 3 Months (Cohort 3 Only)

    Time from registration to the date of progression or last follow-up, whichever comes first, assessed up to 3 months

Other Outcomes (6)

  • Change in Blood Markers for Angiogenesis

    Baseline to up to 3 years

  • Proportion of Patients With Differentiated Thyroid Cancer and Medullary Thyroid Cancer Who Have Not Failed Treatment at 6 Months (3 Months for Anaplastic Thyroid Cancer)

    Up to 6 months

  • Overall Survival

    Time from registration to date of last follow-up or death due to any cause, assessed up to 3 years

  • +3 more other outcomes

Study Arms (4)

Cohort 1 (DTC)

EXPERIMENTAL

Patients with differentiated thyroid cancer (DTC) receive 800 mg pazopanib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Other: Laboratory Biomarker AnalysisDrug: Pazopanib Hydrochloride

Cohort 2 (MTC)

EXPERIMENTAL

Patients with medullary thyroid cancer (MTC) receive 800 mg pazopanib hydrochloride PO QD on days 1-28. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Drug: Pazopanib Hydrochloride

Cohort 3 (ATC)

EXPERIMENTAL

Patients with anaplastic thyroid cancer (ATC) receive 800 mg pazopanib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Other: Laboratory Biomarker Analysis

Expansion Cohort (DTC)

EXPERIMENTAL

Patients with confirmed, differentiated thyroid cancer (DTC) who are thyroglobulin antibody negative receive 800 mg pazopanib hydrochloride PO QD on days 1-28. Courses repeat every 28 days in the absence of disease progression or unacceptable toxicity.

Other: Laboratory Biomarker AnalysisDrug: Pazopanib Hydrochloride

Interventions

Correlative studies

Cohort 1 (DTC)Cohort 3 (ATC)Expansion Cohort (DTC)

Given PO

Also known as: GW786034B, Votrient
Cohort 1 (DTC)Cohort 2 (MTC)Expansion Cohort (DTC)

Eligibility Criteria

Age19 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically or cytologically confirmed differentiated, medullary or anaplastic thyroid cancer that is now advanced or metastatic; NOTE: patients with thyroid lymphomas or sarcomas are specifically excluded, as are patients with metastatic disease from other sites of origin to thyroid
  • Patients with confirmed differentiated thyroid cancer to be enrolled in the expanded/additional differentiated thyroid cancer (DTC) cohort must be thyroglobulin antibody negative
  • Zero, one or two prior therapeutic regimens (this includes cytotoxic plus non-cytotoxic therapeutic regimens)
  • Absence of sensitivity to therapeutic radioiodine (differentiated only)
  • Measurable disease, defined as at least one lesion that can be accurately measured in at least one dimension (longest diameter to be recorded) as \> 20 mm with conventional techniques or as \> 10 mm with spiral computed tomography (CT) scan; NOTE: disease that is measurable by physical examination only is not eligible
  • Life expectancy \> 3 months
  • Eastern Cooperative Oncology Group (ECOG) performance status (PS) 0, 1, or 2 (Karnofsky \>= 60%)
  • Leukocytes \> 3,000/mcL obtained =\< 7 days prior to registration
  • Absolute neutrophil count \> 1,500/mcL obtained =\< 7 days prior to registration
  • Platelets \> 100,000/mcL obtained =\< 7 days prior to registration
  • Total bilirubin =\< 1.5 X institutional upper limit of normal (ULN) obtained =\< 7 days prior to registration (if there is reason to believe that the patient has Gilbert's syndrome, the bilirubin can be fractionated; if the fractionated bilirubin is consistent with Gilbert's syndrome and there is no other possible explanation for the elevated indirect bilirubin, the patient may be eligible for the study if and only if the direct bilirubin is =\< 1.5 X institutional ULN)
  • Aspartate aminotransferase (AST) (serum glutamic oxaloacetic transaminase \[SGOT\]) \< 2.5 X institutional ULN obtained =\< 7 days prior to registration
  • Creatinine =\< 1.5 X ULN obtained =\< 7 days prior to registration
  • Proteinuria =\< + on urinalysis (may re-check) obtained =\< 7 days prior to registration
  • International normalized ratio (INR) =\< 1.2 X the ULN obtained =\< 7 days prior to registration
  • +7 more criteria

You may not qualify if:

  • Anaplastic, differentiated, medullary: a total of \> 2 prior therapeutic regimens (this total includes cytotoxic plus non-cytotoxic regimens); Note: enrollment of anaplastic, differentiated, and medullary patients who have had zero, one or two prior therapeutic regimens (cytotoxic plus non-cytotoxic regimens) is allowed - provided therapy ceased \> 21 days prior to registration;
  • NOTE: the principal investigator of the study should be contacted in the event of uncertainty related patient eligibility based upon prior therapies
  • Disease that is measurable by physical examination only
  • Any of the following:
  • Radiotherapy =\< 4 weeks prior to registration
  • Major surgery =\< 4 weeks prior to registration
  • Radiotherapy to \>= 25% of bone marrow
  • Concurrent therapy with octreotide unless tumor progression on this therapy has been demonstrated
  • Any other ongoing investigational agents
  • History of allergic reactions attributed to compounds of similar chemical or biologic composition to GW786034 (pazopanib) or other agents used in the study
  • \> +1 proteinuria (\< 30 mg/dL) on two consecutive dipstick or other urine assessments taken at least 1 week apart; NOTE: (in cases where questions arise related to disparate proteinuria measurements, the study principal investigator \[PI\] should be consulted for assistance in determining patient study eligibility)
  • Corrected QT interval (QTc) prolongation (defined as a QTc interval \>= 480 msecs) or other significant electrocardiogram (ECG) abnormalities (e.g. frequent ventricular ectopy, evidence of ongoing myocardial ischemia); NOTE: the principal investigator of the study should be contacted in the event of uncertainty related patient eligibility based upon ECG changes
  • Receiving cytochrome P450 (CYP) interactive concomitant medications; certain medications that act through the CYP450 system are specifically prohibited in patients receiving GW786034 (pazopanib) because in vitro data indicate that the agent has the potential to interact with the cytochrome P450 isoenzymes cytochrome P450, family 2, subfamily C, polypeptide 9 (CYP2C9) and cytochrome P450, family 3, subfamily A, polypeptide 4 (CYP3A4); certain other agents should be used with caution
  • Any condition (e.g., gastrointestinal tract disease resulting in an inability to take oral medication or a requirement for IV alimentation, prior surgical procedures affecting absorption, or active peptic ulcer disease) that impairs their ability to swallow and retain GSK786034 (pazopanib)
  • Any of the following conditions:
  • +14 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (22)

