NCT00559962

Brief Summary

To determine safety and effectiveness of low-dose therapeutic AEGR-733 +/- atorvastatin, ezetimibe or fenofibrate (compared to placebo) on liver fat accumulation measured by Magnetic Resonance Spectroscopy

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
260

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Oct 2007

Shorter than P25 for phase_2

Geographic Reach
1 country

15 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2007

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

November 15, 2007

Completed
4 days until next milestone

First Posted

Study publicly available on registry

November 19, 2007

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2008

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2008

Completed
4.3 years until next milestone

Results Posted

Study results publicly available

February 22, 2013

Completed
Last Updated

February 23, 2018

Status Verified

February 1, 2018

Enrollment Period

1 year

First QC Date

November 15, 2007

Results QC Date

January 18, 2013

Last Update Submit

February 21, 2018

Conditions

Keywords

LDLhepatic fat

Outcome Measures

Primary Outcomes (1)

  • Absolute Change From Baseline in Percent Hepatic Fat

    Absolute change from Baseline in percent hepatic fat

    Baseline and 12 weeks on study drug

Secondary Outcomes (1)

  • Absolute Change From Baseline in Percent Hepatic Fat

    Baseline and 12 weeks on study drug

Study Arms (8)

1

PLACEBO COMPARATOR

Placebo

Drug: placebo

2

ACTIVE COMPARATOR

2.5 mg AEGR-733

Drug: AEGR-733

3

ACTIVE COMPARATOR

5 mg AEGR-733

Drug: AEGR-733

4

ACTIVE COMPARATOR

7.5 mg AEGR-733

Drug: AEGR-733

5

ACTIVE COMPARATOR

10 mg AEGR-733

Drug: AEGR-733

6

ACTIVE COMPARATOR

5 mg AEGR-733 + 20 mg atorvastatin

Drug: AEGR-733 and atorvastatin

7

ACTIVE COMPARATOR

5 mg AEGR-733 + 145 mg fenofibrate

Drug: AEGR-733 and fenofibrate

8

ACTIVE COMPARATOR

5 mg AEGR-733 + 10 mg ezetimibe

Drug: AEGR-733 and ezetimibe

Interventions

3 capsules each evening for each 4-week period

2

3 capsules each evening for each 4-week period

1

3 capsules each evening for each 4-week period

6

3 capsules each evening for each 4-week period

7

3 capsules each evening for each 4-week period

8

Eligibility Criteria

Age18 Years - 70 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • LDL-C between 100 and 190 mg/dL
  • Hepatic fat under 6.2% per MRS

You may not qualify if:

  • Pregnant or lactating females
  • Uncontrolled hypertension \>180/95 mmHg
  • Chronic renal insufficiency - serum creatinine \>2.5 mg/dL at screen
  • Liver disease; i.e., hepatitis, cirrhosis
  • Major surgery within 3 months of screen
  • Cardiac insufficiency
  • Hx of malignancy other than basal or squamous cell within past 5 yrs
  • Participation in any investigational drug study within 6 wks of screen
  • Prior exposure to AEGR-733 in past 12 months
  • Serious or unstable medical or psychological conditions
  • More than one alcoholic drink per day
  • Regular consumption of grapefruit juice or meds known to be metabolized by CYP 3A4
  • Currently taking corticosteroids
  • Other lipid-lowering meds (washout permitted)
  • Fish oil, niacin grater than 200 mg/day and herbal weight loss products (washout permitted)
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

Scripps Clinic

San Diego, California, 92128, United States

Location

Radiant Research

Santa Rosa, California, 95405, United States

Location

MedStar Research Institute

Washington D.C., District of Columbia, 20003, United States

Location

Radiant Research

Chicago, Illinois, 60610, United States

Location

University of Iowa

Iowa City, Iowa, 52242, United States

Location

LMARC

Louisville, Kentucky, 40213, United States

Location

Maine Research Associates

Auburn, Maine, 04210, United States

Location

Health Trends Research

Baltimore, Maryland, 21209, United States

Location

Johns Hopkins

Baltimore, Maryland, 21287, United States

Location

Washington Univ. School of Medicine

St Louis, Missouri, 63110, United States

Location

Sterling Research Group

Cincinnati, Ohio, 45219, United States

Location

University of Pennsylvania

Philadelphia, Pennsylvania, 19104, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

Clinical Trial Network

Houston, Texas, 77074, United States

Location

dgd Research

San Antonio, Texas, 78229, United States

Location

MeSH Terms

Conditions

Hyperlipidemias

Interventions

BMS201038AtorvastatinFenofibrateEzetimibe

Condition Hierarchy (Ancestors)

DyslipidemiasLipid Metabolism DisordersMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

PyrrolesAzolesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsHeptanoic AcidsFatty AcidsLipidsFibric AcidsIsobutyratesButyratesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsPhenyl EthersEthersBenzophenonesBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPhenolsKetonesAzetidinesAzetines

Results Point of Contact

Title
Mark Sumeray, MD, Chief Medical Officer
Organization
Aegerion Pharmaceuticals

Study Officials

  • William Sasiela, PhD

    Aegerion Pharmaceuticals, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

November 15, 2007

First Posted

November 19, 2007

Study Start

October 1, 2007

Primary Completion

October 1, 2008

Study Completion

November 1, 2008

Last Updated

February 23, 2018

Results First Posted

February 22, 2013

Record last verified: 2018-02

Locations