NCT00607984

Brief Summary

The prognosis of children and adolescents with high risk tumors of the central nervous system and other miscellaneous solid tumors is poor despite modern treatment protocols. Frequently, physicians suggest additional therapy with high dose chemotherapy after a good initial response to standard doses of treatment has been obtained, so as to reduce the chance that the tumor will recur. We propose a regimen of high dose thiotepa and melphalan followed by rescue of the patient's previously stored hematopoietic (blood manufacturing) system with blood stem cells. The aim of this study is to prove that this therapy is tolerable in children and adolescents, that it results in tolerable levels of toxicity, and that it improves the survival of this group of children as compared to standard therapy given in the past

Trial Health

55
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Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
20

participants targeted

Target at below P25 for not_applicable

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2006

Completed
1.6 years until next milestone

First Submitted

Initial submission to the registry

January 23, 2008

Completed
14 days until next milestone

First Posted

Study publicly available on registry

February 6, 2008

Completed
2.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2010

Completed
Last Updated

February 6, 2008

Status Verified

January 1, 2008

Enrollment Period

4.5 years

First QC Date

January 23, 2008

Last Update Submit

February 5, 2008

Conditions

Keywords

thiotepamelphalanbrain tumortumors of central nervous system and other solid tumors

Outcome Measures

Primary Outcomes (1)

  • survival

    10 yeaer follow up

Secondary Outcomes (1)

  • toxicity

    180 days

Study Arms (1)

single

EXPERIMENTAL
Drug: thiotepa melphalan

Interventions

thiotepa 900 mg per meter squared total, on days -11,-10,-4,-3 melphalan 140 mg per meter squared total on days -11,-10,-4,-3 autologous stem cell transplant in day 0

single

Eligibility Criteria

Age1 Year - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Age 1-21 years
  • CNS tumors, hepatic tumors and other solid tumors that are chemosensitive
  • Minimal disease as determined by either radiological studies or biochemical markers (as determined by treating physician).
  • Consent of patient or surrogate.

You may not qualify if:

  • Not pregnant or nursing
  • Fertile patients must use effective contraception
  • No known HIV or AIDS infection
  • No active bacterial, fungal, or viral infection
  • No medical condition that would preclude study treatment
  • Positive pregnancy test or failure to use contraceptives.
  • Creatinine \>1.5 times limit of normal for age
  • SGOT or SGPT more than 3 times normal.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Schneider Children's Medical Center of Israel

Petah Tikva, 49202, Israel

RECRUITING

MeSH Terms

Conditions

Central Nervous System NeoplasmsNeoplasmsBrain Neoplasms

Condition Hierarchy (Ancestors)

Nervous System NeoplasmsNeoplasms by SiteNervous System DiseasesBrain DiseasesCentral Nervous System Diseases

Study Officials

  • Jerry Stein, MD

    Schneider Children's Medical Center, Israel

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Jerry Stein, MD

CONTACT

Isaac Yaniv, MD

CONTACT

Study Design

Study Type
interventional
Phase
not applicable
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER

Study Record Dates

First Submitted

January 23, 2008

First Posted

February 6, 2008

Study Start

June 1, 2006

Primary Completion

December 1, 2010

Last Updated

February 6, 2008

Record last verified: 2008-01

Locations