Mayo Clinic in Arizona

Scottsdale, Arizona, 85259, United States

Location

University of Colorado Hospital

Aurora, Colorado, 80045, United States

Location

Mayo Clinic in Florida

Jacksonville, Florida, 32224-9980, United States

Location

University of Iowa/Holden Comprehensive Cancer Center

Iowa City, Iowa, 52242, United States

Location

Johns Hopkins University/Sidney Kimmel Cancer Center

Baltimore, Maryland, 21287, United States

Location

Wayne State University/Karmanos Cancer Institute

Detroit, Michigan, 48201, United States

Location

Fairview Ridges Hospital

Burnsville, Minnesota, 55337, United States

Location

Fairview-Southdale Hospital

Edina, Minnesota, 55435, United States

Location

Unity Hospital

Fridley, Minnesota, 55432, United States

Location

Minnesota Oncology Hematology PA-Maplewood

Maplewood, Minnesota, 55109, United States

Location

Abbott-Northwestern Hospital

Minneapolis, Minnesota, 55407, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Park Nicollet Clinic - Saint Louis Park

Saint Louis Park, Minnesota, 55416, United States

Location

United Hospital

Saint Paul, Minnesota, 55102, United States

Location

Washington University School of Medicine

St Louis, Missouri, 63110, United States

Location

University of Wisconsin Hospital and Clinics

Madison, Wisconsin, 53792, United States

Location

Sir Charles Gairdner Hospital

Nedlands, Western Australia, 6009, Australia

Location

Chinese University of Hong Kong-Prince of Wales Hospital

Shatin, Hong Kong, China

Location

National University Hospital Singapore

Singapore, 119074, Singapore

Location

National Cancer Centre

Singapore, 169610, Singapore

Location

Johns Hopkins Singapore

Singapore, 308433, Singapore

Location

National Taiwan University Hospital

Taipei, 100, Taiwan

Location

Related Publications (2)

  • Bible KC, Menefee ME, Lin CJ, Millward MJ, Maples WJ, Goh BC, Karlin NJ, Kane MA, Adkins DR, Molina JR, Donehower RC, Lim WT, Flynn PJ, Richardson RL, Traynor AM, Rubin J, LoRusso PM, Smallridge RC, Burton JK, Suman VJ, Kumar A, Voss JS, Rumilla KM, Kipp BR, Chintakuntlawar AV, Harris P, Erlichman C. An International Phase 2 Study of Pazopanib in Progressive and Metastatic Thyroglobulin Antibody Negative Radioactive Iodine Refractory Differentiated Thyroid Cancer. Thyroid. 2020 Sep;30(9):1254-1262. doi: 10.1089/thy.2019.0269. Epub 2020 Jul 29.

  • Bible KC, Suman VJ, Molina JR, Smallridge RC, Maples WJ, Menefee ME, Rubin J, Sideras K, Morris JC 3rd, McIver B, Burton JK, Webster KP, Bieber C, Traynor AM, Flynn PJ, Goh BC, Tang H, Ivy SP, Erlichman C; Endocrine Malignancies Disease Oriented Group; Mayo Clinic Cancer Center; Mayo Phase 2 Consortium. Efficacy of pazopanib in progressive, radioiodine-refractory, metastatic differentiated thyroid cancers: results of a phase 2 consortium study. Lancet Oncol. 2010 Oct;11(10):962-72. doi: 10.1016/S1470-2045(10)70203-5. Epub 2010 Sep 17.

MeSH Terms

Conditions

Thyroid NeoplasmsCarcinoma, MedullaryThyroid Carcinoma, Anaplastic

Interventions

pazopanib

Condition Hierarchy (Ancestors)

Endocrine Gland NeoplasmsNeoplasms by SiteNeoplasmsHead and Neck NeoplasmsEndocrine System DiseasesThyroid DiseasesCarcinoma, NeuroendocrineNeuroendocrine TumorsNeuroectodermal TumorsNeoplasms, Germ Cell and EmbryonalNeoplasms by Histologic TypeAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms, Ductal, Lobular, and MedullaryNeoplasms, Nerve Tissue

Results Point of Contact

Title
Keith C. Bible, M.D., Ph.D.
Organization
Mayo Clinic

Study Officials

  • Keith C Bible

    Mayo Clinic

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
LTE60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
NIH
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 27, 2008

First Posted

February 28, 2008

Study Start

February 22, 2008

Primary Completion

December 21, 2018

Study Completion

August 13, 2019

Last Updated

February 26, 2020

Results First Posted

February 26, 2020

Record last verified: 2020-02

Locations